Observational Study in Cystic Fibrosis Patients Using TOBI® PODHALER® or Other FDA Approved Inhaled Antipseudomonal Antibacterial Drugs

NCT ID: NCT02449031

Last Updated: 2022-03-22

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Total Enrollment

409 participants

Study Classification

OBSERVATIONAL

Study Start Date

2015-05-05

Study Completion Date

2021-12-31

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This is a multicenter, prospective, two cohort, observational study over a 5-year period in Cystic Fibrosis (CF) patients with chronic Pseudomonas aeruginosa infection.The study will collect data over 1 year on respiratory function, antibacterial effectiveness, and clinical outcomes of treatment with inhaled antipseudomonal antibiotics and data over 5 years on microbiological and safety assessments.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

This study will include CF patients chronically colonized with P. aeruginosa enrolled in the Cystic Fibrosis Foundation (CFF) PortCF registry and using TOBI® PODHALER® or another FDA-approved inhaled antipseudomonal antibiotic. No therapeutic intervention will be assigned and physicians will use their discretion in choosing a treatment regimen for their patients.

Sputum samples (primarily collected during routine clinical follow-up) from patients able to spontaneously produce sputum will be sent to a central laboratory for analysis.

In addition, this study will include two optional sub-studies for qualifying patients in the first study year - Sputum microbiology sub-study and TOBI® PODHALER® sputum pharmacokinetics (PK) sub-study.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Pseudomonas Aeruginosa in Cystic Fibrosis

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Observational Model Type

COHORT

Study Time Perspective

PROSPECTIVE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

TOBI® PODHALER® cohort

TOBI® PODHALER®

Intervention Type DRUG

non-TOBI® PODHALER® cohort

Approximately 250 patients treated with other FDA-approved inhaled antipseudomonal antibacterial drugs at enrollment

TOBI®

Intervention Type DRUG

tobramycin inhalation solution, USP

Bethkis®

Intervention Type DRUG

tobramycin inhalation solution

Cayston®

Intervention Type DRUG

aztreonam for inhalation solution

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

TOBI® PODHALER®

Intervention Type DRUG

TOBI®

tobramycin inhalation solution, USP

Intervention Type DRUG

Bethkis®

tobramycin inhalation solution

Intervention Type DRUG

Cayston®

aztreonam for inhalation solution

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* ≥ 6 years of age.
* Documented FEV1 ≥ 25% predicted in the previous year.
* Diagnosis of cystic fibrosis.
* Established diagnosis of chronic P. aeruginosa infection of the lungs defined as two or more positive P. aeruginosa cultures in the previous year as documented in the subject's medical history (this may include a history of one positive culture in the year prior to enrollment and one positive culture from the specimen collected at the baseline visit).
* Prescribed and initiated chronic treatment with FDA-approved inhaled antipseudomonal antibiotic for chronic P. aeruginosa infection (e.g. TOBI® PODHALER®, TOBI®, Cayston® and Bethkis®).
* Actively enrolled or willingness to enroll in PortCF registry.
* Willing and able to provide written informed consent or, parent/guardian consent and where applicable pediatric assent, for participation and use of relevant clinical data previously captured in PortCF.
* Anticipated to have good adherence to routine visits, defined as the investigator having good knowledge that the patient has been to at least 2-3 routine visits in the previous year.

Exclusion Criteria

* Documented FEV1 \< 25% predicted in the previous year.
* Current participation in an interventional clinical study with an inhaled antibiotic treatment.
* Treatment with compounded tobramycin (e.g. the use of tobramycin IV solution adapted for use by inhalation).
* Treatment with inhaled antipseudomonal antibacterial drug(s) that are not FDA approved.
* Patients undergoing an early eradication regimen for CF (first line therapy).
Minimum Eligible Age

6 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Cystic Fibrosis Foundation

OTHER

Sponsor Role collaborator

Mylan Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Novartis Investigative Site

Anchorage, Alaska, United States

Site Status

Novartis Investigative Site

Little Rock, Arkansas, United States

Site Status

Novartis Investigative Site

Bellflower, California, United States

Site Status

Novartis Investigative Site

Fullerton, California, United States

Site Status

Novartis Investigative Site

Los Angeles, California, United States

Site Status

Novartis Investigative Site

Madera, California, United States

Site Status

Novartis Investigative Site

Hartford, Connecticut, United States

Site Status

Novartis Investigative Site

New Haven, Connecticut, United States

Site Status

Novartis Investigative Site

Stamford, Connecticut, United States

Site Status

Novartis Investigative Site

Gainesville, Florida, United States

Site Status

Novartis Investigative Site

Miami, Florida, United States

Site Status

Novartis Investigative Site

Orlando, Florida, United States

Site Status

Novartis Investigative Site

Tampa, Florida, United States

Site Status

Novartis Investigative Site

Atlanta, Georgia, United States

Site Status

Novartis Investigative Site

Boise, Idaho, United States

Site Status

Novartis Investigative Site

Chicago, Illinois, United States

Site Status

Novartis Investigative Site

Indianapolis, Indiana, United States

Site Status

Novartis Investigative Site

Iowa City, Iowa, United States

Site Status

Novartis Investigative Site

New Orleans, Louisiana, United States

Site Status

Novartis Investigative Site

Boston, Massachusetts, United States

Site Status

Novartis Investigative Site

Detroit, Michigan, United States

Site Status

Novartis Investigative Site

Grand Rapids, Michigan, United States

Site Status

Novartis Investigative Site

Ypsilanti, Michigan, United States

Site Status

Novartis Investigative Site

Jackson, Mississippi, United States

Site Status

Novartis Investigative Site

Kansas City, Missouri, United States

Site Status

Novartis Investigative Site

Billings, Montana, United States

Site Status

Novartis Investigative Site

Omaha, Nebraska, United States

Site Status

Novartis Investigative Site

Lebanon, New Hampshire, United States

Site Status

Novartis Investigative Site

New Brunswick, New Jersey, United States

Site Status

Novartis Investigative Site

New Hyde Park, New York, United States

Site Status

Novartis Investigative Site

Winston-Salem, North Carolina, United States

Site Status

Novartis Investigative Site

Akron, Ohio, United States

Site Status

Novartis Investigative Site

Oklahoma City, Oklahoma, United States

Site Status

Novartis Investigative Site

Hershey, Pennsylvania, United States

Site Status

Novartis Investigative Site

Philadelphia, Pennsylvania, United States

Site Status

Novartis Investigative Site

Philadelphia, Pennsylvania, United States

Site Status

Novartis Investigative Site

Charleston, South Carolina, United States

Site Status

Novartis Investigative Site

Sioux Falls, South Dakota, United States

Site Status

Novartis Investigative Site

Nashville, Tennessee, United States

Site Status

Novartis Investigative Site

Austin, Texas, United States

Site Status

Novartis Investigative Site

Dallas, Texas, United States

Site Status

Novartis Investigative Site

Tyler, Texas, United States

Site Status

Novartis Investigative Site

Salt Lake City, Utah, United States

Site Status

Novartis Investigative Site

Burlington, Vermont, United States

Site Status

Novartis Investigative Site

Norfolk, Virginia, United States

Site Status

Novartis Investigative Site

Richmond, Virginia, United States

Site Status

Novartis Investigative Site

Spokane, Washington, United States

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

CTBM100C2407

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.