Randomized, Controlled Study of CF Patients Between 3 Months and Less Than 7 Years

NCT ID: NCT01082367

Last Updated: 2016-07-15

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

50 participants

Study Classification

INTERVENTIONAL

Study Start Date

2010-04-30

Study Completion Date

2015-06-30

Brief Summary

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This study investigated the efficacy of inhaled TOBI treatment for early infections of P. aeruginosa in paediatric patients with cystic fibrosis.

Detailed Description

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Conditions

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Treatment of Early Pulmonary Infections With P. Aeruginosa in Cystic Fibrosis Patients

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

CROSSOVER

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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TOBI (tobramycin inhaled solution)/Placebo

Participants randomized to TOBI received the investigational treatment for 28 days twice daily (bi)d in the first treatment cycle. At the end of first treatment cycle, participants who were positive for P. aeruginosa entered the open label (OL) phase of the study and received TOBI for 28 days bid. Participants who were negative for P. aeruginosa at the end of first treatment cycle and agreed to participate in the cross-over treatment period received placebo for 28 days bid (second treatment cycle).

Group Type EXPERIMENTAL

TOBI

Intervention Type DRUG

TOBI (tobramycin inhaled solution)

Placebo

Intervention Type DRUG

Placebo

Placebo/TOBI

Participants randomized to placebo group received 0.9 % saline (NaCl) for 28 days bid in the first treatment cycle. At the end of first treatment cycle, participants who were positive for P. aeruginosa entered the OL phase of the study and received TOBI for 28 days bid. Participants who were negative for P. aeruginosa at the end of first treatment cycle and agreed to participate in the cross-over treatment period received TOBI for 28 days bid (second treatment cycle).

Group Type PLACEBO_COMPARATOR

TOBI

Intervention Type DRUG

TOBI (tobramycin inhaled solution)

Placebo

Intervention Type DRUG

Placebo

Interventions

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TOBI

TOBI (tobramycin inhaled solution)

Intervention Type DRUG

Placebo

Placebo

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Diagnosis of cystic fibrosis
* Early lower respiratory tract infection with P. aeruginosa,

Exclusion Criteria

* Known local or systemic hypersensitivity to aminoglycosides or inhaled antibiotics.
* Administration of loop diuretics within 7 days prior to study drug administration.
Minimum Eligible Age

3 Months

Maximum Eligible Age

6 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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Novartis Investigative Site

Toronto, Ontario, Canada

Site Status

Novartis Investigative Site

Montreal, Quebec, Canada

Site Status

Novartis Investigative Site

Alexandria, , Egypt

Site Status

Novartis Investigative Site

Bordeaux, , France

Site Status

Novartis Investigative Site

Paris, , France

Site Status

Novartis Investigative Site

Dresden, , Germany

Site Status

Novartis Investigative Site

Pátrai, Greece, Greece

Site Status

Novartis Investigative Site

Thessaloniki, GR, Greece

Site Status

Novartis Investigative Site

Thessaloniki, GR, Greece

Site Status

Novartis Investigative Site

Debrecen, Hungary, Hungary

Site Status

Novartis Investigative Site

Kaposvár, Hungary, Hungary

Site Status

Novartis Investigative Site

Szeged, Hungary, Hungary

Site Status

Novartis Investigative Site

Debrecen, , Hungary

Site Status

Novartis Investigative Site

Milan, MI, Italy

Site Status

Novartis Investigative Site

Bucharest, , Romania

Site Status

Novartis Investigative Site

Kazan', , Russia

Site Status

Novartis Investigative Site

Voronezh, , Russia

Site Status

Novartis Investigative Site

Yaroslavl, , Russia

Site Status

Novartis Investigative Site

Zurich, Switzerland, Switzerland

Site Status

Countries

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Canada Egypt France Germany Greece Hungary Italy Romania Russia Switzerland

References

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Ratjen F, Moeller A, McKinney ML, Asherova I, Alon N, Maykut R, Angyalosi G; EARLY study group. Eradication of early P. aeruginosa infection in children <7 years of age with cystic fibrosis: The early study. J Cyst Fibros. 2019 Jan;18(1):78-85. doi: 10.1016/j.jcf.2018.04.002. Epub 2018 Apr 21.

Reference Type DERIVED
PMID: 29685813 (View on PubMed)

Other Identifiers

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2009-016590-15

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CTBM100C2304

Identifier Type: -

Identifier Source: org_study_id

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