Trial of Aeroquin Versus Tobramycin Inhalation Solution (TIS) in Cystic Fibrosis (CF) Patients

NCT ID: NCT01270347

Last Updated: 2024-12-13

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

282 participants

Study Classification

INTERVENTIONAL

Study Start Date

2011-01-31

Study Completion Date

2013-06-30

Brief Summary

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Patients with cystic fibrosis (CF) suffer from chronic infections of the lower respiratory tract that can be caused by one or multiple bacteria, including Pseudomonas aeruginosa, which has been particularly problematic to eradicate and been implicated as the major cause of morbidity and mortality in CF patients. Aerosol delivery of antibiotics directly to the lung increases the local concentrations of antibiotic at the site of infection resulting in improved antimicrobial effects compared to systemic administration. Bacterial resistance to current aerosol antibiotic treatments indicate a need for improved therapies to treat CF patients with pulmonary infections caused by multi-drug resistant Pseudomonas aeruginosa and other bacteria. High concentrations of MP-376 delivered directly to the lung are projected to have antimicrobial effects on even the most resistant organisms.

Detailed Description

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This study will assess the comparative safety of MP-376 (Aeroquin) and Tobramycin Inhalation solution (TIS) \[TOBI® Novartis Pharmaceuticals\] over three consecutive cycles of 28-days treatment followed by 28-days off in stable CF patients with chronic P. aeruginosa lung infection. Efficacy data for MP-376 and TIS at the end of the first 28-day treatment period will also be compared, as well as explored over multiple treatment cycles.

Study patients participating in Mpex 209 will be given the option to participate in a six-month open label extension phase of the Mpex 209 protocol. The open label extension will allow enrolled patients to receive three additional courses of MP-376 (levofloxacin inhalation solution, Aeroquin™).

Study with completed results acquired from Horizon in 2024.

Conditions

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Cystic Fibrosis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Aeroquin

Aeroquin, Inhaled Levofloxacin (MP-376)

Group Type EXPERIMENTAL

MP-376 (Levofloxacin Solution for Inhalation)

Intervention Type DRUG

MP-376 (Aeroquin, Levofloxacin solution for Inhalation) 240 mg administered BID for 28-days treatment followed by 28 days off treatment

TIS

Tobramycin Inhalation solution (TIS) \[TOBI® Novartis Pharmaceuticals\]

Group Type ACTIVE_COMPARATOR

TIS (Tobramycin Inhalation Solution)

Intervention Type DRUG

Tobramycin Inhalation Solution administered BID over 3 consecutive cycles of 28-days treatment followed by 28 days off treatment

Interventions

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MP-376 (Levofloxacin Solution for Inhalation)

MP-376 (Aeroquin, Levofloxacin solution for Inhalation) 240 mg administered BID for 28-days treatment followed by 28 days off treatment

Intervention Type DRUG

TIS (Tobramycin Inhalation Solution)

Tobramycin Inhalation Solution administered BID over 3 consecutive cycles of 28-days treatment followed by 28 days off treatment

Intervention Type DRUG

Other Intervention Names

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(Aeroquin, Levofloxacin solution for Inhalation) TOBI

Eligibility Criteria

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Inclusion Criteria

* \> 12 years of age
* Confirmed Diagnosis of Cystic Fibrosis
* Positive sputum culture for P. aeruginosa within the past 12 months
* Patients are able to elicit an FEV1 \>/= 25% but \</= 85% of predicted value at screening
* Have received at least 3 courses of inhaled tobramycin over the preceding 12 months
* Clinically stable with no changes in health status within the last 28 days
* Able to reproducibly produce sputum and perform spirometry

Exclusion Criteria

* Use of any nebulized or systemic antibiotics within 28 days prior to baseline
* History of hypersensitivity to fluoroquinolones or inhaled or systemic aminoglycosides including tobramycin or any excipients
* Evidence of acute upper within 10 days or lower respiratory infections within 28 days prior to dosing
* CrCl \< 20 at Screening
* History of lung transplantation

Extension Portion of the Study: Patients enrolled in Mpex 209 are permitted to participate in the open label extension as long as they complete Visit 7 (Day 168), provide informed consent for participation in the open label extension of in the study and are clinically stable, as assessed by the Investigator.
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Forest Laboratories

INDUSTRY

Sponsor Role collaborator

Amgen

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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MD

Role: STUDY_DIRECTOR

Amgen

Locations

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Mobile, Alabama, United States

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Anchorage, Alaska, United States

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Phoenix, Arizona, United States

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Tucson, Arizona, United States

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Little Rock, Arkansas, United States

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La Jolla, California, United States

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Long Beach, California, United States

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Childrens Hospital

Los Angeles, California, United States

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Los Angeles, California, United States

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Oakland, California, United States

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Orange, California, United States

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Palo Alto, California, United States

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Sacramento, California, United States

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San Diego, California, United States

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San Diego, California, United States

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San Francisco, California, United States

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Aurora, Colorado, United States

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Denver, Colorado, United States

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Hartford, Connecticut, United States

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New Haven, Connecticut, United States

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Wilmington, Delaware, United States

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Gainesville, Florida, United States

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Jacksonville, Florida, United States

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Miami, Florida, United States

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Orlando, Florida, United States

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St. Petersburg, Florida, United States

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Tampa, Florida, United States

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Atlanta, Georgia, United States

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Boise, Idaho, United States

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Chicago, Illinois, United States

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Chicago, Illinois, United States

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Glenview, Illinois, United States

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Niles, Illinois, United States

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Peoria, Illinois, United States

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Indianapolis, Indiana, United States

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Indianapolis, Indiana, United States

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Wichita, Kansas, United States

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Lexington, Kentucky, United States

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Louisville, Kentucky, United States

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Portland, Maine, United States

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Baltimore, Maryland, United States

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Boston, Massachusetts, United States

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Boston, Massachusetts, United States

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Worcester, Massachusetts, United States

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Ann Arbor, Michigan, United States

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Detroit, Michigan, United States

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Grand Rapids, Michigan, United States

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Minneapolis, Minnesota, United States

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Jackson, Mississippi, United States

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Columbia, Missouri, United States

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Kansas City, Missouri, United States

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St Louis, Missouri, United States

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Omaha, Nebraska, United States

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Las Vegas, Nevada, United States

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Lebanon, New Hampshire, United States

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Manchester, New Hampshire, United States

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Livingston, New Jersey, United States

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Morristown, New Jersey, United States

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Albuquerque, New Mexico, United States

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Albany Medical College #2

Albany, New York, United States

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Albany, New York, United States

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New Hyde Park, New York, United States

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New York, New York, United States

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New York, New York, United States

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Syracuse, New York, United States

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Valhalla, New York, United States

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Durham, North Carolina, United States

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Akron, Ohio, United States

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Cincinnati, Ohio, United States

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Columbus, Ohio, United States

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Dayton, Ohio, United States

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Toledo, Ohio, United States

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Oklahoma CF Center

Oklahoma City, Oklahoma, United States

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Oklahoma City, Oklahoma, United States

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Hershey, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Pittsburgh, Pennsylvania, United States

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Charleston, South Carolina, United States

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Columbia, South Carolina, United States

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Sioux Falls, South Dakota, United States

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Memphis, Tennessee, United States

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Nashville, Tennessee, United States

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Austin, Texas, United States

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Dallas, Texas, United States

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Fort Worth, Texas, United States

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Houston, Texas, United States

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San Antonio, Texas, United States

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Tyler, Texas, United States

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Salt Lake City, Utah, United States

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Colchester, Vermont, United States

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Charlottesville, Virginia, United States

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Norfolk, Virginia, United States

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Portsmouth, Virginia, United States

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Richmond, Virginia, United States

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Seattle, Washington, United States

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Morgantown, West Virginia, United States

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Milwaukee, Wisconsin, United States

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Milwaukee, Wisconsin, United States

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Hôpital Pellegrin Enfants - CHU Bordeaux

Bordeaux, , France

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CRCM adultes et enfants Service des maladies respiratoires et pédiatrie 1 CHU- Arnaud de Villeneuve

Montpellier, , France

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Hôpital Cochin

Paris, , France

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Hôpital Necker-Enfants Malades

Paris, , France

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Hôpital Haut-Lévêque CHU de Bordeaux

Pessac, , France

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CRCM adulte Hôpital Larrey-CHU de Toulouse

Toulouse, , France

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Charité Campus Virchow-Klinikum

Berlin, , Germany

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Universitätskinderklinik Dresden Mukoviszidose-Ambulanz

Dresden, , Germany

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Universitätsklinikum Essen

Essen, , Germany

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Katharina-Kasper Kliniken GmbH St. Elisabethen-Krankenhaus Medizinische Klinik

Frankfurt, , Germany

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Universitätsklinikum Frankfurt

Frankfurt, , Germany

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Universitätsklinik Gießen und Marburg GmbH Zentrum für Kinderheilkunde und Jugendmedizin

Gieben, , Germany

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Kinderärztliche Gemeinschaftspraxis Dr. H. E. Heuer, Dr. C. Runge, W. Sextro

Hamburg, , Germany

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Universitätsklinikum Kiel

Kiel, , Germany

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Dr. von Haunersches Kinderspital der Universität München Christiane Herzog Ambulanz

Munich, , Germany

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Ludwig-Maximilians Universität Klinikum Innenstadt

München, , Germany

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Universitätsklinik für Kinder- und Jugendmedizin

Tübingen, , Germany

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Cork University Hospital

Cork, , Ireland

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Beaumont Hospital

Dublin, , Ireland

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National Children's Hospital Tallaght

Dublin, , Ireland

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St. Vincent's University Hospital

Dublin, , Ireland

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Rambam Medical Center

Haifa, , Israel

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Hadassah Medical Center Mount Scopus

Jerusalem, , Israel

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Schneider Childrens Medical Center of Israel

Petah Tikva, , Israel

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Safra Childrens Hospital, Sheba Medical Center

Ramat Gan, , Israel

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Belfast City Hospital

Belfast, , United Kingdom

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Birmingham Heartlands Hospital

Birmingham, , United Kingdom

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Castle Hill Hospital

Cottingham, , United Kingdom

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St James's University Hospital

Leeds, , United Kingdom

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King's College Hospital

London, , United Kingdom

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University Hospital Llandough, Penarth

Penarth, , United Kingdom

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Countries

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United States France Germany Ireland Israel United Kingdom

References

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Elborn JS, Flume PA, Cohen F, Loutit J, VanDevanter DR. Safety and efficacy of prolonged levofloxacin inhalation solution (APT-1026) treatment for cystic fibrosis and chronic Pseudomonas aeruginosa airway infection. J Cyst Fibros. 2016 Sep;15(5):634-40. doi: 10.1016/j.jcf.2016.01.005. Epub 2016 Feb 28.

Reference Type DERIVED
PMID: 26935334 (View on PubMed)

Other Identifiers

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2010-019634-26

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

Mpex-209

Identifier Type: -

Identifier Source: org_study_id