ALPN-101 (Acazicolcept) in Systemic Lupus Erythematosus

NCT ID: NCT04835441

Last Updated: 2025-08-15

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

76 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-06-22

Study Completion Date

2024-07-09

Brief Summary

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This is Phase 2, multinational, randomized, blinded study to evaluate the safety, tolerability, efficacy, immunogenicity, pharmacokinetics and pharmacodynamics of ALPN-101 (acazicolcept) in adults with moderate to severe active systemic lupus erythematosus (SLE)

Detailed Description

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Conditions

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Systemic Lupus Erythematosus

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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ALPN-101 (Acazicolcept)

Participants received a weight-based dose of 3 milligrams/kilogram (mg/kg) ALPN-101 once every 2 weeks (Q2W) up to 24 weeks.

Group Type EXPERIMENTAL

ALPN-101

Intervention Type DRUG

Intravenous infusion via an infusion pump.

Placebo

Participants received placebo matched to ALPN-101 up to 24 weeks.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Intravenous infusion via an infusion pump.

Interventions

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ALPN-101

Intravenous infusion via an infusion pump.

Intervention Type DRUG

Placebo

Intravenous infusion via an infusion pump.

Intervention Type DRUG

Other Intervention Names

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Acazicolcept

Eligibility Criteria

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Inclusion Criteria

* SLE onset ≥ 6 months prior to Screening
* Positive ANA and/or elevated anti-dsDNA and/or elevated anti-Smith antibody test
* Active lupus at Screening and Baseline, as defined per-protocol and confirmed by the study's medical monitor, including a SLEDAI score at Screening of ≥ 6 and a clinical score at Baseline of ≥ 4
* Standard lupus medications must be stable prior to Screening

Exclusion Criteria

* Life-threatening or organ system-threatening lupus activity that is anticipated to require increased treatment during the study
* Proteinuria consistent with nephrotic syndrome
* Active lupus-related neuropsychiatric disease
* Drug-induced lupus
* Recent or serious ongoing infection; risk or history of serious infection
* Receipt of live vaccination within 8 weeks of Day 1, or expected to require live vaccination during the study
* Prior diagnosis of, or fulfills diagnostic criteria for, another rheumatic disease that overlaps with lupus or another autoimmune or inflammatory disease that may confound clinical assessments or increase subject risk in the study
* Diagnosis of, or fulfills diagnostic criteria for fibromyalgia
* Functional class IV
* Serious lupus disease activity, which warrants immediate immunosuppressive therapy not appropriate for the study or which makes the possibility of receiving placebo or investigational agent an inappropriate risk
Minimum Eligible Age

18 Years

Maximum Eligible Age

70 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Alpine Immune Sciences Inc, A Subsidiary of Vertex

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Investigational Site (107)

Anniston, Alabama, United States

Site Status

Investigational Site (189)

Phoenix, Arizona, United States

Site Status

Investigational Site (155)

Los Angeles, California, United States

Site Status

Investigational Site (109)

San Diego, California, United States

Site Status

Investigational Site (169)

Santa Barbara, California, United States

Site Status

Investigational Site (106)

DeBary, Florida, United States

Site Status

Investigational Site (120)

Hialeah, Florida, United States

Site Status

Investigational Sites (134)

Miami, Florida, United States

Site Status

Investigational Site (152)

Ormond Beach, Florida, United States

Site Status

Investigational Site (133)

Plantation, Florida, United States

Site Status

Investigational Site (190)

Tamarac, Florida, United States

Site Status

Investigational Site (163)

Tampa, Florida, United States

Site Status

Investigational Site (173)

Idaho Falls, Idaho, United States

Site Status

Investigational Site (156)

Skokie, Illinois, United States

Site Status

Investigational Site (138)

Grand Blanc, Michigan, United States

Site Status

Investigational Site (164)

Las Vegas, Nevada, United States

Site Status

Investigational Site (175)

Brooklyn, New York, United States

Site Status

Investigational Site (115)

Manhasset, New York, United States

Site Status

Investigational Site (179)

Charlotte, North Carolina, United States

Site Status

Investigational Site (112)

Crossville, Tennessee, United States

Site Status

Investigational Site (186)

Memphis, Tennessee, United States

Site Status

Investigational Site (171)

Baytown, Texas, United States

Site Status

Investigational Site (143)

Bellaire, Texas, United States

Site Status

Investigational Site (118)

Colleyville, Texas, United States

Site Status

Investigational Site (166)

Fort Worth, Texas, United States

Site Status

Investigational Site (121)

Houston, Texas, United States

Site Status

Investigational Site (104)

Mesquite, Texas, United States

Site Status

Investigational Site (162)

San Antonio, Texas, United States

Site Status

Investigational Site (127)

San Antonio, Texas, United States

Site Status

Investigational Site (149)

Marseille, , France

Site Status

Investigational Site (128)

Paris, , France

Site Status

Investigational Site (161)

Paris, , France

Site Status

Investigational Site (181)

Budapest, , Hungary

Site Status

Investigational Site (180)

Gyula, , Hungary

Site Status

Investigational Site (183)

Székesfehérvár, , Hungary

Site Status

Investigational Site (160)

Elblag, , Poland

Site Status

Investigational Site (110)

Krakow, , Poland

Site Status

Investigational Site (108)

Poznan, , Poland

Site Status

Investigational Site (119)

Poznan, , Poland

Site Status

Investigational Site (165)

Wroclaw, , Poland

Site Status

Investigational Site (191)

Caguas, , Puerto Rico

Site Status

Investigational Site (187)

San Juan, , Puerto Rico

Site Status

Investigational Site (137)

A Coruña, , Spain

Site Status

Investigational Site (139)

Seville, , Spain

Site Status

Investigational Site (184)

Taichung, , Taiwan

Site Status

Investigational Site (182)

Taipei, , Taiwan

Site Status

Countries

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United States France Hungary Poland Puerto Rico Spain Taiwan

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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AIS-A03

Identifier Type: -

Identifier Source: org_study_id

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