Phase 2 Placebo-Controlled Study to Assess the Safety and Efficacy of ESK-001 in Active Systemic Lupus Erythematosus

NCT ID: NCT05966480

Last Updated: 2025-08-01

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE2

Total Enrollment

408 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-06-26

Study Completion Date

2027-09-01

Brief Summary

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The purpose of this study is to assess the clinical efficacy, safety, PK, and PD of multiple dose levels of ESK-001 compared with placebo in adult patients with SLE.

Detailed Description

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This study will consist of a 5 week screening period, 48 week treatment period, and a 4 week follow up period for a total of 57 weeks. Each participant will be randomized to receive ESK-001 or placebo for 48 weeks. An open label extension study will be available for those patients who complete the study.

Conditions

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SLE

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors

Study Groups

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ESK-001 Dose Level 1

ESK-001 administered as an oral tablet

Group Type EXPERIMENTAL

ESK-001

Intervention Type DRUG

Oral tablet

ESK-001 Dose Level 2

ESK-001 administered as an oral tablet

Group Type EXPERIMENTAL

ESK-001

Intervention Type DRUG

Oral tablet

ESK-001 Dose Level 3

ESK-001 administered as an oral tablet

Group Type EXPERIMENTAL

ESK-001

Intervention Type DRUG

Oral tablet

Placebo

Placebo administered as an oral tablet

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Oral tablet

Interventions

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ESK-001

Oral tablet

Intervention Type DRUG

Placebo

Oral tablet

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

Patients with 6 or more months of SLE according to the 2019 EULAR/ACR criteria, have positive autoantibodies or low complement at screening, and have active SLE as measured by SLEDAI-2K of 6 or more, or 4 or more if joint involvement is present.

Patients need to be on treatment which can be:

* A stable dose of oral corticosteroid (≤40 mg/day prednisone or equivalent) for a minimum of 2 weeks prior to signing of the informed consent form (ICF) at the Screening Visit. The dose of oral corticosteroid the patient is taking should not increase between screening and Week 0 (Day 1).
* And/or antimalarial treatment (e.g., hydroxychloroquine, chloroquine, quinacrine),
* And/or no more than 1 of the following conventional DMARDS:

* Azathioprine ≤200 mg/day
* Mycophenolate mofetil ≤2 g/day or mycophenolic acid ≤1.44 g/day
* Oral, subcutaneous, or intramuscular (IM) methotrexate ≤20 mg/week.

Exclusion Criteria

* Drug-induced SLE or other autoimmune diseases that, in the opinion of the Investigator, are likely to confound efficacy assessments
* Active, proliferative lupus nephritis that in the Investigator's opinion may require treatment not allowed by the protocol
* Current disease other than SLE that, in the opinion of the Investigator, is likely to interfere with SLE disease activity assessments. Examples include severe fibromyalgia, severe osteoarthritis and severe cardiorespiratory diseases.
* Active severe or unstable neuropsychiatric SLE including, but not limited to the following: aseptic meningitis; cerebral vasculitis; myelopathy; demyelination syndromes (ascending or transverse myelitis, acute inflammatory demyelinating polyradiculopathy); acute confusional state; impaired level of consciousness; psychosis; acute stroke or stroke syndrome; cranial neuropathy; new seizures; cerebellar ataxia; and mononeuritis multiplex.

* That would make the patient unable to fully understand the ICF, or
* Where, in the opinion of the Principal Investigator, protocol-specified SOC is insufficient and utilization of a more aggressive therapeutic approach not permitted in the protocol, is indicated
* Known history of a primary immunodeficiency or an underlying condition such as HIV infection or splenectomy that predisposes the patient to infection
* Currently active, clinically significant infection of any kind
* Clinically significant chronic infection (eg, osteomyelitis, bronchiectasis) within 8 weeks prior to signing the ICF (chronic fungal nail infections are allowed)
* Any infection requiring hospitalization or treatment with IV anti-infectives not completed at least 4 weeks prior to signing the ICF
* Any infection requiring oral anti-infectives (including antivirals) within 2 weeks prior to Day 1
* Any severe herpes infection at any time prior to Week 0 (Day 1), including, but not limited to, disseminated herpes (ever), herpes encephalitis (ever), recurrent herpes zoster (defined as 2 episodes within 2 years), or ophthalmic herpes (ever)

* Active herpes zoster infection within 12 weeks of prior to signing the ICF
* Active herpes simplex virus within 4 weeks of Day 1
Minimum Eligible Age

18 Years

Maximum Eligible Age

70 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Alumis Inc

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Investigator Site #1046

Anniston, Alabama, United States

Site Status

Investigator Site #1104

La Jolla, California, United States

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Investigator Site #1050

Los Alamitos, California, United States

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Investigator Site #1168

Mission Hills, California, United States

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Investigator Site #1174

Napa, California, United States

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Investigator Site #1061

Upland, California, United States

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Investigator Site #1048

Aventura, Florida, United States

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Investigator Site #1063

Avon Park, Florida, United States

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Investigator Site #1176

Bradenton, Florida, United States

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Investigator Site #1045

Clearwater, Florida, United States

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Investigator Site #1055

Coral Gables, Florida, United States

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Investigator Site #1097

Coral Springs, Florida, United States

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Investigator Site #1091

Daytona Beach, Florida, United States

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Investigator Site #1051

DeBary, Florida, United States

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Investigator Site #1087

Hollywood, Florida, United States

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Investigator Site #1135

Kissimmee, Florida, United States

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Investigator Site #1060

Miami, Florida, United States

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Investigator Site #1093

Miami, Florida, United States

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Investigator Site #1057

Miami, Florida, United States

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Investigator Site #1067

Miami Lakes, Florida, United States

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Investigator Site #1090

Plantation, Florida, United States

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Investigator Site #1089

Tampa, Florida, United States

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Investigator Site #1170

Atlanta, Georgia, United States

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Investigator Site #1052

College Park, Georgia, United States

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Investigator Site #1204

Chesterfield, Missouri, United States

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Investigator site #1209

Las Vegas, Nevada, United States

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Investigator Site #1189

Sparta, New Jersey, United States

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Investigator Site #1101

Albuquerque, New Mexico, United States

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Investigator Site #1058

Brooklyn, New York, United States

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Investigator Site #1088

New York, New York, United States

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Investigator Site #1175

Queens, New York, United States

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Investigator Site #1095

Charlotte, North Carolina, United States

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Investigator Site #1056

Charlotte, North Carolina, United States

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Investigator Site #1173

Charlotte, North Carolina, United States

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Investigator Site #1171

Philadelphia, Pennsylvania, United States

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Investigator Site #1062

Pittsburgh, Pennsylvania, United States

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Investigator Site #1044

Memphis, Tennessee, United States

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Investigator Site #1195

Carrollton, Texas, United States

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Investigator Site #1049

Colleyville, Texas, United States

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Investigator Site #1071

Fort Worth, Texas, United States

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Investigator Site #1094

Houston, Texas, United States

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Investigator Site #1169

Houston, Texas, United States

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Investigator site #1178

Houston, Texas, United States

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Investigator Site #1187

Red Oak, Texas, United States

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Investigator site #1053

San Antonio, Texas, United States

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Investigator Site #1186

San Antonio, Texas, United States

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Investigator Site #1172

Spring, Texas, United States

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Investigator Site #1194

Tomball, Texas, United States

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Investigator Site #3012

CABA, Buenos Aires, Argentina

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Investigator Site #3001

Ciudad Autonoma de Buenos Aires, Buenos Aires, Argentina

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Investigator Site #3016

La Plata, Buenos Aires, Argentina

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Investigator Site #3009

San Miguel de Tucumán, Tucman, Argentina

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Investigator Site #3010

San Miguel de Tucumán, Tucman, Argentina

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Investigator Site #3015

San Miguel de Tucumán, Tucumán Province, Argentina

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Investigator Site #3023

Buenos Aires, , Argentina

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Investigator Site #3008

Mendoza, , Argentina

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Investigator Site #5603

Haskovo, , Bulgaria

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Investigator Site #5602

Pleven, , Bulgaria

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Investigator Site #5525

Plovdiv, , Bulgaria

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Investigator Site #5521

Plovdiv, , Bulgaria

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Investigator Site #5529

Rousse, , Bulgaria

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Investigator Site #5522

Sofia, , Bulgaria

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Investigator Site #5547

Sofia, , Bulgaria

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Investigator Site #3006

Providencia, , Chile

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Investigator Site #3002

Santiago, , Chile

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Investigator Site #3019

Barranquilla, , Colombia

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Investigator Site #3011

Barranquilla, , Colombia

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Investigator Site #3021

Bogotá, , Colombia

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Investigator Site #3022

Bogotá, , Colombia

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Investigator Site #3020

Cali, , Colombia

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Investigator Site #3003

Chía, , Colombia

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Investigator Site #3014

Medellín, , Colombia

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Investigator Site #5542

Rijeka, , Croatia

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Investigator Site #5543

Split, , Croatia

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Investigator Site #4012

Aarhus, , Denmark

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Investigator Site #4011

Køge, , Denmark

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Investigator Site #5516

Tbilisi, , Georgia

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Investigator Site #5523

Tbilisi, , Georgia

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Investigator Site #5538

Tbilisi, , Georgia

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Investigator Site #5536

Tbilisi, , Georgia

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Investigator Site #5534

Tbilisi, , Georgia

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Investigator Site #5517

Tbilisi, , Georgia

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Investigator Site #4003

Leipzig, , Germany

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Investigator Site #4005

Mainz, , Germany

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Investigator Site #4006

Munich, , Germany

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Investigator Site #5548

Debrecen, , Hungary

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Investigator Site #5544

Gyula, , Hungary

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Investigator Site # 6015

New Delhi, National Capital Territory of Delhi, India

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Investigator Site #6005

Ahmedabad, , India

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Investigator Site #6010

Ahmedabad, , India

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Investigator Site #6016

Ahmedabad, , India

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Investigator Site #6006

Ahmedabad, , India

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Investigator Site #6001

Bangalore, , India

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Investigator Site #6009

Bengaluru, , India

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Investigator Site #6012

Chandigarh, , India

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Investigator Site #6004

Haryāna, , India

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Investigator Site #6013

Jaipur, , India

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Investigator Site #6011

Lucknow, , India

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Investigator Site #6008

Nagpur, , India

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Investigator Site #6014

Pune, , India

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Investigator Site #6007

Pune, , India

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Investigator Site #6002

Surat, , India

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Investigator Site #6003

Surat, , India

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Investigator Site #2501

Chihuahua City, , Mexico

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Investigator Site #2504

Cuauhtémoc, , Mexico

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Investigator Site #2502

Guadalajara, , Mexico

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Investigator Site #2512

Guadalajara, , Mexico

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Investigator Site #2507

Guadalajara, , Mexico

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Investigator Site #2508

Madero, , Mexico

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Investigator Site #2509

Mexico City, , Mexico

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Investigator Site #2514

Mexico City, , Mexico

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Investigator Site #2503

Mexico City, , Mexico

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Investigator Site #2506

Mexico City, , Mexico

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Investigator Site #2511

Mérida, , Mexico

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Investigator Site #2516

Mérida, , Mexico

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Investigator Site # 2517

Naucalpan, , Mexico

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Investigator Site #2510

Oaxaca City, , Mexico

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Investigator Site #2505

San Luis Potosí City, , Mexico

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Investigator Site #2513

Torreón, , Mexico

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Investigator Site #3013

Lima, , Peru

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Investigator Site #3004

Lima, , Peru

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Investigator Site #3018

San Martín de Porres, , Peru

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Investigator Site #3005

Santiago de Surco, , Peru

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Investigator Site #3017

Trujillo, , Peru

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Investigator Site #8003

Angeles City, , Philippines

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Investigator Site #8009

Iloilo City, , Philippines

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Investigator Site #8011

Lipa City, , Philippines

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Investigator Site #8001

Manila, , Philippines

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Investigator Site #8010

Manila, , Philippines

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Investigator Site #8018

Manila, , Philippines

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Investigator Site #8006

Quezon City, , Philippines

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Investigator Site #5519

Bialystok, , Poland

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Investigator Site #5546

Bialystok, , Poland

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Investigator Site #5518

Bialystok, , Poland

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Investigator Site #5531

Bydgoszcz, , Poland

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Investigator Site #5520

Bytom, , Poland

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Investigator Site #5539

Częstochowa, , Poland

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Investigator Site #5533

Krakow, , Poland

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Investigator Site #5537

Nadarzyn, , Poland

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Investigator Site #5545

Poznan, , Poland

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Investigator Site #5535

Sosnowiec, , Poland

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Investigator Site #5532

Szczecin, , Poland

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Investigator Site #5527

Warsaw, , Poland

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Investigator Site #5540

Warsaw, , Poland

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Investigator Site #5528

Wroclaw, , Poland

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Investigator site #3028

Caguas, , Puerto Rico

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Investigator site #3029

San Juan, , Puerto Rico

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Investigator Site #5530

Bucharest, , Romania

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Investigator Site #5549

Bucharest, , Romania

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Investigator Site #5526

Bucharest, , Romania

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Investigator Site #8007

Anyang-si, , South Korea

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Investigator Site #8004

Busan, , South Korea

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Investigator Site #8016

Seoul, , South Korea

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Investigator Site #8019

Seoul, , South Korea

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Investigator Site #8012

Seoul, , South Korea

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Investigator Site #4013

A Coruña, , Spain

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Investigator Site #4008

Alicante, , Spain

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Investigator Site #4007

Barcelona, , Spain

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Investigator Site #4002

Seville, , Spain

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Investigator Site #4009

Valencia, , Spain

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Investigator Site #8013

Chiayi City, , Taiwan

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Investigator Site #8014

Kaohsiung City, , Taiwan

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Investigator Site #8008

Taichung, , Taiwan

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Investigator Site #8015

Taichung, , Taiwan

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Investigator Site #8017

Taipei, , Taiwan

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Investigator Site #4017

Leeds, , United Kingdom

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Investigator Site #4015

London, , United Kingdom

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Investigator Site #4016

London, , United Kingdom

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Investigator Site #4014

Southampton, , United Kingdom

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Countries

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United States Argentina Bulgaria Chile Colombia Croatia Denmark Georgia Germany Hungary India Mexico Peru Philippines Poland Puerto Rico Romania South Korea Spain Taiwan United Kingdom

Other Identifiers

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ESK-001-010

Identifier Type: -

Identifier Source: org_study_id

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