A Phase 3 Study to Evaluate the Safety and Efficacy of Efgartigimod PH20 Subcutaneous in Adult Patients With Primary Immune Thrombocytopenia

NCT ID: NCT04812925

Last Updated: 2026-01-12

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

173 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-11-17

Study Completion Date

2026-10-01

Brief Summary

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A Phase 3 study to evaluate the safety and efficacy of efgartigimod PH20 subcutaneous in adult patients with primary immune thrombocytopenia

Detailed Description

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Conditions

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Primary Immune Thrombocytopenia

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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efgartigimod PH20 SC

Patients receiving efgartigimod PH20 SC treatment

Group Type EXPERIMENTAL

efgartigimod PH20 SC

Intervention Type BIOLOGICAL

Subcutaneous injection with efgartigimod PH20 SC

Interventions

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efgartigimod PH20 SC

Subcutaneous injection with efgartigimod PH20 SC

Intervention Type BIOLOGICAL

Other Intervention Names

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ARGX-113 PH20 SC

Eligibility Criteria

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Inclusion Criteria

1. Ability to understand the requirements of the trial and provide written informed consent (including consent for the use and disclosure of research-related health information), willing and able to comply with the trial protocol procedures (including attending the required trial visits).
2. Participants enrolled in the ARGX-113-2004 trial who completed the 24-week trial period.

Note: If a participant has had an SAE during the ARGX-113-2004 trial, their eligibility should be evaluated by the investigator and the sponsor's trial physician. The decision of enrolling the participant will be evaluated case by case.

3a. Agree to use contraceptives consistent with local regulations and the following:

• Female participants of childbearing potential must have a negative urine pregnancy test at baseline before receiving IMP.

In addition to the above criteria, for participants who want to continue receiving efgartigimod during an additional 52-week treatment period (only applicable in case efgartigimod is not yet commercially available for patients with primary ITP or available through another patient program for patients with primary ITP), the following criteria apply:

4\. Ability to understand the requirements of the additional 52-week treatment period of the trial, to provide written informed consent (including consent for the use and disclosure of research-related health information), and to comply with the trial protocol procedures (including required trial visits).

5\. Participant has completed a 52-week treatment period.

Exclusion Criteria

1. Introduction or continuation of nonpermitted medications during the ARGX-113-2004 trial (such as anti-CD20 therapy, romiplostim, monoclonal antibodies, Fc fusion proteins, or live/live-attenuated vaccines)
2. Use of any other investigational drug or participation in any other investigational trial
3. Known hypersensitivity reaction to efgartigimod PH20 SC or any of its excipients
4. Pregnant or lactating females and those who intend to become pregnant during the trial or within 90 days after last dose of efgartigimod PH20 SC
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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argenx

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Investigator Site 0010116

Bentonville, Arkansas, United States

Site Status

Investigator site 0010045

Washington D.C., District of Columbia, United States

Site Status

Investigator Site 0010062

Fort Wayne, Indiana, United States

Site Status

Investigator site US0010042

Iowa City, Iowa, United States

Site Status

Investigator Site 0010095

Oklahoma City, Oklahoma, United States

Site Status

Investigator Site 0540001

Buenos Aires, , Argentina

Site Status

Investigator site 540004

Buenos Aires, , Argentina

Site Status

Investigator Site 0610012

Garran, , Australia

Site Status

Investigator Site 0610003

West Perth, , Australia

Site Status

Investigator site 610005

Westmead, , Australia

Site Status

Investigator Site 3590017

Plovdiv, , Bulgaria

Site Status

Investigator site 0560003

Reñaca, , Chile

Site Status

Investigator site 560002

Santiago, , Chile

Site Status

Investigator site 0560004

Temuco, , Chile

Site Status

Investigator site 860013

Beijing, , China

Site Status

Investigator Site 0860008

Bengbu, , China

Site Status

Investigator site 860055

Huizhou, , China

Site Status

Investigator Site 0860015

Shenzhen, , China

Site Status

Investigator Site 0860001

Tianjin, , China

Site Status

Investigator Site 0860010

Wuhan, , China

Site Status

Investigator Site 0860002

Wuxi, , China

Site Status

Investigator Site 0860011

Zhengzhou, , China

Site Status

Investigator site 860058

Zhenjiang, , China

Site Status

Investigator Site 9950007

Tbilisi, , Georgia

Site Status

Investigator site 9950009

Tbilisi, , Georgia

Site Status

Investigator site 9950011

Tbilisi, , Georgia

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Investigator site 300008

Athens, , Greece

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Investigator Site 0300009

Thessaloniki, , Greece

Site Status

Investigator site 3530003

Dublin, , Ireland

Site Status

Investigator site 390043

Ferrara, , Italy

Site Status

Investigator Site 0390032

Milan, , Italy

Site Status

Investigator Site 0390044

Napoli, , Italy

Site Status

Investigator site 390041

Napoli, , Italy

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Investigator site JP0810015

Hirakata, , Japan

Site Status

Investigator Site 0810017

Iruma, , Japan

Site Status

Investigator Site 0810053

Kanagawa, , Japan

Site Status

Investigator Site 0810051

Kitakyushu, , Japan

Site Status

Investigator site 0810016

Shibukawa, , Japan

Site Status

Investigator site 810023

Shimotsuke, , Japan

Site Status

Investigator Site 0810038

Tama, , Japan

Site Status

Investigator site 9620001

Irbid, , Jordan

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Investigator site 520002

Aguascalientes, , Mexico

Site Status

Investigator site 640005

Christchurch, , New Zealand

Site Status

Investigator site 0470003

Sarpsborg, , Norway

Site Status

Investigator site PL0480013

Katowice, , Poland

Site Status

Investigator Site 0480026

Nowy Sącz, , Poland

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Investigator Site 0480037

Skorzewo, , Poland

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Investigator Site 3510007

Lisbon, , Portugal

Site Status

Investigator site 3510004

Porto, , Portugal

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Investigator site 3510001

Vila Nova de Gaia, , Portugal

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Investigator Site 0400005

Bucharest, , Romania

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Investigator site 400012

Bucharest, , Romania

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Investigator Site 0400007

Craiova, , Romania

Site Status

Investigator site 0070040

Kirov, , Russia

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Investigator Site 0070026

Moscow, , Russia

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Investigator Site 0070038

Nizhny Novgorod, , Russia

Site Status

Investigator Site 0070037

Novosibirsk, , Russia

Site Status

Investigator site 270003

Johannesburg, , South Africa

Site Status

Investigator site 270004

Observatory, , South Africa

Site Status

Investigator site 270001

Pretoria, , South Africa

Site Status

Investigator site 270002

Randburg, , South Africa

Site Status

Investigator site 820004

Seoul, , South Korea

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Investigator site KO0820007

Seoul, , South Korea

Site Status

Investigator Site 0660002

Bangkok, , Thailand

Site Status

Investigator Site 0660003

Bangkok, , Thailand

Site Status

Investigator site 660005

Bangkok, , Thailand

Site Status

Investigator Site 0660001

Bangkok Noi, , Thailand

Site Status

Investigator site 0660004

Chiang Mai, , Thailand

Site Status

Investigator site TH0660009

Khon Kaen, , Thailand

Site Status

Investigator site 2610001

Sousse, , Tunisia

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Investigator site 2160002

Tunis, , Tunisia

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Investigator Site 0900007

Adapazarı, , Turkey (Türkiye)

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Investigator Site 0900003

Ankara, , Turkey (Türkiye)

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Investigator Site 0900008

Ankara, , Turkey (Türkiye)

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Investigator Site 0900015

Ankara, , Turkey (Türkiye)

Site Status

Investigator site 900004

Izmir, , Turkey (Türkiye)

Site Status

Investigator Site 0900014

Kocaeli, , Turkey (Türkiye)

Site Status

Investigator site 900010

Mersin, , Turkey (Türkiye)

Site Status

Investigator site 0900017

Tekirdağ, , Turkey (Türkiye)

Site Status

Investigator site 900019

Trabzon, , Turkey (Türkiye)

Site Status

Investigator site 440005

Coventry, , United Kingdom

Site Status

Investigator site UK044041

London, , United Kingdom

Site Status

Investigator site UK0440014

Penzance, , United Kingdom

Site Status

Countries

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United States Argentina Australia Bulgaria Chile China Georgia Greece Ireland Italy Japan Jordan Mexico New Zealand Norway Poland Portugal Romania Russia South Africa South Korea Thailand Tunisia Turkey (Türkiye) United Kingdom

Other Identifiers

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ARGX-113-2005

Identifier Type: -

Identifier Source: org_study_id

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