A Efficacy and Safety Study of R935788 in the Treatment of Persistent/Chronic Immune Thrombocytopenic Purpura (ITP)

NCT ID: NCT02076399

Last Updated: 2019-02-12

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

76 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-07-14

Study Completion Date

2016-04-21

Brief Summary

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The purpose of this study is to determine whether fostamatinib is safe and effective in the treatment of persistent/chronic Immune Thrombocytopenic Purpura (ITP).

Detailed Description

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Conditions

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Immune Thrombocytopenic Purpura

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Fostamatinib Disodium

Subjects begin with Fostamatinib Disodium tablet 100 mg PO bid and increase to 150 mg big after week 4 based on platelet count and tolerability.

Group Type EXPERIMENTAL

Fostamatinib disodium

Intervention Type DRUG

Fostamatinib (100 mg PO bid or 150 mg PO bid)

Placebo

Placebo tablet PO bid (morning and evening) over the course of 24 weeks

Group Type OTHER

Placebo

Intervention Type DRUG

Placebo tablet PO bid (morning and evening) over the course of 24 weeks

Interventions

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Fostamatinib disodium

Fostamatinib (100 mg PO bid or 150 mg PO bid)

Intervention Type DRUG

Placebo

Placebo tablet PO bid (morning and evening) over the course of 24 weeks

Intervention Type DRUG

Other Intervention Names

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R935788 R788 Fostamatinib

Eligibility Criteria

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Inclusion Criteria

* Clinical diagnosis of persistent/chronic ITP for at least 3 months.
* Average platelet count \< 30,000/µL (and none \> 35,000 unless as a result of rescue therapy) from at least 3 qualifying counts

Exclusion Criteria

* Clinical diagnosis of autoimmune hemolytic anemia
* Uncontrolled or poorly controlled hypertension
* History of coagulopathy including prothrombotic conditions
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Rigel Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Rigel Pharmaceuticals, Inc.

Role: STUDY_DIRECTOR

Rigel Pharmaceuticals,Inc.

Locations

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Arizona Oncology Associates

Tucson, Arizona, United States

Site Status

University of Southern California

Los Angeles, California, United States

Site Status

Lakeland Regional Cancer Center

Lakeland, Florida, United States

Site Status

Bleeding & Clotting Disorders Institute

Peoria, Illinois, United States

Site Status

Horizon Oncology Research, Inc

Lafayette, Indiana, United States

Site Status

Center for Cancer and Blood Disorders

Bethesda, Maryland, United States

Site Status

Weill Cornell Medical College/New York Presbyterian Hospital

New York, New York, United States

Site Status

Pitt County Memorial Hospital

Greenville, North Carolina, United States

Site Status

Bill Hefner VA Medical Center

Salisbury, North Carolina, United States

Site Status

Cleveland Clinic

Cleveland, Ohio, United States

Site Status

Signal Point Clinical Research Center LLC

Middletown, Ohio, United States

Site Status

University of Utah Health Sciences Center

Salt Lake City, Utah, United States

Site Status

University of Virginia

Charlottesville, Virginia, United States

Site Status

Concord Repatriation General Hospital

Concord, New South Wales, Australia

Site Status

St George Hospital

Kogarah, New South Wales, Australia

Site Status

Liverpool Hospital

Liverpool, New South Wales, Australia

Site Status

Prince of Wales Hospital

Randwick, New South Wales, Australia

Site Status

Westmead Hospital

Westmead, New South Wales, Australia

Site Status

Launceston General Hospital

Launceston, Tasmania, Australia

Site Status

Frankston Hospital

Frankston, Victoria, Australia

Site Status

Dept of Haematology, The Alfred Hospital and Monash Medical Centre

Melbourne, Victoria, Australia

Site Status

Perth Blood Institute

Nedlands, Western Australia, Australia

Site Status

Hamilton Health Sciences Corporation

Hamilton, Ontario, Canada

Site Status

Ottawa Hospital Research Institute

Ottawa, Ontario, Canada

Site Status

St. Michael's Hospital

Toronto, Ontario, Canada

Site Status

Herlev Hospital University of Copenhagen, Department of Hematology L124

Herlev, DK, Denmark

Site Status

Dept. of Haematology, Odense University Hospital

Odense C, DK, Denmark

Site Status

Hematological department, Roskilde Hospital

Roskilde, DK, Denmark

Site Status

Aarhus University Hospital

Aalborg, , Denmark

Site Status

Semmelweis University 1st

Budapest, , Hungary

Site Status

University of Debrecen

Debrecen, , Hungary

Site Status

Pecs University

Pécs, , Hungary

Site Status

Ematologia - Padigilione 8, Policinico S. Orsola Malpighi, Azienda Ospedaliero Universitaria di Bologna

Bologna, , Italy

Site Status

Ospedale San Raffaele S.r.l. Dipartimento di Oncoematologia

Milan, , Italy

Site Status

Universitã Federico II di Napoli

Napoli, , Italy

Site Status

OspedaleCivile-ClinicaEmatologica/PUGD

Udine, , Italy

Site Status

ULSS 6 Vicenza-Ospedale San Bortolo di Vicenza

Vicenza, , Italy

Site Status

HAGA ziekenhuis

Haag, NL, Netherlands

Site Status

Kent & Canterbury Hospital

Kent, Canterbury, United Kingdom

Site Status

Colchester General Hospital

Colchester, Essex, United Kingdom

Site Status

Royal Liverpool University Hospital

Liverpool, UK, United Kingdom

Site Status

St. James's Hospital

Leeds, , United Kingdom

Site Status

Leicester Royal Infirmary

Leicester, , United Kingdom

Site Status

Royal London Hospital

London, , United Kingdom

Site Status

Hammersmith Hospital, Catherine Lewis Centre

London, , United Kingdom

Site Status

University College Hospital

London, , United Kingdom

Site Status

Manchester Royal Infirmary

Manchester, , United Kingdom

Site Status

Royal Victoria Infirmary

Newcastle upon Tyne, , United Kingdom

Site Status

James Paget University Hospital

Norfolk, , United Kingdom

Site Status

Oxford University Hospital

Oxford, , United Kingdom

Site Status

University Hospital of North Staffordshire

Stoke-on-Trent, , United Kingdom

Site Status

Sandwell General Hospital

West Bromwich, , United Kingdom

Site Status

Countries

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United States Australia Canada Denmark Hungary Italy Netherlands United Kingdom

References

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Cooper N, Altomare I, Thomas MR, Nicolson PLR, Watson SP, Markovtsov V, Todd LK, Masuda E, Bussel JB. Assessment of thrombotic risk during long-term treatment of immune thrombocytopenia with fostamatinib. Ther Adv Hematol. 2021 Apr 30;12:20406207211010875. doi: 10.1177/20406207211010875. eCollection 2021.

Reference Type DERIVED
PMID: 33995988 (View on PubMed)

Other Identifiers

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2013-005452-15

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

C-935788-047

Identifier Type: -

Identifier Source: org_study_id

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