A Study to Find How Safe and Effective GAMMAPLEX® is in Subjects With Chronic Idiopathic Thrombocytopenic Purpura (ITP)

NCT ID: NCT00504075

Last Updated: 2013-03-01

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

35 participants

Study Classification

INTERVENTIONAL

Study Start Date

2007-09-30

Study Completion Date

2011-08-31

Brief Summary

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To determine if GAMMAPLEX raises the platelet count of subjects with chronic ITP to a threshold of 50 x 109/L, similar to that of published response \>60%. Also to assess the safety of GAMMAPLEX and determine if platelet counts are maintained at 50 x 109/L in subjects with chronic ITP for.

Detailed Description

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The primary objective is to determine if BPL's GAMMAPLEX raises the platelet count of subjects with chronic ITP to a threshold of 50 x 109/L, similar to that of published response \>60%. The secondary objectives are: 1) to determine the safety of GAMMAPLEX at the dosage used in this study. 2) to determine if GAMMAPLEX maintains platelet counts of ³ 50 x 109/L in subjects with chronic ITP for a period of time similar to that of a published data.

Conditions

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Chronic Idiopathic Thrombocytopenic Purpura

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Gammaplex (intravenous immunoglobulin)

Group Type EXPERIMENTAL

Gammaplex, intravenous immunoglobulin

Intervention Type BIOLOGICAL

Dosage form: Gammaplex® is a sterile liquid of 5 % w/v normal immunoglobulin. Gammaplex® contains 5 g/100 mL of human normal immunoglobulin (i.e. 50 g/L, of which virtually 100% is IgG).

The first course of GAMMAPLEX will be administered as an intravenous infusion of 1 g/kg on each of 2 consecutive days. If required, a further 1 or 2 courses on the same dosage regimen may be administered in the period Day 32 to Day 90 following the first course of GAMMAPLEX.

Interventions

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Gammaplex, intravenous immunoglobulin

Dosage form: Gammaplex® is a sterile liquid of 5 % w/v normal immunoglobulin. Gammaplex® contains 5 g/100 mL of human normal immunoglobulin (i.e. 50 g/L, of which virtually 100% is IgG).

The first course of GAMMAPLEX will be administered as an intravenous infusion of 1 g/kg on each of 2 consecutive days. If required, a further 1 or 2 courses on the same dosage regimen may be administered in the period Day 32 to Day 90 following the first course of GAMMAPLEX.

Intervention Type BIOLOGICAL

Other Intervention Names

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Gammaplex

Eligibility Criteria

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Inclusion Criteria

1. Males and females aged between 18 and 70 years.
2. Confirmed diagnosis of chronic ITP of at least 6 months duration.
3. Platelet count of less than or equal to 20 x 10 9/L at enrollment.
4. Absence of other conditions that, in the opinion of the investigator, could cause thrombocytopenia.
5. If subjects were treated with corticosteroids the treatment regimen/dose must have been stable (for a minimum of 2 weeks before screening). The dose of corticosteriod or other immunosuppressant should have remained constant until Day 32. 6) If subjects were being treated with cyclophosphamide, azathioprine or attenuated androgens, the treatment regimen and dose must have been stable for a minimum of 2 months before Day 1. The dose of corticosteriod or other immunosuppressant should have remained constant until Day 32. 7) Splenectomized subjects and both Rh(D)+ and Rh(D)- subjects may be included.

8\) The subject has signed an informed consent form (subjects must be at least 18 years old), and/or the subject's legal guardian has signed the informed consent form if indicated 9) If a subject is a female of child-bearing potential, she must have a negative result on a urine-based HCG pregnancy test.

10\) If a subject is a female who is or becomes sexually active, she must practice contraception by using a method of proven reliability for the duration of the study.

Exclusion Criteria

1. A history of any severe or anaphylactic reaction to blood or any blood-derived product, or any severe reaction to IGIV or any other IgG preparation.
2. Intolerance to any component of the investigational product.
3. Received any live virus vaccine within the last 3 months prior to Day1.
4. Received an IGIV preparation within 1 month prior to Day 1.
5. Were currently receiving, or has received, any investigational agent within the 1 month prior to Day 1.
6. Received any blood, blood product, or blood derivative within the 1 month prior to Day 1.
7. Received Rituximab within the 3 months before Day 1.
8. Pregnant or nursing.
9. Tested positive for any of the following at screening: HBsAg, NAT for HCV, NAT for HIV, Antibodies to HCV or HIV 1 or 2.
10. Had levels greater than 2.5 times the upper limit of normal at screening, as defined by the central laboratory, of alanine aminotransferase or aspartate aminotransferase.
11. Had severe renal impairment (defined as serum creatinine greater than 2 times the upper limit of normal or BUN greater than 2.5 times the upper limit of normal for the range of the laboratory doing the analysis); on dialysis; a history of acute renal failure.
12. Known to have abused alcohol, opiates, psychotropic agents, or other chemicals or drugs within the past 12 months.
13. History of deep vein thrombosis (DVT) or thrombotic complications of IGIV therapy.
14. Any history or sign of hyperviscosity, transient ischemic attack (TIA), stroke, other thromboembolic event, or unstable angina.
15. Suffered from any acute or chronic medical conditions (e.g., renal disease or predisposing conditions for renal disease, coronary artery disease, or protein losing enteropathy) that, in the opinion of the investigator, may interfere with the conduct of the study.
16. An acquired medical condition, such as chronic lymphocytic leukemia, lymphoma, multiple myeloma, chronic or recurrent neutropenia (defined as an absolute neutrophil count (ANC) \< 1 x 109/L).
17. Non-controlled arterial hypertension (systolic blood pressure \>160 mmHg and/or diastolic blood pressure \>90 mmHg).
18. Anemic (hemoglobin \<10 g/dL) at screening.
19. Unlikely to adhere to the protocol requirements of the study or is likely to be uncooperative.
Minimum Eligible Age

18 Years

Maximum Eligible Age

70 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Bio Products Laboratory

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Tim J Aldwinckle, MD

Role: PRINCIPAL_INVESTIGATOR

Bio Products Laboratory

Locations

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Mid Florida Hematology & Oncology

Orange City, Florida, United States

Site Status

Rush University Medical Center

Chicago, Illinois, United States

Site Status

Center for Cancer & Blood Disorders

Bethesda, Maryland, United States

Site Status

New York Hospital / Cornell University, Division of Pediatrics

New York, New York, United States

Site Status

Department of Pediatrics, SUNY at Stony Brook

Stony Brook, New York, United States

Site Status

Oregon Health & Science University

Portland, Oregon, United States

Site Status

Cancer Care Centers of South Texas

San Antonio, Texas, United States

Site Status

Hospital Churruca

Capital Federal, Buenos Aires, Argentina

Site Status

Hospital Italiano de La Plata

La Plata, Buenos Aires, Argentina

Site Status

CER San Juan

San Juan, San Juan Province, Argentina

Site Status

Instituto de Diagnóstico Hematológico Ambulatorio (IDHEA)

Rosario, Sante Fe, Argentina

Site Status

I. A. D. T. (Instituto Argentino de Diagnóstico y Tratamiento)

Buenos Aires, , Argentina

Site Status

Hospital Britanico

Buenos Aires, , Argentina

Site Status

Centro de Educación Médica e Investigaciones Clinicas Dr. Norberto Quirno (CEMIC)

Buenos Aires, , Argentina

Site Status

J.R. Vidal Hospital

Corrientes, , Argentina

Site Status

Hospital Privado de Cordoba

Córdoba, , Argentina

Site Status

Apollo Hospitals

Hyderabad, Andhra Pradesh, India

Site Status

Mahavir Hospital

Hyderabad, Andhra Pradesh, India

Site Status

City Cancer Centre,

Suryarao Pet, Vijayawada, Andhra Pradesh, India

Site Status

M. S Ramaiah Hospital

Karnataka, Bangalore, India

Site Status

Vedanta

Ahmedabad, Gujarat, India

Site Status

Gurukrupa Hospital

Ahmedabad, Gujarat, India

Site Status

M S Patel Cancer Centre, Shree Krishna Hospital

Gokal Nagar, Karamsad, Gujarat, India

Site Status

Manipal Hospital

Bangalore, Karnataka, India

Site Status

Vinaya Hospital & research Centre

Mangalore, Karnataka, India

Site Status

Kasturba Medical College, Manipal Acunova KMC Research Centre

Mangalore, Karnataka, India

Site Status

Father Muller Medical College Hospital

Mangalore, Karnataka, India

Site Status

Deenanath Mangeshkar Hospital

Pune, Maharashtra, India

Site Status

S.K. Soni Hospital Sect 5

Jaipur, Rajasthan, India

Site Status

Sir Ganga Ram Hospital

New Delhi, , India

Site Status

Countries

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United States Argentina India

References

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Dash CH, Gillanders KR, Stratford Bobbitt ME, Gascoigne EW, Leach SJ. Safety and efficacy of Gammaplex(R) in idiopathic thrombocytopenic purpura (ClinicalTrials.gov--NCT00504075). PLoS One. 2014 Jun 3;9(6):e96600. doi: 10.1371/journal.pone.0096600. eCollection 2014.

Reference Type DERIVED
PMID: 24892422 (View on PubMed)

Related Links

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http://www.bpl.co.uk

Sponsor website

Other Identifiers

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GMX02

Identifier Type: -

Identifier Source: org_study_id

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