A Long-term Study to Assess the Safety and Efficacy of Efgartigimod in Adult Patients With Primary Immune Thrombocytopenia (ITP).

NCT ID: NCT04225156

Last Updated: 2025-09-25

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

101 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-06-02

Study Completion Date

2026-03-11

Brief Summary

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This is an open-label long-term multicenter phase 3 trial to evaluate the efficacy and safety of ARGX-113 in adult patients with primary ITP.

Detailed Description

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Conditions

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Primary Immune Thrombocytopenia

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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efgartigimod

patients receiving efgartigimod

Group Type EXPERIMENTAL

efgartigimod

Intervention Type BIOLOGICAL

Intravenous infusion of efgartigimod

Interventions

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efgartigimod

Intravenous infusion of efgartigimod

Intervention Type BIOLOGICAL

Other Intervention Names

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ARGX-113

Eligibility Criteria

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Inclusion Criteria

1. Ability to understand the requirements of the trial, to provide written informed consent (including consent for the use and disclosure of research-related health information), and to comply with the trial protocol procedures (including required trial visits).
2. Patients enrolled in the ARGX-113-1801 trial who completed the 24-weeks trial period.
3. Women of childbearing potential must have a negative urine pregnancy test at baseline before trial medication (infusion) can be administered.
4. Women of childbearing potential should use a highly effective or acceptable method of contraception during the trial and for 90 days after the last administration of the IMP. They must be on a stable regimen, for at least 1 month (as listed in the protocol)

6\. Ability to understand the requirements of the additional 52-week treatment period of the trial, to provide written informed consent (including consent for the use and disclosure of research-related health information), and to comply with the trial protocol procedures (including required trial visits).

7\. Patient has completed a 52-week treatment period.

Exclusion Criteria

1. Introduction or continuation of non-permitted medications during the ARGX-113-1801 trial (such as anti-CD20 therapy, romiplostim, monoclonal antibodies, Fc fusion proteins or live/live-attenuated vaccines).
2. Pregnant or lactating women, and those intending to become pregnant during the trial or within 90 days after the last dosing.
3. Patients with known medical history of hypersensitivity to any of the ingredients of efgartigimod.
4. Use of any other investigational drug or participation in any other investigational trial.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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argenx

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Investigator Site 0010045

Washington D.C., District of Columbia, United States

Site Status

Investigator Site 0010037

Ocala, Florida, United States

Site Status

Investigator Site 0010042

Iowa City, Iowa, United States

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Investigator Site 0010040

Columbus, Ohio, United States

Site Status

Investigator Site 0430002

Vienna, , Austria

Site Status

Investigator Site 0430003

Vienna, , Austria

Site Status

Investigator Site 0320012

Brasschaat, , Belgium

Site Status

Investigator Site 0320011

Bruges, , Belgium

Site Status

Investigator Site 0320014

Turnhout, , Belgium

Site Status

Investigator Site 0320002

Yvoir, , Belgium

Site Status

Investigator Site 3590001

Pleven, , Bulgaria

Site Status

Investigator Site 3590002

Sofia, , Bulgaria

Site Status

Investigator Site 4200001

Brno, , Czechia

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Investigator Site 4200008

Olomouc, , Czechia

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Investigator Site 4200006

Ostrava, , Czechia

Site Status

Investigator Site 4200007

Prague, , Czechia

Site Status

Investigator Site 0330009

Créteil, , France

Site Status

Investigator Site 0330018

Montpellier, , France

Site Status

Investigator Site 0330008

Pessac, , France

Site Status

Investigator Site 0330016

Périgueux, , France

Site Status

Investigator site 9950007

Tbilisi, , Georgia

Site Status

Investigator site 9950008

Tbilisi, , Georgia

Site Status

Investigator site 9950009

Tbilisi, , Georgia

Site Status

Investigator site 9950011

Tbilisi, , Georgia

Site Status

Investigator site 9950012

Tbilisi, , Georgia

Site Status

Investigator Site 0490010

Düsseldorf, , Germany

Site Status

Investigator Site 0490008

Essen, , Germany

Site Status

Investigator Site 0360004

Budapest, , Hungary

Site Status

Investigator Site 0360006

Debrecen, , Hungary

Site Status

Investigator Site 0360015

Győr, , Hungary

Site Status

Investigator Site 0360010

Nyíregyháza, , Hungary

Site Status

Investigator Site 0360014

Szombathely, , Hungary

Site Status

Investigator Site 0390014

Milan, , Italy

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Investigator Site 0390020

Monza, , Italy

Site Status

Investigator Site 0390015

Novara, , Italy

Site Status

Investigator Site 0390010

Ravenna, , Italy

Site Status

Investigator Site 0390011

Reggio Calabria, , Italy

Site Status

Investigator Site 0390018

Reggio Emilia, , Italy

Site Status

Investigator Site 0390019

Rimini, , Italy

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Investigator Site 0390009

Siena, , Italy

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Investigator Site 0390016

Trieste, , Italy

Site Status

Investigator Site 0810015

Hirakata, , Japan

Site Status

Investigator Site 0810010

Hiroshima, , Japan

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Investigator Site 0810017

Iruma, , Japan

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Investigator Site 0810022

Kashiwa, , Japan

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Investigator Site 0810018

Maebashi, , Japan

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Investigator Site 0810021

Niigata, , Japan

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Investigator Site 0810014

Sapporo, , Japan

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Investigator Site 0810016

Shibukawa, , Japan

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Investigator Site 0810023

Shimotsuke, , Japan

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Investigator Site 0310005

Rotterdam, , Netherlands

Site Status

Investigator Site 0310006

The Hague, , Netherlands

Site Status

Investigator Site 0480012

Gdansk, , Poland

Site Status

Investigator Site 0480013

Katowice, , Poland

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Investigator Site 0480011

Lodz, , Poland

Site Status

Investigator Site 0480014

Lublin, , Poland

Site Status

Investigator Site 0480026

Nowy Sącz, , Poland

Site Status

Investigator Site 0070006

Kaluga, , Russia

Site Status

Investigator Site 0070008

Moscow, , Russia

Site Status

Investigator Site 0070007

Petrozavodsk, , Russia

Site Status

Investigator Site 0070013

Rostov-on-Don, , Russia

Site Status

Investigator Site 0070015

Syktyvkar, , Russia

Site Status

Investigator Site 0070012

Tula, , Russia

Site Status

Investigator Site 0070010

Ufa, , Russia

Site Status

Investigator Site 0340006

Barcelona, , Spain

Site Status

Investigator Site 0340007

Barcelona, , Spain

Site Status

Investigator Site 0340009

Madrid, , Spain

Site Status

Investigator Site 0340014

Madrid, , Spain

Site Status

Investigator Site 0340012

Palma de Mallorca, , Spain

Site Status

Investigator Site 0340015

Pozuelo de Alarcón, , Spain

Site Status

Investigator Site 0340013

Seville, , Spain

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Investigator Site 0340004

Valencia, , Spain

Site Status

Investigator Site 0340011

Valencia, , Spain

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Investigator Site 0900003

Ankara, , Turkey (Türkiye)

Site Status

Investigator Site 0900006

Ankara, , Turkey (Türkiye)

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Investigator Site 0900015

Ankara, , Turkey (Türkiye)

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Investigator Site 0900016

Edirne, , Turkey (Türkiye)

Site Status

Investigator Site 0900013

Istanbul, , Turkey (Türkiye)

Site Status

Investigator Site 0900004

Izmir, , Turkey (Türkiye)

Site Status

Investigator Site 0900010

Mersin, , Turkey (Türkiye)

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Investigator Site 0900007

Sakarya, , Turkey (Türkiye)

Site Status

Investigator Site 0900009

Samsun, , Turkey (Türkiye)

Site Status

Investigator Site 0900017

Tekirdağ, , Turkey (Türkiye)

Site Status

Investigator Site 0900019

Trabzon, , Turkey (Türkiye)

Site Status

Investigator Site 3800006

Mykolaiv, , Ukraine

Site Status

Investigator Site 0440008

London, , United Kingdom

Site Status

Investigator Site 0440012

Southampton, , United Kingdom

Site Status

Countries

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United States Austria Belgium Bulgaria Czechia France Georgia Germany Hungary Italy Japan Netherlands Poland Russia Spain Turkey (Türkiye) Ukraine United Kingdom

Other Identifiers

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2019-002101-21

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

ARGX-113-1803

Identifier Type: -

Identifier Source: org_study_id

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