ESCORT-HU Extension: European Sickle Cell Disease Cohort - Hydroxyurea - Extension Study

NCT ID: NCT04707235

Last Updated: 2024-08-27

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Total Enrollment

2093 participants

Study Classification

OBSERVATIONAL

Study Start Date

2020-08-21

Study Completion Date

2025-08-21

Brief Summary

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As safety information pertaining to the long-term use of HU remains incomplete in spite of the first safety study (ESCORT-HU), an extension of the latter is proposed. ESCORT-HU Extension study aims at evaluating the long-term safety of Siklos® focusing on some questions regarding its safety when used in current practice in adults and paediatric patients treated with Siklos® and followed for up to 5 years. The study will focus on the following concerns : occurrence and incidence of malignancies, leg ulcers, male fertility impairment and serious unexpected AEs causally related to Siklos®.

Detailed Description

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Conditions

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Sickle Cell Disease

Study Design

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Observational Model Type

COHORT

Study Time Perspective

PROSPECTIVE

Study Groups

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Sickle cell disease patients treated with Siklos

Hydroxycarbamide

Intervention Type DRUG

Patients, aged ≥ 2 years old, with symptomatic SCD, treated with Siklos®.

Interventions

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Hydroxycarbamide

Patients, aged ≥ 2 years old, with symptomatic SCD, treated with Siklos®.

Intervention Type DRUG

Other Intervention Names

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Siklos Hydroxyurea

Eligibility Criteria

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Inclusion Criteria

* Male or female patients with symptomatic SCD,
* ≥ 2 years old,
* Treated with Siklos®,
* Having been informed of the study by the investigator and consenting to participate, or whose parents or legal guardians are consenting for their child to participate.

To allow risk evaluation, participants must belong at least to one of the subpopulations defined below:

* Participants previously enrolled in ESCORT-HU who agree to participate in ESCORT-HU Extension study,
* New participants with any of the following criteria:

* history of HU treatment for more than 5 years or
* prepubescent over 10 years of age for girls and 13 years of age for boys at enrolment, or
* with history of leg ulcer, or
* pregnant women without interruption of Siklos® 3 months before the beginning of the pregnancy or,
* males treated with Siklos® whose partner is pregnant and without discontinuation of Siklos® 3 months before the beginning of the pregnancy.
Minimum Eligible Age

2 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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International Clinical Trials Association

OTHER

Sponsor Role collaborator

Theravia

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Mariane de Montalembert, MD, PhD

Role: STUDY_CHAIR

Hospital Necker enfants malades

Frédéric Galactéros, MD, PhD

Role: STUDY_CHAIR

Henri Mondor University Hospital

Locations

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Amiens - Picardie Hospital Adults

Amiens, , France

Site Status

Amiens Picardie Hospital Children

Amiens, , France

Site Status

Clinique de l'Europe Amiens

Amiens, , France

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Angers Hospital Adults

Angers, , France

Site Status

Angers Hospital Center Children

Angers, , France

Site Status

Robert Ballanger Hospital Adults

Aulnay-sous-Bois, , France

Site Status

Robert Ballanger Hospital Children

Aulnay-sous-Bois, , France

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Avicenne Hospital Adults

Bobigny, , France

Site Status

Jean Verdier Hospital Children

Bondy, , France

Site Status

Bordeaux Hospital Adults

Bordeaux, , France

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Bordeaux Hospital Children

Bordeaux, , France

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Ambroise Paré Hospital Children

Boulogne-Billancourt, , France

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Tours Regional University Hospital Center Adults

Chambray-lès-Tours, , France

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Estaing Hospital Children

Clermont-Ferrand, , France

Site Status

Louis Mourier Hospital Adults

Colombes, , France

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Louis Mourier Hospital Children

Colombes, , France

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Sud Francilien Hospital Center Adults

Corbeil-Essonnes, , France

Site Status

Centre Hospitalier Sud Francilien

Corbeil-Essonnes, , France

Site Status

Sud Oise Public Hospital Group Adults

Creil, , France

Site Status

Henri Mondor Hospital Adults

Créteil, , France

Site Status

Intercommunal Hospital Center of Créteil Adults and Children

Créteil, , France

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Dreux Hospital Center Children

Dreux, , France

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Gonesse Hospital Children

Gonesse, , France

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Marne-La-Vallée Hospital Center Children

Jossigny, , France

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Grenoble Hospital Adults

La Tronche, , France

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Grenoble Hospital Children

La Tronche, , France

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Bicêtre Hospital Adults

Le Kremlin-Bicêtre, , France

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Hôpital Bicêtre

Le Kremlin-Bicêtre, , France

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CH du Mans

Le Mans, , France

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Jeanne De Flandre Hospital Children

Lille, , France

Site Status

Hôpital Saint-Vincent de Paul

Lille, , France

Site Status

Hôpital Mère-Enfant - CHU de Limoges

Limoges, , France

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Edouard Herriot Hospital Adults

Lyon, , France

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Hematology and oncology institute Children

Lyon, , France

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Timone Hospital Adults

Marseille, , France

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Timone Hospital Children

Marseille, , France

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Meaux Hospital Center Adults

Meaux, , France

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Meaux Hospital Center Children

Meaux, , France

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St Eloi Hospital Adults

Montpellier, , France

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Montpellier Hospital Children

Montpellier, , France

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Emile Muller Hospital Adults

Mulhouse, , France

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Nantes Hospital Children

Nantes, , France

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Nantes Hospital Adults

Nantes, , France

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Nice Hospital Children

Nice, , France

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Orléans Hospital Adults

Orléans, , France

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Armand Trousseau Hospital Children

Paris, , France

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Saint-Antoine Hospital Adults

Paris, , France

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Georges Pompidou European Hospital Adults

Paris, , France

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Necker Hospital Adults

Paris, , France

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Necker Hospital Children

Paris, , France

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Robert Debré Hospital Children

Paris, , France

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Centre hospitalier Perpignan

Perpignan, , France

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Poitiers Hospital Adults

Poitiers, , France

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American Hospital Children

Reims, , France

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Reims Hospital Adults

Reims, , France

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Pontchaillou Hospital Adults

Rennes, , France

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Charles Nicolle Hospital Adults

Rouen, , France

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Rouen Hospital Children

Rouen, , France

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Yves Le Foll. Hospital Center Children

Saint-Brieuc, , France

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Delafontaine Hospital Center Adults

Saint-Denis, , France

Site Status

Delafontaine Hospital Center Children

Saint-Denis, , France

Site Status

Saint-Quentin Hospital Center Adults

Saint-Quentin, , France

Site Status

Hautepierre Hospital Children

Strasbourg, , France

Site Status

Children Hospital

Toulouse, , France

Site Status

Toulouse University Institute of cancer Adults

Toulouse, , France

Site Status

Clocheville Regional University Hospital Center Children

Tours, , France

Site Status

Nancy Hospital Children

Vandœuvre-lès-Nancy, , France

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Versailles Hospital Center Children

Versailles, , France

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CH de Cayenne

Cayenne, , French Guiana

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Centre hospitalier de Kourou Children

Kourou, , French Guiana

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Centre Hospitalier de l'Ouest Guyanais Franck Joly Adults

Saint-Laurent-du-Maroni, , French Guiana

Site Status

Centre Hospitalier de l'Ouest Guyanais Franck Joly Children

Saint-Laurent-du-Maroni, , French Guiana

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Charité Hospital Children

Berlin, , Germany

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Düsseldorf Hospital Children

Düsseldorf, , Germany

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Freiburg Hospital Children

Freiburg im Breisgau, , Germany

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Hamburg Hospital Children

Hamburg, , Germany

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Koblenz Hospital Children

Koblenz, , Germany

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Laiko General Hospital Adults

Athens, , Greece

Site Status

Hôpital RICOU - CHU Pointe-à-Pitre Abymes Children

Pointe-à-Pitre, , Guadeloupe

Site Status

Hôpital RICOU - CHU Pointe-à-Pitre Abymes

Pointe-à-Pitre, , Guadeloupe

Site Status

AUO Policlinico di Modena

Modena, , Italy

Site Status

Napoli Hospital Children

Napoli, , Italy

Site Status

Padova Hospital Children

Padua, , Italy

Site Status

Verona Hospital Children

Verona, , Italy

Site Status

CHU Fort de France Children

Fort-de-France, , Martinique

Site Status

CHU Martinique Adults

Le Lamentin, , Martinique

Site Status

CHU Sud Réunion

Saint-Pierre, , Reunion

Site Status

Countries

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France French Guiana Germany Greece Guadeloupe Italy Martinique Reunion

Other Identifiers

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ESCORT-HU Extension

Identifier Type: -

Identifier Source: org_study_id

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