A Study of the Efficacy and Safety of ICA-17043 (With or Without Hydroxyurea) in Patients With Sickle Cell Anemia.

NCT ID: NCT00040677

Last Updated: 2011-07-18

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

90 participants

Study Classification

INTERVENTIONAL

Study Start Date

2002-02-28

Study Completion Date

2004-01-31

Brief Summary

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ICA-17043 is being developed for the chronic treatment of patients with sickle cell disease (SCD) in both adults and children. ICA-17043 is a potent and specific inhibitor of a channel in human red blood cells (RBCs) that blocks RBC dehydration. ICA-17043 is expected to inhibit RBC dehydration and thus should prevent or delay the sickling process. By reducing sickled cells, an improvement in anemia, a reduction in painful crises, and ultimately, less end-organ disease is anticipated.

Detailed Description

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Conditions

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Sickle Cell Disease Sickle Cell Anemia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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ICA-17043 Low Dose 6 mg/day

Active study medication: 100 mg loading dose; 6 mg maintenance dose per day

Group Type EXPERIMENTAL

Low Dose ICA-17043

Intervention Type DRUG

Low dose arm

Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo Loading dose capsules and maintenance dose tablets matched 10 mg active treatment group

ICA-17043 High Dose 10 mg/day

Active study medication: 150 mg loading dose; 10 mg maintenance dose per day

Group Type EXPERIMENTAL

High dose ICA-17043

Intervention Type DRUG

150 mg Loading Dose; 10 mg daily dose

Interventions

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Low Dose ICA-17043

Low dose arm

Intervention Type DRUG

High dose ICA-17043

150 mg Loading Dose; 10 mg daily dose

Intervention Type DRUG

Placebo

Placebo Loading dose capsules and maintenance dose tablets matched 10 mg active treatment group

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Homozygous (HbSS) Sickle Cell Anemia
* Otherwise healthy (based on medical history, physical examination, 12-lead ECG, and clinical laboratory tests)
* Patients may be receiving hydroxyurea, but must have been dose stabilized for at least 3 months
* Patient has a history of at least one acute vaso-occlusive event requiring hospitalization

Exclusion Criteria

* Patient participating in a chronic transfusion program
* Patient having a total hemoglobin of \< 4.0 g/dL or \> 10.0 g/dL
* Patient having a HbA \> 10%
* Patient considering undergoing an elective surgery
* Patient taking prohibited medications such as Epoetin, Warfarin, etc.
* Patient who has had previous gastrointestinal surgery, except cholecystectomy or appendectomy
* Patient with significant active cardiovascular, neurologic, endocrine, hepatic, or renal disorders unrelated to sickle cell anemia
Minimum Eligible Age

18 Years

Maximum Eligible Age

60 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Icagen

INDUSTRY

Sponsor Role lead

Responsible Party

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Icagen

Principal Investigators

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Kenneth I Ataga, MD

Role: PRINCIPAL_INVESTIGATOR

University of North Carolina, Chapel Hill

Locations

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Study Site

Birmingham, Alabama, United States

Site Status

Study Site

Oakland, California, United States

Site Status

Study Site

San Francisco, California, United States

Site Status

Study Site

Washington D.C., District of Columbia, United States

Site Status

Study Site

Augusta, Georgia, United States

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Study Site

Chicago, Illinois, United States

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Study Site

Baltimore, Maryland, United States

Site Status

Study Site

Boston, Massachusetts, United States

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Study Site

Detroit, Michigan, United States

Site Status

Study Site

Jackson, Mississippi, United States

Site Status

Study Site

Brooklyn, New York, United States

Site Status

Study Site

New York, New York, United States

Site Status

Study Site

Chapel Hill, North Carolina, United States

Site Status

Study Site

Durham, North Carolina, United States

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Study Site

Philadelphia, Pennsylvania, United States

Site Status

Study Site

Pittsburgh, Pennsylvania, United States

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Study Site

Nashville, Tennessee, United States

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Study Site

Houston, Texas, United States

Site Status

Study Site

Richmond, Virginia, United States

Site Status

Countries

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United States

References

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Ataga KI, Smith WR, De Castro LM, Swerdlow P, Saunthararajah Y, Castro O, Vichinsky E, Kutlar A, Orringer EP, Rigdon GC, Stocker JW; ICA-17043-05 Investigators. Efficacy and safety of the Gardos channel blocker, senicapoc (ICA-17043), in patients with sickle cell anemia. Blood. 2008 Apr 15;111(8):3991-7. doi: 10.1182/blood-2007-08-110098. Epub 2008 Jan 11.

Reference Type RESULT
PMID: 18192510 (View on PubMed)

Related Links

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http://www.icagen.com

For more information about Icagen

http://www.SCInfo.org

For more information about Sickle Cell Disease

Other Identifiers

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ICA-17043-05

Identifier Type: -

Identifier Source: org_study_id

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