Study of TL-895 in Subjects With Myelofibrosis or Indolent Systemic Mastocytosis

NCT ID: NCT04655118

Last Updated: 2024-05-10

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

121 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-10-22

Study Completion Date

2025-12-31

Brief Summary

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This study evaluates TL-895, a potent, orally-available and highly selective irreversible tyrosine kinase inhibitor for the treatment of Myelofibrosis (Cohorts 1-3) or Indolent Systemic Mastocytosis (Cohort 5). Participants must be diagnosed with Myelofibrosis and be relapsed/refractory (e.g., having failed prior therapy), intolerant, or ineligible to receive JAKi treatment, or be diagnosed with Indolent Systemic Mastocytosis.

Detailed Description

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Conditions

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Myelofibrosis Indolent Systemic Mastocytosis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Cohort 1a, Relapsed/Refractory Myelofibrosis

150 mg of TL-895 will be administered orally, twice daily (BID) continuously starting on Day 1 in a 28-day cycle.

Group Type EXPERIMENTAL

TL-895

Intervention Type DRUG

TL-895 is an experimental tyrosine kinase inhibitor drug taken by mouth.

Cohort 1b, Relapsed/Refractory Myelofibrosis

300 mg of TL-895 will be administered orally, once daily (QD) continuously starting on Day 1 in a 28-day cycle.

Group Type EXPERIMENTAL

TL-895

Intervention Type DRUG

TL-895 is an experimental tyrosine kinase inhibitor drug taken by mouth.

Cohort 1c, Relapsed/Refractory Myelofibrosis

300 mg of TL-895 will be administered orally, twice daily (BID) continuously starting on Day 1 in a 28-day cycle.

Group Type EXPERIMENTAL

TL-895

Intervention Type DRUG

TL-895 is an experimental tyrosine kinase inhibitor drug taken by mouth.

Cohort 1d, Relapsed/Refractory Myelofibrosis

450 mg of TL-895 will be administered orally, twice daily (BID) continuously starting on Day 1 in a 28-day cycle.

Group Type EXPERIMENTAL

TL-895

Intervention Type DRUG

TL-895 is an experimental tyrosine kinase inhibitor drug taken by mouth.

Cohort 2a, JAKi Intolerant Myelofibrosis

150 mg of TL-895 will be administered orally, twice daily (BID) continuously starting on Day 1 in a 28-day cycle.

Group Type EXPERIMENTAL

TL-895

Intervention Type DRUG

TL-895 is an experimental tyrosine kinase inhibitor drug taken by mouth.

Cohort 2b, JAKi Intolerant Myelofibrosis

300 mg of TL-895 will be administered orally, once daily (QD) continuously starting on Day 1 in a 28-day cycle.

Group Type EXPERIMENTAL

TL-895

Intervention Type DRUG

TL-895 is an experimental tyrosine kinase inhibitor drug taken by mouth.

Cohort 3a, JAKi Ineligible Myelofibrosis with platelet count of ≥ 25 and < 50 × 109/L

150 mg of TL-895 will be administered orally, twice daily (BID) continuously starting on Day 1 in a 28-day cycle.

Group Type EXPERIMENTAL

TL-895

Intervention Type DRUG

TL-895 is an experimental tyrosine kinase inhibitor drug taken by mouth.

Cohort 3b, JAKi Ineligible Myelofibrosis with platelet count of ≥ 25 and < 50 × 109/L

300 mg of TL-895 will be administered orally, once daily (QD) continuously starting on Day 1 in a 28-day cycle.

Group Type EXPERIMENTAL

TL-895

Intervention Type DRUG

TL-895 is an experimental tyrosine kinase inhibitor drug taken by mouth.

Cohort 5a, Indolent Systemic Mastocytosis

TL-895 will be administered orally, twice daily (BID) continuously starting on Day 1 in a 28-day cycle in combination with best supportive care (BSC).

Group Type EXPERIMENTAL

TL-895

Intervention Type DRUG

TL-895 is an experimental tyrosine kinase inhibitor drug taken by mouth.

Cohort 5b, Indolent Systemic Mastocytosis

TL-895 will be administered orally, twice daily (BID) continuously starting on Day 1 in a 28-day cycle in combination with BSC.

Group Type EXPERIMENTAL

TL-895

Intervention Type DRUG

TL-895 is an experimental tyrosine kinase inhibitor drug taken by mouth.

Cohort 5c, Indolent Systemic Mastocytosis

TL-895 will be administered orally, twice daily (BID) continuously starting on Day 1 in a 28-day cycle in combination with BSC.

Group Type EXPERIMENTAL

TL-895

Intervention Type DRUG

TL-895 is an experimental tyrosine kinase inhibitor drug taken by mouth.

Cohort 5d, Indolent Systemic Mastocytosis

TL-895 will be administered orally, twice daily (BID) continuously starting on Day 1 in a 28-day cycle in combination with BSC.

Group Type EXPERIMENTAL

TL-895

Intervention Type DRUG

TL-895 is an experimental tyrosine kinase inhibitor drug taken by mouth.

Cohort 5e, Indolent Systemic Mastocytosis

Placebo to match TL-895 will be administered orally, twice daily (BID) continuously starting on Day 1 in a 28-day cycle in combination with BSC.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo to match TL-895

Interventions

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TL-895

TL-895 is an experimental tyrosine kinase inhibitor drug taken by mouth.

Intervention Type DRUG

Placebo

Placebo to match TL-895

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Adults ≥18 years of age
* Confirmed diagnosis of PMF, post-PV MF, or post-ET MF, as assessed by treating physician according to the World Health Organization (WHO) criteria
* Eastern Cooperative Oncology Group (ECOG) performance status of ≤2
* Adequate hematologic, hepatic, and renal functions
* MF symptoms as defined by having at least 2 symptoms with an average baseline (Day -7 to Day -1) score of at least 1 for each of the 2 symptoms per MFSAF v4.0
* Cohort 3 only: Ineligibility for JAKi treatment with a platelet count of ≥ 25 and \< 50 x 10\^9/L


* Adults ≥18 years of age
* Confirmed diagnosis of ISM as defined by WHO diagnostic criteria based on review of bone marrow biopsy pathology report results
* Subject must have moderate-to-severe symptoms

Exclusion Criteria

* Prior treatment with any BTK or BMX inhibitors
* Prior treatment with JAKi within 28 days prior to study treatment
* Prior splenectomy or splenic irradiation within 24 weeks prior to first dose of study treatment

Cohort 5


* Prior treatment with any BTK or BMX inhibitors
* Prior treatment with Avapritinib, bezuclastinib, or BLU-263/elenestinib
* Diagnosis with another myeloproliferative disorder
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Telios Pharma, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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University of Colorado - Aurora Cancer Center

Aurora, Colorado, United States

Site Status COMPLETED

Mayo Clinic - Rochester

Rochester, Minnesota, United States

Site Status RECRUITING

Gabrail Cancer Center

Canton, Ohio, United States

Site Status COMPLETED

University of Cincinnati (UC) Physicians Company, LLC

Cincinnati, Ohio, United States

Site Status ACTIVE_NOT_RECRUITING

Ohio State University

Columbus, Ohio, United States

Site Status ACTIVE_NOT_RECRUITING

University of Texas, MD Anderson Cancer Center

Houston, Texas, United States

Site Status RECRUITING

Border Medical Oncology

East Albury, , Australia

Site Status COMPLETED

Southern Oncology Specialists

Kogarah, , Australia

Site Status COMPLETED

Royal Perth Hospital

Perth, , Australia

Site Status RECRUITING

St Vincent's Hospital Sydney

Sydney, , Australia

Site Status RECRUITING

Chu De Liège

Liège, , Belgium

Site Status RECRUITING

Cliniques Universitaires Saint-Luc

Woluwe-Saint-Lambert, , Belgium

Site Status ACTIVE_NOT_RECRUITING

Instituto de Estudos e Pesquisas Sao Lucas - IEP - Sao Lucas

São Paulo, , Brazil

Site Status COMPLETED

University Hospital "St Ivan Rilski"

Sofia, , Bulgaria

Site Status COMPLETED

Military Medical Academy

Sofia, , Bulgaria

Site Status ACTIVE_NOT_RECRUITING

CH Le Mans

Le Mans, , France

Site Status ACTIVE_NOT_RECRUITING

CHU de Nantes - Hôtel-Dieu

Nantes, , France

Site Status COMPLETED

CHU de Nice - Hopital L' Archet II

Nice, , France

Site Status COMPLETED

Universitaetsklinikum Carl Gustav Carus Dresden

Dresden, , Germany

Site Status RECRUITING

Marien Hospital Duesseldorf

Düsseldorf, , Germany

Site Status COMPLETED

Klinik fur Innere Medizin IV - Hamatologie/Onkologie, Universitatsklinikum Hall

Halle, , Germany

Site Status RECRUITING

Universitaetsklinikum Jena

Jena, , Germany

Site Status RECRUITING

Praxisklinik fur Hamatologie und Onkologie

Koblenz, , Germany

Site Status COMPLETED

Debreceni Egyetem Klinikai Kozpont

Debrecen, , Hungary

Site Status COMPLETED

Markhot Ferenc Oktatokorhaz es Rendelointezet

Eger, , Hungary

Site Status COMPLETED

Szabolcs-Szatmár-Bereg Megyei Önkormányzat Jósa András Oktatókórház Megyei-Városi Tüdőgondozó Intézete

Nyíregyháza, , Hungary

Site Status COMPLETED

Fejer Megyei Szent Gyorgy Egyetemi Oktato Korhaz

Székesfehérvár, , Hungary

Site Status COMPLETED

Azienda Ospedaliero Universitaria Policlinico G. Rodolico-San Marco - Presidio Ospedaliero G. Rodolico

Catania, , Italy

Site Status ACTIVE_NOT_RECRUITING

Istituto Romagnolo per lo Studio dei Tumori Dino Amadori

Meldola, , Italy

Site Status ACTIVE_NOT_RECRUITING

Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico di Milano

Milan, , Italy

Site Status ACTIVE_NOT_RECRUITING

ASST Grande Ospedale Metropolitano Niguarda

Milan, , Italy

Site Status ACTIVE_NOT_RECRUITING

Azienda Ospedaliero Universitaria Maggiore Della Carita'

Novara, , Italy

Site Status ACTIVE_NOT_RECRUITING

Azienda Ospedaliera di Perugia-Ospedale S. Maria della Misericordia

Perugia, , Italy

Site Status ACTIVE_NOT_RECRUITING

AUSL della Romagna-Ospedale S.Maria delle Croci

Ravenna, , Italy

Site Status ACTIVE_NOT_RECRUITING

Grande Ospedale Metropolitano Bianchi Melacrino Morelli

Reggio Calabria, , Italy

Site Status ACTIVE_NOT_RECRUITING

Azienda Ospedaliero Universitaria Policlinico Umberto I

Roma, , Italy

Site Status ACTIVE_NOT_RECRUITING

Szpital Uniwersytecki Nr 2 im. Dr Jana Biziela w Bydgoszczy, Klinika Hematologi

Bydgoszcz, , Poland

Site Status ACTIVE_NOT_RECRUITING

Uniwersyteckie Centrum Kliniczne, Klinika Hematologii i Transplantologii

Gdansk, , Poland

Site Status ACTIVE_NOT_RECRUITING

Klinika Hematologii Collegium Medicum Uniwersytetu Jagiellonskiego

Krakow, , Poland

Site Status NOT_YET_RECRUITING

Uniwersytecki Szpital Kliniczny im. Jana Mikulicza-Radeckiego we Wroclawiu, Klinika Hematologii, Nowotworów Krwi i Transplantacji Szpiku

Wroclaw, , Poland

Site Status RECRUITING

Kyungpook National University Hospital

Daegu, , South Korea

Site Status COMPLETED

Seoul National University Hospital

Seoul, , South Korea

Site Status COMPLETED

Seoul St. Mary's Hospital, The Catholic University of Korea

Seoul, , South Korea

Site Status COMPLETED

Institut Catala d'Oncologia - L'Hospitalet

Barcelona, , Spain

Site Status RECRUITING

Hospital Germans Trias i Pujol

Barcelona, , Spain

Site Status RECRUITING

Hospital Universitario 12 de Octubre

Madrid, , Spain

Site Status RECRUITING

Salamanca University Hospital

Salamanca, , Spain

Site Status COMPLETED

Hospital Quirónsalud Zaragoza

Zaragoza, , Spain

Site Status RECRUITING

Kaohsiung Medical University Chung-Ho Memorial Hospital (KMUH)

Kaohsiung City, , Taiwan

Site Status ACTIVE_NOT_RECRUITING

Chang Gung Memorial Hospital - Kaohsiung Branch

Kaohsiung City, , Taiwan

Site Status COMPLETED

China Medical University Hospital

Taichung, , Taiwan

Site Status COMPLETED

National Taiwan University Hospital

Taipei, , Taiwan

Site Status COMPLETED

Countries

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United States Australia Belgium Brazil Bulgaria France Germany Hungary Italy Poland South Korea Spain Taiwan

Central Contacts

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John Mei

Role: CONTACT

650-542-0136

Emily Houlihan

Role: CONTACT

401-954-8042

Other Identifiers

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TL-895-201

Identifier Type: -

Identifier Source: org_study_id

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