A Study of Selinexor Monotherapy in Subjects with JAK Inhibitor-naïve Myelofibrosis and Moderate Thrombocytopenia

NCT ID: NCT05980806

Last Updated: 2025-02-05

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

118 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-04-22

Study Completion Date

2028-10-31

Brief Summary

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The main purpose of this study with corresponding optional expansion is to evaluate the efficacy of selinexor in JAKi-naïve participants with myelofibrosis (MF) and moderate thrombocytopenia based on spleen volume reduction (SVR). Additional efficacy and safety parameters will also be assessed during the study.

Detailed Description

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Conditions

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Myelofibrosis Moderate Thrombocytopenia

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Selinexor 60 mg (Arm 1)

Participants will receive selinexor 60 milligrams (mg) oral tablets once weekly (QW) (Days 1, 8, 15, and 22 of each 28-day cycle) until PD, intolerable toxicity, or until they meet the criteria for discontinuation of study treatment, death, or withdrawal of consent, whichever comes first and followed by optional add-on medication dosing may be initiated based on Spleen Volume Reduction (SVR) values.

Group Type EXPERIMENTAL

Selinexor 60 mg

Intervention Type DRUG

Participants will receive selinexor 60 mg oral tablets QW.

Ruxolitinib

Intervention Type DRUG

Participants will receive ruxolitinib 5 mg or 10 mg twice daily.

Pacritinib

Intervention Type DRUG

Participants will receive pacritinib 200 mg twice daily.

Momelotinib

Intervention Type DRUG

Participants will receive momelotinib 200 mg once daily.

Selinexor 40 mg (Arm 2)

Participants will receive selinexor 40 mg oral tablets QW (Days 1, 8, 15, and 22 of each 28-day cycle) until PD, intolerable toxicity, or until they meet the criteria for discontinuation of study treatment, death, or withdrawal of consent, whichever comes first and followed by optional add-on medication dosing may be initiated based on SVR values.

Group Type EXPERIMENTAL

Selinexor 40 mg

Intervention Type DRUG

Participants will receive selinexor 40 mg oral tablets QW.

Ruxolitinib

Intervention Type DRUG

Participants will receive ruxolitinib 5 mg or 10 mg twice daily.

Pacritinib

Intervention Type DRUG

Participants will receive pacritinib 200 mg twice daily.

Momelotinib

Intervention Type DRUG

Participants will receive momelotinib 200 mg once daily.

Selinexor 60 mg (Optional Expansion Arm)

Participants will receive selinexor 60 mg oral tablets QW (Days 1, 8, 15, and 22 of each 28-day cycle) until PD, intolerable toxicity, or until they meet the criteria for discontinuation of study treatment, death, or withdrawal of consent, whichever comes first. Optional add-on medication (ruxolitinib \[5 mg or 10 mg twice daily\], pacritinib \[200 mg twice daily\], or momelotinib \[200 mg once daily\]) may be initiated for participants whose SVR is less than (\<) 10% at Week 12 or \<35% at Week 24 based on the participants platelet count values (i.e., ruxolitinib if platelets greater than or equal to \[\>=\] 50 x 10\^9/L, pacritinib if platelets \<50 x 10\^9/L, momelotinib if platelets is \>=50 x 10\^9/L and hemoglobin level is \< 10 gram per deciliter \[g/dL\]).

Group Type EXPERIMENTAL

Selinexor 60 mg

Intervention Type DRUG

Participants will receive selinexor 60 mg oral tablets QW.

Ruxolitinib

Intervention Type DRUG

Participants will receive ruxolitinib 5 mg or 10 mg twice daily.

Pacritinib

Intervention Type DRUG

Participants will receive pacritinib 200 mg twice daily.

Momelotinib

Intervention Type DRUG

Participants will receive momelotinib 200 mg once daily.

Selinexor 40 mg (Optional Expansion Arm)

Participants will receive selinexor 40 mg oral tablets QW (Days 1, 8, 15, and 22 of each 28-day cycle) until PD, intolerable toxicity, or until they meet the criteria for discontinuation of study treatment, death, or withdrawal of consent, whichever comes first. Optional add-on medication (ruxolitinib \[5 mg or 10 mg twice daily\], pacritinib \[200 mg twice daily\], or momelotinib \[200 mg once daily\]) may be initiated for participants whose SVR is \<10% at Week 12 or \<35% at Week 24 based on the participants platelet count values (i.e., ruxolitinib if platelets \>= 50 x 10\^9/L, pacritinib if platelets \<50 x 10\^9/L, momelotinib if platelets is \>=50 x 10\^9/L and hemoglobin level is \< 10 g/dL).

Group Type EXPERIMENTAL

Selinexor 40 mg

Intervention Type DRUG

Participants will receive selinexor 40 mg oral tablets QW.

Ruxolitinib

Intervention Type DRUG

Participants will receive ruxolitinib 5 mg or 10 mg twice daily.

Pacritinib

Intervention Type DRUG

Participants will receive pacritinib 200 mg twice daily.

Momelotinib

Intervention Type DRUG

Participants will receive momelotinib 200 mg once daily.

Interventions

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Selinexor 60 mg

Participants will receive selinexor 60 mg oral tablets QW.

Intervention Type DRUG

Selinexor 40 mg

Participants will receive selinexor 40 mg oral tablets QW.

Intervention Type DRUG

Ruxolitinib

Participants will receive ruxolitinib 5 mg or 10 mg twice daily.

Intervention Type DRUG

Pacritinib

Participants will receive pacritinib 200 mg twice daily.

Intervention Type DRUG

Momelotinib

Participants will receive momelotinib 200 mg once daily.

Intervention Type DRUG

Other Intervention Names

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KPT-330 KPT-330 JAKAFI VONJO OJJAARA

Eligibility Criteria

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Inclusion Criteria

* A diagnosis of MF or post-ET or post-PV MF according to the 2016 World Health Organization (WHO) classification of MPN, confirmed by the most recent local pathology report.
* Measurable splenomegaly during the screening period as demonstrated by spleen volume of greater than equal to (\>=) 450 cubic square centimeter (cm\^3) by MRI or CT scan (results from MRI or CT imaging performed within 28 days prior to screening are acceptable).
* Participants with DIPSS risk category of intermediate-1 with symptoms, or intermediate-2, or high-risk.
* ECOG Performance Status less than or equal to (\<=) 2.
* Platelet count of 50 to less than (\<) 100 x 10\^9/L without platelet transfusion within 7 days prior to the first dose of selinexor.
* Absolute neutrophil count (ANC) \>=1.0 × 10\^9/L without need for growth factors within 7 days prior to the first dose of selinexor.
* Adequate liver function as defined by the following: aspartate transaminase (AST) and alanine aminotransferase (ALT) \<= 2.5 × upper limit normal (ULN) and serum total bilirubin \<= 3×ULN.
* Calculated creatinine clearance (CrCl) greater than (\>) 15 milliliter per minute (mL/min) based on the Cockcroft and Gault formula.
* Active symptoms of MF as determined by presence of at least 2 symptoms with a score \>= 3 or total score of \>= 10 at screening using the MFSAF V4.0.
* Participants must provide bone marrow biopsy samples (samples obtained up to 3 months prior to C1D1 are permitted) at screening and during the study.
* Participants currently not a candidate for stem cell transplantation.
* Participants must be willing to complete the MFSAF V4.0 daily during the study for evaluating the symptom response (i.e., TSS50).

Exclusion Criteria

* More than 10% blasts in peripheral blood or bone marrow (accelerated or blast phase).
* Previous treatment with JAK inhibitors for MF.
* Previous treatment with selinexor or other XPO1 inhibitors.
* Female participants who are pregnant or lactating.
* Prior splenectomy, or splenic radiation within 6 months prior to C1D1.
* History of myocardial infarction, unstable angina, percutaneous transluminal coronary angioplasty (PTCA) or coronary artery bypass graft (CABG), cerebrovascular accident (stroke or transient ischemic attack \[TIA\]), ventricular arrhythmias, congestive heart failure New York Heart Association (NYHA) class \> 2 within 6 months of C1D1.
* Participants unable to tolerate two forms of antiemetics prior to each dose for the first two cycles.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Karyopharm Therapeutics Inc

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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City of Hope - Duarte Main Site

Duarte, California, United States

Site Status RECRUITING

Maryland Oncology Hematology - Independent of SCRI/ US Oncology

Columbia, Maryland, United States

Site Status RECRUITING

Weill Cornell Medicine NewYork-Presbyterian

New York, New York, United States

Site Status RECRUITING

Duke University

Durham, North Carolina, United States

Site Status RECRUITING

Cleveland Clinic

Cleveland, Ohio, United States

Site Status RECRUITING

Huntsman Cancer Institute

Salt Lake City, Utah, United States

Site Status RECRUITING

UZ Gent

Ghent, , Belgium

Site Status RECRUITING

UZ Leuven - Campus Gasthuisberg

Leuven, , Belgium

Site Status RECRUITING

University Multiprofile Hospital for Active Treatment Sveti George - Base 1

Plovdiv, , Bulgaria

Site Status RECRUITING

University Hospital Sv.Ivan Rilski - Sofia

Sofia, , Bulgaria

Site Status RECRUITING

University Multiprofile Hospital for Active Treatment Aleksandrovska

Sofia, , Bulgaria

Site Status RECRUITING

Specialized Hospital for Active Treatment of Hematological Diseases - EAD Sofia

Sofia, , Bulgaria

Site Status RECRUITING

University Multiprofile Hospital for Active Treatment - Prof. Dr. Stoyan Kirkovich AD Department of Clinical Hematology

Stara Zagora, , Bulgaria

Site Status RECRUITING

Research Institute of the McGill University Health Centre

Montreal, Quebec, Canada

Site Status RECRUITING

Centre Hospitalier Lyon-Sud

Pierre-Bénite, Auvergne-Rhône-Alpes, France

Site Status RECRUITING

CHU Tours, Hôpital Bretonneau Service d'Hématologie thérapie cellulaire

Tours, Indre-et-Loire, France

Site Status RECRUITING

Chu De Nîmes - Institut De Cancérologie Du Gard

Nîmes, Occitanie, France

Site Status RECRUITING

Centre Hospitalier Universitaire d'Angers

Angers, Pays de la Loire Region, France

Site Status RECRUITING

Hôpital Saint-Louis

Paris, , France

Site Status RECRUITING

Hôpital Cochin

Paris, , France

Site Status RECRUITING

Centre Hospitalier Universitaire de Saint-Etienne

Saint-Priest-en-Jarez, , France

Site Status RECRUITING

Marien Hospital Düsseldorf

Düsseldorf, , Germany

Site Status RECRUITING

University Hospital Jena

Jena, , Germany

Site Status RECRUITING

Semmelweis Egyetem

Budapest, , Hungary

Site Status RECRUITING

Hematology Division, Mauriziano Hospital, University of Turin

Orbassano, Torino, Italy

Site Status RECRUITING

IRCCS Azienda Ospedaliero-Universitaria di Bologna

Bologna, , Italy

Site Status RECRUITING

IRCCS Ospedale Policlinico San Martino

Genova, , Italy

Site Status RECRUITING

Istituto Romagnolo per lo Studio dei Tumori Dino Amadori - IRST

Meldola, , Italy

Site Status RECRUITING

Fondazione IRCCS Cà Granda - Ospedale Maggiore Policlinico

Milan, , Italy

Site Status RECRUITING

Istituto Europeo di Oncologia

Milan, , Italy

Site Status RECRUITING

Fondazione IRCCS Policlinico San Matteo

Pavia, , Italy

Site Status RECRUITING

Università Campus Bio-Medico di Roma

Rome, , Italy

Site Status RECRUITING

Spaarne Gasthuis

Hoofddorp, , Netherlands

Site Status RECRUITING

Samodzielny Publiczny Szpital Kliniczny Nr 4 w Lublinie

Lublin, , Poland

Site Status RECRUITING

AIDPORT

Skórzewo, , Poland

Site Status RECRUITING

Medicover Clinical Integrated Systems Sp. z o.o.

Torun, , Poland

Site Status RECRUITING

Coltea - Spital Clinic

Bucharest, , Romania

Site Status RECRUITING

Spitalul Filantropia - Craiova

Craiova, , Romania

Site Status RECRUITING

Seoul St. Mary's Hospital, The Catholic University of Korea

Seocho-gu, Seoul, South Korea

Site Status RECRUITING

Severance Hospital

Seoul, Seoul Teugbyeolsi, South Korea

Site Status RECRUITING

Pusan National University Hospital

Busan, , South Korea

Site Status RECRUITING

Hospital Clínico Universitario Virgen de la Arrixaca

El Palmar, Murcia, Spain

Site Status RECRUITING

Hospital Universitario Central de Asturias

Oviedo, Principality of Asturias, Spain

Site Status RECRUITING

Hospital San Pedro de Alcantara

Cáceres, , Spain

Site Status RECRUITING

Institut Català d'Oncologia Girona

Girona, , Spain

Site Status RECRUITING

Hospital Universitario de Gran Canaria Doctor Negrin

Las Palmas de Gran Canaria, , Spain

Site Status RECRUITING

Complejo Asistencial Universitario de Salamanca - Hospital Clínico

Salamanca, , Spain

Site Status RECRUITING

Hospital Clínico Universitario de Valencia

Valencia, , Spain

Site Status RECRUITING

Countries

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United States Belgium Bulgaria Canada France Germany Hungary Italy Netherlands Poland Romania South Korea Spain

Central Contacts

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Karyopharm Medical Information

Role: CONTACT

(888) 209-9326

Facility Contacts

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Haris Ali

Role: primary

6263564673

Haris Ali

Role: backup

Mohit Narang

Role: primary

304-942-9220

Mohit Narang

Role: backup

Ellen Ritche

Role: primary

646-962-4580

Ellen Ritche

Role: backup

Lindsay Rein

Role: primary

919-684-8964

Lindsay Rein

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Aaron Gerds

Role: primary

216-445-9840

Aaron Gerds

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Srinivas Tantravahi

Role: primary

801-213-6170

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Dominiek Mazure

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+32 9 332 21 25

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Role: backup

Timothy Devos

Role: primary

+32 (0) 16 346880

Timothy Devos

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Zhanet Grudeva-Popova

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Atanas Radinoff

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Evgueniy Hadjiev

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Martin Donchev

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Mariya Todorova

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Mariya Todorova

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Jonathan How

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Jonathan How

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Fiorenza Barraco

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Antoine Machet

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Stefan Wickenhauser

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Françoise Boyer-Perrard

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Jean-Jacques Kiladjian

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Jean-Jacques Kiladjian

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Lise Willems

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Philippe Renaudier

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Philippe Renaudier

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Stefanie Groepper

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Carl Crodel

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Zsolt Nagy

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Daniela Cilloni

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Francesca Palandri

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Roberto Lemoli

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Alessandro Lucchesi

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Alessandra Lurlo

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Federica Gigli

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Elisa Rumi

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Dominik Charaniuk

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Gabriela Borsaru

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Luminita Ocroteala

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Sung-Eun Lee

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June-Won Cheong

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HoJin Shin

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HoJin Shin

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Raúl Perez López

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Maria Angeles Fernandez Rodriguez

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Victor Higuero Saavedra

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Anna Angona

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Adrián Segura Diaz

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Jesús Maria Hernández Rivas

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Irene Pastor Galan

Role: primary

+34 961973842

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Role: backup

Other Identifiers

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XPORT-MF-044

Identifier Type: -

Identifier Source: org_study_id

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