INCB000928 Administered as a Monotherapy or in Combination With Ruxolitinib in Participants With Anemia Due to Myeloproliferative Disorders

NCT ID: NCT04455841

Last Updated: 2025-12-23

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE1/PHASE2

Total Enrollment

84 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-03-19

Study Completion Date

2027-11-26

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This Phase 1/2, open-label, dose-finding study is intended to evaluate the safety and tolerability, PK, PD, and efficacy of INCB000928 administered as monotherapy or in combination with ruxolitinib in participants with MF who are transfusion-dependent or presenting with symptomatic anemia. This study will consist of 2 parts: dose escalation and expansion.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Anemia Post-essential Thrombocythemia Myelofibrosis Post-polycythemia Vera Myelofibrosis

Keywords

Explore important study keywords that can help with search, categorization, and topic discovery.

anemia

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

NON_RANDOMIZED

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Treatment Group A (TGA)

INCB000928 will be administered once daily (QD).

Group Type EXPERIMENTAL

INCB000928

Intervention Type DRUG

INCB000928 will be administered at protocol defined dose.

Treatment Group B (TGB)

INCB000928 will be administered in combination with ruxolitinib.

Group Type EXPERIMENTAL

INCB000928

Intervention Type DRUG

INCB000928 will be administered at protocol defined dose.

ruxolitinib

Intervention Type DRUG

Ruxolitinib will be administered at protocol defined dose.

Treatment Group C (TGC)

INCB000928 will be administered in combination with ruxolitinib.

Group Type EXPERIMENTAL

INCB000928

Intervention Type DRUG

INCB000928 will be administered at protocol defined dose.

ruxolitinib

Intervention Type DRUG

Ruxolitinib will be administered at protocol defined dose.

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

INCB000928

INCB000928 will be administered at protocol defined dose.

Intervention Type DRUG

ruxolitinib

Ruxolitinib will be administered at protocol defined dose.

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Participants with MF who are transfusion-dependent or present with symptomatic anemia, defined as follows:

1. Anemia: An Hgb value \< 10 g/dL demonstrated during screening recorded on 3 separate occasions with at least 7 days between measurements (Note: RBC transfusion must be at least 2 weeks before the Hgb measurement during screening).
2. Transfusion-dependent: Participant has received at least 4 units of RBC transfusions during the 28 days immediately preceding Cycle 1 Day 1 OR has received an average of at least 4 units of RBC transfusions in the 8 weeks immediately preceding Cycle 1 Day 1, for an Hgb level of \< 8.5 g/dL, in the absence of bleeding or treatment-induced anemia. In addition, the most recent transfusion episode must have occurred in the 28 days before Cycle 1 Day 1.
* ECOG performance status score of the following:

1. 0 or 1 for the dose-escalation stages.
2. 0, 1, or 2 for the dose-expansion stage.
* Life expectancy is greater than 6 months
* Agreement to avoid pregnancy or fathering children.
* Ineligible to receive or have not responded to available therapies for anemia such as ESAs.
* For TGA:
* Participants previously treated with JAK inhibitors for at least 12 weeks.
* Participants with intermediate-2 or high DIPSS MF according to IWG-MRT criteria.
* For TGB:
* Participants must have been on a therapeutic and stable regimen of ruxolitinib for at least 12 consecutive weeks immediately preceding the first dose of study treatment.
* Participants with intermediate-1, intermediate-2, or high DIPSS MF according to IWG-MRT criteria.
* For TGC:
* Participants must be JAK inhibitor treatment naive (no prior treatment with any JAK inhibitor) and have an indication for initiation of ruxolitinib treatment.
* Participants with intermediate-1, intermediate-2, or high DIPSS MF according to IWG-MRT criteria.

Exclusion Criteria

* Undergone any prior allogenic or autologous stem cell transplantation or a candidate for such transplantation.
* Any prior chemotherapy, immunomodulatory drug therapy, immunosuppressive therapy, biological therapy, endocrine therapy, targeted therapy, antibody or hypomethylating agent to treat the participant's disease, with the exception of ruxolitinib for TGB only, within 5 half-lives or 28 days (whichever is shorter) before the first dose of study treatment.
* Laboratory Values outside of protocol defined range at screening.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Incyte Corporation

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Amanda McBride, MD

Role: STUDY_DIRECTOR

Incyte Corporation

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

City of Hope National Medical Center

Duarte, California, United States

Site Status

City of Hope Orange County

Irvine, California, United States

Site Status

Usc Norris Comprehensive Cancer Center

Los Angeles, California, United States

Site Status

Stanford Cancer Center

Palo Alto, California, United States

Site Status

Prebys Cancer Center

San Diego, California, United States

Site Status

Emory University - Winship Cancer Institute

Atlanta, Georgia, United States

Site Status

Emory University-Winship Cancer Institute

Atlanta, Georgia, United States

Site Status

Start Midwest

Grand Rapids, Michigan, United States

Site Status

Washington University School of Medicine

St Louis, Missouri, United States

Site Status

Weill Cornell Medical Centers

New York, New York, United States

Site Status

Duke University Medical Center, Department of Hematologic Malignancies and Cellular Therapy

Durham, North Carolina, United States

Site Status

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status

Md Anderson Cancer Center

Houston, Texas, United States

Site Status

Princess Margaret Cancer Center

Toronto, Ontario, Canada

Site Status

McGill University Jewish General Hospital

Montreal, Quebec, Canada

Site Status

Centre Hospitalier D'Angers

Angers, , France

Site Status

Institut Paoli Calmettes

Marseille, , France

Site Status

Hospital Saint Louis

Paris, , France

Site Status

Azienda Ospedaliera Papa Giovanni Xxiii

Bergamo, , Italy

Site Status

S Orsolas University Hospital Seragnoli Institute of Hematology

Bologna, , Italy

Site Status

Azienda Ospedaliero-Universitaria Careggi (Aouc)

Florence, , Italy

Site Status

Azienda Ospedaliera Universitaria San Luigi Gonzaga Orbassano

Orbassano, , Italy

Site Status

Comitato Di Bioetica Della Fondazione Irccs Policlinico San Matteo

Pavia, , Italy

Site Status

Ospedale Santa Maria Della Misericordia Perugia

Perugia, , Italy

Site Status

Tokyo Medical and Dental University Hospital

Bunkyō City, , Japan

Site Status

Chiba Cancer Center

Chiba, , Japan

Site Status

Gifu Municipal Hospital

Gifu, , Japan

Site Status

Kansai Medical University Hospital

Hirakata, , Japan

Site Status

Kumamoto Shinto General Hospital

Kumamoto, , Japan

Site Status

Osaka International Cancer Institute

Osaka, , Japan

Site Status

University Hospital of Wales

Cardiff, WLS, United Kingdom

Site Status

United Lincolnshire Hospitals

Boston, , United Kingdom

Site Status

Lincoln County Hospital

Lincoln, , United Kingdom

Site Status

Royal Cornwall Hospital Truro Sunrise Centre

Truro, , United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Canada France Italy Japan United Kingdom

Related Links

Access external resources that provide additional context or updates about the study.

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2023-503625-19-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

2020-004029-21

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

INCB 00928-104

Identifier Type: -

Identifier Source: org_study_id