Staccato Granisetron® (AZ 010) for the Treatment of Cyclic Vomiting Syndrome

NCT ID: NCT04645953

Last Updated: 2025-06-11

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

150 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-02-05

Study Completion Date

2022-07-26

Brief Summary

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This is a multicenter, randomized, double-blind, parallel group, placebo-controlled, efficacy and safety study of adult outpatients diagnosed with CVS and experiencing recurring episodes of stereotypical vomiting.

Detailed Description

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A Randomized, Double-Blind, Placebo Controlled Study to Evaluate the Safety and Efficacy of Staccato Granisetron (AZ-010) for the Acute Treatment of Moderate to Severe Cyclic Vomiting Syndrome

Conditions

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Cyclic Vomiting Syndrome

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors
Double Blind

Study Groups

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1mg AZ010

Single orally-inhaled dose

Group Type EXPERIMENTAL

1mg AZ010

Intervention Type COMBINATION_PRODUCT

Subjects who received a single inhaled dose (1mg)

3mg AZ010

Single orally-inhaled dose

Group Type EXPERIMENTAL

3mg AZ-010

Intervention Type COMBINATION_PRODUCT

Subjects who received a single inhaled dose (3mg)

Placebo

Single orally-inhaled dose

Group Type EXPERIMENTAL

Staccato Placebo

Intervention Type COMBINATION_PRODUCT

Subject who received a single inhaled dose (Staccato Placebo)

Interventions

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3mg AZ-010

Subjects who received a single inhaled dose (3mg)

Intervention Type COMBINATION_PRODUCT

1mg AZ010

Subjects who received a single inhaled dose (1mg)

Intervention Type COMBINATION_PRODUCT

Staccato Placebo

Subject who received a single inhaled dose (Staccato Placebo)

Intervention Type COMBINATION_PRODUCT

Eligibility Criteria

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Inclusion Criteria

* Adult males and females between 18 and 60 years of age, inclusive at the time of signing the informed consent document.
* Diagnosis of cyclic vomiting syndrome (CVS) using the Rome IV diagnostic criteria.
* Otherwise healthy, as determined by the responsible physician, based on a medical evaluation including history, physical examination, vital signs, electrocardiograms (ECGs) and laboratory tests assessed at the screening visit
* Negative urine tests for selected drugs of abuse and alcohol breath test at Screening.

Exclusion Criteria

* Any significant medical or psychiatric condition that could, in the Investigator's opinion, compromise the subject's safety or interfere with the completion of this protocol.
* Any condition, including the presence of laboratory abnormalities or pulmonary condition, which according to the Investigator places the subject at unacceptable risk if he/she were to participate in the study.
* A diagnosis of any gastrointestinal disorder other than CVS that in the judgement of the Investigator could compromise the subject's safety or interfere with the interpretation of safety or efficacy data.
Minimum Eligible Age

18 Years

Maximum Eligible Age

60 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

Yes

Sponsors

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Alexza Pharmaceuticals, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Larry Carter, PhD

Role: STUDY_DIRECTOR

Alexza Pharmaceuticals, Inc.

Locations

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Om Research

Lancaster, California, United States

Site Status

Axis Clinical Trials

Los Angeles, California, United States

Site Status

Precision Research Institute, LLC

San Diego, California, United States

Site Status

University of South Florida

Tampa, Florida, United States

Site Status

Summit Clinical Studies

Athens, Georgia, United States

Site Status

Infinite Clinical Trials

Morrow, Georgia, United States

Site Status

Kansas University Medical Center

Kansas City, Kansas, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

Henry Ford Health System

Detroit, Michigan, United States

Site Status

Mayo Clinic

Rochester, Minnesota, United States

Site Status

NY Scientific

Brooklyn, New York, United States

Site Status

Temple University Hospital

Philadelphia, Pennsylvania, United States

Site Status

University of Pittsburgh Medical Center

Pittsburgh, Pennsylvania, United States

Site Status

New Phase Research & Development, LLC

Knoxville, Tennessee, United States

Site Status

Baylor College of Medicine

Houston, Texas, United States

Site Status

Pioneer Research Solutions

Houston, Texas, United States

Site Status

Sante Clinical Research

Kerrville, Texas, United States

Site Status

Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Site Status

Countries

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United States

Provided Documents

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Document Type: Study Protocol and Statistical Analysis Plan

View Document

Other Identifiers

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AMDC 010-201

Identifier Type: -

Identifier Source: org_study_id

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