CB-PRP in Retinitis Pigmentosa and Dry Age-related Macular Degeneration

NCT ID: NCT04636853

Last Updated: 2023-01-11

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

20 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-12-23

Study Completion Date

2021-12-02

Brief Summary

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The study will provides the enrollment of patients with genetic retinal dystrophies with primary rod impairment and dry age-related macular degeneration (Geographic type) A subretinal injection of umbilical cord blood platelet-rich plasma (CB-PRP) will be performed only in one eye, the other eye will be considered as a control group.

A complete morpho-functional ophthalmological evaluation will be performed in all patients at each control.

Detailed Description

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All patients underwent genetic evaluation and they reported different types of mutations that induce anatomic-functional impairment of the rods.

Patients affected by bilateral dry age-related macular degeneration (Geographic type) will be recruited as well.

After selecting the patients to be enrolled, the study will proceed with the vitrectomy surgery and subretinal injection of umbilical cord blood platelet-rich plasma (CB-PRP) provided by the Umbilical Cord Bank according to the procedures provided for by the current legislation on blood components for non-transfusion use.

A complete ophthalmological examination will be performed at 1, 3, 6, and 12 months. They will include:

* Anterior segment biomicroscopy
* direct and indirect ophthalmoscopy
* ETDRS visual acuity assessment
* intraocular pressure measurement
* optical coherence tomography (OCT)
* OCT Angiography (OCTA)

The following assessments will be performed at baseline and at 6 and 12 months.

* Microperimetry
* Electroretinogram (ERG)
* Visually evoked potential (VEP)
* contrast sensitivity (MARS tables)
* Goldmann perimetry

Some morpho-functional data will also be collected in the contralateral eye and used as the control group.

To ensure the best safety for the patient, the first 5 eyes will be separated by a minimum of 20 days in order to observe the post-surgical evolution.

Conditions

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Retinitis Pigmentosa Dry Age-related Macular Degeneration

Study Design

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Allocation Method

NA

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Affected Individual

A subretinal injection of umbilical cord blood platelet-rich plasma (CB-PRP) will be performed only in one eye, the other eye will be considered as a control group.

Group Type EXPERIMENTAL

Subretinal injection of umbilical cord blood platelet-rich plasma (CB-PRP)

Intervention Type BIOLOGICAL

A subretinal injection of umbilical cord blood platelet-rich plasma (CB-PRP) will be performed only in one eye, the other eye will be considered as a control group.

A complete morpho-functional ophthalmological evaluation will be performed in all patient at each control.

Interventions

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Subretinal injection of umbilical cord blood platelet-rich plasma (CB-PRP)

A subretinal injection of umbilical cord blood platelet-rich plasma (CB-PRP) will be performed only in one eye, the other eye will be considered as a control group.

A complete morpho-functional ophthalmological evaluation will be performed in all patient at each control.

Intervention Type BIOLOGICAL

Eligibility Criteria

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Inclusion Criteria

* Retinal dystrophies with compromised rods (only for RP patients)
* Visual Field (Manual Goldmann) V / 4e \< 30 ° (only for RP patients)
* Best corrected visual acuity \> Light perception
* Known genotype
* No or minimal opacity of ocular media
* No concomitant ocular (eg glaucoma, amblyopia)
* Dry Age-related Macular Degeneration (Geographic type)

Exclusion Criteria

* Age\<18 years
* Pregnancy
* Previous inflammatory / infectious events involving the eyes
Minimum Eligible Age

18 Years

Maximum Eligible Age

70 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Fondazione Policlinico Universitario Agostino Gemelli IRCCS

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Alfonso Savastano

Role: PRINCIPAL_INVESTIGATOR

Fondazione Policlinico Universitario A. Gemelli, IRCCS

Locations

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Alfonso Savastano

Rome, , Italy

Site Status

Countries

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Italy

References

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Valentini CG, Nuzzolo ER, Bianchi M, Orlando N, Iachininoto MG, Pinci P, Teofili L. Cord Blood Platelet Lysate: In Vitro Evaluation to Support the Use in Regenerative Medicine. Mediterr J Hematol Infect Dis. 2019 Jan 1;11(1):e2019021. doi: 10.4084/MJHID.2019.021. eCollection 2019.

Reference Type RESULT
PMID: 30858959 (View on PubMed)

Rizzo S, Savastano MC, Falsini B, Bernardinelli P, Boselli F, De Vico U, Carla MM, Giannuzzi F, Fossataro C, Gambini G, Crincoli E, Ferrara S, Ripa M, Killian R, Rizzo C, Valentini CG, Orlando N, Placidi G, Teofili L, Savastano A. Safety Results for Geographic Atrophy Associated with Age-Related Macular Degeneration Using Subretinal Cord Blood Platelet-Rich Plasma. Ophthalmol Sci. 2024 Jan 24;4(6):100476. doi: 10.1016/j.xops.2024.100476. eCollection 2024 Nov-Dec.

Reference Type DERIVED
PMID: 39149709 (View on PubMed)

Other Identifiers

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3417

Identifier Type: -

Identifier Source: org_study_id

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