A Safety and Efficacy Study of a One-time Intravitreal Injection of SAR446597 in Participants With Geographic Atrophy Secondary to Age-related Macular Degeneration

NCT ID: NCT07215234

Last Updated: 2025-11-06

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE1/PHASE2

Total Enrollment

104 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-10-09

Study Completion Date

2032-07-22

Brief Summary

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This is a sequential Phase 1/2, two-part, multicenter study on safety, tolerability, and efficacy of one-time intravitreal SAR446597 for the treatment of participants with Geographic Atrophy (GA) secondary to Age-related Macular Degeneration (AMD).

The core phase duration will be approximately 2 years for each participant. An Extended Follow-Up (EFU) phase of 3 years follows the core phase.

The treatment is a one-time intravitreal injection of SAR446597 (or sham as applicable in Part II).

Detailed Description

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Conditions

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Geographic Atrophy

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Outcome Assessors

Study Groups

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Part I - SAR446597 open-label (OL)

Participants will receive SAR at a dose specified for each cohort. Multiple dose levels of SAR446597 will be evaluated in successive cohorts of participants.

Group Type EXPERIMENTAL

SAR446597

Intervention Type DRUG

Intravitreal injection

Part II - SAR446597 Dose A

Participants will receive SAR at a dose specified for each arm.

Group Type EXPERIMENTAL

SAR446597

Intervention Type DRUG

Intravitreal injection

Part II - SAR446597 Dose B

Participants will receive SAR at a dose specified for each arm.

Group Type EXPERIMENTAL

SAR446597

Intervention Type DRUG

Intravitreal injection

Part II - Sham control

Participants will receive Sham at a dose specified for each arm.

Group Type SHAM_COMPARATOR

Sham Comparator

Intervention Type DRUG

Sham periocular injection

Interventions

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SAR446597

Intravitreal injection

Intervention Type DRUG

Sham Comparator

Sham periocular injection

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* 60 years old or above
* Participants with diagnosis of GA secondary to age-related macular degeneration (AMD)
* Study eye with best corrected visual acuity (BCVA) ETDRS Snellen equivalent for dose escalation (Part I) between 20/40 and 20/320 and for expansion (Part II) equal or better than 20/200
* Study eye with GA lesion measuring between 2.5 and 17.5 mm2 for dose escalation (Part I) and between 2.5 and 14.0 mm2 for expansion (Part II). For multifocal disease, study eye with at least one single lesion of more than 1.25mm2 for both Part I and Part II

Exclusion Criteria

* GA in the study eye caused by a disease different than AMD
* Presence of neovascularization or a history of treatment with an anti vascular endothelial growth factor agent in the study eye
* Any condition or treatment (ocular or systemic) or medical or surgical history in the study eye that may prevent visual acuity improvement or interfere with ocular safety or efficacy assessments
* Current or history of systemic complement targeting treatment in the past 12 months
* Use of ocular corticosteroids for 4 months (for ocular or periocular injections), 6 months (for intraocular implants) or 3 years (for long lasting intraocular implants) prior to screening in the study eye
* History of macular laser photocoagulation treatment, photodynamic- or thermotherapy or photo biomodulation in the study eye
* History of active ocular infection in the study eye in 6 months prior to screening
* Presence of active ocular or periocular infections
* Active uncontrolled glaucoma in the study eye
* History of uveitis or scleritis in either eye
* Previous gene therapy in either eye
* Any significant poorly controlled illness that would preclude study compliance and follow up
Minimum Eligible Age

60 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Sanofi

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Associated Retina Consultants - Peoria - DocTrials - PPDS- Site Number : 8400011

Peoria, Arizona, United States

Site Status RECRUITING

Retina Macula Institute of Arizona- Site Number : 8400028

Scottsdale, Arizona, United States

Site Status RECRUITING

Vitreo Retinal Associates - Gainesville- Site Number : 8400004

Gainesville, Florida, United States

Site Status RECRUITING

University Retina - Lemont- Site Number : 8400005

Lemont, Illinois, United States

Site Status RECRUITING

Oregon Retina- Site Number : 8400017

Eugene, Oregon, United States

Site Status RECRUITING

Countries

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United States

Central Contacts

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Trial Transparency email recommended (Toll free for US & Canada)

Role: CONTACT

Phone: 800-633-1610

Email: [email protected]

Related Links

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Other Identifiers

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DFI18231

Identifier Type: -

Identifier Source: org_study_id