A Phase 2b Study in Subjects With Alcoholic Hepatitis to Evaluate Safety and Efficacy of DUR-928 Treatment

NCT ID: NCT04563026

Last Updated: 2024-09-05

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

307 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-01-22

Study Completion Date

2023-09-06

Brief Summary

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This is a randomized, double-blind, placebo-controlled, phase 2b clinical Trial evaluating Safety and Efficacy of DUR-928 (an experimental medication) in Patients with Alcoholic Hepatitis (AH).

Detailed Description

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Conditions

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Alcoholic Hepatitis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

This is a Phase 2b randomized, double-blind, placebo-controlled, multi-arm, multi-center, parallel design trial.
Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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DUR-928 (larsucosterol, 30 mg)

Group Type EXPERIMENTAL

DUR-928 30 mg

Intervention Type DRUG

IV infusion

DUR-928 (larsucosterol, 90 mg)

Group Type EXPERIMENTAL

DUR-928 90 mg

Intervention Type DRUG

IV infusion

(Placebo) Sterile Water for Injection

Group Type PLACEBO_COMPARATOR

Placebo+ Standard of Care (SOC)

Intervention Type DRUG

IV infusion

Interventions

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DUR-928 30 mg

IV infusion

Intervention Type DRUG

DUR-928 90 mg

IV infusion

Intervention Type DRUG

Placebo+ Standard of Care (SOC)

IV infusion

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Able to provide written informed consent (either from subject or subject's legally acceptable representative).
2. Onset of jaundice within prior 8 weeks.
3. Average daily consumption of \>40 (females) or \>60 (males) grams of alcohol for 6 months or longer, with \< 8 weeks of abstinence before the onset of jaundice.
4. The determination of AH may be based on typical serum chemistry (as determined by local laboratory) or liver biopsy at any time during the current episode of AH:

* Serum total bilirubin \> 3.0 mg/dL
* 50 \< AST \< 400 IU/L
* ALT \< 400 IU/L
* AST/ALT \> 1.5
5. Maddrey discriminant function (MDF) ≥ 32 assuming a control prothrombin time of 12 seconds.
6. Model for End-stage Liver Disease (MELD) score: 21-30.
7. Liver biopsy is not required, but may be used to confirm the diagnosis of AH at the Investigator's discretion. Biopsy, if used as a diagnostic criterion, must have occurred during the current episode.
8. Male or female subjects 18 years of age or older.
9. Subjects must agree to use effective methods to prevent pregnancy while participating in the study.
10. Subjects must agree to participate in an alcohol abstinence support program recommended by the local institution's addiction specialists.

Exclusion Criteria

1. Subjects taking systemic corticosteroids for a duration exceeding 8 days in the 30 days prior to screening.
2. Subjects experiencing or considered at high risk for alcohol withdrawal seizures or delirium tremens.
3. Active infection (such as spontaneous bacterial peritonitis \[SBP\], urinary tract infection \[UTI\], bacteremia, acute viral hepatitis, uncontrolled HIV, and active SARS CoV2 infection).
4. Serum creatinine \>2.5 mg/dL.
5. Subjects undergoing continuous veno-venous hemodialysis (CVVH).
6. Uncontrolled gastrointestinal bleeding.
7. A history of pre-admission refractory ascites defined as more than 4 paracenteses in the previous 8 weeks despite diuretic therapy.
8. Liver biopsy (if carried out) with findings not compatible with AH.
9. Stage ≥3 hepatic encephalopathy by West Haven criteria.
10. Any severe concomitant cardiovascular, renal, endocrine, pulmonary, psychiatric disorder, or multi-organ failure.
11. Other concomitant cause(s) of liver disease.
12. Any active malignancy or any malignancy diagnosed within the last five years other than curable skin cancer (basal cell or squamous cell carcinomas).
13. Positive Urine Drug Screen (amphetamines, barbiturates, benzodiazepines, cocaine and opiates) except THC and prescription medications.
14. Existing or intended pregnancy or breast feeding.
15. Participation in another interventional clinical trial within 30 days of Screening.
16. History of organ transplantation, other than a corneal transplant.
17. Underlying diseases that, in the opinion of the site investigator, might be complicated or exacerbated by proposed treatments or might confound assessment of study drug.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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CTI Clinical Trial and Consulting Services

OTHER

Sponsor Role collaborator

Durect

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Robert Gordon, MD, FACS

Role: STUDY_DIRECTOR

CTI Clinical Trial and Consulting Services

Locations

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University of Alabama at Birmingham (UAB) Hospital

Birmingham, Alabama, United States

Site Status

Mayo Clinic Hospital

Phoenix, Arizona, United States

Site Status

Southern California Research Center

Coronado, California, United States

Site Status

Keck Hospital of University of Southern California (USC)

Los Angeles, California, United States

Site Status

Cedars-Sinai Medical Center

Los Angeles, California, United States

Site Status

University of California Davis (UC Davis) Medical Center

Sacramento, California, United States

Site Status

University of California San Francisco (UCSF) Medical Center

San Francisco, California, United States

Site Status

Stanford University Medical Center

Stanford, California, United States

Site Status

Yale University School of Medicine

New Haven, Connecticut, United States

Site Status

MedStar Health - MedStar Georgetown University Hospital

Washington D.C., District of Columbia, United States

Site Status

Piedmont Atlanta Hospital

Atlanta, Georgia, United States

Site Status

Northwestern Memorial Hospital

Chicago, Illinois, United States

Site Status

Rush University Medical Center

Chicago, Illinois, United States

Site Status

University of Chicago Medical Center

Chicago, Illinois, United States

Site Status

Loyola University Medical Center

Maywood, Illinois, United States

Site Status

Richard Roudebush VA Hospital

Indianapolis, Indiana, United States

Site Status

University of Louisville

Louisville, Kentucky, United States

Site Status

Tulane Medical Center

New Orleans, Louisiana, United States

Site Status

University of Maryland Medical Center

Baltimore, Maryland, United States

Site Status

Johns Hopkins Hospital

Baltimore, Maryland, United States

Site Status

Tufts Medical Center

Boston, Massachusetts, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

Henry Ford Hospital

Detroit, Michigan, United States

Site Status

University of Minnesota Medical School

Minneapolis, Minnesota, United States

Site Status

Saint Luke's Health System - Saint Luke's Hospital of Kansas City

Kansas City, Missouri, United States

Site Status

Washington University School of Medicine

St Louis, Missouri, United States

Site Status

University of Nebraska Medical Center (UNMC)

Omaha, Nebraska, United States

Site Status

Rutgers-New Jersey Medical School

Newark, New Jersey, United States

Site Status

University of New Mexico (UNM) Hospital

Albuquerque, New Mexico, United States

Site Status

Northwell Health - North Shore University Hospital

Manhasset, New York, United States

Site Status

Mount Sinai Hospital

New York, New York, United States

Site Status

New York-Presbyterian - Weill Cornell Medical Center

New York, New York, United States

Site Status

Atrium Health

Charlotte, North Carolina, United States

Site Status

Cleveland Clinic

Cleveland, Ohio, United States

Site Status

Medical University of South Carolina (MUSC) Health - University Medical Center

Charleston, South Carolina, United States

Site Status

Methodist Dallas Medical Center

Dallas, Texas, United States

Site Status

Parkland Memorial Hospital

Dallas, Texas, United States

Site Status

Baylor Scott and White Health

Dallas, Texas, United States

Site Status

University of Texas Southwestern (Clements University Hospital)

Dallas, Texas, United States

Site Status

University of Texas Southwestern Medical Center

Dallas, Texas, United States

Site Status

Doctors Hospital at Renaissance (DHR)

Edinburg, Texas, United States

Site Status

Baylor College of Medicine Medical Center

Houston, Texas, United States

Site Status

Houston Methodist Hospital

Houston, Texas, United States

Site Status

Utah Health - The University of Utah Hospital

Salt Lake City, Utah, United States

Site Status

University of Virginia (UVA) Health - University Hospital

Charlottesville, Virginia, United States

Site Status

Bon Secours Liver Institute of Richmond

Richmond, Virginia, United States

Site Status

Virginia Commonwealth University Medical Center

Richmond, Virginia, United States

Site Status

Harborview Medical Center - University of Washington

Seattle, Washington, United States

Site Status

Royal Prince Alfred Hospital

Camperdown, New South Wales, Australia

Site Status

Nepean Hospital

Kingswood, New South Wales, Australia

Site Status

Mater Health - Mater Hospital Brisbane

South Brisbane, Queensland, Australia

Site Status

Royal Adelaide Hospital

Adelaide, South Australia, Australia

Site Status

Flinders Medical Centre

Bedford Park, South Australia, Australia

Site Status

Eastern Health - Box Hill Hospital

Box Hill, Victoria, Australia

Site Status

Sir Charles Gairdner Hospital

Nedlands, Western Australia, Australia

Site Status

Royal Perth Hospital

Perth, Western Australia, Australia

Site Status

Landeskrankenhaus (LKH) - Universitätsklinikum Graz

Graz, , Austria

Site Status

Université libre de Bruxelles (ULB) - Hôpital Erasme

Brussels, , Belgium

Site Status

Universitair Ziekenhuis Antwerpen (UZA)

Edegem, , Belgium

Site Status

Centre Hospitalier Régional Universitaire (CHRU) Besançon - Hôpital Jean Minjoz

Besançon, , France

Site Status

Centre Hospitalier Universitaire (CHU) de Lille - Hôpital Jeanne de Flandre

Lille, , France

Site Status

Hospices Civils de Lyon - Hôpital de la Croix-Rousse

Lyon, , France

Site Status

Hôpital St Joseph

Marseille, , France

Site Status

Barts Health NHS Trust - The Royal London Hospital

London, England, United Kingdom

Site Status

King's College Hospital NHS Foundation Trust

London, England, United Kingdom

Site Status

Imperial College Healthcare NHS Trust - St. Mary's Hospital

London, England, United Kingdom

Site Status

University Hospitals Plymouth NHS Trust - Derriford Hospital

Plymouth, England, United Kingdom

Site Status

Royal Free London NHS Foundation Trust Hospital

London, , United Kingdom

Site Status

Countries

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United States Australia Austria Belgium France United Kingdom

References

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Shiffman M, Da B, Goel A, Kwong A, Stein L, Moreno C, Nicoll A, Mehta A, Louvet A, Flamm S, Pyrsopoulos N, Satapathy S, Kuo A, Ganger D, Aloman C, Strasser SI, Tse E, Russo MW, Rockey D, Gray M, Mitchell M, Thursz M, Krebs W, Scott D, Blevins C, Ellis D, Brown J, Sussman N, Lin W. Larsucosterol for the Treatment of Alcohol-Associated Hepatitis. NEJM Evid. 2025 Feb;4(2):EVIDoa2400243. doi: 10.1056/EVIDoa2400243. Epub 2025 Jan 28.

Reference Type DERIVED
PMID: 39873544 (View on PubMed)

Other Identifiers

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C928-011

Identifier Type: -

Identifier Source: org_study_id

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