Study to Evaluate the Efficacy and Safety of HepaStem in Patients With Acute on Chronic Liver Failure (ACLF)

NCT ID: NCT04229901

Last Updated: 2024-05-22

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

133 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-01-21

Study Completion Date

2024-05-10

Brief Summary

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This is an interventional, double blind, randomized (2:1), and placebo-controlled study of 2 infusions of a 1 dose regimen of HepaStem in patients recently diagnosed (≤1 week) with ACLF grade 1 or 2 on top of Standard of Care (SoC), and for whom the diagnosis is not resolved on the day of infusion.

Detailed Description

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Conditions

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Acute on Chronic Liver Failure

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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HepaStem

Patients in the HepaStem arm will receive 2 infusions of HepaStem (i.v) at 1.0 million of cells/kg of total body weight (7 day interval)

Group Type EXPERIMENTAL

HepaStem

Intervention Type DRUG

HepaStem will be administered as an intravenous (IV) infusion

Placebo

Patients in the placebo arm will receive 2 infusions of placebo (i.v) (7 day interval)

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo will be administered as an intravenous (IV) infusion

Interventions

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HepaStem

HepaStem will be administered as an intravenous (IV) infusion

Intervention Type DRUG

Placebo

Placebo will be administered as an intravenous (IV) infusion

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Are adults aged between 18 and 75 years old.
2. Have an initial diagnosis of ACLF at the investigational site.
3. Have ACLF grade 1 or 2 according to the EASL-CLIF Consortium definition.
4. Have a total bilirubin ≥ 5 mg/dL.
5. Are able to read, understand and give written informed consent.

Exclusion Criteria

1. Have a MELD-Na score \> 35.
2. Have underlying cirrhosis due to biliary disease.
3. Have underlying cirrhosis due to autoimmune hepatitis.
4. Have active bleeding at a non-compressible site or at a compressible site that, in the opinion of the investigator, poses an unacceptable risk for the patient's participation in the study.
5. Have received treatment for bleeding complications during the current hospitalization and has a persistent high risk for re-bleeding that, in the opinion of the investigator, poses an unacceptable risk for the patient's participation in the study.
6. Have a complete portal vein thrombosis.
7. Have coagulation disturbances defined as:

* fibrinogen \< 80 mg/dL
* platelets \< 50 x 10³/mm³
8. Are requiring chronic dialysis therapy.
9. Have had a cerebrovascular, myocardial, limb arterial thrombotic event, or history for both thrombotic and hemorrhagic cerebrovascular events within 12 months prior to the Screening and not considered stabilized by the investigator.
10. Have a previous history of myocardial infarction and/or cardiac failure, with an ejection fraction rate (EFR) ≤ 40%.
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Cellaion SA

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Medical University Of Vienna

Vienna, , Austria

Site Status

UZ Antwerpen

Antwerp, , Belgium

Site Status

CHU Brugmann

Brussels, , Belgium

Site Status

CHU Erasme

Brussels, , Belgium

Site Status

Universitair Ziekenhuis Gent

Ghent, , Belgium

Site Status

UZ Leuven

Leuven, , Belgium

Site Status

CHC MontLégia

Liège, , Belgium

Site Status

Cliniques Universitaires Saint-Luc

Woluwe-Saint-Lambert, , Belgium

Site Status

University Multiprofile Hospital for Active Treatment "Dr. Georgi Stranski"

Pleven, , Bulgaria

Site Status

UMHAT Medica

Rousse, , Bulgaria

Site Status

Military Medical Academy

Sofia, , Bulgaria

Site Status

UMHAT Sveta Anna

Sofia, , Bulgaria

Site Status

UMHAT Tzarita Joanna

Sofia, , Bulgaria

Site Status

Aarhus University Hospital

Aarhus, , Denmark

Site Status

North Estonia Regional Hospital

Tallinn, , Estonia

Site Status

Lääne-Tallinna Keskhaigla AS

Tallinn, , Estonia

Site Status

CHU Angers

Angers, , France

Site Status

Hopital Beaujon

Clichy, , France

Site Status

Assistance Publique Hopitaux De Paris

Créteil, , France

Site Status

Centre Hospitalier Universitaire Grenoble Alpes

Grenoble, , France

Site Status

Hospices Civils De Lyon

Lyon, , France

Site Status

Assistance Publique Hopitaux De Marseille

Marseille, , France

Site Status

CHU Montpellier

Montpellier, , France

Site Status

Assistance Publique-Hopitaux de Paris - Hopitaux Universitaires Pitie-Salpetriere

Paris, , France

Site Status

Les Hopitaux Universitaires De Strasbourg

Strasbourg, , France

Site Status

CHU De Toulouse

Toulouse, , France

Site Status

Hospital Paul Brousse

Villejuif, , France

Site Status

Medizinische Hochschule Hannover

Hanover, , Germany

Site Status

University Hospital Of Leipzig

Leipzig, , Germany

Site Status

University Hospital Of Ulm AöR

Ulm, , Germany

Site Status

Azienda Ospedaliera Ospedale Niguarda CA' Granda

Milan, , Italy

Site Status

Azienda Ospedaliera Universitaria Policlinico

Palermo, , Italy

Site Status

Azienda Sanitaria Universitaria Friuli Centrale

Udine, , Italy

Site Status

Pauls Stradins Clinical University Hospital

Riga, , Latvia

Site Status

Lietuvos Sveikatos Mokslų Universiteto Ligoninė Kauno Klinikos

Kaunas, , Lithuania

Site Status

PHI General City Hospital "8mi Septemvri"

Skopje, , North Macedonia

Site Status

PHI University Clinic of Gastroenterohepatology

Skopje, , North Macedonia

Site Status

Id Clinic

Mysłowice, , Poland

Site Status

Kliniczny Szpital Wojewódzki Nr 2 Im. Św. Jadwigi Królowej W Rzeszowie

Rzeszów, , Poland

Site Status

F.D. Roosevelt University General Hospital Of Banská Bystrica

Banská Bystrica, , Slovakia

Site Status

Hospital Universitari Vall D'Hebron

Barcelona, , Spain

Site Status

Hospital Universitario Reina Sofia

Córdoba, , Spain

Site Status

University Hospital Ramón Y Cajal

Madrid, , Spain

Site Status

Hospital Universitario Puerta De Hierro De Majadahonda

Majadahonda, , Spain

Site Status

Sabadell Hospital

Sabadell, , Spain

Site Status

Hospital Clinico Universitario Lozano Blesa

Zaragoza, , Spain

Site Status

Hospital Unviersitario Miguel Servet

Zaragoza, , Spain

Site Status

Countries

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Austria Belgium Bulgaria Denmark Estonia France Germany Italy Latvia Lithuania North Macedonia Poland Slovakia Spain

Related Links

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Other Identifiers

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HEP102

Identifier Type: -

Identifier Source: org_study_id

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