Assess the Long Term Efficacy and Safety of Ruxolitinib Cream in Participants With Vitiligo

NCT ID: NCT04530344

Last Updated: 2025-08-14

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

458 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-09-24

Study Completion Date

2022-11-14

Brief Summary

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The purpose of this study is to evaluate the duration of response following withdrawal of ruxolitinib cream (Cohort A vehicle group), safety and maintenance of response with continued use of ruxolitinib cream in participants who have completed either Study NCT04052425 or NCT04057573 (parent studies) in which the participants will have been using ruxolitinib cream BID for the previous 28 to 52 weeks depending on their initial randomization in the parent study.

Detailed Description

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Conditions

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Vitiligo

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators
Double Blind

Study Groups

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Cohort A : ruxolitinib cream

Participants who achieve complete or almost complete facial repigmentation (achieve ≥ F VASI90) at Week 52 in the parent study will be assigned to Cohort A and will be randomized 1:1 to ruxolitinib cream.

Group Type EXPERIMENTAL

ruxolitinib

Intervention Type DRUG

ruxolitinib cream is a topical formulation applied as a thin film to affected areas BID.

Cohort A : Vehicle

Participants who achieve complete or almost complete facial repigmentation (ie, achieve ≥ F VASI90) at Week 52 in the parent study will be assigned to Cohort A and will be randomized 1:1 to vehicle cream.

Group Type PLACEBO_COMPARATOR

Vehicle

Intervention Type DRUG

Vehicle cream is a topical formulation applied as a thin film to affected areas.

Cohort B : roxolitinib cream

Participants who did not achieve ≥ F-VASI90 at Week 52 of the parent studies will be assigned to Cohort B and will continue ruxolitinib cream.

Group Type EXPERIMENTAL

ruxolitinib

Intervention Type DRUG

ruxolitinib cream is a topical formulation applied as a thin film to affected areas BID.

Interventions

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ruxolitinib

ruxolitinib cream is a topical formulation applied as a thin film to affected areas BID.

Intervention Type DRUG

Vehicle

Vehicle cream is a topical formulation applied as a thin film to affected areas.

Intervention Type DRUG

Other Intervention Names

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INCB018424 Cream

Eligibility Criteria

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Inclusion Criteria

* Currently enrolled and receiving treatment in INCB 18424-306 (NCT04052425) or INCB 18424-307 (NCT04057573) studies evaluating ruxolitinib cream in participants with vitiligo.
* Currently tolerating ruxolitinib cream in the parent study and no safety concerns per investigators judgment.
* Has demonstrated compliance, as assessed by the investigator, with the parent study protocol requirements.
* Willingness and ability to comply with scheduled visits, treatment plans, and any other study procedures indicated in this protocol.
* Male and female participants must be willing to take appropriate contraceptive measures to avoid pregnancy or fathering a child.
* Ability to comprehend and willingness to sign an ICF or written informed consent of the parent(s) or legal guardian and written assent from the participant when possible.

Exclusion Criteria

* Has been permanently discontinued from study treatment in the parent study for any reason.
* Participants with an uncontrolled intercurrent illness or any concurrent condition that, in the investigator's opinion, would jeopardize the safety of the participant or compliance with the Protocol.
* Pregnant or breastfeeding woman.
* Participants who live with anyone participating in any current Incyte-sponsored ruxolitinib cream study.
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Incyte Corporation

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Kathleen Butler, MD

Role: STUDY_CHAIR

Incyte Corporation

Locations

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Cahaba Dermatology

Hoover, Alabama, United States

Site Status

Desert Sky Dermatology

Gilbert, Arizona, United States

Site Status

First Oc Dermatology

Fountain Valley, California, United States

Site Status

Center For Dermatology Cosmetic and Laser Surgery

Fremont, California, United States

Site Status

Marvel Clinical Research Llc

Huntington Beach, California, United States

Site Status

Vitiligo & Pigmentation Institute of Southern California

Los Angeles, California, United States

Site Status

Dermatology Research Associates

Los Angeles, California, United States

Site Status

Acrc Studies

San Diego, California, United States

Site Status

University of California San Francisco

San Francisco, California, United States

Site Status

Colorado Medical Research Center Inc

Denver, Colorado, United States

Site Status

Harmony Medical Research Institute

Hialeah, Florida, United States

Site Status

Advanced Pharma

Miami, Florida, United States

Site Status

San Marcus Research Clinic Inc.

Miami Lakes, Florida, United States

Site Status

Leavitt Medical Associates of Florida

Ormond Beach, Florida, United States

Site Status

Avita Clinical Research

Tampa, Florida, United States

Site Status

Olympian Clinical Research

Tampa, Florida, United States

Site Status

Forcare Clinical Research Fcr Forward Clinical Trials, Inc

Tampa, Florida, United States

Site Status

Metabolic Research Institute Inc

West Palm Beach, Florida, United States

Site Status

Northwestern University

Chicago, Illinois, United States

Site Status

Randall Dermatology

West Lafayette, Indiana, United States

Site Status

Delricht Clinical Research - Clinedge - Ppds Baton Rouge

Baton Rouge, Louisiana, United States

Site Status

Tufts Medical Center

Boston, Massachusetts, United States

Site Status

Metro Boston Clinical Partners

Brighton, Massachusetts, United States

Site Status

Great Lakes Research Group Inc

Bay City, Michigan, United States

Site Status

Henry Ford Medical Center

Detroit, Michigan, United States

Site Status

Minnesota Clinical Study Center

Minneapolis, Minnesota, United States

Site Status

Jdr Dermatology Research

Las Vegas, Nevada, United States

Site Status

Suny Downstate Medical Center

Brooklyn, New York, United States

Site Status

Forest Hills Dermatology Group

Kew Gardens, New York, United States

Site Status

The Dermatology Specialists Greenwich

New York, New York, United States

Site Status

Icahn School of Medicine At Mount Sinai

New York, New York, United States

Site Status

Derm Research Center of New York Inc

Stony Brook, New York, United States

Site Status

Wake Research Associates Llc

Raleigh, North Carolina, United States

Site Status

Wake Forest University

Winston-Salem, North Carolina, United States

Site Status

Central Sooner Research

Norman, Oklahoma, United States

Site Status

Kgl Skin Study Center

Broomall, Pennsylvania, United States

Site Status

Dermatology Associates of Plymouth Meeting

Plymouth Meeting, Pennsylvania, United States

Site Status

Palmetto Clinical Trial Services

Anderson, South Carolina, United States

Site Status

International Clinical Research Tennessee Llc

Murfreesboro, Tennessee, United States

Site Status

Innovative Dermatology

Plano, Texas, United States

Site Status

Progressive Clinical Research

San Antonio, Texas, United States

Site Status

The Dermatology and Laser Center of San Antonio

San Antonio, Texas, United States

Site Status

Clinical Research Partners Llc

Richmond, Virginia, United States

Site Status

Dermatology Specialists of Spokane

Spokane, Washington, United States

Site Status

Medical Center Unimed Eood

Sevlievo, , Bulgaria

Site Status

Diagnostic Consultative Center Ii Sofia Eood

Sofia, , Bulgaria

Site Status

University Multiprofile Hospital For Active Treatment Aleksandrovska

Sofia, , Bulgaria

Site Status

Diagnostic Consultative Center Xxviii - Sofia - Eood

Sofia, , Bulgaria

Site Status

Medical Center Eurohealth

Sofia, , Bulgaria

Site Status

Dermatology Research Institute

Calgary, Alberta, Canada

Site Status

Simcoderm Medical and Surgical Dermatology Center

Barrie, Ontario, Canada

Site Status

Kingsway Clinical Research

Etobicoke, Ontario, Canada

Site Status

Lynderm Research Inc

Markham, Ontario, Canada

Site Status

Skin Centre For Dermatology

Peterborough, Ontario, Canada

Site Status

K. Papp Clinical Research

Waterloo, Ontario, Canada

Site Status

Xlr8 Medical Research

Windsor, Ontario, Canada

Site Status

Siena Medical Research Corporation

Westmount, Quebec, Canada

Site Status

Le Bateau Blanc

Martigues, , France

Site Status

Hopital Archet 2 Derm Dept

Nice, , France

Site Status

Centre Hospitalier Universitaire de Bordeaux - Hospital Haut-Leveque

Pessac, , France

Site Status

Hopital Charles Nicolle Chu Rouen Hospital de Bois-Guillaume

Rouen, , France

Site Status

Chu de Toulouse Hopital Larrey Centre de Reference Des Maladies Rares de La Peau Service de Dermatol

Toulouse, , France

Site Status

Universitaetsklinikum Carl Gustav Carus

Dresden, , Germany

Site Status

Hautarztpraxis Mahlow

Mahlow, , Germany

Site Status

Universitatsmedizin Der Johannes Gutenberg-Universitat Mainz Iii

Mainz, , Germany

Site Status

Universitatsklinik Munster Dermatologie

Münster, , Germany

Site Status

Amsterdam University Medical Centre

Amsterdam, , Netherlands

Site Status

Synexus - Polska Sp Z Oo Oddzial W Gdansk

Gdansk, , Poland

Site Status

Synexus Polska Sp. Z O.O. Oddzial W Gdyni

Gdynia, , Poland

Site Status

Synexus - Sp Z Oo Oddzial W Katowice

Katowice, , Poland

Site Status

Synexus Affiliate - Krakowskie Centrum Medyczne

Krakow, , Poland

Site Status

Synexus Polska Sp Z Oo Oddzial W Lodzi

Lodz, , Poland

Site Status

Synexus Polska Sp Z Oo Oddzial W Czestochowie

Lublin, , Poland

Site Status

Dermedic Dr. Zdybski

Ostrowiec Świętokrzyski, , Poland

Site Status

Synexus Polska Sp. Z O.O. Oddzial W Poznaniu

Poznan, , Poland

Site Status

Lubeskie Centrum Diagnostyczne

Świdnik, , Poland

Site Status

Poradnia Dermatologiczno-Wenerologiczna Mediderm S.C. Nzoz

Torun, , Poland

Site Status

Synexus Polska Sp. Z O.O. Oddzial Warszawie

Warsaw, , Poland

Site Status

High-Med Przychodnia Specjalistycza

Warsaw, , Poland

Site Status

Synexus Polska Sp. Z O.O. Oddzial We Wroclawiu

Wroclaw, , Poland

Site Status

Dermmedica Sp. Z O.O.

Wroclaw, , Poland

Site Status

Ico Hospital Germans Trias I Pujol

Badalona, , Spain

Site Status

Dermomedic

Madrid, , Spain

Site Status

Clinica Universidad de Navarra (Cun)

Pamplona, , Spain

Site Status

Countries

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United States Bulgaria Canada France Germany Netherlands Poland Spain

References

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Rosmarin D, Pandya AG, Passeron T, Forman SB, Zdybski J, Amster M, Feser C, Papp KA, Nuara A, Kornacki D, Wei S, Ren H, Harris JE, Ezzedine K. Long-Term Integrated Safety Summary of Ruxolitinib Cream in Phase 3 Clinical Trials of Patients with Vitiligo. Dermatol Ther (Heidelb). 2025 Oct 22. doi: 10.1007/s13555-025-01555-3. Online ahead of print.

Reference Type DERIVED
PMID: 41125994 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2020-000987-53

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

INCB 18424-308

Identifier Type: -

Identifier Source: org_study_id

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