Topical Ruxolitinib Evaluation in Vitiligo Study 2 (TRuE-V2)

NCT ID: NCT04057573

Last Updated: 2025-08-22

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

344 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-10-03

Study Completion Date

2021-10-01

Brief Summary

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The purpose of this study is to evaluate the efficacy and safety of ruxolitinib cream in adolescent and adult participants with non-segmental vitiligo for whom total body involved vitiligo area (facial and nonfacial) does not exceed 10% body surface area (BSA).

Detailed Description

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Conditions

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Non-segmental Vitiligo

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

CROSSOVER

Participants will receive ruxolitinib cream or vehicle for 24 weeks, after which they will be offered the opportunity to continue in the treatment extension period. Participants initially randomized to vehicle will be crossed over to active drug, and participants treated with ruxolitinib cream will receive an additional 28 weeks of treatment with ruxolitinib cream.
Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors

Study Groups

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Double-Blind Period: Ruxolitinib cream 1.5% BID

Participants applied ruxolitinib 1.5% cream twice daily (BID) for 24 weeks.

Group Type EXPERIMENTAL

Ruxolitinib cream

Intervention Type DRUG

Ruxolitinib cream is a topical formulation applied as a thin film to affected areas.

Double-Blind Period: Vehicle cream BID

Participants applied matching vehicle cream BID for 24 weeks.

Group Type PLACEBO_COMPARATOR

Vehicle

Intervention Type DRUG

Vehicle cream is a topical formulation applied as a thin film to affected areas.

Treatment-Extension Period: Ruxolitinib cream 1.5% BID

Participants who completed the Week 24 assessments with no safety concerns could continue into the 28-week Treatment-Extension Period. Participants who applied ruxolitinib cream 1.5% BID during the Double-Blind Period continued to apply ruxolitinib cream 1.5% BID for an additional 28 weeks in the Treatment-Extension Period.

Group Type EXPERIMENTAL

Ruxolitinib cream

Intervention Type DRUG

Ruxolitinib cream is a topical formulation applied as a thin film to affected areas.

Treatment-Extension Period: Vehicle cream to Ruxolitinib cream 1.5% BID

Participants who completed the Week 24 assessments with no safety concerns could continue into the 28-week Treatment-Extension Period. Participants who applied vehicle cream BID during the Double-Blind Period applied ruxolitinib cream 1.5%m BID for 28 weeks in the Treatment-Extension Period.

Group Type EXPERIMENTAL

Ruxolitinib cream

Intervention Type DRUG

Ruxolitinib cream is a topical formulation applied as a thin film to affected areas.

Vehicle

Intervention Type DRUG

Vehicle cream is a topical formulation applied as a thin film to affected areas.

Interventions

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Ruxolitinib cream

Ruxolitinib cream is a topical formulation applied as a thin film to affected areas.

Intervention Type DRUG

Vehicle

Vehicle cream is a topical formulation applied as a thin film to affected areas.

Intervention Type DRUG

Other Intervention Names

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INCB018424 cream

Eligibility Criteria

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Inclusion Criteria

* Clinical diagnosis of non-segmental vitiligo with depigmented area including ≥ 0.5% BSA on the face, ≥ 0.5 F-VASI, ≥ 3% BSA on nonfacial areas, ≥ 3 T-VASI, and total body vitiligo area (facial and nonfacial) not exceeding 10% BSA.
* Agree to discontinue all agents used to treat vitiligo from screening through the final safety follow-up visit. Over-the-counter preparations deemed acceptable by the investigator and camouflage makeups are permitted.
* Must be willing to take appropriate contraceptive measures to avoid pregnancy or fathering a child for the duration of study participation.

Exclusion Criteria

* No pigmented hair within any of the vitiligo areas on the face.
* Other forms of vitiligo (eg, segmental) or other differential diagnosis of vitiligo or other skin depigmentation disorders (eg, piebaldism, pityriasis alba, leprosy, postinflammatory hypopigmentation, progressive macule hypomelanosis, nevus anemicus, chemical leukoderma, and tinea versicolor).
* Have used depigmentation treatments (eg, monobenzone) for past treatment of vitiligo or other pigmented areas.
* Use of protocol-defined treatments within the indicated washout period before baseline.
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Incyte Corporation

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Kathleen Butler, MD

Role: STUDY_DIRECTOR

Incyte Corporation

Locations

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Desert Sky Dermatology

Gilbert, Arizona, United States

Site Status

Center For Dermatology Cosmetic and Laser Surgery

Fremont, California, United States

Site Status

Uci Beckman Laser Institute and Medical Clinic

Irvine, California, United States

Site Status

UCI Health Beckman Laser Institute and Medical Center

Irvine, California, United States

Site Status

Vitiligo & Pigmentation Institute of Southern California

Los Angeles, California, United States

Site Status

Dermatology Research Associates

Los Angeles, California, United States

Site Status

Dermatology Specialists Inc

Murrieta, California, United States

Site Status

Dermatology Specialists Inc

Oceanside, California, United States

Site Status

Integrative Skin Science and Research

Sacramento, California, United States

Site Status

Acrc Studies

San Diego, California, United States

Site Status

Central Sooner Research

San Diego, California, United States

Site Status

Colorado Medical Research Center Inc

Denver, Colorado, United States

Site Status

Advanced Pharma Cr

Miami, Florida, United States

Site Status

Leavitt Medical Associates of Florida

Ormond Beach, Florida, United States

Site Status

Avita Clinical Research

Tampa, Florida, United States

Site Status

Olympian Clinical Research

Tampa, Florida, United States

Site Status

Ashira Dermatology Llc

Gurnee, Illinois, United States

Site Status

Randall Dermatology of West Lafayette

West Lafayette, Indiana, United States

Site Status

Randall Dermatology

West Lafayette, Indiana, United States

Site Status

Delricht Clinical Research - Clinedge - Ppds Baton Rouge

Baton Rouge, Louisiana, United States

Site Status

Tufts Medical Center

Boston, Massachusetts, United States

Site Status

Tufts Medical Center

Boston, Massachusetts, United States

Site Status

Metro Boston Clinical Partners

Brighton, Massachusetts, United States

Site Status

University of Massachusetts

Worcester, Massachusetts, United States

Site Status

Henry Ford Hospital

Detroit, Michigan, United States

Site Status

Henry Ford Medical Center

Detroit, Michigan, United States

Site Status

Minnesota Clinical Study Center

Minneapolis, Minnesota, United States

Site Status

Jdr Dermatology Research

Las Vegas, Nevada, United States

Site Status

Northwell Physician Partners

New Hyde Park, New York, United States

Site Status

Icahn School of Medicine At Mount Sinai

New York, New York, United States

Site Status

Derm Research Center of New York Inc

Stony Brook, New York, United States

Site Status

Central Sooner Research

Norman, Oklahoma, United States

Site Status

Oregon Medical Research Center

Portland, Oregon, United States

Site Status

Clinical Research Partners Llc

Richmond, Virginia, United States

Site Status

Medical Center Unimed Eood

Sevlievo, , Bulgaria

Site Status

Medical Center Unimed EOOD

Sevlievo, , Bulgaria

Site Status

Diagnostic Consultative Center Ii Sofia Eood

Sofia, , Bulgaria

Site Status

University Multiprofile Hospital For Active Treatment Aleksandrovska

Sofia, , Bulgaria

Site Status

Diagnostic Consultative Center II Sofia EOOD

Sofia, , Bulgaria

Site Status

Diagnostic Consultative Center II Sofia EOOD

Sofia, , Bulgaria

Site Status

University Hospital Prof Dr Stoyan Kirkovich

Stara Zagora, , Bulgaria

Site Status

University Hospital " Prof. Dr Stoyan Kirkovich"

Stara Zagora, , Bulgaria

Site Status

Simcoderm Medical and Surgical Dermatology Center

Barrie, Ontario, Canada

Site Status

Kingsway Clinical Research

Etobicoke, Ontario, Canada

Site Status

Lynderm Research Inc

Markham, Ontario, Canada

Site Status

K. Papp Clinical Research

Waterloo, Ontario, Canada

Site Status

Xlr8 Medical Research

Windsor, Ontario, Canada

Site Status

Centre Hospitalier Universitaire de Besancon

Besançon, , France

Site Status

CHU Besancon

Besançon, , France

Site Status

Centre Hospitalier Universitaire de Bordeaux

Bordeaux, , France

Site Status

CHU de Bordeaux, Hospital Saint Andre

Bordeaux, , France

Site Status

University Hospital Henri Mondor

Créteil, , France

Site Status

CENTRE HOSpITALIER UNIVERSITAIRE HENRI MONDOR

Créteil, , France

Site Status

Le Bateau Blanc

Martigues, , France

Site Status

Emovis GMBH

Berlin, , Germany

Site Status

Universitatsklinikum Bonn Aoer

Bonn, , Germany

Site Status

Hautarztpraxis Mahlow

Mahlow, , Germany

Site Status

Universitatsmedizin Der Johannes Gutenberg-Universitat Mainz Iii

Mainz, , Germany

Site Status

University Medical Center (Universitätsmedizin der Johannes Gutenberg-Universität Mainz)

Mainz, , Germany

Site Status

Policlinico S. Orsola Malpighi

Bologna, , Italy

Site Status

Istituto Dermatologico San Gallicano

Rome, , Italy

Site Status

Amsterdam University Medical Centre

Amsterdam, , Netherlands

Site Status

Synexus Polska Sp. Z o.o. Oddział w Częstochowie

Częstochowa, , Poland

Site Status

Synexus Affiliate - Krakowskie Centrum Medyczne

Krakow, , Poland

Site Status

Synexus Polska Sp Z Oo Oddzial W Lodzi

Lodz, , Poland

Site Status

Synexus Polska Sp Z Oo Oddzial W Czestochowie

Lublin, , Poland

Site Status

Lubeskie Centrum Diagnostyczne

Świdnik, , Poland

Site Status

Synexus Polska Sp. Z O.O. Oddzial Warszawie

Warsaw, , Poland

Site Status

High-Med Przychodnia Specjalistycza

Warsaw, , Poland

Site Status

Dermmedica Sp. Z O.O.

Wroclaw, , Poland

Site Status

Ico Hospital Germans Trias I Pujol

Badalona, , Spain

Site Status

Hospital Universitari Germans Trias i Pujol

Barcelona, , Spain

Site Status

Dermomedic

Madrid, , Spain

Site Status

IDEI (Instituto de Dermatología Integral).

Madrid, , Spain

Site Status

Hospital La Paz (Hospital Universitario La Paz )

Madrid, , Spain

Site Status

Hospital Universitario de La Paz

Madrid, , Spain

Site Status

Countries

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United States Bulgaria Canada France Germany Italy Netherlands Poland Spain

References

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Rosmarin D, Pandya AG, Passeron T, Forman SB, Zdybski J, Amster M, Feser C, Papp KA, Nuara A, Kornacki D, Wei S, Ren H, Harris JE, Ezzedine K. Long-Term Integrated Safety Summary of Ruxolitinib Cream in Phase 3 Clinical Trials of Patients with Vitiligo. Dermatol Ther (Heidelb). 2025 Oct 22. doi: 10.1007/s13555-025-01555-3. Online ahead of print.

Reference Type DERIVED
PMID: 41125994 (View on PubMed)

Seneschal J, Wolkerstorfer A, Desai SR, Grimes P, Ezzedine K, Pandya AG, Kornacki D, Wei S, Passeron T, Rosmarin D. Efficacy and Safety of Ruxolitinib Cream in Vitiligo by Patient Characteristic Subgroups: Descriptive Pooled Analysis From Two Phase 3 Studies. Dermatol Ther (Heidelb). 2025 May;15(5):1227-1238. doi: 10.1007/s13555-025-01381-7. Epub 2025 Mar 29.

Reference Type DERIVED
PMID: 40156697 (View on PubMed)

Bibeau K, Butler K, Wang M, Skaltsa K, Hamzavi IH. Psychometric Evaluation of the Facial and Total Vitiligo Area Scoring Index Instruments in the TRuE-V Phase 3 Studies. Dermatol Ther (Heidelb). 2024 Aug;14(8):2223-2234. doi: 10.1007/s13555-024-01223-y. Epub 2024 Jul 30.

Reference Type DERIVED
PMID: 39078582 (View on PubMed)

Rosmarin D, Passeron T, Pandya AG, Grimes P, Harris JE, Desai SR, Lebwohl M, Ruer-Mulard M, Seneschal J, Wolkerstorfer A, Kornacki D, Sun K, Butler K, Ezzedine K; TRuE-V Study Group. Two Phase 3, Randomized, Controlled Trials of Ruxolitinib Cream for Vitiligo. N Engl J Med. 2022 Oct 20;387(16):1445-1455. doi: 10.1056/NEJMoa2118828.

Reference Type DERIVED
PMID: 36260792 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2019-000847-28

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

INCB 18424-307

Identifier Type: -

Identifier Source: org_study_id

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