Evaluation of the Impact of the Update SMM Criteria on the Natural History of SMM to Establish New Recommendations.

NCT ID: NCT04144387

Last Updated: 2024-03-06

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

NA

Total Enrollment

395 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-02-11

Study Completion Date

2028-12-31

Brief Summary

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This study is a prospective open label interventional multicenter study evaluating the impact of the update multiple myeloma criteria on the natural history of smoldering myeloma in order to establish new recommendations about follow up and prognostic evaluation of smoldering myeloma.

Detailed Description

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In 2014, the International Myeloma Working Group (IMWG) proposed a revised classification of multiple myeloma (MM) and smoldering myeloma (SMM). Since the new definition of SMM proposed excludes "ultra-high risk SMM", the evolution profile of SMM will change. Therefore, investigators need to update their knowledge of SMM to optimize the management of patients. This project is expected to describe more precisely the new landscape of SMM.

The results will help to establish new recommendations for the standard care of SMM and especially for defining accurate follow-up and risk stratifying.

Conditions

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Smoldering Multiple Myeloma

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

SCREENING

Blinding Strategy

NONE

Study Groups

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Test group

Each patient included in the study will be followed for 5 years

Group Type EXPERIMENTAL

Myelogram

Intervention Type PROCEDURE

Two additional myelograms will be performed comparing to standard of care.

Interventions

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Myelogram

Two additional myelograms will be performed comparing to standard of care.

Intervention Type PROCEDURE

Eligibility Criteria

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Inclusion Criteria

* Age ≥ 18 years.
* SMM defined by IMWG 2014 criteria

1. Serum monoclonal protein (IgG or IgA) ≥30 g/L and/or urinary monoclonal protein ≥500 mg per 24 h and/or clonal bone marrow plasma cells 10-60%
2. Absence of myeloma defining events or amyloidosis
* Diagnosed less than 1 year before the inclusion
* Able and willing to give valid written informed consent. Patients must give written informed consent (IC) in accordance with institutional and local guidelines.

Exclusion Criteria

* Previous antimyeloma treatment including bisphosphonates
* Second Primary Malignancy and/or auto-immune disease treated by immunosuppressive drugs.
* Evidence of end organ damage that can be attributed to the underlying SMM:

1. Hypercalcaemia: serum calcium \>0.25 mmol/L (\>10 mg/L) higher than the upper limit of normal or \>2.75 mmol/L (\>110 mg/L)
2. Renal insufficiency: creatinine clearance \<40 mL/min or serum creatinine \>177 μmol/L (\>20 mg/L)
3. Anaemia: haemoglobin value of \>2 g/dL below the lower limit of normal, or a haemoglobin value \<10 g/dL
4. Bone lesions: one or more osteolytic lesions on skeletal radiography, CT, or Positron Emission Tomography-Computed Tomography (PET-CT)
* Presence of one of the following biomarkers of malignancy:

1. Clonal bone marrow plasmocytosis ≥60%
2. Involved/uninvolved serum Free Light Chain (FLC) ratio ≥ 100 (The involved free light chain must be ≥100 mg/L)
3. Presence of one or more focal lesions on MRI studies (each focal lesion must be 5 mm or more in size)
* History of malignancy other than SMM within 3 years before inclusion
* Amyloidosis
* POEMS syndrome
* Contraindication to MRI
* Pregnancy
* Nursing mother
* Legally protected adults (under judicial protection, guardianship, or supervision)
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Intergroupe Francophone du Myelome

NETWORK

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pr. Olivier Decaux

Role: PRINCIPAL_INVESTIGATOR

Rennes University Hospital

Locations

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Cliniques Universitaires Saint-Luc

Brussels, , Belgium

Site Status

Institut Jules Bordet

Brussels, , Belgium

Site Status

CHU UCL Namur ASBL Site Godinne

Yvoir, , Belgium

Site Status

Centre Hospitalier

Abbeville, , France

Site Status

CHU Amiens Sud

Amiens, , France

Site Status

CHRU - Hôpital du Bocage

Angers, , France

Site Status

Ch Annecy Genevois

Annecy, , France

Site Status

Centre Hospitalier d'Argenteuil Victor Dupouy

Argenteuil, , France

Site Status

CH d'Arras

Arras, , France

Site Status

Centre Hospitalier de Auch

Auch, , France

Site Status

Centre Hospitalier H. Duffaut

Avignon, , France

Site Status

Centre hospitalier de la Côte Basque

Bayonne, , France

Site Status

Hôpital Nord Franche Comté

Belfort, , France

Site Status

Centre Hospitalier Simone Veil

Blois, , France

Site Status

Hôpital Avicenne

Bobigny, , France

Site Status

Institut Bergonié - Pavillon Saint Genès - 1er étage

Bordeaux, , France

Site Status

Polyclinique Bordeaux Nord Aquitaine

Bordeaux, , France

Site Status

Centre hospitalier Pierre Oudot

Bourgoin, , France

Site Status

CHRU Brest - Hôpital A. Morvan

Brest, , France

Site Status

CHU Caen - Côte de Nacre

Caen, , France

Site Status

Centre Hospitalier

Cannes, , France

Site Status

CH René Dubos

Cergy-Pontoise, , France

Site Status

Médipôle de Savoie

Challes-les-Eaux, , France

Site Status

Centre Hospitalier William Morey

Chalon-sur-Saône, , France

Site Status

CH Chambéry

Chambéry, , France

Site Status

Hôpital d'Instruction des Armées Percy

Clamart, , France

Site Status

Centre Hospitalier Sud Francilien

Corbeil-Essonnes, , France

Site Status

CHU Henri Mondor

Créteil, , France

Site Status

Centre Hospitalier

Dax, , France

Site Status

CHU François Mitterand

Dijon, , France

Site Status

Centre Hospitalier de Dunkerque

Dunkirk, , France

Site Status

Hôpital de Fréjus

Fréjus, , France

Site Status

CHU de Grenoble

Grenoble, , France

Site Status

Institut Daniel Hollard

Grenoble, , France

Site Status

CHD Vendée

La Roche-sur-Yon, , France

Site Status

Groupe Hospitalier de La Rochelle

La Rochelle, , France

Site Status

Hospital Jacques Monod

Le Havre, , France

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Centre Hospitalier

Le Mans, , France

Site Status

Centre Hospitalier

Lens, , France

Site Status

Centre hospitalier Robert Boulin

Libourne, , France

Site Status

CHRU Hôpital Claude Huriez

Lille, , France

Site Status

Centre Hospitalier Universitaire (CHU) de Limoges

Limoges, , France

Site Status

Hôpital du Scorff

Lorient, , France

Site Status

Centre Hospitalier Lyon Sud

Lyon, , France

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Centre Léon Bérard

Lyon, , France

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CH Meaux

Meaux, , France

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Hospital Sainte Blandine

Metz, , France

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Hôpital de Mercy (CHR Metz-Thionville)

Metz, , France

Site Status

Centre de Recherche Clinique / GHT des Landes

Mont-de-Marsan, , France

Site Status

Clinique du Parc

Montpellier, , France

Site Status

Hopital Saint Eloi - CHU Montpellier

Montpellier, , France

Site Status

Hôpital E. Muller

Mulhouse, , France

Site Status

CHRU Hôpitaux de Brabois

Nancy, , France

Site Status

Centre Catherine de Sienne

Nantes, , France

Site Status

CHRU Hôtel Dieu

Nantes, , France

Site Status

Hôpital Archet 1

Nice, , France

Site Status

CHU Carémeau, Institut de Cancérologie du Guard

Nîmes, , France

Site Status

CH La Source

Orléans, , France

Site Status

CHU Hôpital Saint Antoine

Paris, , France

Site Status

Hôpital Cochin

Paris, , France

Site Status

Hôpital Necker

Paris, , France

Site Status

Hôpital Saint Louis

Paris, , France

Site Status

La Pitié

Paris, , France

Site Status

CH Saint Jean

Perpignan, , France

Site Status

CHRU - Hôpital du Haut Lévêque - Centre François Magendie

Pessac, , France

Site Status

Centre Hospitalier de Perigueux

Périgueux, , France

Site Status

CHU Poitiers - Pôle régional de Cancérologie

Poitiers, , France

Site Status

Centre Hospitalier de Quimper Cornouaille

Quimper, , France

Site Status

Hôpital Robert Debré

Reims, , France

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CHRU Hôpital de Pontchaillou

Rennes, , France

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Hôpital Privé Sévigné

Rennes, , France

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Centre Hospitalier Jacques Puel

Rodez, , France

Site Status

CH Roubaix

Roubaix, , France

Site Status

Centre Henri Becquerel

Rouen, , France

Site Status

Centre Hospitalier Yves Le Foll

Saint-Brieuc, , France

Site Status

Institut de Cancérologie Lucien Neuwirth

Saint-Priest, , France

Site Status

Centre Hospitalier

Saint-Quentin, , France

Site Status

CH Saint Malo

St-Malo, , France

Site Status

CHU Strasbourg - Hôpital de Hautepierre

Strasbourg, , France

Site Status

Strasbourg Oncologie Libérale

Strasbourg, , France

Site Status

Centre hospitalier de Tarbes

Tarbes, , France

Site Status

Hôpital Inter-Armées Ste Anne

Toulon, , France

Site Status

Pôle IUCT Oncopole CHU

Toulouse, , France

Site Status

CHRU Hôpital Bretonneau - Centre Henry Kaplan

Tours, , France

Site Status

Centre Hospitalier de Troyes

Troyes, , France

Site Status

Centre Hospitalier de Valence

Valence, , France

Site Status

Centre Hospitalier

Valenciennes, , France

Site Status

CH Bretagne Atlantique Vannes et Auray - P. Chubert

Vannes, , France

Site Status

CHV André Mignot - Université de Versailles

Versailles, , France

Site Status

Centre Hospitalier Princesse Grace

Monaco, , Monaco

Site Status

Countries

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Belgium France Monaco

Other Identifiers

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2016-002650-20

Identifier Type: OTHER

Identifier Source: secondary_id

IFM 2017-04

Identifier Type: -

Identifier Source: org_study_id

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