Phase 3 Study With Carfilzomib and Dexamethasone Versus Bortezomib and Dexamethasone for Relapsed Multiple Myeloma Patients

NCT ID: NCT01568866

Last Updated: 2022-11-14

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

929 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-06-20

Study Completion Date

2018-02-05

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The primary objective of this study was to compare progression-free survival in patients with multiple myeloma who relapsed after 1 to 3 prior therapies treated with carfilzomib plus dexamethasone or bortezomib plus dexamethasone.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Multiple Myeloma

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Carfilzomib plus Dexamethasone

Participants received 20 mg/m² carfilzomib administered by intravenous (IV) infusion on Days 1 and 2 of Cycle 1, followed by 56 mg/m² on Days 8, 9, 15, and 16 of Cycle 1 and for each 28-day cycle thereafter. Additionally, participants received 20 mg dexamethasone on Days 1, 2, 8, 9, 15, 16, 22, and 23 of each 28 day cycle.

Group Type EXPERIMENTAL

Carfilzomib

Intervention Type DRUG

Carfilzomib is administered over 30 minutes as an infusion.

Dexamethasone

Intervention Type DRUG

Tablet for oral administration; On days when carfilzomib or bortezomib was administered, the dexamethasone was to be given 30 minutes to 4 hours prior to the carfilzomib or bortezomib dose.

Bortezomib plus Dexamethasone

Participants received bortezomib 1.3 mg/m² administered IV or subcutaneously (SC) on Days 1, 4, 8, and 11 of a 21-day cycle plus dexamethasone 20 mg administered on Days 1, 2, 4, 5, 8, 9, 11, and 12 of each 21-day cycle.

Group Type ACTIVE_COMPARATOR

Bortezomib

Intervention Type DRUG

Bortezomib is administered as a 3-5 second bolus IV injection or SC injection (in accordance with regulatory approval)

Dexamethasone

Intervention Type DRUG

Tablet for oral administration; On days when carfilzomib or bortezomib was administered, the dexamethasone was to be given 30 minutes to 4 hours prior to the carfilzomib or bortezomib dose.

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Carfilzomib

Carfilzomib is administered over 30 minutes as an infusion.

Intervention Type DRUG

Bortezomib

Bortezomib is administered as a 3-5 second bolus IV injection or SC injection (in accordance with regulatory approval)

Intervention Type DRUG

Dexamethasone

Tablet for oral administration; On days when carfilzomib or bortezomib was administered, the dexamethasone was to be given 30 minutes to 4 hours prior to the carfilzomib or bortezomib dose.

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

PR-171 Krypolis Velcade

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

1. Multiple myeloma with relapsing or progressing disease at study entry.
2. Patients must have evaluable multiple myeloma with, at least one of the following (assessed within 21 days prior to randomization):

* Serum M-protein ≥ 0.5 g/dL, or
* Urine M-protein ≥ 200 mg/24 hour, or
* In patients without detectable serum or urine M-protein, serum free light chain (SFLC) \> 100 mg/L (involved light chain) and an abnormal serum kappa/lamda ratio, or
* For immunoglobulin (Ig) A patients whose disease can only be reliably measured by serum quantitative immunoglobulin (qIgA) ≥ 750 mg/dL (0.75 g/dL).
3. Patients must have documented at least partial response (PR) to at least 1 line of prior therapy. PR documentation can be based on Investigator assessment.
4. Received 1, but no more than 3 prior treatment regimens or lines of therapy for multiple myeloma. (Induction therapy followed by stem cell transplant and consolidation/maintenance therapy will be considered as one line of therapy).
5. Prior therapy with Velcade is allowed as long as the patient had at least a PR to prior Velcade therapy, was not removed from Velcade therapy due to toxicity, and will have at least a 6 month Velcade treatment-free interval from last dose received until first study treatment. (Patients may receive maintenance therapy with drugs that are not in the proteasome inhibitor class during this 6 month Velcade treatment-free interval).
6. Prior therapy with carfilzomib is allowed as long as the patient had at least a PR to prior carfilzomib therapy, was not removed from carfilzomib therapy due to toxicity, and had at least a 6-month carfilzomib treatment-free interval from last dose received until first study treatment. (Patients may receive maintenance therapy with drugs that are not in the proteasome inhibitor class during this 6 month carfilzomib treatment-free interval). The exception to this is patients randomized or previously randomized in any other Onyx-Sponsored Phase 3 trial.
7. Males and females ≥ 18 years of age.
8. Eastern Cooperative Oncology Group (ECOG) Performance Status of 0 to 2.
9. Adequate hepatic function within 21 days prior to randomization, with bilirubin \< 1.5 times the upper limit of normal (ULN), and aspartate aminotransferase (AST) and alanine aminotransferase (ALT) \< 3 times the ULN.
10. Left ventricular ejection fraction (LVEF) ≥ 40%.
11. Absolute neutrophil count (ANC) ≥ 1000/mm³ within 21 days prior to randomization. Screening ANC should be independent of growth factor support for ≥ 1 week.
12. Hemoglobin ≥ 8.0 g/dL within 21 days prior to randomization. Use of erythropoietic stimulating factors and red blood cell (RBC) transfusions per institutional guidelines is allowed, however most recent RBC transfusion may not have been done within 7 days prior to obtaining screening hemoglobin.
13. Platelet count ≥ 50,000/mm³ (≥ 30,000/mm³ if myeloma involvement in the bone marrow is \> 50%) within 21 days prior to randomization. Patients should not have received platelet transfusions for at least 1 week prior to obtaining the screening platelet count.
14. Calculated or measured creatinine clearance (CrCl) of ≥ 15 mL/min within 21 days prior to randomization. Calculation should be based on standard formula such as the Cockcroft and Gault:

\[(140 - Age) x Mass (kg) / (72 x Creatinine mg/dL)\]; multiply result by 0.85 if female.
15. Written informed consent in accordance with federal, local, and institutional guidelines.
16. Female patients of child-bearing potential (FCBP) must have a negative serum pregnancy test within 21 days prior to randomization and agree to use an effective method of contraception during and for 3 months following last dose of drug (more frequent pregnancy tests may be conducted if required per local regulations). FCBP is defined as a sexually mature woman who: 1) has not undergone a hysterectomy or bilateral oophorectomy or 2) has not been naturally postmenopausal (amenorrhea following cancer therapy does not rule out childbearing potential) for at least 12 consecutive months (i.e., has had menses at any time in the preceding 12 consecutive months).
17. Male patients must use an effective barrier method of contraception during study and for 3 months following the last dose if sexually active with a FCBP.

Exclusion Criteria

1. Multiple Myeloma of IgM subtype.
2. Glucocorticoid therapy (prednisone \> 30 mg/day or equivalent) within 14 days prior to randomization.
3. POEMS syndrome (polyneuropathy, organomegaly, endocrinopathy, monoclonal protein, and skin changes).
4. Plasma cell leukemia or circulating plasma cells ≥ 2 × 10\^9/L.
5. Waldenstrom's Macroglobulinemia.
6. Patients with known amyloidosis.
7. Chemotherapy with approved or investigational anticancer therapeutics within 21 days prior to randomization.
8. Patients randomized or previously randomized in any other Onyx-Sponsored Phase 3 trial.
9. Focal radiation therapy within 7 days prior to randomization. Radiation therapy to an extended field involving a significant volume of bone marrow within 21 days prior to randomization (i.e., prior radiation must have been to less than 30% of the bone marrow).
10. Immunotherapy within 21 days prior to randomization.
11. Major surgery (excluding kyphoplasty) within 28 days prior to randomization.
12. Active congestive heart failure (New York Heart Association \[NYHA\] Class III to IV), symptomatic ischemia, or conduction abnormalities uncontrolled by conventional intervention. Myocardial infarction within four months prior to randomization.
13. Acute active infection requiring systemic antibiotics, antiviral (except antiviral therapy directed at hepatitis B) or antifungal agents within 14 days prior to randomization.
14. Known human immunodeficiency (HIV) seropositive, hepatitis C infection, and/or hepatitis B (except for patients with hepatitis B surface antigen \[SAg\] or core antibody receiving and responding to antiviral therapy directed at hepatitis B: these patients are allowed).
15. Patients with known cirrhosis.
16. Second malignancy within the past 3 years except:

* adequately treated basal cell or squamous cell skin cancer
* carcinoma in situ of the cervix
* prostate cancer \< Gleason score 6 with stable prostate-specific antigen (PSA) over 12 months
* breast carcinoma in situ with full surgical resection
* treated medullary or papillary thyroid cancer
17. Patients with myelodysplastic syndrome.
18. Significant neuropathy (Grades 3 to 4, or Grade 2 with pain) within 14 days prior to randomization.
19. Female patients who are pregnant or lactating.
20. Known history of allergy to Captisol(a cyclodextrin derivative used to solubilize carfilzomib).
21. Patients with hypersensitivity to carfilzomib, Velcade, boron, or mannitol.
22. Patients with contraindication to dexamethasone.
23. Contraindication to any of the required concomitant drugs or supportive treatments, including hypersensitivity to antiviral drugs, or intolerance to hydration due to preexisting pulmonary or cardiac impairment.
24. Ongoing graft-vs-host disease.
25. Patients with pleural effusions requiring thoracentesis or ascites requiring paracentesis within 14 days prior to randomization.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Amgen

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

MD

Role: STUDY_DIRECTOR

Amgen

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Providence St. Joseph Medical Center

Burbank, California, United States

Site Status

UCSD Moore Cancer Center

La Jolla, California, United States

Site Status

UCLA Medical Center

Los Angeles, California, United States

Site Status

Central Coast Medical Oncology Group

Santa Maria, California, United States

Site Status

Colorado Blood Cancer Institute

Denver, Colorado, United States

Site Status

MAB Oncology/Hematology

Melbourne, Florida, United States

Site Status

Palm Beach Cancer Institute

West Palm Beach, Florida, United States

Site Status

Winship Cancer Institute

Atlanta, Georgia, United States

Site Status

Hematology Oncology of Indiana, PC

Indianapolis, Indiana, United States

Site Status

Center for Cancer and Blood Disorders

Bethesda, Maryland, United States

Site Status

Associates in Oncology/Hematology PC

Rockville, Maryland, United States

Site Status

University of Michigan

Ann Arbor, Michigan, United States

Site Status

University of Kansas

Kansas City, Missouri, United States

Site Status

Hackensack University Medical Ctr

Hackensack, New Jersey, United States

Site Status

Clinical Research Alliance Inc.

New York, New York, United States

Site Status

Weill Cornell Medical College

New York, New York, United States

Site Status

Montefiore Medical Center

The Bronx, New York, United States

Site Status

Wake Forest University Health Sciences, Section on Hematology and Oncology

Winston-Salem, North Carolina, United States

Site Status

Gabrail Cancer Center

Canton, Ohio, United States

Site Status

The Christ Hospital

Cincinnati, Ohio, United States

Site Status

Western Pennsylvania Hospital

Pittsburgh, Pennsylvania, United States

Site Status

Hematology/Oncology Associates of SC

Greenville, South Carolina, United States

Site Status

Vanderbilt Ingram Cancer Center

Nashville, Tennessee, United States

Site Status

MD Anderson

Houston, Texas, United States

Site Status

The Methodist Cancer Center

Houston, Texas, United States

Site Status

Scott & White Memorial Hospital

Temple, Texas, United States

Site Status

University of Utah School of Medicine

Salt Lake City, Utah, United States

Site Status

Royal Prince Alfred Hospital

Camperdown, New South Wales, Australia

Site Status

St. Vincent's Public Hospital Sydney

Darlinghurst, New South Wales, Australia

Site Status

Saint George Hospital

Kogarah, New South Wales, Australia

Site Status

Liverpool Hospital

Liverpool, New South Wales, Australia

Site Status

Royal North Shore Hospital

Saint Leonards, New South Wales, Australia

Site Status

Calvary Mater Newcastle

Waratah, New South Wales, Australia

Site Status

Westmead Hospital

Westmead, New South Wales, Australia

Site Status

Royal Brisbane and Women's Hospital

Herston, Queensland, Australia

Site Status

Haematology & Oncology Clinics of Australia

South Brisbane, Queensland, Australia

Site Status

Haematology and Oncology Clinics of Australia at Chermside

South Brisbane, Queensland, Australia

Site Status

Haematology and Oncology Clinics of Australia at Wesley

South Brisbane, Queensland, Australia

Site Status

Royal Adelaide Hospital

Adelaide, South Australia, Australia

Site Status

The Queen Elizabeth Hospital

Woodville, South Australia, Australia

Site Status

Box Hill Hospital

Box Hill, Victoria, Australia

Site Status

Monash Medical Centre

Clayton, Victoria, Australia

Site Status

Saint Vincent's Hospital

East Melbourne, Victoria, Australia

Site Status

Western Hospital

Footscray, Victoria, Australia

Site Status

The Alfred Hospital

Melbourne, Victoria, Australia

Site Status

Sunshine Hospital

St Albans, Victoria, Australia

Site Status

Fremantle Hospital

Fremantle, Western Australia, Australia

Site Status

Royal Perth Hospital

Perth, Western Australia, Australia

Site Status

Medizinische Universität Innsbruck

Innsbruck, Tyrol, Austria

Site Status

Krankenhaus der Elisabethinen Linz, I Interne Abteilung

Linz, Upper Austria, Austria

Site Status

Wilhelminenspital der Stadt Wien

Vienna, Vienna, Austria

Site Status

Universitair Ziekenhuis Leuven

Leuven, Flemish Brabant, Belgium

Site Status

Cliniques Universitaires UCL de Mont-Godinne

Yvoir, Namur, Belgium

Site Status

Universitair Ziekenhuis Gent

Ghent, Oost-vlaanderen, Belgium

Site Status

Ziekenhuis Netwerk Antwerpen

Antwerp, , Belgium

Site Status

Cliniques Universitaires Saint Luc

Brussels, , Belgium

Site Status

Universitair Ziekenhuis Brussel

Brussels, , Belgium

Site Status

Liga Norte Riograndense Contra o Câncer

Natal, Rio Grande do Norte, Brazil

Site Status

Clínica de Oncologia de Porto Alegre

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Hospital de Clínicas de Porto Alegre

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Hospital São Lucas da PUCRS

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Hemocentro Campinas-Unicamp

Campinas, São Paulo, Brazil

Site Status

Hospital Universitário Clementino Fraga Filho da Universidade Federal do Rio de Janeiro

Rio de Janeiro, , Brazil

Site Status

Instituto Centros Oncológicos Integrados de Educação e Pesquisa

Rio de Janeiro, , Brazil

Site Status

Instituto Nacional do Câncer-INCA

Rio de Janeiro, , Brazil

Site Status

Irmandade da Santa Casa de Misericórdia de São Paulo

São Paulo, , Brazil

Site Status

Military Medical Academy Hospital for Active Treatment

Sofia, Sofia, Bulgaria

Site Status

Shato, Ead

Sofia, Sofia, Bulgaria

Site Status

University Multiprofile Hospital for Active Treatment "Sveti Georgi" EAD

Plovdiv, , Bulgaria

Site Status

Multiprofile Hospital for Active Treatment, "Sveta Marina''

Varna, , Bulgaria

Site Status

University of Alberta Hospital

Edmonton, Alberta, Canada

Site Status

British Columbia Cancer Agency

Kelowna, British Columbia, Canada

Site Status

Saint John Regional Hospital

Saint John, New Brunswick, Canada

Site Status

Queen Elizabeth II Health Science Centre

Halifax, Nova Scotia, Canada

Site Status

London Health Sciences Centre

London, Ontario, Canada

Site Status

The Ottawa Hospital Regional Cancer Centre

Ottawa, Ontario, Canada

Site Status

Windsor Regional Hospital

Windsor, Ontario, Canada

Site Status

Hopital Maisonneuve-Rosemont

Montreal, Quebec, Canada

Site Status

Fakultní nemocnice Královské Vinohrady

Prague, Prague, Czechia

Site Status

Fakultní nemocnice Olomouc

Olomouc, Severomoravsky KRAJ, Czechia

Site Status

FN Ostrava

Ostrava, Severomoravsky KRAJ, Czechia

Site Status

Fakultní nemocnice Hradec Králové

Hradec Kralové, Vychodocesky KRAJ, Czechia

Site Status

Fakultní nemocnice Brno

Brno, , Czechia

Site Status

Všeobecná fakultní nemocnice v Praze

Prague, , Czechia

Site Status

Centre Hospitalier de la Cote Basque

Bayonne, Aquitaine, France

Site Status

Centre Hospitalier Lyon Sud

Pierre-Bénite, Auvergne-Rhône-Alpes, France

Site Status

Centre Hospitalier Universitaire Brest

Brest, Brittany Region, France

Site Status

Centre Hospitalier Universitaire de Rennes, Hôpital Pontchaillou

Rennes, Brittany Region, France

Site Status

Hopital Hotel-Dieu - Service d'Hematologie

Nantes, Cedex 1, France

Site Status

Centre Henri-Becquerel

Rouen, Haute-normandie, France

Site Status

Hôpital Claude Huriez

Lille, Hauts-de-France, France

Site Status

Hôpital Hôtel-Dieu

Nantes, Pays de la Loire Region, France

Site Status

Institut Paoli Calmettes

Marseille, Provence-Alpes-Côte d'Azur Region, France

Site Status

Centre Hospitalier de Versailles

Le Chesnay, Île-de-France Region, France

Site Status

Hôpital Saint Louis

Paris, Île-de-France Region, France

Site Status

Hôpital Saint-Antoine

Paris, Île-de-France Region, France

Site Status

Universitätsklinik Heidelberg

Heidelberg, Baden-Wurttemberg, Germany

Site Status

Universitätsklinikum Tübingen

Tübingen, Baden-Wurttemberg, Germany

Site Status

Universitätsklinikum Ulm

Ulm, Baden-Wurttemberg, Germany

Site Status

Medizinische Klinik der Universität Würzburg

Würzburg, Bavaria, Germany

Site Status

Medizinische Hochschule Hannover

Hanover, Lower Saxony, Germany

Site Status

Universitätsklinikum Aachen

Aachen, North Rhine-Westphalia, Germany

Site Status

Universitätsklinikum Münster

Münster, North Rhine-Westphalia, Germany

Site Status

Universitätsmedizin der Johannes Gutenberg Universität

Mainz, Rhineland-Palatinate, Germany

Site Status

Universitätsklinikum des Saarlandes

Homburg / Saar, Saarland, Germany

Site Status

Klinikum Chemnitz gGmbH

Chemnitz, Saxony, Germany

Site Status

Universitätsklinikum Carl Gustav Carus, Med. Klinik und Poliklinik I

Dresden, Saxony, Germany

Site Status

Universitätsklinikum Leipzig

Leipzig, Saxony, Germany

Site Status

Universitätsklinikum Jena

Jena, Thuringia, Germany

Site Status

Universitatsklinikum Freiburg

Freiburg im Breisgau, , Germany

Site Status

Universitätsklinikum Hamburg Eppendorf

Hamburg, , Germany

Site Status

Alexandra General Hospital

Athens, Attica, Greece

Site Status

Pécsi Tudományegyetem

Pécs, Baranya, Hungary

Site Status

Bács-Kiskun Megyei Kórház Szegedi Tudományegyetem Általános Orvostudományi Kar Oktató Kórháza

Kecskemét, Bács-Kiskun county, Hungary

Site Status

Szegedi Tudományegyetem

Szeged, Csongrád megye, Hungary

Site Status

Debreceni Egyetem Klinikai Központ

Debrecen, Hajdú-Bihar, Hungary

Site Status

Egyesített Szent István és Szent László Kórház-Rendelointézet

Budapest, , Hungary

Site Status

Somogy Megyei Kaposi Mac okato Korhoz

Kaposvár, , Hungary

Site Status

Somogy Megyei Kaposi Mór Oktató Kórház

Kaposvár, , Hungary

Site Status

Rambam Health Corp.

Haifa, , Israel

Site Status

Hadassah Medical Center

Jerusalem, , Israel

Site Status

Meir Medical Center

Kfar Saba, , Israel

Site Status

Tel Aviv Sourasky Medical Center

Tel Aviv, , Israel

Site Status

The Chaim Sheba Medical Center at Tel Hashomer

Tel Litwinsky, , Israel

Site Status

IRCCS Centro di Riferimento Oncologico di Basilicata di Rionero in Vulture

Rionero in Vulture, Potenza, Italy

Site Status

Azienda Ospedaliero-Univesitaria San Luigi Gonzaga

Orbassano, Torino, Italy

Site Status

Azienda Ospedaliero Universitaria Ospedali Riuniti di Ancona

Ancona, , Italy

Site Status

Azienda Ospedaliero-Universitaria di Bologna - Policlinico S.Orsola-Malpighi

Bologna, , Italy

Site Status

Azienda Ospedaliera Spedali Civili di Brescia

Brescia, , Italy

Site Status

IRCCS Azienda Ospedaliera Universitaria San Martino

Genova, , Italy

Site Status

Azienda Ospedaliera Universitaria Maggiore della Carità

Novara, , Italy

Site Status

Azienda Unità Sanitaria Locale di Piacenza-Ospedale Guglielmo da Saliceto

Piacenza, , Italy

Site Status

Azienda Ospedaliera Pisana Ospedale Santa Chiara

Pisa, , Italy

Site Status

Aienda Policknico Umberto I di Roma

Roma, , Italy

Site Status

Azienda Policknico Umberto l di Roma

Roma, , Italy

Site Status

Università Tor Vergata Ospedale Sant Eugenio

Roma, , Italy

Site Status

Azienda Ospedaliera Universitaria Senese - Policlinico S. Maria alle Scotte

Siena, , Italy

Site Status

Azienda Ospedaliera Città della Salute e della Scienza di Torino

Torino, , Italy

Site Status

Nagoya City University Hospital

Nagoya, Aichi-ken, Japan

Site Status

Toyohashi Municipal Hospital

Toyohashi, Aichi-ken, Japan

Site Status

National Hospital Organization Kyushu Cancer Center

Fukuoka, Fukuoka, Japan

Site Status

Ogaki Municipal Hospital

Ōgaki, Gifu, Japan

Site Status

Gunma University Hospital

Maebashi, Gunma, Japan

Site Status

National Hospital Organization Nishigunma National Hospital

Shibukawa, Gunma, Japan

Site Status

Sapporo Medical University Hospital

Sapporo, Hokkaido, Japan

Site Status

Kobe City Medical Center General Hospital

Kobe, Hyōgo, Japan

Site Status

Tokai University Hospital

Isehara, Kanagawa, Japan

Site Status

Niigata Cancer Center Hospital

Niigata, Niigata, Japan

Site Status

Osaka University Hospital

Suita, Osaka, Japan

Site Status

Saitama Medical Center

Kawagoe, Saitama, Japan

Site Status

Tochigi Cancer Center

Utsunomiya, Tochigi, Japan

Site Status

National Cancer Center Hospital

Chuo-ku, Tokyo, Japan

Site Status

The Cancer Institute Hospital Of Japanese Foundation For Cancer Research

Koto-ku, Tokyo, Japan

Site Status

Toranornon Hospital

Shinagawa, Tokyo, Japan

Site Status

Tokyo Medical University Hospital

Shinjuku, Tokyo, Japan

Site Status

National Hospital Organization Disaster Medical Center

Tachikawa, Tokyo, Japan

Site Status

Kyushu University Hospital

Fukuoka, , Japan

Site Status

Social Insurance Kyoto Hospital of All Japan Federation of Social Insurance Associations

Kyoto, , Japan

Site Status

University Hospital, Kyoto Prefectural University of Medicine

Kyoto, , Japan

Site Status

National Hospital Organization Okayama Medical Center

Okayama, , Japan

Site Status

Tokushima Prefectural Central Hospital

Tokushima, , Japan

Site Status

Japanese Red Cross Medical Center

Tokyo, , Japan

Site Status

North Shore Hospital

North Shore, Auckland, New Zealand

Site Status

Middlemore Hospital

Otahuhu, Auckland, New Zealand

Site Status

Auckland City Hospital

Grafton, Aukland, New Zealand

Site Status

Christchurch Hospital

Christchurch, , New Zealand

Site Status

Dunedin Hospital

Dunedin, , New Zealand

Site Status

Szpital Kliniczny Przemienienia Panskiego Uniwersytetu Medycznego im K. Marcinkowskiego w Poznaniu

Poznan, Greater Poland Voivodeship, Poland

Site Status

Specjalistyczny Szpital Miejski im. Mikolaja Kopernika

Torun, Kuyavian-Pomeranian Voivodeship, Poland

Site Status

Szpital Uniwersytecki w Krakowie

Krakow, Lesser Poland Voivodeship, Poland

Site Status

Zamojski Szpital Niepubliczny Sp. z o.o.

Zamość, Lublin Voivodeship, Poland

Site Status

Instytut Hematologii i Transfuzjologii

Warsaw, Masovian Voivodeship, Poland

Site Status

Uniwersyteckie Centrum Kliniczne

Gdansk, Pomeranian Voivodeship, Poland

Site Status

Samodzielny Publiczny Zaklad Opieki Zdrowotnej Zespól Szpitali Miejskich

Chorzów, Silesian Voivodeship, Poland

Site Status

Spitalul Universitar de Urgenta Bucuresti

Bucharest, București, Romania

Site Status

Policlinica de Diagnostic Rapid SA, Compartiment Medical Oncologie-Hematologie

Brasov, , Romania

Site Status

Spitalul Clinic Judetean de Urgenta Brasov (Bumbea, Horia)

Brasov, , Romania

Site Status

Institutul Clinic Fundeni

Bucharest, , Romania

Site Status

Institutul Regional de Oncologie Iasi

Iași, , Romania

Site Status

Republican Clinical Hospital #1

Izhevsk, , Russia

Site Status

City Clinical Hospital n.a. S. P. Botkin

Moscow, , Russia

Site Status

Non-state Healthcare Institution "N.A. Semashko Central Clinical Hospital #2 of JSC "Russian Railway

Moscow, , Russia

Site Status

Ryazan Regional Clinical Hospital

Ryazan, , Russia

Site Status

Clinical Hospital Number 31

Saint Petersburg, , Russia

Site Status

Federal Almazov Medical Research Centre

Saint Petersburg, , Russia

Site Status

FGU Russian Scientific Research Institute of Hematology and Transfusiology

Saint Petersburg, , Russia

Site Status

First Saint Petersburg I.P. Pavlov State Medical University

Saint Petersburg, , Russia

Site Status

GUZ Samara Regional Clinical Hospital n.a. M.I. Kalinin

Samara, , Russia

Site Status

National University Cancer Institute

Singapore, , Singapore

Site Status

Singapore General Hospital

Singapore, , Singapore

Site Status

Singapore Oncology Consultants

Singapore, , Singapore

Site Status

Univerzitná nemocnica Bratislava

Bratislava, , Slovakia

Site Status

Gachon University Gil Medical Center

Incheon, Gyeonggi-do, South Korea

Site Status

Seoul National University Bundang Hospital

Seongnam-si, Gyeonggi-do, South Korea

Site Status

Pusan National University Hospital

Pusan, Gyeongsangnam-do, South Korea

Site Status

Kyungpook National University Hospital

Daegu, , South Korea

Site Status

Asan Medical Center

Seoul, , South Korea

Site Status

Samsung Medical Center

Seoul, , South Korea

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Seoul Saint Mary's Hospital

Seoul, , South Korea

Site Status

Severance Hospital, Yonsei University Health System

Seoul, , South Korea

Site Status

Hospital Son Llàtzer

Palma de Mallorca, Balearic Islands, Spain

Site Status

Hospital Universitari Germans Trias i Pujol

Badalona, Barcelona, Spain

Site Status

Hospital Clinic I Provincial de Barcelona

Barcelona, , Spain

Site Status

Institut Universitari Dexeus

Barcelona, , Spain

Site Status

Centro Integral Oncológico Clara Campal, Hospital de Madrid Norte-San Chinarro

Madrid, , Spain

Site Status

Hospital Universitario 12 de Octubre

Madrid, , Spain

Site Status

Hospital Universitario La Princesa

Madrid, , Spain

Site Status

Hospital Clínico Universitario de Salamanca

Salamanca, , Spain

Site Status

Hospital Universitario Virgen del Rocio

Seville, , Spain

Site Status

Hospital Universitari i Politecnic La Fé de Valencia

Valencia, , Spain

Site Status

Chang Gung Memorial Hospital

Kaohsiung City, , Taiwan

Site Status

China Medical University Hospital

Taichung, , Taiwan

Site Status

National Cheng-Kung University Hospital

Tainan City, , Taiwan

Site Status

National Taiwan University Hospital

Taipei, , Taiwan

Site Status

Taipei Veterans General Hospital

Taipei, , Taiwan

Site Status

Chang Gung Medical Foundation-LinKou Branch

Taoyuan District, , Taiwan

Site Status

King Chulalongkorn Memorial Hospital

Bangkok, Bangkok Metropolis, Thailand

Site Status

Ramathibodi Hospital

Bangkok, Bangkok Metropolis, Thailand

Site Status

Srinagarind Hospital

Khon Kaen, , Thailand

Site Status

City Hematology Center

Dnipro, Dnipropretrovsk, Ukraine

Site Status

Municipal Institution of Health Protection "Clinical Hospital #8"

Kharkiv, Kharkivs’ka Oblast’, Ukraine

Site Status

Cherkassy Regional Oncology Center

Cherkassy, , Ukraine

Site Status

MI "Dnipropetrovsk City Multifield Clinical Hospital #4" of Dnipropetrovsk Regional Council", City Hematology Center

Dnipropetrovsk, , Ukraine

Site Status

Institute of Urgent and Reparative Surgury of Ukraine Academy of Medical Sciences

Donetsk, , Ukraine

Site Status

Khmelnytsky Regional Clinical Hospital

Khmelnytsky, , Ukraine

Site Status

Khmelnytsky Regional Hospital, Department of Hematology

Khmelnytsky, , Ukraine

Site Status

National Institute of Cancer, Oncohematology Department

Kiev, , Ukraine

Site Status

Kyiv Bone Marrow Transplantation Center

Kyiv, , Ukraine

Site Status

Lviv Regional Oncology Dispensary

Lviv, , Ukraine

Site Status

Lviv State Oncology Regional Treatment-Prophylactic Center, Department of Chemotherapy

Lviv, , Ukraine

Site Status

Regional Clinical Hospital

Mykolayiv, , Ukraine

Site Status

Royal Free Hospital

London, England, United Kingdom

Site Status

University College Hospital

London, England, United Kingdom

Site Status

Manchester Royal Infirmary

Manchester, England, United Kingdom

Site Status

Nottingham University Hospitals NHS Trust

Nottingham, England, United Kingdom

Site Status

Churchill Hospital

Oxford, England, United Kingdom

Site Status

Derriford Hospital

Plymouth, England, United Kingdom

Site Status

Royal Hallamshire Hospital

Sheffield, England, United Kingdom

Site Status

Royal Marsden Hospital

Surrey, England, United Kingdom

Site Status

Royal Wolverhampton Hospitals Trust

Wolverhampton, England, United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Australia Austria Belgium Brazil Bulgaria Canada Czechia France Germany Greece Hungary Israel Italy Japan New Zealand Poland Romania Russia Singapore Slovakia South Korea Spain Taiwan Thailand Ukraine United Kingdom

References

Explore related publications, articles, or registry entries linked to this study.

Moreau P, Joshua D, Chng WJ, Palumbo A, Goldschmidt H, Hajek R, Facon T, Ludwig H, Pour L, Niesvizky R, Oriol A, Rosinol L, Suvorov A, Gaidano G, Pika T, Weisel K, Goranova-Marinova V, Gillenwater HH, Mohamed N, Aggarwal S, Feng S, Dimopoulos MA. Impact of prior treatment on patients with relapsed multiple myeloma treated with carfilzomib and dexamethasone vs bortezomib and dexamethasone in the phase 3 ENDEAVOR study. Leukemia. 2017 Jan;31(1):115-122. doi: 10.1038/leu.2016.186. Epub 2016 Jul 4.

Reference Type BACKGROUND
PMID: 27491641 (View on PubMed)

Chng WJ, Goldschmidt H, Dimopoulos MA, Moreau P, Joshua D, Palumbo A, Facon T, Ludwig H, Pour L, Niesvizky R, Oriol A, Rosinol L, Suvorov A, Gaidano G, Pika T, Weisel K, Goranova-Marinova V, Gillenwater HH, Mohamed N, Feng S, Aggarwal S, Hajek R. Carfilzomib-dexamethasone vs bortezomib-dexamethasone in relapsed or refractory multiple myeloma by cytogenetic risk in the phase 3 study ENDEAVOR. Leukemia. 2017 Jun;31(6):1368-1374. doi: 10.1038/leu.2016.390. Epub 2016 Dec 27.

Reference Type BACKGROUND
PMID: 28025582 (View on PubMed)

Dimopoulos MA, Goldschmidt H, Niesvizky R, Joshua D, Chng WJ, Oriol A, Orlowski RZ, Ludwig H, Facon T, Hajek R, Weisel K, Hungria V, Minuk L, Feng S, Zahlten-Kumeli A, Kimball AS, Moreau P. Carfilzomib or bortezomib in relapsed or refractory multiple myeloma (ENDEAVOR): an interim overall survival analysis of an open-label, randomised, phase 3 trial. Lancet Oncol. 2017 Oct;18(10):1327-1337. doi: 10.1016/S1470-2045(17)30578-8. Epub 2017 Aug 23.

Reference Type BACKGROUND
PMID: 28843768 (View on PubMed)

Ludwig H, Dimopoulos MA, Moreau P, Chng WJ, Goldschmidt H, Hajek R, Facon T, Pour L, Niesvizky R, Oriol A, Rosinol L, Suvorov A, Gaidano G, Pika T, Weisel K, Goranova-Marinova V, Palumbo A, Gillenwater HH, Mohamed N, Aggarwal S, Feng S, Joshua D. Carfilzomib and dexamethasone vs bortezomib and dexamethasone in patients with relapsed multiple myeloma: results of the phase 3 study ENDEAVOR (NCT01568866) according to age subgroup. Leuk Lymphoma. 2017 Oct;58(10):2501-2504. doi: 10.1080/10428194.2017.1298755. Epub 2017 Mar 17. No abstract available.

Reference Type BACKGROUND
PMID: 28306371 (View on PubMed)

Chari A, Stewart AK, Russell SD, Moreau P, Herrmann J, Banchs J, Hajek R, Groarke J, Lyon AR, Batty GN, Ro S, Huang M, Iskander KS, Lenihan D. Analysis of carfilzomib cardiovascular safety profile across relapsed and/or refractory multiple myeloma clinical trials. Blood Adv. 2018 Jul 10;2(13):1633-1644. doi: 10.1182/bloodadvances.2017015545.

Reference Type BACKGROUND
PMID: 29991494 (View on PubMed)

Dimopoulos M, Siegel D, White DJ, Boccia R, Iskander KS, Yang Z, Kimball AS, Mezzi K, Ludwig H, Niesvizky R. Carfilzomib vs bortezomib in patients with multiple myeloma and renal failure: a subgroup analysis of ENDEAVOR. Blood. 2019 Jan 10;133(2):147-155. doi: 10.1182/blood-2018-06-860015. Epub 2018 Nov 26.

Reference Type BACKGROUND
PMID: 30478094 (View on PubMed)

Facon T, Niesvizky R, Mateos MV, Siegel D, Rosenbaum C, Bringhen S, Weisel K, Ho PJ, Ludwig H, Kumar S, Wang K, Obreja M, Yang Z, Klippel Z, Mezzi K, Goldrick A, Tekle C, Dimopoulos MA. Efficacy and safety of carfilzomib-based regimens in frail patients with relapsed and/or refractory multiple myeloma. Blood Adv. 2020 Nov 10;4(21):5449-5459. doi: 10.1182/bloodadvances.2020001965.

Reference Type BACKGROUND
PMID: 33166401 (View on PubMed)

Hari P, Mateos MV, Abonour R, Knop S, Bensinger W, Ludwig H, Song K, Hajek R, Moreau P, Siegel DS, Feng S, Obreja M, Aggarwal SK, Iskander K, Goldschmidt H. Efficacy and safety of carfilzomib regimens in multiple myeloma patients relapsing after autologous stem cell transplant: ASPIRE and ENDEAVOR outcomes. Leukemia. 2017 Dec;31(12):2630-2641. doi: 10.1038/leu.2017.122. Epub 2017 Apr 25.

Reference Type BACKGROUND
PMID: 28439109 (View on PubMed)

Leleu X, Martin TG, Einsele H, Lyons RM, Durie BGM, Iskander KS, Ailawadhi S. Role of Proteasome Inhibitors in Relapsed and/or Refractory Multiple Myeloma. Clin Lymphoma Myeloma Leuk. 2019 Jan;19(1):9-22. doi: 10.1016/j.clml.2018.08.016. Epub 2018 Sep 5.

Reference Type BACKGROUND
PMID: 30287200 (View on PubMed)

Ludwig H, Moreau P, Dimopoulos MA, Mateos MV, Kaiser M, Hajek R, Feng S, Cocks K, Buchanan J, Weisel K. Health-related quality of life in the ENDEAVOR study: carfilzomib-dexamethasone vs bortezomib-dexamethasone in relapsed/refractory multiple myeloma. Blood Cancer J. 2019 Feb 22;9(3):23. doi: 10.1038/s41408-019-0181-0.

Reference Type BACKGROUND
PMID: 30796199 (View on PubMed)

Mateos MV, Goldschmidt H, San-Miguel J, Mikhael J, DeCosta L, Zhou L, Obreja M, Blaedel J, Szabo Z, Leleu X. Carfilzomib in relapsed or refractory multiple myeloma patients with early or late relapse following prior therapy: A subgroup analysis of the randomized phase 3 ASPIRE and ENDEAVOR trials. Hematol Oncol. 2018 Apr;36(2):463-470. doi: 10.1002/hon.2499. Epub 2018 Feb 15.

Reference Type BACKGROUND
PMID: 29446103 (View on PubMed)

Moreau P, Stewart KA, Dimopoulos M, Siegel D, Facon T, Berenson J, Raje N, Berdeja JG, Orlowski RZ, Yang H, Ma H, Klippel Z, Zahlten-Kumeli A, Mezzi K, Iskander K, Mateos MV. Once-weekly (70 mg/m2 ) vs twice-weekly (56 mg/m2 ) dosing of carfilzomib in patients with relapsed or refractory multiple myeloma: A post hoc analysis of the ENDEAVOR, A.R.R.O.W., and CHAMPION-1 trials. Cancer Med. 2020 May;9(9):2989-2996. doi: 10.1002/cam4.2945. Epub 2020 Feb 28.

Reference Type BACKGROUND
PMID: 32108443 (View on PubMed)

Dimopoulos MA, Moreau P, Iida S, Huang SY, Takezako N, Chng WJ, Zahlten-Kumeli A, Sersch MA, Li J, Huang M, Lee JH. Outcomes for Asian patients with multiple myeloma receiving once- or twice-weekly carfilzomib-based therapy: a subgroup analysis of the randomized phase 3 ENDEAVOR and A.R.R.O.W. Trials. Int J Hematol. 2019 Oct;110(4):466-473. doi: 10.1007/s12185-019-02704-z. Epub 2019 Aug 6.

Reference Type BACKGROUND
PMID: 31388932 (View on PubMed)

Goldschmidt H, Moreau P, Ludwig H, Niesvizky R, Chng WJ, Joshua D, Weisel K, Spencer A, Orlowski RZ, Feng S, Iskander KS, Dimopoulos MA. Carfilzomib-dexamethasone versus subcutaneous or intravenous bortezomib in relapsed or refractory multiple myeloma: secondary analysis of the phase 3 ENDEAVOR study. Leuk Lymphoma. 2018 Jun;59(6):1364-1374. doi: 10.1080/10428194.2017.1376743. Epub 2017 Sep 22.

Reference Type BACKGROUND
PMID: 28937327 (View on PubMed)

Jakubowiak AJ, Houisse I, Majer I, Benedict A, Campioni M, Panjabi S, Ailawadhi S. Cost-effectiveness of carfilzomib plus dexamethasone compared with bortezomib plus dexamethasone for patients with relapsed or refractory multiple myeloma in the United States. Expert Rev Hematol. 2017 Dec;10(12):1107-1119. doi: 10.1080/17474086.2017.1391088.

Reference Type BACKGROUND
PMID: 29027825 (View on PubMed)

Weisel K, Mateos MV, Gay F, Delforge M, Cook G, Szabo Z, Desgraz R, DeCosta L, Moreau P. Efficacy and safety profile of deep responders to carfilzomib-based therapy: a subgroup analysis from ASPIRE and ENDEAVOR. Leukemia. 2021 Jun;35(6):1732-1744. doi: 10.1038/s41375-020-01049-5. Epub 2020 Oct 16.

Reference Type BACKGROUND
PMID: 33067574 (View on PubMed)

Weisel K, Majer I, DeCosta L, Oriol A, Goldschmidt H, Ludwig H, Campioni M, Szabo Z, Dimopoulos M. Carfilzomib and dexamethasone versus eight cycles of bortezomib and dexamethasone in patients with relapsed or refractory multiple myeloma: an indirect comparison using data from the phase 3 ENDEAVOR and CASTOR trials. Leuk Lymphoma. 2020 Jan;61(1):37-46. doi: 10.1080/10428194.2019.1648806. Epub 2019 Oct 22.

Reference Type BACKGROUND
PMID: 31640435 (View on PubMed)

Orlowski RZ, Moreau P, Niesvizky R, Ludwig H, Oriol A, Chng WJ, Goldschmidt H, Yang Z, Kimball AS, Dimopoulos M. Carfilzomib-Dexamethasone Versus Bortezomib-Dexamethasone in Relapsed or Refractory Multiple Myeloma: Updated Overall Survival, Safety, and Subgroups. Clin Lymphoma Myeloma Leuk. 2019 Aug;19(8):522-530.e1. doi: 10.1016/j.clml.2019.04.018. Epub 2019 May 2.

Reference Type BACKGROUND
PMID: 31160237 (View on PubMed)

Majer IM, Castaigne JG, Palmer S, DeCosta L, Campioni M. Modeling Covariate-Adjusted Survival for Economic Evaluations in Oncology. Pharmacoeconomics. 2019 May;37(5):727-737. doi: 10.1007/s40273-018-0759-6.

Reference Type DERIVED
PMID: 30610657 (View on PubMed)

Rosenthal A, Luthi J, Belohlavek M, Kortum KM, Mookadam F, Mayo A, Fonseca R, Bergsagel PL, Reeder CB, Mikhael JR, Stewart AK. Carfilzomib and the cardiorenal system in myeloma: an endothelial effect? Blood Cancer J. 2016 Jan 15;6(1):e384. doi: 10.1038/bcj.2015.112.

Reference Type DERIVED
PMID: 26771810 (View on PubMed)

Dimopoulos MA, Moreau P, Palumbo A, Joshua D, Pour L, Hajek R, Facon T, Ludwig H, Oriol A, Goldschmidt H, Rosinol L, Straub J, Suvorov A, Araujo C, Rimashevskaya E, Pika T, Gaidano G, Weisel K, Goranova-Marinova V, Schwarer A, Minuk L, Masszi T, Karamanesht I, Offidani M, Hungria V, Spencer A, Orlowski RZ, Gillenwater HH, Mohamed N, Feng S, Chng WJ; ENDEAVOR Investigators. Carfilzomib and dexamethasone versus bortezomib and dexamethasone for patients with relapsed or refractory multiple myeloma (ENDEAVOR): a randomised, phase 3, open-label, multicentre study. Lancet Oncol. 2016 Jan;17(1):27-38. doi: 10.1016/S1470-2045(15)00464-7. Epub 2015 Dec 5.

Reference Type DERIVED
PMID: 26671818 (View on PubMed)

Related Links

Access external resources that provide additional context or updates about the study.

http://www.amgentrials.com

AmgenTrials clinical trials website

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2012-000128-16

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

2011-003

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.