A Study to Investigate the Long-Term Safety of ZX008 (Fenfluramine Hydrochloride) Oral Solution in Children and Adults With Epileptic Encephalopathy Including Dravet Syndrome and Lennox-Gastaut Syndrome

NCT ID: NCT03936777

Last Updated: 2025-11-17

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

412 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-04-22

Study Completion Date

2025-05-08

Brief Summary

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This is an international, multicenter, open-label, long-term safety study of ZX008 in subjects with Dravet syndrome, Lennox-Gastaut syndrome or epileptic encephalopathy

Detailed Description

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This is an international, multicenter, open-label, long-term safety study of ZX008 in patients with epileptic encephalopathy, including Dravet syndrome or Lennox-Gastaut syndrome. Subjects eligible for participation are those with Dravet syndrome who are currently enrolled in Study ZX008-1503, or those with Lennox-Gastaut syndrome who have successfully completed Study ZX008-1601-Part 2, and are candidates for continued treatment with ZX008 for an extended period of time, or those with Dravet syndrome, Lennox-Gastaut syndrome, or another epileptic encephalopathy who have completed participation in another Zogenix-sponsored study and have been invited to participate in this study.

Conditions

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Dravet Syndrome Lennox Gastaut Syndrome Epileptic Encephalopathy

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Single Group Assisgnment
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

None (open label)

Study Groups

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ZX008 (Fenfluramine Hydrochloride)

ZX008 is supplied as an open-label oral solution.Doses will include up to 0.8 mg/kg/day divided into 2 daily doses, up to a maximum of 30 mg/day (subjects taking concomitant STP will receive up to 0.5 mg/kg/day, up to a maximum of 20 mg/day) in a concentration of 2.5 mg/mL.

Group Type EXPERIMENTAL

ZX008 (Fenfluramine Hydrochloride)

Intervention Type DRUG

Fenfluramine hydrochloride provided in a concentration of 2.5 mg/mL.

Interventions

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ZX008 (Fenfluramine Hydrochloride)

Fenfluramine hydrochloride provided in a concentration of 2.5 mg/mL.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Male or nonpregnant, nonlactating female
* Satisfactory completion of a core study
* Has a rare seizure disorder, such as epileptic encephalopathy and has successfully completed another Zogenix-sponsored clinical trials with ZX008
* Subject's caregiver is willing and able to be compliant with study procedures, visit schedule and study drug accountability

Exclusion Criteria

* Current cardiac valvulopathy or pulmonary hypertension that is clinically significant
* Moderate or severe hepatic impairment
* Receiving monoamine oxidase inhibitors, serotonin agonists, serotonin antagonists, and serotonin reuptake inhibitors within 14 days of receiving ZX008
Minimum Eligible Age

2 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Zogenix International Limited, Inc., a subsidiary of Zogenix, Inc.

INDUSTRY

Sponsor Role collaborator

Zogenix, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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UCB Cares

Role: STUDY_DIRECTOR

001 844 599 2273

Locations

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Tucson, Arizona, United States

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Los Angeles, California, United States

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San Diego, California, United States

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San Francisco, California, United States

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Aurora, Colorado, United States

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Gulf Breeze, Florida, United States

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Miami, Florida, United States

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Orlando, Florida, United States

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Winter Park, Florida, United States

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Atlanta, Georgia, United States

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Chicago, Illinois, United States

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Bethesda, Maryland, United States

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Boston, Massachusetts, United States

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Rochester, Minnesota, United States

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Roseville, Minnesota, United States

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Hackensack, New Jersey, United States

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Livingston, New Jersey, United States

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Hawthorne, New York, United States

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New York, New York, United States

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Cleveland, Ohio, United States

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Memphis, Tennessee, United States

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Dallas, Texas, United States

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Fort Worth, Texas, United States

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Salt Lake City, Utah, United States

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Seattle, Washington, United States

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Tacoma, Washington, United States

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Heidelberg, , Australia

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South Brisbane, , Australia

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Westmead, , Australia

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Brussels, , Belgium

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Edegem, , Belgium

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Jette, , Belgium

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Montreal, , Canada

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Toronto, , Canada

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Vancouver, , Canada

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Dianalund, , Denmark

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Bordeaux, , France

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Lille, , France

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Marseille, , France

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Paris, , France

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Paris, , France

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Salouël, , France

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Bielefeld, , Germany

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Freiburg im Breisgau, , Germany

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Jena, , Germany

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Kiel, , Germany

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Radeberg, , Germany

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Vogtareuth, , Germany

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Florence, , Italy

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Genova, , Italy

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Mantova, , Italy

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Milan, , Italy

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Roma, , Italy

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Roma, , Italy

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Verona, , Italy

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Guadalajara, , Mexico

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Heeze, , Netherlands

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Zwolle, , Netherlands

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Bydgoszcz, , Poland

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Krakow, , Poland

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Barcelona, , Spain

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Barcelona, , Spain

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Esplugues de Llobregat, , Spain

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Madrid, , Spain

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Pamplona, , Spain

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Gothenburg, , Sweden

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Birmingham, , United Kingdom

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Glasgow, , United Kingdom

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Liverpool, , United Kingdom

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London, , United Kingdom

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London, , United Kingdom

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Countries

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United States Australia Belgium Canada Denmark France Germany Italy Mexico Netherlands Poland Spain Sweden United Kingdom

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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ZX008-1900

Identifier Type: -

Identifier Source: org_study_id

2019-001331-31

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

U1111-1309-4338

Identifier Type: OTHER

Identifier Source: secondary_id

2024-515680-61

Identifier Type: REGISTRY

Identifier Source: secondary_id

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