Pharmacokinetics and Safety Profile of Digoxin in Infants With Single Ventricle Congenital Heart Disease

NCT ID: NCT03877965

Last Updated: 2022-10-12

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Total Enrollment

50 participants

Study Classification

OBSERVATIONAL

Study Start Date

2019-08-05

Study Completion Date

2022-01-17

Brief Summary

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This is a prospective, multi-center, open-label, PK and safety profile study of enteral digoxin in children \<6 months old at time of enrollment, post-surgical or hybrid stage 1 palliation, but prior to surgical stage 2 palliation.

Detailed Description

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The Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) funded this protocol titled "Pharmacokinetics and Safety Profile of Digoxin in Infants with Single Ventricle Congenital Heart Disease", protocol number NICHD-2018-DGX01. The Investigational New Drug (IND) Sponsor and Principal Investigator for this protocol is Christopher P. Hornik, MD, MPH. The Contracting Officer's Technical Representative (COTR) to represent the Government for this task order is Perdita Taylor-Zapata. The Duke IRB number for this study is Pro00102130. This study employs a central IRB, the WIRB-Copernicus Group (WCG). The c-IRB (WCG) study number is 20190888 / NICHD-2018-DGX01.

This is a prospective, multicenter Phase 1 study with a primary objective to characterize the pharmacokinetics of enteral digoxin in infants with single ventricle congenital heart disease. The secondary objective is to determine the safety profile of enteral digoxin in infants with single ventricle congenital heart disease. Digoxin is used for the treatment of heart failure in pediatric patients and acts by controlling numerous functions of the cardiovascular system. Digoxin use in single ventricle congenital heart disease may decrease interstage mortality.

The study will be conducted in approximately 48 subjects at approximately 13 investigational centers. The proposed duration of the study is approximately 196 (±) days.

Please see the protocol and synopsis for more information.

Conditions

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Congenital Heart Disease

Study Design

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Observational Model Type

COHORT

Study Time Perspective

PROSPECTIVE

Study Groups

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Children with single ventricle congenital heart disease

Receiving digoxin per standard of care during the interstage period

Digoxin

Intervention Type DRUG

Drug administered per standard of care, with a dosing regimen within the labeled dose range of 7.5-20 mcg/kg/day divided in 2 or 3 equal doses

Interventions

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Digoxin

Drug administered per standard of care, with a dosing regimen within the labeled dose range of 7.5-20 mcg/kg/day divided in 2 or 3 equal doses

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Diagnosis of single ventricle congenital heart disease
* Status post-surgical or hybrid stage 1 palliation but prior to surgical stage 2 palliation
* Age ≤ 30 days of life at time of stage 1 palliation
* Age \< 6 months at time of enrollment
* Require treatment with enteral digoxin per their treating medical provider if their planned maintenance treatment dosing regimen is within the labeled dose range of 7.5 - 20 mcg/kg/day divided in 2 or 3 equal doses
* Informed consent from parent(s) or legal guardian(s)

Exclusion Criteria

* Serum creatinine \> 2 mg/dL at enrollment
* Diagnosis of second degree or higher atrioventricular conduction block at enrollment
* Diagnosis of clinically significant sinus bradycardia requiring intervention at enrollment
* Known hypersensitivity to digoxin or other forms of digitalis
* Extracorporeal life support (i.e., ECMO, dialysis, ventricular assist device) at enrollment
* Received digoxin prior to enrollment
* Received or anticipated to receive a loading dose of digoxin.
* Any condition that would make the participant, in the opinion of the investigator, unsuitable for the study
Maximum Eligible Age

6 Months

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)

NIH

Sponsor Role collaborator

The Emmes Company, LLC

INDUSTRY

Sponsor Role collaborator

Christoph P Hornik, MD MPH

OTHER

Sponsor Role lead

Responsible Party

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Christoph P Hornik, MD MPH

Associate Professor of Pediatrics

Responsibility Role SPONSOR_INVESTIGATOR

Principal Investigators

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Christoph Hornik, MD

Role: PRINCIPAL_INVESTIGATOR

Duke University

Locations

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Mattel Children's Hospital at UCLA

Los Angeles, California, United States

Site Status

Rady Childrens Hospital and Health Center

San Diego, California, United States

Site Status

The Children's Hospital Colorado

Aurora, Colorado, United States

Site Status

Alfred I. DuPont Hospital for Children

Wilmington, Delaware, United States

Site Status

Nicklaus Children's Hospital

Miami, Florida, United States

Site Status

St. Louis Children's Hospital

St Louis, Missouri, United States

Site Status

Morgan Stanley Children's Hospital of New York Presbyterian

New York, New York, United States

Site Status

Duke University Medical Center

Durham, North Carolina, United States

Site Status

Cincinnati Childrens Hospital Medical Center

Cincinnati, Ohio, United States

Site Status

Medical University of South Carolina

Charleston, South Carolina, United States

Site Status

Children's Memorial Hermann Hospital

Houston, Texas, United States

Site Status

Countries

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United States

Other Identifiers

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NICHD-2018-DGX01

Identifier Type: OTHER

Identifier Source: secondary_id

HHSN27500002

Identifier Type: OTHER_GRANT

Identifier Source: secondary_id

Pro00102130

Identifier Type: -

Identifier Source: org_study_id

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