Evaluation of Safety and Efficacy of Avacopan in Subjects With Moderate to Severe Hidradenitis Suppurativa (AURORA)

NCT ID: NCT03852472

Last Updated: 2025-03-17

Study Results

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

435 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-12-21

Study Completion Date

2021-03-09

Brief Summary

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Phase 2 study of Avacopan in Subjects with Moderate to Severe Hidradenitis Suppurativa

Detailed Description

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A Randomized, Double-Blind, Placebo-Controlled, Parallel Group, Phase 2 study in subjects with moderate to severe Hidradenitis Suppurativa.

The study is multicenter and will consist of three subject groups. Subjects will be randomized 1:1:1 to a treatment of 10mg avacopan twice daily, 30 mg avacopan twice daily or placebo twice daily for 12 weeks.

Following the 12 weeks double-blind treatment period, subjects on placebo will be re-randomized 1:1 to receive 10 mg or 30 mg avacopan twice daily for additional 24 weeks. Subjects treated with avacopan will continue to receive the same dose (either 10 mg or 30 mg twice daily) for additional 24 weeks.

Subjects will be on study treatment for 36 weeks and will be followed for 44 weeks for assessment of safety and efficacy.

Study acquired by Amgen and all disclosures were done by previous sponsor ChemoCentryx.

Primary efficacy analysis will be at 12 weeks.

Conditions

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Hidradenitis Suppurativa Acne Inversa

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Group A

Placebo twice daily (BID) for Period 1 of the study

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

Placebo

Group B

Avacopan 10 mg twice daily (BID) for Period 1+2 of the study

Group Type EXPERIMENTAL

Avacopan

Intervention Type DRUG

Active treatment

Group C

Avacopan 30 mg twice daily (BID) for Period 1+2 of the study

Group Type EXPERIMENTAL

Avacopan

Intervention Type DRUG

Active treatment

Placebo to Avacopan 10 mg

Treatment period 2, subjects randomized to placebo during period 1 were rerandomized 1:1 to receive 10 mg or 30 mg avacopan BID in period 2.

Group Type EXPERIMENTAL

Avacopan

Intervention Type DRUG

Active treatment

Placebo to Avacopan 30 mg

Treatment period 2, subjects randomized to placebo during period 1 were rerandomized 1:1 to receive 10 mg or 30 mg avacopan BID in period 2.

Group Type EXPERIMENTAL

Avacopan

Intervention Type DRUG

Active treatment

Interventions

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Avacopan

Active treatment

Intervention Type DRUG

Placebo

Placebo

Intervention Type OTHER

Other Intervention Names

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CCX168

Eligibility Criteria

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Inclusion Criteria

* At least 18 years of age
* Clinical diagnosis of HS (Hurley Stage II or III), confirmed by a dermatologist, for at least 6 months prior to Screening
* HS lesions are present in at least 2 distinct anatomic areas
* Inadequate or loss of response to a systemic course of antibiotics typically of at least 90 days
* Must have at least 5 inflammatory nodules or abscesses at screening
* Use adequate birth control for subject and partners of child bearing potential
* Willing and able to give written Informed Consent

Exclusion Criteria

* Pregnant or breast-feeding
* Any other skin disease that may interfere with the assessment of HS
* Rapidly progressive, expanding HS within 30 days prior to screening
* More than 20 draining fistulae at screening
* Any anti-TNF-α treatment for HS or for other conditions prior to Day 1 visit will be prohibited. Exception: Subjects who were previously treated with an anti-TNF-α drug and discontinued treatment \>12 weeks prior to Day 1 visit are allowed for enrollment
* Systemic antibiotics are generally excluded
* Topical antibiotics use within 14 days prior to Day 1 is excluded
* Have started a topical prescription medicine for HS within 14 days prior to screening
* A systemic medicine for HS, including biologics and other systemic therapies
* Have received within 14 days prior to Day 1 visit or is expected to require oral or transdermal opioid analgesics (except for tramadol) for any reason
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Amgen

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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MD

Role: STUDY_DIRECTOR

Amgen

Locations

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Clinical Site

Birmingham, Alabama, United States

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Birmingham, Alabama, United States

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Mobile, Alabama, United States

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Phoenix, Arizona, United States

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Scottsdale, Arizona, United States

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Fort Smith, Arkansas, United States

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Rogers, Arkansas, United States

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Fountain Valley, California, United States

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Fremont, California, United States

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Fullerton, California, United States

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Huntington Beach, California, United States

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Inglewood, California, United States

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Los Angeles, California, United States

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Los Angeles, California, United States

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Los Angeles, California, United States

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Manhattan Beach, California, United States

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Newport Beach, California, United States

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Northridge, California, United States

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Redwood City, California, United States

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Thousand Oaks, California, United States

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Walnut Creek, California, United States

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Boca Raton, Florida, United States

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Clearwater, Florida, United States

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Hialeah, Florida, United States

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Hollywood, Florida, United States

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Homestead, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Ocala, Florida, United States

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Orlando, Florida, United States

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Pembroke Pines, Florida, United States

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Tampa, Florida, United States

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Tampa, Florida, United States

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Tampa, Florida, United States

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Weston, Florida, United States

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Atlanta, Georgia, United States

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Marietta, Georgia, United States

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Newnan, Georgia, United States

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Sandy Springs, Georgia, United States

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Boise, Idaho, United States

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Skokie, Illinois, United States

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Skokie, Illinois, United States

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Crown Point, Indiana, United States

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Evansville, Indiana, United States

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Indianapolis, Indiana, United States

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Louisville, Kentucky, United States

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Metairie, Louisiana, United States

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New Orleans, Louisiana, United States

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Largo, Maryland, United States

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Beverly, Massachusetts, United States

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Boston, Massachusetts, United States

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Quincy, Massachusetts, United States

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Clarkston, Michigan, United States

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Fort Gratiot, Michigan, United States

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Saint Joseph, Michigan, United States

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Troy, Michigan, United States

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Minneapolis, Minnesota, United States

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St Louis, Missouri, United States

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Omaha, Nebraska, United States

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Verona, New Jersey, United States

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New York, New York, United States

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Rochester, New York, United States

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Chapel Hill, North Carolina, United States

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Charlotte, North Carolina, United States

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Charlotte, North Carolina, United States

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Charlotte, North Carolina, United States

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Wilmington, North Carolina, United States

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Athens, Ohio, United States

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Bexley, Ohio, United States

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Cleveland, Ohio, United States

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Marion, Ohio, United States

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Mason, Ohio, United States

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Norman, Oklahoma, United States

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Portland, Oregon, United States

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Drexel Hill, Pennsylvania, United States

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Hershey, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Warwick, Rhode Island, United States

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Charleston, South Carolina, United States

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Nashville, Tennessee, United States

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Austin, Texas, United States

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Austin, Texas, United States

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Dallas, Texas, United States

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Houston, Texas, United States

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Houston, Texas, United States

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Houston, Texas, United States

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San Antonio, Texas, United States

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Sugar Land, Texas, United States

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Spokane, Washington, United States

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Morgantown, West Virginia, United States

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Countries

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United States

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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CL016_168

Identifier Type: -

Identifier Source: org_study_id

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