Expanded Access to Mepsevii

NCT ID: NCT03775174

Last Updated: 2026-01-12

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

AVAILABLE

Study Classification

EXPANDED_ACCESS

Brief Summary

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Individual patient expanded access requests may be considered for patients who have no other treatment options

Detailed Description

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Expanded access may be available outside of the US in countries prior to approval by the local regulatory agencies. For full details, please visit the links provided below.

Conditions

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MPS VII Mucopolysaccharidosis VII Sly Syndrome

Interventions

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Mepsevii

Intervention Type DRUG

Other Intervention Names

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UX003 recombinant human beta-glucuronidase rhGUS vestronidase alfa

Eligibility Criteria

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Inclusion Criteria

\-

Exclusion Criteria

\-
Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Ultragenyx Pharmaceutical Inc

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Central Contacts

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Early Access

Role: CONTACT

1-415-483-8800

Related Links

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https://www.mepsevii.com/en/

Mepsevii Patient and Prescribing Information Page

Other Identifiers

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UX003-EAP

Identifier Type: -

Identifier Source: org_study_id

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