Extension Study of AGT-181-102 to Evaluate Long Term Safety and Activity of AGT-181

NCT ID: NCT02597114

Last Updated: 2018-09-25

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

3 participants

Study Classification

INTERVENTIONAL

Study Start Date

2015-11-30

Study Completion Date

2018-08-02

Brief Summary

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AGT-181 is a fusion protein containing alpha-L-Iduronidase that is intended to deliver the enzyme peripherally and to the brain, when administered intravenously. This study is an extension of a safety and dose ranging study to obtain long term safety and exposure data, as well as information on the biological activity of the investigational drug

Detailed Description

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Conditions

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Mucopolysaccharidosis I

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Open Label

Study Groups

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AGT-181

AGT-181 (fusion protein of anti-human insulin receptor monoclonal antibody and alpha-L-iduronidase) administered once weekly x 26 weeks at same dose level as subject received in core study

Group Type EXPERIMENTAL

AGT-181

Intervention Type DRUG

intravenous infusion over 3-4 hours

Interventions

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AGT-181

intravenous infusion over 3-4 hours

Intervention Type DRUG

Other Intervention Names

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HIRMAb-IDUA fusion protein of monoclonal antibody to human insulin receptor fused to alpha-L-iduronidase

Eligibility Criteria

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Inclusion Criteria

* Must have completed clinical trial AGT-181-102
* Voluntary written consent by patient or legally responsible representative
* All women of childbearing potential and sexually mature males must be advised to use a medically accepted method of contraception throughout the study.
* Negative pregnancy test (females)

Exclusion Criteria

* Refusal to complete screening evaluations.
* Any medical condition or other circumstances that may significantly interfere with study compliance
* Patient is pregnant or lactating
* Clinically significant spinal cord compression, evidence of cervical instability.
* Subject developed clinically relevant hypersensitivity to AGT-181
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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ArmaGen, Inc

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Patrice Rioux, MD PhD

Role: STUDY_DIRECTOR

ArmaGen, Inc

Other Identifiers

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AGT-181-103

Identifier Type: -

Identifier Source: org_study_id

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