A Phase 2b Study To Evaluate The Efficacy And Safety Profile Of PF-06651600 And PF-06700841 In Active Non-segmental Vitiligo Subjects

NCT ID: NCT03715829

Last Updated: 2022-03-25

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

366 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-11-26

Study Completion Date

2021-02-05

Brief Summary

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This is a Phase 2b, randomized, double blind, parallel group, multicenter study with an extension period. The study will have a maximum duration of approximately 60 weeks. This includes an up to 4 weeks Screening Period, a 24 week dose ranging period, an up to 24 week extension period and a 8 week Follow up Period.

Detailed Description

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Conditions

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Active Non-segmental Vitiligo

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Dose ranging period is a parallel design. Extension period is a sequential design.
Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors
Dose ranging period is blinded. The partially blinded extension period includes open arms and blinded arms.

Study Groups

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Cohort 1

Induction dose 1 given once a day(QD) for 4 weeks followed by maintenance dose A given QD for 20 weeks

Group Type EXPERIMENTAL

PF-06651600

Intervention Type DRUG

Induction dose 1. Oral tablet taken QD

PF-06651600

Intervention Type DRUG

Maintenance dose A. Oral tablet taken QD

Cohort 2

Induction dose 2 given QD for 4 weeks followed by maintenance dose A given QD for 20 weeks

Group Type EXPERIMENTAL

PF-06651600

Intervention Type DRUG

Induction dose 2. Oral tablet taken QD

PF-06651600

Intervention Type DRUG

Maintenance dose A. Oral tablet taken QD

Cohort 3

Maintenance dose A given QD for 24 weeks

Group Type EXPERIMENTAL

PF-06651600

Intervention Type DRUG

Maintenance dose A. Oral tablet taken QD

Cohort 4

Maintenance dose B given QD for 24 weeks

Group Type EXPERIMENTAL

PF-06651600

Intervention Type DRUG

Maintenance Dose B. Oral tablet taken QD

Cohort 5

Maintenance dose C given QD for 24 weeks

Group Type EXPERIMENTAL

PF-06651600

Intervention Type DRUG

Maintenance Dose C. Oral tablet taken QD

Cohort 6

Placebo given QD for 24 weeks

Group Type PLACEBO_COMPARATOR

placebo

Intervention Type DRUG

placebo

Extension Cohort 1

4 week drug holiday (no drug given) followed by PF-06700841 oral tablet QD for 20 weeks

Group Type EXPERIMENTAL

PF06700841

Intervention Type DRUG

Oral tablet taken QD

Extension Cohort 2

Induction dose 1 given QD for 4 weeks followed by maintenance dose A given QD for 20 weeks in conjunction with narrow band UVB phototherapy

Group Type EXPERIMENTAL

PF-06651600

Intervention Type DRUG

Induction dose 1. Oral tablet taken QD

PF-06651600

Intervention Type DRUG

Maintenance dose A. Oral tablet taken QD

narrow-band UVB phototherapy

Intervention Type DEVICE

Phototherapy will be combined with PF-06651600

Extension Cohort 3

Induction dose 1 given QD for 4 weeks followed by maintenance dose A given QD for 20 weeks

Group Type EXPERIMENTAL

PF-06651600

Intervention Type DRUG

Induction dose 1. Oral tablet taken QD

PF-06651600

Intervention Type DRUG

Maintenance dose A. Oral tablet taken QD

Extension Cohort 4

Maintenance dose A given QD for 24 weeks

Group Type EXPERIMENTAL

PF-06651600

Intervention Type DRUG

Maintenance dose A. Oral tablet taken QD

Extension Cohort 5

Maintenance dose B given QD for 24 weeks

Group Type EXPERIMENTAL

PF-06651600

Intervention Type DRUG

Maintenance Dose B. Oral tablet taken QD

Extension Cohort 6

Observation period for 24 weeks

Group Type NO_INTERVENTION

No interventions assigned to this group

Interventions

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PF-06651600

Induction dose 1. Oral tablet taken QD

Intervention Type DRUG

PF-06651600

Induction dose 2. Oral tablet taken QD

Intervention Type DRUG

PF-06651600

Maintenance dose A. Oral tablet taken QD

Intervention Type DRUG

PF-06651600

Maintenance Dose B. Oral tablet taken QD

Intervention Type DRUG

PF-06651600

Maintenance Dose C. Oral tablet taken QD

Intervention Type DRUG

placebo

placebo

Intervention Type DRUG

PF06700841

Oral tablet taken QD

Intervention Type DRUG

narrow-band UVB phototherapy

Phototherapy will be combined with PF-06651600

Intervention Type DEVICE

Eligibility Criteria

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Inclusion Criteria

* Male or female subjects between 18-65 years of age, inclusive, at time of informed consent.
* Must have moderate to severe active non-segmental vitiligo.

Exclusion Criteria

* History of human immunodeficiency virus (HIV) or positive HIV serology at screening,
* Infected with hepatitis B or hepatitis C viruses.
* Have evidence of active or latent or inadequately treated infection with Mycobacterium tuberculosis (TB)
Minimum Eligible Age

18 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Pfizer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Locations

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Marvel Research, LLC

Huntington Beach, California, United States

Site Status

University of California, Irvine, Dermatology Clinical Research Center

Irvine, California, United States

Site Status

Vitiligo and Pigmentation Institute Of Southern California

Los Angeles, California, United States

Site Status

Dermatology Specialist, Inc.

Murrieta, California, United States

Site Status

Dermatology Specialists, Inc.

Oceanside, California, United States

Site Status

UC Davis Health

Sacramento, California, United States

Site Status

Brookside Dermatology Associates

Bridgeport, Connecticut, United States

Site Status

New England Research Associates, LLC

Bridgeport, Connecticut, United States

Site Status

New Horizon Research Center

Miami, Florida, United States

Site Status

Park Avenue Dermatology

Orange Park, Florida, United States

Site Status

ForCare Clinical Research

Tampa, Florida, United States

Site Status

Advanced Skin and MOHS Surgery Center, c/o TrialSpark, Inc.

Chicago, Illinois, United States

Site Status

Chevy Chase Dermatology Center (TrialSpark, Inc.)

Chevy Chase, Maryland, United States

Site Status

TrialSpark - Samantha Toerge, MD

Chevy Chase, Maryland, United States

Site Status

TrialSpark - Ronald Shore, MD

Rockville, Maryland, United States

Site Status

Tobias & Battite, Inc.

Boston, Massachusetts, United States

Site Status

Tufts Medical Center

Boston, Massachusetts, United States

Site Status

UMass Memorial Medical Center, Hahnemann Campus

Worcester, Massachusetts, United States

Site Status

Investigational Drug Service Pharmacy

Worcester, Massachusetts, United States

Site Status

UMass Memorial Medical Center Ear Nose and Throat

Worcester, Massachusetts, United States

Site Status

University of Massachusetts Medical School

Worcester, Massachusetts, United States

Site Status

Henry Ford Hospital Department of Dermatology

Detroit, Michigan, United States

Site Status

University of Minnesota Department of Dermatology

Minneapolis, Minnesota, United States

Site Status

The Dermatology Group, P.C.

Verona, New Jersey, United States

Site Status

Icahn School of Medicine at Mount Sinai

New York, New York, United States

Site Status

Upper West Side Dermatology c/o TrialSpark, Inc

New York, New York, United States

Site Status

MDCS: Medical Dermatology & Cosmetic Surgery (TrialSpark, Inc.)

New York, New York, United States

Site Status

South Nassau Dermatology

Oceanside, New York, United States

Site Status

TrialSpark, Inc. - Russell W. Cohen, MD

Oceanside, New York, United States

Site Status

PMG Research of Wilmington, LLC

Wilmington, North Carolina, United States

Site Status

Remington-Davis, Inc. Clinical Research

Columbus, Ohio, United States

Site Status

ForeFront Dermatology

Columbus, Ohio, United States

Site Status

Vital Prospects Clinical Research Institute, PC

Tulsa, Oklahoma, United States

Site Status

University Physicians Group

Austin, Texas, United States

Site Status

University of Texas Southwestern Medical Center

Dallas, Texas, United States

Site Status

Pickens Academic Tower

Houston, Texas, United States

Site Status

The University of Texas Health Science Center at Houston

Houston, Texas, United States

Site Status

The University of Texas MD Anderson Cancer Center

Houston, Texas, United States

Site Status

Virginia Clinical Research, Inc

Norfolk, Virginia, United States

Site Status

Tamjidi Skin Institute (TrialSpark, Inc.)

Vienna, Virginia, United States

Site Status

The Skin Hospital

Darlinghurst, New South Wales, Australia

Site Status

Premier Specialists Pty Ltd

Kogarah, New South Wales, Australia

Site Status

Veracity Clinical Research Pty Ltd

Woolloongabba, Queensland, Australia

Site Status

Skin Health Institute

Carlton, Victoria, Australia

Site Status

Sinclair Dermatology

East Melbourne, Victoria, Australia

Site Status

The Royal Melbourne Hospital

Parkville, Victoria, Australia

Site Status

The Royal Melbourne Hospital

Parkville, Victoria, Australia

Site Status

Hôpital Erasme Dermatology

Brussels, , Belgium

Site Status

UZ Brussel - Dermatology

Brussels, , Belgium

Site Status

UZ Gent - Dermatology

Ghent, , Belgium

Site Status

Dr. Chih-ho Hong Medical Inc.

Surrey, British Columbia, Canada

Site Status

Enverus Medical Research

Surrey, British Columbia, Canada

Site Status

University of British Columbia

Vancouver, British Columbia, Canada

Site Status

Wiseman Dermatology Research Inc.

Winnipeg, Manitoba, Canada

Site Status

CCA Medical Research

Ajax, Ontario, Canada

Site Status

Guenther Research Inc.

London, Ontario, Canada

Site Status

Lynderm Research Inc.

Markham, Ontario, Canada

Site Status

DermEdge Research

Mississauga, Ontario, Canada

Site Status

North York Research Inc.

North York, Ontario, Canada

Site Status

The Centre for Clinical Trials

Oakville, Ontario, Canada

Site Status

The Centre for Dermatology

Richmond Hill, Ontario, Canada

Site Status

K.Papp Clinical Research

Waterloo, Ontario, Canada

Site Status

Innovaderm Research Inc.

Montreal, Quebec, Canada

Site Status

Centre de Recherche Dermatologique du Quebec metropolitain (CRDQ)

Québec, Quebec, Canada

Site Status

Centre de Recherche Saint-Louis

Québec, Quebec, Canada

Site Status

Centre de Recherche Saint-Louis

Québec, Quebec, Canada

Site Status

Diex Research Sherbrooke Inc.

Sherbrooke, Quebec, Canada

Site Status

Fachklinik Bad Bentheim, Fachbereich Dermatologie und Allergologie, Dermatologische Ambulanz

Bad Bentheim, , Germany

Site Status

Universitaetsklinikum Erlangen Hautklinik Studienambulanz

Erlangen, , Germany

Site Status

Universitätsklinikum Frankfurt, Klinik für Dermatologie, Venerologie und Allergologie

Frankfurt am Main, , Germany

Site Status

Universitaetsklinikum Schleswig-Holstein, Campus Luebeck CCIM

Lübeck, , Germany

Site Status

Universitaetsmedizin der Johannes Gutenberg-Universitaet Mainz

Mainz, , Germany

Site Status

Universitaetsklinikum Muenster

Münster, , Germany

Site Status

Istituti Fisioterapici Ospitalieri, Istituto di Ricovero e Cura a Carattere Scientifico,

Roma, RM, Italy

Site Status

Nagoya City University Hospital - Dermatology

Nagoya, Aichi-ken, Japan

Site Status

Tohoku University Hospital

Sendai, Miyagi, Japan

Site Status

Nippon Medical School Hospital

Bunkyo-ku, Tokyo, Japan

Site Status

Tokyo Medical University Hospital

Shinjuku-ku, Tokyo, Japan

Site Status

Yamanashi Prefectural Central Hospital

Kofu, Yamanashi, Japan

Site Status

Dongguk University Ilsan Hospital

Goyang-si, Gyeonggi-do, South Korea

Site Status

The Catholic University of Korea, St. Vincent's Hospital

Suwon, Gyeonggi-do, South Korea

Site Status

Ajou University Hospital

Suwon, Gyeonggi-do, South Korea

Site Status

Inha University Hospital

Incheon, , South Korea

Site Status

Severance Hospital, Yonsei University Health System

Seoul, , South Korea

Site Status

Hospital de la Santa Creu i Sant Pau

Barcelona, , Spain

Site Status

Hospital Universitario Reina Sofia

Córdoba, , Spain

Site Status

Hospital Universitario Ramón y Cajal

Madrid, , Spain

Site Status

Hospital Universitario La Paz

Madrid, , Spain

Site Status

Hospital Universitari i Politecnic La Fe

Valencia, , Spain

Site Status

Chang Gung Medical Foundation - Kaohsiung Chang Gung Memorial Hospital

Kaohsiung City, , Taiwan

Site Status

National Cheng Kung University Hospital

Tainan City, , Taiwan

Site Status

National Taiwan University Hospital

Taipei, , Taiwan

Site Status

Countries

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United States Australia Belgium Canada Germany Italy Japan South Korea Spain Taiwan

References

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Yamaguchi Y, Peeva E, Duca ED, Facheris P, Bar J, Shore R, Cox LA, Sloan A, Thaci D, Ganesan A, Han G, Ezzedine K, Ye Z, Guttman-Yassky E. Ritlecitinib, a JAK3/TEC family kinase inhibitor, stabilizes active lesions and repigments stable lesions in vitiligo. Arch Dermatol Res. 2024 Jul 18;316(7):478. doi: 10.1007/s00403-024-03182-y.

Reference Type DERIVED
PMID: 39023568 (View on PubMed)

Wojciechowski J, S Purohit V, Huh Y, Banfield C, Nicholas T. Evolution of Ritlecitinib Population Pharmacokinetic Models During Clinical Drug Development. Clin Pharmacokinet. 2023 Dec;62(12):1765-1779. doi: 10.1007/s40262-023-01318-3. Epub 2023 Nov 2.

Reference Type DERIVED
PMID: 37917289 (View on PubMed)

Guttman-Yassky E, Del Duca E, Da Rosa JC, Bar J, Ezzedine K, Ye Z, He W, Hyde C, Hassan-Zahraee M, Yamaguchi Y, Peeva E. Improvements in immune/melanocyte biomarkers with JAK3/TEC family kinase inhibitor ritlecitinib in vitiligo. J Allergy Clin Immunol. 2024 Jan;153(1):161-172.e8. doi: 10.1016/j.jaci.2023.09.021. Epub 2023 Sep 28.

Reference Type DERIVED
PMID: 37777018 (View on PubMed)

Ezzedine K, Peeva E, Yamaguchi Y, Cox LA, Banerjee A, Han G, Hamzavi I, Ganesan AK, Picardo M, Thaci D, Harris JE, Bae JM, Tsukamoto K, Sinclair R, Pandya AG, Sloan A, Yu D, Gandhi K, Vincent MS, King B. Efficacy and safety of oral ritlecitinib for the treatment of active nonsegmental vitiligo: A randomized phase 2b clinical trial. J Am Acad Dermatol. 2023 Feb;88(2):395-403. doi: 10.1016/j.jaad.2022.11.005. Epub 2022 Nov 9.

Reference Type DERIVED
PMID: 36370907 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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https://pmiform.com/clinical-trial-info-request?StudyID=B7981019

To obtain contact information for a study center near you, click here.

Other Identifiers

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2018-001271-20

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

B7981019

Identifier Type: -

Identifier Source: org_study_id

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