A Study to Compare the Efficacy and Safety of Luspatercept (ACE-536) Versus Epoetin Alfa for the Treatment of Anemia Due to IPSS-R Very Low, Low, or Intermediate Risk Myelodysplastic Syndromes (MDS) Participants Who Require Red Blood Cell Transfusions and Are ESA Naïve

NCT ID: NCT03682536

Last Updated: 2024-11-20

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

363 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-01-02

Study Completion Date

2027-09-28

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The purpose of this study is to determine the effectiveness of luspatercept (ACE-536) compared to epoetin alfa on red blood cell (RBC) transfusion independence (for at least 12 weeks) with a concurrent hemoglobin increase of at least 1.5 g/dL in participants with anemia due to revised international prognostic scoring system (IPSS-R) very low, low, or intermediate risk myelodysplastic syndromes (MDS) who require RBC transfusions and have never been exposed to erythropoiesis stimulating agent (ESA).

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Myelodysplastic Syndromes

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Luspatercept

Group Type EXPERIMENTAL

Luspatercept

Intervention Type DRUG

Specified dose on specified days

Epoetin alfa

Group Type ACTIVE_COMPARATOR

Epoetin alfa

Intervention Type DRUG

Specified dose on specified days

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Luspatercept

Specified dose on specified days

Intervention Type DRUG

Epoetin alfa

Specified dose on specified days

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

ACE-536 EPREX® ERYPO® PROCRIT®

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Documented diagnosis of Myelodysplastic syndromes (MDS) according to WHO 2016 classification that meets revised international prognostic scoring system (IPSS-R) classification of very low, low, or intermediate risk disease, and have \< 5% blasts in bone marrow
* Endogenous serum erythropoietin (sEPO) level of \< 500 U/L
* Requires Red blood cell (RBC) transfusions, as documented by the criteria: Average transfusion requirement of 2 - 6 units/8 weeks of packed red blood cells (pRBCs) confirmed for a minimum of 8 weeks immediately preceding randomization
* Eastern Cooperative Oncology Group (ECOG) score of 0, 1, or 2

Exclusion Criteria

* Clinically significant anemia due to iron, vitamin B12, or folate deficiencies, or autoimmune or hereditary hemolytic anemia, or hypothyroidism, or any type of known clinically significant bleeding or sequestration or drug induced anemia
* Known history of diagnosis of Acute myeloid leukemia (AML)
* Uncontrolled hypertension, defined as repeated elevations of systolic blood pressure (SBP) of ≥ 150 mmHg and/or diastolic blood pressure (DBP) ≥ 100 mmHg despite adequate treatment
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Acceleron Pharma, Inc., a wholly-owned subsidiary of Merck & Co., Inc., Rahway, NJ USA

INDUSTRY

Sponsor Role collaborator

Celgene

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Bristol-Myers Squibb

Role: STUDY_DIRECTOR

Bristol-Myers Squibb

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Local Institution - 107

Berkeley, California, United States

Site Status

Local Institution - 115

San Diego, California, United States

Site Status

Local Institution - 101

Whittier, California, United States

Site Status

Local Institution - 104

New Haven, Connecticut, United States

Site Status

Local Institution - 136

Washington D.C., District of Columbia, United States

Site Status

Local Institution - 119

Hudson, Florida, United States

Site Status

Local Institution - 120

St. Petersburg, Florida, United States

Site Status

Local Institution - 122

Tallahassee, Florida, United States

Site Status

Local Institution - 108

Tampa, Florida, United States

Site Status

Local Institution - 118

West Palm Beach, Florida, United States

Site Status

Local Institution - 102

Paducah, Kentucky, United States

Site Status

Local Institution - 123

Bethesda, Maryland, United States

Site Status

Local Institution - 117

Kansas City, Missouri, United States

Site Status

Local Institution - 134

East Brunswick, New Jersey, United States

Site Status

Local Institution - 113

Hackensack, New Jersey, United States

Site Status

Local Institution - 105

Greenville, North Carolina, United States

Site Status

Local Institution - 131

Portland, Oregon, United States

Site Status

Univ of Pittsburgh Medical Center

Pittsburgh, Pennsylvania, United States

Site Status

Local Institution - 111

Rock Hill, South Carolina, United States

Site Status

Tennessee Oncology

Nashville, Tennessee, United States

Site Status

Baylor University Medical Center

Dallas, Texas, United States

Site Status

Local Institution - 109

Houston, Texas, United States

Site Status

Local Institution - 114

Salt Lake City, Utah, United States

Site Status

Local Institution - 132

Charlottesville, Virginia, United States

Site Status

Local Institution - 127

Chesapeake, Virginia, United States

Site Status

Local Institution - 206

Albury, New South Wales, Australia

Site Status

Local Institution - 213

Blacktown, New South Wales, Australia

Site Status

Local Institution - 200

Concord, New South Wales, Australia

Site Status

Local Institution - 215

Kogarah, New South Wales, Australia

Site Status

Local Institution - 211

Nowra, New South Wales, Australia

Site Status

Local Institution - 210

Waratah, New South Wales, Australia

Site Status

Local Institution - 207

Wollongong, New South Wales, Australia

Site Status

Local Institution - 208

Auchenflower, Queensland, Australia

Site Status

Local Institution - 202

Adelaide, South Australia, Australia

Site Status

Local Institution - 204

Clayton, Victoria, Australia

Site Status

Local Institution - 203

Malvern, Victoria, Australia

Site Status

Local Institution - 209

Melbourne, Victoria, Australia

Site Status

Local Institution - 205

West Perth, Western Australia, Australia

Site Status

Local Institution - 212

Randwick, , Australia

Site Status

Local Institution - 442

Linz, , Austria

Site Status

Local Institution - 441

Vienna, , Austria

Site Status

Local Institution - 475

Antwerp, , Belgium

Site Status

Local Institution - 471

Brasschaat, , Belgium

Site Status

Local Institution - 474

Brussels, , Belgium

Site Status

Local Institution - 472

Charleroi, , Belgium

Site Status

Local Institution - 473

Kortrijk, , Belgium

Site Status

Local Institution - 470

Leuven, , Belgium

Site Status

Local Institution - 476

Roeselare, , Belgium

Site Status

Local Institution - 147

Calgary, Alberta, Canada

Site Status

Local Institution - 145

Edmonton, Alberta, Canada

Site Status

Local Institution - 142

Hamilton, Ontario, Canada

Site Status

Local Institution - 140

Ottawa, Ontario, Canada

Site Status

Local Institution - 141

Toronto, Ontario, Canada

Site Status

Local Institution - 144

Montreal, Quebec, Canada

Site Status

Local Institution - 148

Montreal, Quebec, Canada

Site Status

Local Institution - 151

Saskatoon, Saskatchewan, Canada

Site Status

Local Institution - 152

Sherbrooke, , Canada

Site Status

Local Institution - 560

Hradec Králové, , Czechia

Site Status

Local Institution - 564

Ostrava-Poruba, , Czechia

Site Status

Local Institution - 563

Prague, , Czechia

Site Status

Local Institution - 562

Prague, , Czechia

Site Status

Local Institution - 561

Prague, , Czechia

Site Status

Local Institution - 317

Angers, , France

Site Status

Local Institution - 312

Bayonne, , France

Site Status

Local Institution - 311

Caen, , France

Site Status

Local Institution - 306

La Tronche, , France

Site Status

Local Institution - 305

Le Mans, , France

Site Status

Local Institution - 309

Lille, , France

Site Status

Local Institution - 303

Limoges, , France

Site Status

Local Institution - 307

Nantes, , France

Site Status

Local Institution - 301

Nice, , France

Site Status

Local Institution - 302

Paris, , France

Site Status

Local Institution - 313

Paris, , France

Site Status

Local Institution - 308

Pessac, , France

Site Status

Local Institution - 315

Pierre-Bénite, , France

Site Status

Local Institution - 316

Poitiers, , France

Site Status

Local Institution - 314

Strasbourg, , France

Site Status

Local Institution - 300

Toulouse, , France

Site Status

Local Institution - 310

Tours, , France

Site Status

Local Institution - 304

Vandœuvre-lès-Nancy, , France

Site Status

Local Institution - 422

Baden-Warttemberg, , Germany

Site Status

Local Institution - 424

Berlin, , Germany

Site Status

Local Institution - 428

Cologne, , Germany

Site Status

Local Institution - 426

Dresden, , Germany

Site Status

Local Institution - 429

Duisburg, , Germany

Site Status

Local Institution - 420

Düsseldorf, , Germany

Site Status

Local Institution - 431

Hamburg, , Germany

Site Status

Local Institution - 435

Keil, , Germany

Site Status

Local Institution - 423

Koblenz, , Germany

Site Status

Local Institution - 430

Leipzig, , Germany

Site Status

Local Institution - 436

Mannheim, , Germany

Site Status

Local Institution - 421

München, , Germany

Site Status

Local Institution - 425

Winnenden, , Germany

Site Status

Local Institution - 427

Würzburg, , Germany

Site Status

Local Institution - 389

Heraklion, Irakleio, Greece

Site Status

Local Institution - 396

Alexandroupoli, , Greece

Site Status

Local Institution - 397

Athens, , Greece

Site Status

Local Institution - 391

Athens, , Greece

Site Status

Local Institution - 395

Athens, , Greece

Site Status

Local Institution - 392

Athens, , Greece

Site Status

Local Institution - 398

Pátrai, , Greece

Site Status

Local Institution - 393

Rio Patras, , Greece

Site Status

Local Institution - 399

Thessaloniki, , Greece

Site Status

Local Institution - 390

Thessaloniki, , Greece

Site Status

Local Institution - 535

Budapest, , Hungary

Site Status

Local Institution - 534

Debrecen, , Hungary

Site Status

Local Institution - 536

Nyíregyháza, , Hungary

Site Status

Local Institution - 386

Haifa, , Israel

Site Status

Local Institution - 383

Jerusalem, , Israel

Site Status

Local Institution - 384

Jerusalem, , Israel

Site Status

Local Institution - 381

Kfar Saba, , Israel

Site Status

Local Institution - 385

Nahariya, , Israel

Site Status

Local Institution - 382

Tel Aviv, , Israel

Site Status

Local Institution - 380

Ẕerifin, , Israel

Site Status

Local Institution - 331

Orbassano, TO, Italy

Site Status

Local Institution - 324

Bologna, , Italy

Site Status

Local Institution - 327

Florence, , Italy

Site Status

Local Institution - 330

Meldola, , Italy

Site Status

Local Institution - 321

Milan, , Italy

Site Status

Local Institution - 329

Padua, , Italy

Site Status

Local Institution - 326

Reggio Calabria, , Italy

Site Status

Local Institution - 328

Roma, , Italy

Site Status

Local Institution - 332

Roma, , Italy

Site Status

Local Institution - 325

Rome, , Italy

Site Status

Local Institution - 323

Rozzano, , Italy

Site Status

Local Institution - 322

Udine, , Italy

Site Status

Local Institution - 238

Matsuyama, Ehime, Japan

Site Status

Local Institution - 244

Nagasaki, Nagasaki, Japan

Site Status

Local Institution - 236

Sayama, Osaka, Japan

Site Status

Local Institution - 247

Amagasaki-Shi, , Japan

Site Status

Local Institution - 249

Fujisawa-Shi, , Japan

Site Status

Local Institution - 234

Fukuoka, , Japan

Site Status

Local Institution - 237

Hitachi, Ibaraki, , Japan

Site Status

Local Institution - 231

Kamogawa, , Japan

Site Status

Local Institution - 248

Kitakyushu-Shi, , Japan

Site Status

Local Institution - 270

Nagaoka-Shi, , Japan

Site Status

Local Institution - 243

Nagoya, , Japan

Site Status

Local Institution - 235

Okayama, , Japan

Site Status

Local Institution - 242

Osaka, , Japan

Site Status

Local Institution - 241

Ōgaki, , Japan

Site Status

Local Institution - 233

Sagamihara, , Japan

Site Status

Local Institution - 246

Sapporo, , Japan

Site Status

Local Institution - 239

Sendai, , Japan

Site Status

Local Institution - 232

Shibuya-ku, , Japan

Site Status

Local Institution - 245

Shimotsuga-gun, , Japan

Site Status

Local Institution - 230

Shinagawa-ku, Tokyo, , Japan

Site Status

Local Institution - 540

Kaunas, , Lithuania

Site Status

Local Institution - 541

Vilnius, , Lithuania

Site Status

Local Institution - 462

Amsterdam, , Netherlands

Site Status

Local Institution - 464

Nijmegen, , Netherlands

Site Status

Local Institution - 460

Rotterdam, , Netherlands

Site Status

Local Institution - 463

Sittard-Geleen, , Netherlands

Site Status

Local Institution - 461

The Hague, , Netherlands

Site Status

Local Institution - 570

Lodz, Lódzkie, Poland

Site Status

Local Institution - 575

Gdansk, , Poland

Site Status

Local Institution - 572

Lubin, , Poland

Site Status

Local Institution - 576

Poznan, , Poland

Site Status

Local Institution - 573

Rzwszow, , Poland

Site Status

Local Institution - 579

Słupsk, , Poland

Site Status

Local Institution - 578

Wałbrzych, , Poland

Site Status

Local Institution - 577

Wroclaw, , Poland

Site Status

Local Institution - 571

Wroclaw, , Poland

Site Status

Local Institution - 373

Beja, , Portugal

Site Status

Local Institution - 371

Braga, , Portugal

Site Status

Local Institution - 372

Lisbon, , Portugal

Site Status

Local Institution - 370

Porto, , Portugal

Site Status

Local Institution - 374

Setúbal, , Portugal

Site Status

Local Institution - 511

Kaluga, , Russia

Site Status

Local Institution - 505

Kirov, , Russia

Site Status

Local Institution - 509

Krasnoyarsk, , Russia

Site Status

Local Institution - 504

Moscow, , Russia

Site Status

Local Institution - 507

Moscow, , Russia

Site Status

Local Institution - 500

Moscow, , Russia

Site Status

Local Institution - 503

Moscow, , Russia

Site Status

Local Institution - 510

Saint Petersburg, , Russia

Site Status

Local Institution - 506

Saint Petersburg, , Russia

Site Status

Local Institution - 508

Saratov, , Russia

Site Status

Local Institution - 502

Tula, , Russia

Site Status

Local Institution - 251

Busan, , South Korea

Site Status

Local Institution - 257

Daegu, , South Korea

Site Status

Local Institution - 250

Hwasun-Gun, , South Korea

Site Status

Local Institution - 253

Seongnam-si, , South Korea

Site Status

Local Institution - 252

Seoul, , South Korea

Site Status

Local Institution - 256

Seoul, , South Korea

Site Status

Local Institution - 255

Seoul, , South Korea

Site Status

Local Institution - 254

Seoul, , South Korea

Site Status

Local Institution - 358

Barcelona, , Spain

Site Status

Local Institution - 350

Barcelona, , Spain

Site Status

Local Institution - 354

Granada, , Spain

Site Status

Local Institution - 352

Madrid, , Spain

Site Status

Local Institution - 355

Madrid, , Spain

Site Status

Local Institution - 353

Málaga, , Spain

Site Status

Local Institution - 361

Murcia, , Spain

Site Status

Local Institution - 356

Ourense, , Spain

Site Status

Local Institution - 363

Oviedo, , Spain

Site Status

Local Institution - 362

Palma de Mallorca, , Spain

Site Status

Local Institution - 351

Salamanca, , Spain

Site Status

Local Institution - 360

Seville, , Spain

Site Status

Local Institution - 357

Valencia, , Spain

Site Status

Local Institution - 359

Valencia, , Spain

Site Status

Local Institution - 550

Gothenburg, , Sweden

Site Status

Local Institution - 552

Lund, , Sweden

Site Status

Local Institution - 551

Stockholm, , Sweden

Site Status

Local Institution - 450

Bern, , Switzerland

Site Status

Local Institution - 452

Lucerne, , Switzerland

Site Status

Local Institution - 451

Winterthur, , Switzerland

Site Status

Local Institution - 220

Changhua City, Changhua, , Taiwan

Site Status

Local Institution - 222

Niaosong District Kaohsiung City, , Taiwan

Site Status

Local Institution - 223

Taichung, , Taiwan

Site Status

Local Institution - 224

Taichung, , Taiwan

Site Status

Local Institution - 221

Taipei, , Taiwan

Site Status

Local Institution - 342

Ankara, , Turkey (Türkiye)

Site Status

Local Institution - 340

Manisa, , Turkey (Türkiye)

Site Status

Local Institution - 343

Trabzon, , Turkey (Türkiye)

Site Status

Local Institution - 526

Cherkassy, , Ukraine

Site Status

Local Institution - 525

Dnipro, , Ukraine

Site Status

Local Institution - 522

Kyiv, , Ukraine

Site Status

Local Institution - 520

Lviv, , Ukraine

Site Status

Local Institution - 523

Mykolaiv, , Ukraine

Site Status

Local Institution - 521

Ternopil, , Ukraine

Site Status

Local Institution - 401

Aberdeen, , United Kingdom

Site Status

Local Institution - 403

Bournemouth, , United Kingdom

Site Status

Local Institution - 405

Headington, Oxford, , United Kingdom

Site Status

Local Institution - 407

Lincoln, , United Kingdom

Site Status

Local Institution - 404

London, , United Kingdom

Site Status

Local Institution - 400

Manchester, , United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Australia Austria Belgium Canada Czechia France Germany Greece Hungary Israel Italy Japan Lithuania Netherlands Poland Portugal Russia South Korea Spain Sweden Switzerland Taiwan Turkey (Türkiye) Ukraine United Kingdom

References

Explore related publications, articles, or registry entries linked to this study.

Garcia-Manero G, Santini V, Zeidan AM, Komrokji RS, Pozharskaya V, Rose S, Keeperman K, Lai Y, Kalsekar S, Aggarwal B, Miteva D, Valcarcel D, Fenaux P, Shortt J, Della Porta MG, Platzbecker U. Long-Term Transfusion Independence with Luspatercept Versus Epoetin Alfa in Erythropoiesis-Stimulating Agent-Naive, Lower-Risk Myelodysplastic Syndromes in the COMMANDS Trial. Adv Ther. 2025 Jul;42(7):3576-3589. doi: 10.1007/s12325-025-03208-5. Epub 2025 May 16.

Reference Type DERIVED
PMID: 40377899 (View on PubMed)

Della Porta MG, Garcia-Manero G, Santini V, Zeidan AM, Komrokji RS, Shortt J, Valcarcel D, Jonasova A, Dimicoli-Salazar S, Tiong IS, Lin CC, Li J, Zhang J, Pilot R, Kreitz S, Pozharskaya V, Keeperman KL, Rose S, Prebet T, Lai Y, Degulys A, Paolini S, Cluzeau T, Fenaux P, Platzbecker U. Luspatercept versus epoetin alfa in erythropoiesis-stimulating agent-naive, transfusion-dependent, lower-risk myelodysplastic syndromes (COMMANDS): primary analysis of a phase 3, open-label, randomised, controlled trial. Lancet Haematol. 2024 Sep;11(9):e646-e658. doi: 10.1016/S2352-3026(24)00203-5. Epub 2024 Jul 19.

Reference Type DERIVED
PMID: 39038479 (View on PubMed)

Platzbecker U, Della Porta MG, Santini V, Zeidan AM, Komrokji RS, Shortt J, Valcarcel D, Jonasova A, Dimicoli-Salazar S, Tiong IS, Lin CC, Li J, Zhang J, Giuseppi AC, Kreitz S, Pozharskaya V, Keeperman KL, Rose S, Shetty JK, Hayati S, Vodala S, Prebet T, Degulys A, Paolini S, Cluzeau T, Fenaux P, Garcia-Manero G. Efficacy and safety of luspatercept versus epoetin alfa in erythropoiesis-stimulating agent-naive, transfusion-dependent, lower-risk myelodysplastic syndromes (COMMANDS): interim analysis of a phase 3, open-label, randomised controlled trial. Lancet. 2023 Jul 29;402(10399):373-385. doi: 10.1016/S0140-6736(23)00874-7. Epub 2023 Jun 10.

Reference Type DERIVED
PMID: 37311468 (View on PubMed)

Provided Documents

Download supplemental materials such as informed consent forms, study protocols, or participant manuals.

Document Type: Study Protocol and Statistical Analysis Plan

View Document

Related Links

Access external resources that provide additional context or updates about the study.

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

U1111-1218-1810

Identifier Type: REGISTRY

Identifier Source: secondary_id

2022-501485-22

Identifier Type: OTHER

Identifier Source: secondary_id

ACE-536-MDS-002

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.