A Trial Testing Early vs Late Onset of EPO Alfa Treatment in Lower Risk MDS

NCT ID: NCT03223961

Last Updated: 2025-03-11

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

124 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-03-26

Study Completion Date

2028-10-01

Brief Summary

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This is an open-label, randomized, multicenter, phase III study

Patients with baseline Hb comprised between 9 and 10.5g/dl will be randomized to receive EPO Alfa 60000 UI/week for at least 12 weeks:

* Either at diagnosis Or
* at the Hb threshold chosen for RBC transfusions (must be \< 9g/dl)

Detailed Description

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in this trial we will compare the early introduction of EPO alfa to the delayed introduction in lower risk MDS with non RBC transfusion dependent anemia.

At enrollment patients will be randomised in the 2 arms (early and delayed start of EPO alfa).

Treatment Regimen Epoetin alfa 60000 UI/week for at least 12 weeks

1. Early onset arm: early onset of EPO ALFA 60000 IU/week , at patient inclusion
2. Delayed onset arm: late introduction of EPO ALFA 60000 IU/week, whenever the patient reaches the level chosen RBC transfusions (based on age, comorbidities, anticipated tolerance of anemia).

Conditions

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Myelodysplastic Syndromes

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

randomazed study
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Early onset arm

Intervention: early onset of Eprex60000 IU/week , at patient inclusion

Group Type EXPERIMENTAL

EPREX

Intervention Type DRUG

60 000 U/week for at least 12 weeks

Delayed onset arm

Intervention: late introduction of Eprex60000 IU/week, whenever the patient reaches the level chosen RBC transfusions (based on age, comorbidities, anticipated tolerance of anemia).

Group Type EXPERIMENTAL

EPREX

Intervention Type DRUG

60 000 U/week for at least 12 weeks

Interventions

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EPREX

60 000 U/week for at least 12 weeks

Intervention Type DRUG

Other Intervention Names

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Epoetin alfa

Eligibility Criteria

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Inclusion Criteria

1. Age ≥ 18 years
2. MDS according to WHO 2016 criteria, with low or int 1 classical IPSS
3. Non-RBC transfusion dependent anemia
4. Hb level between 9 and 10.5g/dl (at the center's lab)
5. Hb level should be at least 1g/dl higher than the Hb threshold chosen to start RBC transfusions based on age, comorbidities and predicted clinical tolerance of anemia (this transfusion threshold should be chosen between 8 and 9g/dl)
6. Serum EPO level \<500U/l
7. No other cause of anemia (including iron deficiency, vitamin B12 or B9 deficiency, hemolysis, hypothyroidism….)
8. Performance status \<=2

Exclusion Criteria

1. Higher risk MDS (IPSS intermediate-2 or high)
2. Del 5q
3. Baseline Hemoglobin level \> 10.5 g/dl or \<9g/dl
4. Transfusion threshold (based on age , comorbidities…) \>9g/dl
5. Transfusion threshold less than 1 g/dl below baseline Hb level
6. RBC transfusion dependence. Patients may have received only one transfusion series for MDS prior to inclusion
7. CMML , if \>10 % BM blasts or WBC\>13.000/mm3
8. Uncontrolled hypertension
9. Uncontrolled cardiovascular disease including angina pectoris or cardiac failure
10. Renal failure: Creatinine clearance\<40ml/min (using MDRD formula)
11. Pregnancy (positive bettaHCG) or nursing
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Groupe Francophone des Myelodysplasies

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Sophie Park, Prof

Role: PRINCIPAL_INVESTIGATOR

University Hospital, Grenoble

Locations

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Chu Amiens

Amiens, , France

Site Status

CH Angers

Angers, , France

Site Status

CH Avignon

Avignon, , France

Site Status

Centre Hospitalier de La Cote Basque

Bayonne, , France

Site Status

Hopital Nord Franche-Comté

Belfort, , France

Site Status

CHU de Besançon

Besançon, , France

Site Status

Hopital Avicenne

Bobigny, , France

Site Status

Hôpital Morvan

Brest, , France

Site Status

CHU de Caen

Caen, , France

Site Status

CH de Sevigné

Cesson, , France

Site Status

CH de Cholet

Cholet, , France

Site Status

CHU Estaing

Clermont-Ferrand, , France

Site Status

CHSF Gilles de Corbeil

Corbeil-Essonnes, , France

Site Status

Hôpital Henri-Mondor

Créteil, , France

Site Status

CHU de Grenoble

Grenoble, , France

Site Status

Centre Hospitalier du Mans

Le Mans, , France

Site Status

Clinique Victor Hugo

Le Mans, , France

Site Status

Hopital Saint-Vincent de Paul

Lille, , France

Site Status

CHRU Limoges

Limoges, , France

Site Status

Centre Hospitalier Lyon Sud

Lyon, , France

Site Status

IPC

Marseille, , France

Site Status

Centre Hospitalier du Mont de Marsan

Mont-de-Marsan, , France

Site Status

CHU de Nantes

Nantes, , France

Site Status

CHU de Nice

Nice, , France

Site Status

Hopital St Louis T4

Paris, , France

Site Status

Centre Hospitalier Joffre-Perpignan

Perpignan, , France

Site Status

Sophie Dimicoli-Salazar

Pessac, , France

Site Status

CH de Périgueux

Périgueux, , France

Site Status

CHU de Poitiers

Poitiers, , France

Site Status

CHR d'Annecy

Pringy, , France

Site Status

CHRU de Reims

Reims, , France

Site Status

CHU Pontchaillou

Rennes, , France

Site Status

Centre Henri Becquerel

Rouen, , France

Site Status

CH Saint Nazaire

Saint-Nazaire, , France

Site Status

Centre Hospitalier Universitaire de STRASBOURG

Strasbourg, , France

Site Status

IUCT Oncopole

Toulouse, , France

Site Status

CH de Troyes

Troyes, , France

Site Status

CH Valence

Valence, , France

Site Status

CHU Brabois

Vandœuvre-lès-Nancy, , France

Site Status

Countries

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France

Other Identifiers

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GFM-EPO-PRETAR

Identifier Type: -

Identifier Source: org_study_id

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