Darbepoetin Alpha in Myelodysplastic Syndromes (MDS)

NCT ID: NCT00443339

Last Updated: 2007-05-17

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE2

Total Enrollment

99 participants

Study Classification

INTERVENTIONAL

Study Start Date

2006-12-31

Study Completion Date

2008-07-31

Brief Summary

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This is an evaluation of the effectiveness of darbepoetin alpha in treating anemia of MDS patients with an International Prognostic Scoring System (IPSS) score of low or intermediate 1.

Detailed Description

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Inclusion of MDS with IPSS low or int-1 and hemoglobin \< 10/dL.

Study drug: Darbepoetin alfa (Aranesp) 500 microg every two weeks subcutaneously during 12 weeks, combined to filgrastim 300 microg twice weekly for an additional 12 weeks in non responders.

Response will be evaluated at 12 weeks. Patients with major or minor erythroid response (HI-E major or minor according to IWG 2000 criteria) will be continued on Aranesp. In non-responders, an additional 12 weeks of Aranesp at the same dosing, combined to Filgrastim (300 ug twice weekly, then adjusted to maintain WBC between 5000 and 10000/mm3) will be proposed. In case of response, the treatment will be continued for a total duration of 24 months. If Hb level reaches levels \> 13 g/dl at any time, Aranesp should be discontinued until Hb levels are less than 12 g/dl. Aranesp should then be resumed at 500 µg/injection every 3 weeks. Intervals between injections should be further increased by one week every time they lead to Hb levels \> 13 g/dl. The purpose of this dose adjustment is to reach the Aranesp schedule allowing a maintenance Hb level between 11 and 12 g/dl.

Conditions

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Myelodysplastic Syndromes

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Interventions

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Darbepoetin

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* MDS of the following subtypes:

* RA, RAS, RAEB with marrow blasts \< 10% (according to FAB),
* RA, RARS, RCMD, RAEB 1, CMML 1 with ≤ 10% WBC counts \< 13000/mm3 (according to WHO classification)
* Anemia, defined by Hb \< 10 g/dl or RBC transfusion requirement in the absence of other causes of anemia (especially renal failure, iron, or folate deficiency)
* IPSS ≤ 1(ie IPSS low or intermediate 1)
* EPO level \< 500 UI/L
* Ability to perform physical tests of exercise tolerance
* No renal failure (creatinine ≤ 120% normal upper value for the center)
* No underlying severe condition
* ECOG performance status score of 0, 1, or 2
* Must be 18 years of age or older at the time of screening
* Written informed consent

Exclusion Criteria

* Therapy related MDS
* MDS with IPSS \> 1 (int 2 or high score)
* Chronic myelomonocytic leukemia with \> 10% marrow blasts or WBC \> 13000/mm3
* Uncontrolled systemic hypertension
* Cardiac condition: uncontrolled angina, congestive heart failure, or uncontrolled cardiac arrhythmia
* Creatinine level \> 120% upper normal value for the center.
* Clinically significant systemic infection or chronic inflammatory disease (eg, rheumatoid arthritis) present at the time of screening
* Serum folate ≤ 2.0 ng/mL or vitamin B12 ≤ 200 pg/mL (anemia related to nutritional deficiencies)
* Other causes of anemia (eg, hemolysis, bleeding, sickle cell anemia, renal disease)
* Pregnant (ie, positive βhCG test) or breast feeding female subjects
* Women of childbearing potential and not using adequate contraceptives
* Known positive antibody response to an erythropoietic growth factor
* Known hypersensitivity to darbepoetin alpha or any of its excipients, or to recombinant erythropoietins
* Patient unable to understand the protocol or to be adequately followed up.
* History of seizures
* Previous history of thrombotic events
* Concomitant treatment with thalidomide
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Groupe Francophone des Myelodysplasies

OTHER

Sponsor Role lead

Principal Investigators

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Charikleia KELAIDI, MD

Role: PRINCIPAL_INVESTIGATOR

Groupe Francophone des Myelodysplasies

Locations

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CHU d'Amiens

Amiens, , France

Site Status RECRUITING

CHU d'Angers

Angers, , France

Site Status RECRUITING

CHU d'Avignon

Avignon, , France

Site Status RECRUITING

CH de la Cote Basque

Bayonne, , France

Site Status RECRUITING

CHU de Brest - Hopital Morvan

Brest, , France

Site Status RECRUITING

CHU de Caen

Caen, , France

Site Status RECRUITING

Hopital Percy

Clamart, , France

Site Status RECRUITING

Hopital Henri Mondor

Créteil, , France

Site Status RECRUITING

CHU de Dijon

Dijon, , France

Site Status RECRUITING

CHU Albert Michallon

Grenoble, , France

Site Status RECRUITING

CHRU Hurriez

Lille, , France

Site Status RECRUITING

CHRU Limoges

Limoges, , France

Site Status RECRUITING

Hopital Edouard Herriot

Lyon, , France

Site Status RECRUITING

Hopital Paoli Calmette

Marseille, , France

Site Status RECRUITING

Hopital Hotel Dieu

Nantes, , France

Site Status RECRUITING

CHU Archet

Nice, , France

Site Status RECRUITING

Hopital Hotel Dieu

Paris, , France

Site Status RECRUITING

Hopital Hotel Dieu

Paris, , France

Site Status RECRUITING

Hopital St Louis

Paris, , France

Site Status RECRUITING

Hopital Saint Antoine

Paris, , France

Site Status RECRUITING

Hopital Cochin

Paris, , France

Site Status RECRUITING

Hopital Jean-Bernard

Poitiers, , France

Site Status RECRUITING

CHU Robert Debre

Reims, , France

Site Status RECRUITING

CHU Pontchaillou

Rennes, , France

Site Status RECRUITING

Hopital Henri Becquerel

Rouen, , France

Site Status RECRUITING

Hopital Hautepierre

Strasbourg, , France

Site Status RECRUITING

Hopital Purpan

Toulouse, , France

Site Status RECRUITING

Hopital Bretonneau

Tours, , France

Site Status RECRUITING

CHU Nancy-Brabois

Vandœuvre-lès-Nancy, , France

Site Status RECRUITING

Countries

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France

Central Contacts

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Charikleia KELAIDI, MD

Role: CONTACT

Fatima-Zohra HAMZA, RCA

Role: CONTACT

0033148955890

Facility Contacts

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Ghandi DAMAJ, MD

Role: primary

0033322455915

Mathilde HUNAULT-BERGER, Doctors

Role: primary

0033241354475

Bohrane SLAMA, Doctor

Role: primary

0033432753120

Frederic Bauduer, MD

Role: primary

33 5 59 44 38 33

Christian Berthou, MD

Role: primary

33 2 98 22 35 04

Stéphane CHEZE, MD

Role: primary

0033231272360

Thierry DE REVEL, Profesor

Role: primary

0033141466301

Michel TULLIEZ, Profesor

Role: primary

003314982880

Denis CAILLOT

Role: primary

0033380293645

Jean-Yves CAHN, Professor

Role: primary

0033476769445

Bruno QUESNEL, Profesor

Role: primary

0033320446640

Dominique BOURDESSOULE

Role: primary

0033555056642

Youcef CHELGHOUM, MD

Role: primary

0033472117324

Norbert VEY, MD

Role: primary

0033431223695

Jean-Luc HAROUSSEAU

Role: primary

0033240083271

Laurence LEGROS, DOCTOR

Role: primary

0033492035844

Anne VEKOFF, MD

Role: primary

00033142348586

Nicole CASADEVALL, Profesor

Role: primary

0033142348266

Herve DOMBRET, Profesor

Role: primary

0033142499643

Francoise ISNARD, MD

Role: primary

00033149282622

Francois DREYFUS, Professor

Role: primary

003358412120

Francois GUILHOT, Professor

Role: primary

0033549444201

Chantal HIMBERLIN, Doctor

Role: primary

0033326783644

Martine ESCOFFRE-BARBE

Role: primary

0033299284291

Aspasia STAMATOULLAS, Doctor

Role: primary

0033232082288

Shanti AME, MD

Role: primary

0033388127680

Guy LAURENT, Professor

Role: primary

0033561772078

Philippe COLOMBAT, Profesor

Role: primary

0033247473712

Agnes Guerci-Bresler, MD

Role: primary

33 83 15 32 82 / 81

References

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Kelaidi C, Beyne-Rauzy O, Braun T, Sapena R, Cougoul P, Ades L, Pillard F, Lamberto C, Charniot JC, Guerci A, Choufi B, Stamatoullas A, Slama B, De Renzis B, Ame S, Damaj G, Boyer F, Chaury MP, Legros L, Cheze S, Testu A, Gyan E, Bene MC, Rose C, Dreyfus F, Fenaux P. High response rate and improved exercise capacity and quality of life with a new regimen of darbepoetin alfa with or without filgrastim in lower-risk myelodysplastic syndromes: a phase II study by the GFM. Ann Hematol. 2013 May;92(5):621-31. doi: 10.1007/s00277-013-1686-4. Epub 2013 Jan 29.

Reference Type DERIVED
PMID: 23358617 (View on PubMed)

Other Identifiers

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GFM-DAR500-2006-01

Identifier Type: -

Identifier Source: org_study_id