Dose-Exploration Evaluating the Efficacy and Safety of Voclosporin in Subjects With Focal Segmental Glomerulosclerosis

NCT ID: NCT03598036

Last Updated: 2021-09-16

Study Results

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

5 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-06-21

Study Completion Date

2020-05-19

Brief Summary

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Evaluating the Efficacy and Safety of Voclosporin in Achieving Complete or Partial Remission of Proteinuria in Subjects with Focal Segmental Glomerulosclerosis

Detailed Description

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The aim of the current study to assess the efficacy of voclosporin in achieving complete or partial remission of proteinuria after 24 weeks of therapy in subjects with focal segmental glomerulosclerosis (FSGS). As well as to assess the safety and tolerability of voclosporin over 24 weeks in subjects with FSGS.

Conditions

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Focal Segmental Glomerulosclerosis

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Voclosporin

Cohort 1:

Maximum dose of 3 capsules (7.9mg) BID

Cohort 2

Dosing to be decided based on the safety from the first 5 or 6 subjects in Cohort 1.

Group Type EXPERIMENTAL

Voclosporin

Intervention Type DRUG

Voclosporin softgel capsules. Up to 10 subjects will be enrolled into Cohort 1 and take up to 3 capsules twice daily (BID).

The dose of voclosporin for Cohort 2 (at least 10 subjects) will be determined by analysis of efficacy and safety data at Week 12 from the first 5 or 6 subjects in Cohort 1.

Interventions

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Voclosporin

Voclosporin softgel capsules. Up to 10 subjects will be enrolled into Cohort 1 and take up to 3 capsules twice daily (BID).

The dose of voclosporin for Cohort 2 (at least 10 subjects) will be determined by analysis of efficacy and safety data at Week 12 from the first 5 or 6 subjects in Cohort 1.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Primary FSGS diagnosed by renal biopsy.
2. Urine protein creatinine ratio (UPCR) ≥2.0 mg/mg, serum albumin ≤3.2 g/dL and can be immunosuppressant treatment-naïve, or receiving treatment with steroids.
3. Stable proteinuria, renal function, and BP.

Exclusion Criteria

1. Clinical or histologic evidence of secondary FSGS.
2. Histologic evidence of collapsing variant FSGS.
3. eGFR as calculated by the Chronic Kidney Disease Epidemiology Collaboration (CKD-EPI) equation of ≤30 mL/minute/1.73 m2 at initial screening assessment or ≤45 mL/minute/1.73 m2 at last qualifying assessment.
4. Currently requiring renal dialysis (hemodialysis or peritoneal dialysis) or expected to require dialysis during the study period.
5. Current or medical history of:

* Congenital or acquired immunodeficiency.
* In the opinion of the Investigator, clinically significant drug or alcohol abuse within 2 years prior to screening.
* Malignancy within 5 years of screening, with the exception of basal and squamous cell carcinomas treated by complete excision.
* Current or past lymphoproliferative disease or previous total lymphoid irradiation.
* Severe viral infection within 3 months of screening, or known HIV infection. Severe viral infection is defined as active disease requiring antiviral therapy.
* Active tuberculosis (TB) or known history of TB/evidence of old TB if not taking prophylaxis with isoniazid.
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Aurinia Pharmaceuticals Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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FSGS Investigative Center

Denver, Colorado, United States

Site Status

FSGS Investigative Center

Winter Park, Florida, United States

Site Status

FSGS Investigative Center

Lawrenceville, Georgia, United States

Site Status

FSGS Investigative Center

Chicago, Illinois, United States

Site Status

FSGS Investigative Center

Iowa City, Iowa, United States

Site Status

FSGS Investigative Center

Louisville, Kentucky, United States

Site Status

FSGS Investigative Center

Shreveport, Louisiana, United States

Site Status

FSGS Investigative Center

Detroit, Michigan, United States

Site Status

FSGS Investigative Center

Minneapolis, Minnesota, United States

Site Status

FSGS Investigative Centre

St Louis, Missouri, United States

Site Status

FSGS Investigative Center

Newark, New Jersey, United States

Site Status

FSGS Investigative Center

New York, New York, United States

Site Status

FSGS Investigative Center

Chapel Hill, North Carolina, United States

Site Status

FSGS Investigative Center

Charlotte, North Carolina, United States

Site Status

FSGS Investigative Center

Columbus, Ohio, United States

Site Status

FSGS Investigative Center

Bethlehem, Pennsylvania, United States

Site Status

FSGS Investigative Center

Dallas, Texas, United States

Site Status

FSGS Investigative Center

Dallas, Texas, United States

Site Status

FSGS Investigative Center

El Paso, Texas, United States

Site Status

FSGS Investigative Center

Houston, Texas, United States

Site Status

FSGS Investigative Site

Salt Lake City, Utah, United States

Site Status

FSGS Investigative Centre

Santiago de los Caballeros, , Dominican Republic

Site Status

FSGS Investigative Center

Santo Domingo, , Dominican Republic

Site Status

Countries

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United States Dominican Republic

References

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Ling SY, Huizinga RB, Mayo PR, Larouche R, Freitag DG, Aspeslet LJ, Foster RT. Cytochrome P450 3A and P-glycoprotein drug-drug interactions with voclosporin. Br J Clin Pharmacol. 2014 Jun;77(6):1039-50. doi: 10.1111/bcp.12309.

Reference Type BACKGROUND
PMID: 24330024 (View on PubMed)

Ling SY, Huizinga RB, Mayo PR, Freitag DG, Aspeslet LJ, Foster RT. Pharmacokinetics of voclosporin in renal impairment and hepatic impairment. J Clin Pharmacol. 2013 Dec;53(12):1303-12. doi: 10.1002/jcph.166. Epub 2013 Oct 8.

Reference Type BACKGROUND
PMID: 23996158 (View on PubMed)

Mayo PR, Huizinga RB, Ling SY, Freitag DG, Aspeslet LJ, Foster RT. Voclosporin food effect and single oral ascending dose pharmacokinetic and pharmacodynamic studies in healthy human subjects. J Clin Pharmacol. 2013 Aug;53(8):819-26. doi: 10.1002/jcph.114. Epub 2013 Jun 4.

Reference Type BACKGROUND
PMID: 23736966 (View on PubMed)

Busque S, Cantarovich M, Mulgaonkar S, Gaston R, Gaber AO, Mayo PR, Ling S, Huizinga RB, Meier-Kriesche HU; PROMISE Investigators. The PROMISE study: a phase 2b multicenter study of voclosporin (ISA247) versus tacrolimus in de novo kidney transplantation. Am J Transplant. 2011 Dec;11(12):2675-84. doi: 10.1111/j.1600-6143.2011.03763.x. Epub 2011 Sep 22.

Reference Type BACKGROUND
PMID: 21943027 (View on PubMed)

Provided Documents

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Document Type: Study Protocol and Statistical Analysis Plan: Protocol v1.0

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Document Type: Study Protocol and Statistical Analysis Plan: Protocol v2.0 (Amendment 1)

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Document Type: Study Protocol and Statistical Analysis Plan: Protocol v3.0 (Amendment 2)

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Document Type: Study Protocol and Statistical Analysis Plan: Protocol v4.0 (Amendment 3)

View Document

Other Identifiers

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AUR-VCS-2017-03

Identifier Type: -

Identifier Source: org_study_id

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