A Study of TRPC5 Channel Inhibitor in Patients With Diabetic Nephropathy, Focal Segmental Glomerulosclerosis, and Treatment-Resistant Minimal Change Disease

NCT ID: NCT04387448

Last Updated: 2022-11-15

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

96 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-07-28

Study Completion Date

2022-11-01

Brief Summary

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This is a phase 2a study evaluating the safety and tolerability of multiple ascending doses of GFB-887 in patients with diabetic nephropathy (DN), focal segmental glomerulosclerosis (FSGS), and treatment-resistant minimal change disease (TR-MCD).

Detailed Description

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Approximately 125 patients will be enrolled in this study across the United States. Patients with DN and FSGS/TR-MCD will be randomized in 3 ascending dose cohorts to receive either GFB-887 or placebo.

Conditions

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Kidney Diseases Diabetic Nephropathies Glomerulosclerosis, Focal Segmental Nephrosis, Lipoid Urologic Diseases Diabetes Complications Diabetes Mellitus Endocrine System Diseases Glomerulonephritis Nephritis Nephrosis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Multiple-ascending, placebo-controlled
Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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GFB-887 multiple ascending dose (MAD) active

GFB-887 active once-daily dosing

Group Type EXPERIMENTAL

GFB-887

Intervention Type DRUG

Investigational Medicinal Product (IMP)

GFB-887 MAD placebo

GFB-887 placebo once-daily dosing

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Matching

Interventions

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GFB-887

Investigational Medicinal Product (IMP)

Intervention Type DRUG

Placebo

Matching

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* All patients:

1. Male or female 18-75 years of age, of any race, at the time of signing informed consent.
2. Estimated glomerular filtration rate (eGFR) ≥ 30 mL/min/1.73 m2 at Screening.
3. Currently receiving an angiotensin-converting enzyme (ACE) inhibitor or angiotensin receptor blocker (ARB).
* For DN patients:

1. Diagnosis of type 2 diabetes with glycated hemoglobin (HbA1c) level ≤11% at Screening.
2. UACR ≥ 150 mg/g.
* For FSGS/TR-MCD patients:

1. Diagnosis of FSGS based on either biopsy or genetic testing or TR-MCD based on biopsy.
2. UPCR ≥ 1.0 g/g.

Exclusion Criteria

* All patients:

1. Evidence of another (non-DN, non-FSGS/TR-MCD, respectively) kidney disease.
2. History of malignancy, unless in remission for at least 5 years other than adequately treated basal cell or squamous cell skin cancer, cervical carcinoma in situ, or prostate cancer not expected to require treatment over the course of the study.
3. History of any organ or bone marrow transplant, including kidney grafts.
4. History of alcoholism or drug/chemical abuse within 12 months prior to Screening.
* For DN patients:

1. Renal disease that requires immunosuppressive therapy (currently, or in the past).
2. Body mass index (BMI) \>45 kg/m2.
* For FSGS/TR-MCD patients:

1. Currently on calcineurin inhibitors or history of resistance to calcineurin inhibitors.
2. Body mass index (BMI) \>40 kg/m2.
3. Known history of severe or chronic hepatobiliary disease.
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Goldfinch Bio, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

Aventiv Research - Phoenix

Mesa, Arizona, United States

Site Status

Arizona Kidney Disease & Hypertension Centers (AKDHC)

Scottsdale, Arizona, United States

Site Status

Academic Medical Research Institute (AMRI)

Glendale, California, United States

Site Status

Amicis Research Center

Granada Hills, California, United States

Site Status

Cedars-Sinai Medical Center

Los Angeles, California, United States

Site Status

Amicis Research Center

Northridge, California, United States

Site Status

Valley Renal Medical Group

Northridge, California, United States

Site Status

Respire Research - Palm Springs

Palm Springs, California, United States

Site Status

North American Research Institute

San Dimas, California, United States

Site Status

Dr. Malvin Yan Inc.

South Gate, California, United States

Site Status

Valiance Clinical Research - Tarzana

Tarzana, California, United States

Site Status

Amicis Research Center

Vacaville, California, United States

Site Status

DaVita Mojave Sage Dialysis

Victorville, California, United States

Site Status

University of Colorado Anschutz Medical Campus

Aurora, Colorado, United States

Site Status

Colorado Kidney Care (Denver Nephrology)

Denver, Colorado, United States

Site Status

Western Nephrology - Westminster

Wheat Ridge, Colorado, United States

Site Status

DaVita Hartford North

Hartford, Connecticut, United States

Site Status

Nephrology Associationes, P.A.

Newark, Delaware, United States

Site Status

Prohealth Research Center - Doral

Doral, Florida, United States

Site Status

Clinical Site Partners Leesburg, LLC

Leesburg, Florida, United States

Site Status

Premier Clinical Research Institute

Miami, Florida, United States

Site Status

Kidney & Hypertension Specialists of Miami

Miami, Florida, United States

Site Status

Avanza Medical Research Center

Pensacola, Florida, United States

Site Status

Coastal Nephrology Associates Research Center, LLC

Port Charlotte, Florida, United States

Site Status

Florida Premier Research Institute - Clay Street

Winter Park, Florida, United States

Site Status

Masters of Clinical Research, Inc.

Augusta, Georgia, United States

Site Status

Inova Clinical Trials and Research Center

Tyrone, Georgia, United States

Site Status

Boise Kidney and Hypertension Institute

Meridian, Idaho, United States

Site Status

Research by Design, LLC

Chicago, Illinois, United States

Site Status

Adventist Health Partners

Hinsdale, Illinois, United States

Site Status

Southern Illinois University School of Medicine

Springfield, Illinois, United States

Site Status

University of Iowa College of Public Health

Iowa City, Iowa, United States

Site Status

My Kidney Center, LLC

Manhattan, Kansas, United States

Site Status

Louisiana Kidney Update, LLC

Lafayette, Louisiana, United States

Site Status

Louisiana State University Health Sciences Center - School of Medicine - New Orleans

New Orleans, Louisiana, United States

Site Status

University of Maryland Medical Center

Baltimore, Maryland, United States

Site Status

Tufts Medical Center

Boston, Massachusetts, United States

Site Status

Renal and Transplant Associates of New England, PC

Springfield, Massachusetts, United States

Site Status

University of Michigan

Ann Arbor, Michigan, United States

Site Status

Wayne State University School of Medicine

Detroit, Michigan, United States

Site Status

St. Clair Nephrology

Roseville, Michigan, United States

Site Status

DaVita Clinical Research

Edina, Minnesota, United States

Site Status

University of Minnesota - Center for Pediatric Obesity Medicine

Minneapolis, Minnesota, United States

Site Status

University of Mississippi Medical Center

Jackson, Mississippi, United States

Site Status

Nephrology & Hypertension Associates Ltd

Tupelo, Mississippi, United States

Site Status

Clinical Research Consultants

Kansas City, Missouri, United States

Site Status

DaVita Pelican Point Dialysis

Las Vegas, Nevada, United States

Site Status

Sierra Nevada Nephrology Consultants

Reno, Nevada, United States

Site Status

Mount Sinai Medical Center

New York, New York, United States

Site Status

Columbia University Medical Center

New York, New York, United States

Site Status

Eastern Nephrology Associates PLLC

New Bern, North Carolina, United States

Site Status

Akron Nephrology Associates, Inc.

Akron, Ohio, United States

Site Status

Cleveland Clinic

Cleveland, Ohio, United States

Site Status

The Ohio State University Wexner Medical Center

Columbus, Ohio, United States

Site Status

Northeast Clinical Research Center

Bethlehem, Pennsylvania, United States

Site Status

Rhode Island Hospital

East Providence, Rhode Island, United States

Site Status

South Carolina Nephrology and Hypertension

Orangeburg, South Carolina, United States

Site Status

Southeast Renal Research Institute

Chattanooga, Tennessee, United States

Site Status

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status

Texas Tech University Health Sciences Center - Amarillo

Amarillo, Texas, United States

Site Status

Arlington Nephrology, PC

Arlington, Texas, United States

Site Status

Conroe Willis Medical Research

Conroe, Texas, United States

Site Status

Renal Disease Research Institute

Dallas, Texas, United States

Site Status

El Paso Kidney Specialists, PA

El Paso, Texas, United States

Site Status

Xpress Trials LLC

Houston, Texas, United States

Site Status

Prolato Clinical Research Center

Houston, Texas, United States

Site Status

North Texas Kidney Disease Association

Lewisville, Texas, United States

Site Status

Clinical Advancement Center, PLLC

San Antonio, Texas, United States

Site Status

San Antonio Kidney Disease Center Physicians Group, PLLC

San Antonio, Texas, United States

Site Status

Clear Lake Specialties

Webster, Texas, United States

Site Status

Utah Kidney Research Institute

Salt Lake City, Utah, United States

Site Status

Tidewater Kidney Specialists - Riverview

Norfolk, Virginia, United States

Site Status

Providence Medical Research Center

Spokane, Washington, United States

Site Status

Countries

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United States

Other Identifiers

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GFB-887-201

Identifier Type: -

Identifier Source: org_study_id

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