A Study of Fresolimumab in Patients With Steroid-Resistant Primary Focal Segmental Glomerulosclerosis (FSGS)

NCT ID: NCT01665391

Last Updated: 2015-08-26

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

36 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-08-31

Study Completion Date

2014-11-30

Brief Summary

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The primary objectives of this trial are as follows:

* to compare the achievement of a partial remission (PR) or complete remission (CR) in urinary protein: creatinine ratio (Up/c ratio) in patients treated with fresolimumab versus placebo
* to compare the safety profile of patients treated with fresolimumab versus placebo

The secondary objectives are as follows:

* To compare the reduction in proteinuria in patients treated with fresolimumab versus placebo
* To evaluate fresolimumab dose-dependent reduction in proteinuria
* To compare the change in renal function (estimated glomerular filtration rate \[eGFR\]) in patients treated with fresolimumab versus placebo
* To evaluate the multiple-dose pharmacokinetics of fresolimumab

Detailed Description

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Conditions

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Primary Focal Segmental Glomerulosclerosis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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fresolimumab 1 mg/kg total body weight

Group Type EXPERIMENTAL

fresolimumab

Intervention Type DRUG

1 mg/kg total body weight administered intravenous (IV)

fresolimumab 4 mg/kg total body weight

Group Type EXPERIMENTAL

fresolimumab

Intervention Type DRUG

4 mg/kg total body weight administered intravenous (IV)

Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo administered to match active treatment group

Interventions

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fresolimumab

1 mg/kg total body weight administered intravenous (IV)

Intervention Type DRUG

fresolimumab

4 mg/kg total body weight administered intravenous (IV)

Intervention Type DRUG

Placebo

Placebo administered to match active treatment group

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* The patient's renal biopsy is consistent with the diagnosis of primary Focal Segmental Glomerulosclerosis (FSGS) including all histological subtypes.
* The patient has an eGFR ≥ 30 mL/min/1.73 m2
* The patient has a urinary total protein:creatinine ratio ≥ 3 mg protein/mg creatinine
* In the opinion of the Investigator, the patient has steroid-resistant FSGS. The patient must have been treated for FSGS with a course of high-dose steroid therapy for a minimum of 4 weeks
* The patient has been treated with an ACEi (angiotensin converting enzyme inhibitor) and/or ARB (angiotensin receptor blocker) at a stable dose for a minimum of 4 weeks prior to Visit 2 (treatment start)

Exclusion Criteria

* The patient has FSGS which in the Investigator's opinion is secondary to another condition
* The patient has been taking prednisone at a dose \> 10 mg/day (or equivalent dose of an alternative glucocorticoid) within 4 weeks prior to Visit 1 (Screening Visit).
* The patient has received any other systemically administered immunosuppressive drugs (other than glucocorticoids) within 8 weeks prior to Visit 1.
* The patient has received rituximab within 6 months prior to Visit 1.
* The patient has a history of organ transplantation.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Genzyme, a Sanofi Company

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Medical Monitor

Role: STUDY_DIRECTOR

Genzyme, a Sanofi Company

Locations

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Investigational Site Number 4008

Birmingham, Alabama, United States

Site Status

Investigational Site Number 4029

Phoenix, Arizona, United States

Site Status

Investigational Site Number 4009

San Francisco, California, United States

Site Status

Investigational Site Number 4023

Stanford, California, United States

Site Status

Investigational Site Number 4005

Atlanta, Georgia, United States

Site Status

Investigational Site Number 4019

Springfield, Illinois, United States

Site Status

Investigational Site Number 4004

Baltimore, Maryland, United States

Site Status

Investigational Site Number 4002

Bethesda, Maryland, United States

Site Status

Investigational Site Number 4022

Boston, Massachusetts, United States

Site Status

Investigational Site Number 4012

Ann Arbor, Michigan, United States

Site Status

Investigational Site Number 4025

Detroit, Michigan, United States

Site Status

Investigational Site Number 4006

Rochester, Minnesota, United States

Site Status

Investigational Site Number 4024

St Louis, Missouri, United States

Site Status

Investigational Site Number 4016

New York, New York, United States

Site Status

Investigational Site Number 4003

New York, New York, United States

Site Status

Investigational Site Number 4014

Rosedale, New York, United States

Site Status

Investigational Site Number 4018

Philadelphia, Pennsylvania, United States

Site Status

Investigational Site Number 4001

Chattanooga, Tennessee, United States

Site Status

Investigational Site Number 4020

Dallas, Texas, United States

Site Status

Investigational Site Number 4027

Houston, Texas, United States

Site Status

Investigational Site Number 4013

Seattle, Washington, United States

Site Status

Investigational Site Number 4104

Porto Alegre, , Brazil

Site Status

Investigational Site Number 4302

Aachen, , Germany

Site Status

Investigational Site Number 4301

Düsseldorf, , Germany

Site Status

Investigational Site Number 4304

Hamburg, , Germany

Site Status

Investigational Site Number 4401

Bari, , Italy

Site Status

Investigational Site Number 4404

Bergamo, , Italy

Site Status

Investigational Site Number 4403

Montichiari, , Italy

Site Status

Investigational Site Number 4405

Reggio Calabria, , Italy

Site Status

Investigational Site Number 4503

Barcelona, , Spain

Site Status

Investigational Site Number 4504

Madrid, , Spain

Site Status

Investigational Site Number 4502

Madrid, , Spain

Site Status

Countries

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United States Brazil Germany Italy Spain

References

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Hodson EM, Sinha A, Cooper TE. Interventions for focal segmental glomerulosclerosis in adults. Cochrane Database Syst Rev. 2022 Feb 28;2(2):CD003233. doi: 10.1002/14651858.CD003233.pub3.

Reference Type DERIVED
PMID: 35224732 (View on PubMed)

Other Identifiers

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2010-019545-25

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

U1111-1139-9082

Identifier Type: OTHER

Identifier Source: secondary_id

DRI12792

Identifier Type: OTHER

Identifier Source: secondary_id

GC1008FSGS03110

Identifier Type: -

Identifier Source: org_study_id

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