First Line Antimicrobials in Children With Complicated Severe Acute Malnutrition

NCT ID: NCT03174236

Last Updated: 2020-05-19

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE3

Total Enrollment

2000 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-09-04

Study Completion Date

2020-12-31

Brief Summary

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Children with severe malnutrition who are admitted sick to hospitals have a high mortality(death rate), usually because of infection. All children with severe malnutrition admitted to hospitals are treated with antibiotics(medication used to kill bacteria). However, the current antibiotics used in hospitals may not be the most effective. It is possible that the antibiotics that are currently used after initial antibiotics should be used first. No studies have been carried out to determine if the current antibiotics used for treating malnourished children who are sick and admitted in hospital are the most appropriate. The aim of this study is to find out if a changed antibiotic system for children with malnutrition is safe, reduces the risk of death and improves nutritional recovery.

Detailed Description

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Children with complicated severe acute malnutrition (SAM) admitted to hospital in sub-Saharan Africa have a case fatality(death rate) between 12% and more than 20%. Because children with SAM may not exhibit the usual signs of infection, WHO guidelines recommend routine antibiotics(medication used to kill bacteria). However, this is based on "low quality evidence". There is evidence that because of bacterial resistance to the currently recommended first-line antibiotics (gentamicin plus ampicillin or penicillin) could be less effective than potential alternatives. Some hospitals in Africa are already increasing use of ceftriaxone as a first-line treatment. However, this is not based on any data that ceftriaxone actually improves outcomes. Of concern is that ceftriaxone use may also lead to increased antimicrobial resistance, including inducing extended spectrum beta-lactamase (ESBL) and other classes of resistance.

A further area where evidence for policy is lacking is the use of metronidazole in severely malnourished children. The WHO guidelines recommend "Metronidazole 7.5 mg/kg every 8 h for 7 days may be given in addition to broad-spectrum antibiotics; however, the efficacy of this treatment has not been established in clinical trials." Metronidazole is effective against anaerobic bacteria, small bowel bacterial overgrowth, Clostridium difficile colitis and also Giardia, which is common amongst children with SAM. Small cohort studies of metronidazole usage suggest there may be benefits for nutritional recovery in malnourished children. However, metronidazole can cause nausea and anorexia, potentially impairing recovery from malnutrition and may also rarely cause liver and neurological toxicity.

This multi-centre clinical trial will assess the efficacy of two interventions, ceftriaxone and metronidazole, on mortality and nutritional recovery in sick, severely malnourished children in a 2x2 factorial design. There will also be an analysis of antimicrobial resistance and an economic analysis. To extend our understanding of metronidazole and ceftriaxone pharmacokinetics, additional pharmacokinetic data for the dosing schedule used in the trial will be collected from 120 participants in a sub-study. The trial will be conducted at Kilifi County Hospital, Coast General Hospital, Mbagathi Hospital in Kenya and Mbale Regional Referral Hospital in Uganda. The trial will assess antimicrobial resistance that is carried by children in their intestines and in invasive bacterial isolates. A further sub-study will examine the relative costs of care for SAM for health facilities and for families, including antimicrobial usage will also be assessed. Clear data on the benefits, risks and costs of these antimicrobials will influence policy on case management and antimicrobial stewardship in this vulnerable population.

Conditions

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Malnutrition Severe Antibiotic Resistance Antibiotic Toxicity

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

FACTORIAL

The trial will investigate two separate antimicrobial interventions in a 2x2 factorial design randomised controlled clinical trial. A factorial design allows more than one intervention to be tested and is useful in assessing a potential package of care. Two randomisations will be made. The two interventions will be analysed separately. Ceftriaxone and metronidazole is an effective and commonly used antibiotic combination, hence major interactions that interfere with efficacy are considered unlikely. However, evidence for interaction between the two interventions will be tested.
Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors
Metronidazole and its placebo will be masked. They will both be contained in similar bottles labelled with sequential study numbers according to a prepared blocked randomisation list before the trial begins. They will also be of similar appearance.

Ceftriaxone and penicillin + gentamicin will not be masked.

Study Groups

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Ceftriaxone

Arm 1 IV Ceftriaxone: Participants in this group receive 80mg/kg IV ceftriaxone once a day for a minimum of 48 hours and a usual maximum of seven days.

Group Type EXPERIMENTAL

Ceftriaxone

Intervention Type DRUG

Ceftriaxone a third-generation cephalosporin. Ceftriaxone is active against a broad spectrum of Gram positive and Gram negative bacteria.

Benzyl penicillin plus gentamicin

Arm 2 IV Benzyl penicillin plus gentamicin (usual care): Participants in this group receive 50 000 U/kg IV benzyl penicillin every six hours for a minimum of two days and a maximum of seven days.

Group Type ACTIVE_COMPARATOR

Benzyl penicillin

Intervention Type DRUG

The currently recommended first-line antibiotics for the treatment of severe acute malnutrition are gentamicin plus ampicillin or penicillin.

Gentamicin

Intervention Type DRUG

The currently recommended first-line antibiotics for the treatment of severe acute malnutrition are gentamicin plus ampicillin or penicillin.

Metronidazole

Arm 1 Metronidazole: Participants receive 10 to 16 mg/kg oral metronidazole twice a day for seven days.

Group Type EXPERIMENTAL

Metronidazole

Intervention Type DRUG

The WHO guidelines recommend that Metronidazole may be given in addition to broad-spectrum antibiotics, "however, the efficacy of this treatment has not been established in clinical trials."

Placebo

Arm 2 Placebo: Participants receive an oral placebo dose to match that for Metronidazole twice a day for seven days.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

Suspension manufactured to match metronidazole

Interventions

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Ceftriaxone

Ceftriaxone a third-generation cephalosporin. Ceftriaxone is active against a broad spectrum of Gram positive and Gram negative bacteria.

Intervention Type DRUG

Benzyl penicillin

The currently recommended first-line antibiotics for the treatment of severe acute malnutrition are gentamicin plus ampicillin or penicillin.

Intervention Type DRUG

Metronidazole

The WHO guidelines recommend that Metronidazole may be given in addition to broad-spectrum antibiotics, "however, the efficacy of this treatment has not been established in clinical trials."

Intervention Type DRUG

Placebo

Suspension manufactured to match metronidazole

Intervention Type OTHER

Gentamicin

The currently recommended first-line antibiotics for the treatment of severe acute malnutrition are gentamicin plus ampicillin or penicillin.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Age 2 months to 13 years inclusive
* Severe malnutrition defined as:
* kwashiorkor at any age or:
* for children between 2 to 5 months: MUAC \<11cm or weight-for length Z score \<-3
* for children between 6 to 59 months: MUAC \<11.5cm or weight-for length Z score \<-3
* for children between 5 to 13 years: MUAC \<11.5cm or BMI-for-age Z score \<-3
* Admitted to hospital and eligible for intravenous antibiotics according to WHO guidelines
* Planning to remain within the hospital catchment area and willing to come for specified visits during the 90 day follow up period
* Informed consent provided by the parents/guardian

Exclusion:

* Known allergy or contraindication to penicillin, gentamicin, ceftriaxone or metronidazole
* A specific and documented clinical indication for another class of antibiotic
* Previously enrolled in this study
Minimum Eligible Age

2 Months

Maximum Eligible Age

13 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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University College, London

OTHER

Sponsor Role collaborator

London School of Hygiene and Tropical Medicine

OTHER

Sponsor Role collaborator

Swansea Trials Unit

UNKNOWN

Sponsor Role collaborator

Kenya Medical Research Institute

OTHER

Sponsor Role collaborator

KEMRI-Wellcome Trust Collaborative Research Program

OTHER

Sponsor Role collaborator

University of Oxford

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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James A Berkely, FRCPCH

Role: PRINCIPAL_INVESTIGATOR

KEMRI/Wellcome Trust Research Programme & University of Oxford

Locations

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Kemri Wellcome Trust Research Programme

Kilifi, Coast Province, Kenya

Site Status

Kilifi County Hospital

Kilifi, Coast, Kenya

Site Status

KEMRI WT Clinical Trials Facility

Kilifi, , Kenya

Site Status

Kilifi County Hospital

Kilifi, , Kenya

Site Status

Coast General Hospital - Study site

Mombasa, , Kenya

Site Status

Mbagathi District Hospital

Nairobi, , Kenya

Site Status

Mbagathi Hospital

Nairobi, , Kenya

Site Status

Mbale Regional Referral Hospital

Mbale, , Uganda

Site Status

Countries

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Kenya Uganda

References

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Related Links

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http://apps.who.int/iris/bitstream/10665/43206/1/9241546700.pdf

Pocket book of hospital care for children Guidelines for the management of common illnesses with limited resources Author: World Health Organization

Other Identifiers

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1-17

Identifier Type: OTHER

Identifier Source: secondary_id

105431/Z/14/Z

Identifier Type: OTHER_GRANT

Identifier Source: secondary_id

KEMRI/SERU/CGMR-C/063/3399

Identifier Type: -

Identifier Source: org_study_id

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