A Phase 3 Study of Pembrolizumab + Epacadostat or Placebo in Subjects With Unresectable or Metastatic Melanoma (Keynote-252 / ECHO-301)

NCT ID: NCT02752074

Last Updated: 2025-08-24

Study Results

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

706 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-06-21

Study Completion Date

2019-08-16

Brief Summary

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The purpose of the study is to assess the efficacy, safety, and tolerability when combining pembrolizumab with epacadostat or placebo in participants with unresectable or metastatic melanoma

Detailed Description

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Conditions

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Melanoma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Pembrolizumab + Epacadostat

Pembrolizumab + Epacadostat

Group Type EXPERIMENTAL

pembrolizumab + epacadostat

Intervention Type DRUG

* Pembrolizumab will be administered intravenously every 3 weeks starting at Day 1 (Week 1)
* Epacadostat will be administered orally daily starting at Day 1 (Week 1)

Pembrolizumab + Placebo

Pembrolizumab + Placebo

Group Type ACTIVE_COMPARATOR

pembrolizumab + placebo

Intervention Type DRUG

* Pembrolizumab will be administered intravenously every 3 weeks starting at Day 1 (Week 1)
* Placebo will be administered orally daily starting at Day 1 (Week 1)

Interventions

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pembrolizumab + epacadostat

* Pembrolizumab will be administered intravenously every 3 weeks starting at Day 1 (Week 1)
* Epacadostat will be administered orally daily starting at Day 1 (Week 1)

Intervention Type DRUG

pembrolizumab + placebo

* Pembrolizumab will be administered intravenously every 3 weeks starting at Day 1 (Week 1)
* Placebo will be administered orally daily starting at Day 1 (Week 1)

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Have histologically or cytologically confirmed melanoma
* Have unresectable Stage III or Stage IV melanoma, as per AJCC staging system not amenable to local therapy
* A minimum of 1 measurable lesion by CT or MRI
* Provide a baseline tumor biopsy
* Eastern Cooperative Oncology Group (ECOG) performance status of 0 to 1

Exclusion Criteria

* Has received prior systemic treatment for unresectable or metastatic melanoma (except BRAF directed therapy)
* Has received prior therapy with an anti-PD-1, anti-PD-L1, anti-PD-L2, anti-CD137, or IDO1 inhibitor or any other antibody or drug specifically targeting checkpoint pathways other than anti-CTLA-4 which is permitted in the adjuvant setting
* Has received prior adjuvant therapy, monoclonal antibody or an investigational agent or device within 4 weeks or 5 half-lives (whichever is longer)
* Has an active infection requiring systemic therapy
* Has known history of human immunodeficiency virus (HIV) (HIV 1/2 antibodies)
* Has known history of or is positive for Hepatitis B or Hepatitis C
* Is pregnant or breastfeeding or expecting to conceive or father children within the projected duration of the study, starting with the screening visit through 120 days after the last dose of study treatment
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Merck Sharp & Dohme LLC

INDUSTRY

Sponsor Role collaborator

Incyte Corporation

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Mark Jones, MD

Role: STUDY_DIRECTOR

Incyte Corporation

Locations

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Birmingham, Alabama, United States

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Scottsdale, Arizona, United States

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Little Rock, Arkansas, United States

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Los Angeles, California, United States

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San Francisco, California, United States

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Santa Barbara, California, United States

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Santa Monica, California, United States

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Aurora, Colorado, United States

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Denver, Colorado, United States

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Washington D.C., District of Columbia, United States

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Fort Lauderdale, Florida, United States

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Jacksonville, Florida, United States

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Ocala, Florida, United States

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West Palm Beach, Florida, United States

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Chicago, Illinois, United States

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Peoria, Illinois, United States

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Iowa City, Iowa, United States

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Kansas City, Kansas, United States

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Lutherville, Maryland, United States

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Boston, Massachusetts, United States

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Ann Arbor, Michigan, United States

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Fridley, Minnesota, United States

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Billings, Montana, United States

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Omaha, Nebraska, United States

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Las Vegas, Nevada, United States

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Rochester, New York, United States

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Charlotte, North Carolina, United States

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Philadelphia, Pennsylvania, United States

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Nashville, Tennessee, United States

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Austin, Texas, United States

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Dallas, Texas, United States

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Salt Lake City, Utah, United States

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Fairfax, Virginia, United States

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Spokane, Washington, United States

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Camperdown, New South Wales, Australia

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Westmead, New South Wales, Australia

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Wollstonecraft, New South Wales, Australia

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Cairns, Queensland, Australia

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Greenslopes, Queensland, Australia

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Kurralta Park, South Australia, Australia

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Melbourne, Victoria, Australia

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Brussels, , Belgium

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Ghent, , Belgium

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North Vancouver, British Columbia, Canada

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Ottawa, Ontario, Canada

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Toronto, Ontario, Canada

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Montreal, Quebec, Canada

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Santiago, , Chile

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Viña del Mar, , Chile

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Aarhus, , Denmark

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Herlev, , Denmark

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Odense C, , Denmark

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Bordeaux, , France

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Lille, , France

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Marseille, , France

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Paris, , France

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Pierre-Bénite, , France

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Reims, , France

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Rennes, , France

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Toulouse, , France

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Villejuif, , France

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Buxtehude, , Germany

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Essen, , Germany

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Hanover, , Germany

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Kiel, , Germany

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Tübingen, , Germany

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Cork, , Ireland

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Dublin, , Ireland

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Galway, , Ireland

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Ramat Gan, , Israel

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Bergamo, , Italy

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Genova, , Italy

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Milan, , Italy

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Napoli, , Italy

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Padua, , Italy

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Siena, , Italy

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Susono, Sunto-gun, Japan

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Asahikawa, , Japan

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Chūō, , Japan

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Fukuoka, , Japan

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Kagoshima, , Japan

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Kumamoto, , Japan

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Kurume, , Japan

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Kyoto, , Japan

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Matsumoto, , Japan

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Nagoya, , Japan

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Niigata, , Japan

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Okayama, , Japan

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Osaka, , Japan

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Sapporo, , Japan

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Sendai, , Japan

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Tokyo, , Japan

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Tsukuba, , Japan

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Chihuahua City, , Mexico

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Distrito Federal, , Mexico

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Mexico City, , Mexico

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Monterrey, , Mexico

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Amsterdam, , Netherlands

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Nijmegen, , Netherlands

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Dunedin, , New Zealand

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Tauranga, , New Zealand

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Warsaw, , Poland

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Istra, , Russia

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Moscow, , Russia

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Saint Petersburg, , Russia

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Johannesburg, Gauteng, South Africa

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Sandton, Gauteng, South Africa

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Groenkloof, Pretoria, South Africa

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Cape Town, Western Cape, South Africa

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Kraaifontein, , South Africa

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Seoul, , South Korea

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Donostia / San Sebastian, Guipuzcoa, Spain

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A Coruña, , Spain

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Barcelona, , Spain

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Donostia / San Sebastian, , Spain

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Madrid, , Spain

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Pamplona, , Spain

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Seville, , Spain

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Valencia, , Spain

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Gothenburg, , Sweden

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Lund, , Sweden

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Stockholm, , Sweden

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Uppsala, , Sweden

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Zurich, Canton of Zurich, Switzerland

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Geneva, , Switzerland

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Lausanne, , Switzerland

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Edinburgh, , United Kingdom

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London, , United Kingdom

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Manchester, , United Kingdom

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Countries

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United States Australia Belgium Canada Chile Denmark France Germany Ireland Israel Italy Japan Mexico Netherlands New Zealand Poland Russia South Africa South Korea Spain Sweden Switzerland United Kingdom

References

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Long GV, Dummer R, Hamid O, Gajewski TF, Caglevic C, Dalle S, Arance A, Carlino MS, Grob JJ, Kim TM, Demidov L, Robert C, Larkin J, Anderson JR, Maleski J, Jones M, Diede SJ, Mitchell TC. Epacadostat plus pembrolizumab versus placebo plus pembrolizumab in patients with unresectable or metastatic melanoma (ECHO-301/KEYNOTE-252): a phase 3, randomised, double-blind study. Lancet Oncol. 2019 Aug;20(8):1083-1097. doi: 10.1016/S1470-2045(19)30274-8. Epub 2019 Jun 17.

Reference Type DERIVED
PMID: 31221619 (View on PubMed)

Provided Documents

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Document Type: Study Protocol and Statistical Analysis Plan

View Document

Other Identifiers

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2015-004991-31

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

INCB 24360-301 (ECHO-301)

Identifier Type: -

Identifier Source: org_study_id

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