Study to Evaluate the Safety,Tolerability, Pharmacokinetics and Exploratory Efficacy Parameters of AIR DNase™in Patients With Cystic Fibrosis Previously Treated With Pulmozyme®

NCT ID: NCT02722122

Last Updated: 2016-09-28

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE2

Total Enrollment

15 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-05-31

Brief Summary

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This study evaluates the Safety,Tolerability, Pharmacokinetics and Exploratory Efficacy Parameters of AIR DNase™in Patients with Cystic Fibrosis previously treated with Pulmozyme®.

Detailed Description

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This is a proof-of-concept, open label study, to evaluate the safety, tolerability, pharmacokinetics and exploratory efficacy of 2.5 mg AIR DNase TM administered once daily for 28 days via inhalation to Cystic Fibrosis subjects who have previously been treated with Pulmozyme®.

This multicenter study will be conducted in approximately 10 sites and will enroll up to 15 subjects.

Conditions

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Cystic Fibrosis

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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AIR DNase™ 2.5 mg

2.5 mg of AIR DNase™ administered once daily via inhalation for 28 days

Group Type EXPERIMENTAL

AIR DNase™

Intervention Type DRUG

Interventions

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AIR DNase™

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Age ≥ 12 years of age (inclusive) at the time of screening
2. Weight ≥ 36 kg
3. Prior confirmed diagnosis of CF
4. At least 4 months treatment with Pulmozyme® prior to screening.
5. The subject is medically stable for at least one month prior to the screening visit.
6. Stable inhaled regimen of either: antibiotics, steroids, hypertonic saline at least four months prior to screening visit.
7. FEV1 of \>40% and \<90% and FVC ≥ 40% of predicted normal for age, gender, and height at screening .
8. Female and male subjects whose co-partners are of child bearing potential must agree to use two medically acceptable methods of contraception, not including the rhythm method.
9. Be willing and able to adhere to the study visit schedule and other protocol requirements
10. Be willing and able to provide voluntary written informed consent

Exclusion Criteria

1. Has a history of lung transplantation.
2. Female subjects who are pregnant or lactating.
3. History of severe or unexplained adverse reactions during aerosol delivery of any medicinal product.
4. History or presence of hypersensitivity or reaction to inhaled proteins.
5. Participation in another clinical trial within 60 days prior to screening.
6. Presence of any medical, emotional, behavioral or psychological condition that in the judgment of the Investigator would interfere with the subject's safety or compliance with the requirements of the study.
7. Have positive serology for human immunodeficiency virus (HIV) or Hepatitis B or Hepatitis C infection.
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Protalix

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Einat Dekel, DVM

Role: STUDY_DIRECTOR

Sr. Director Clinical Development

Locations

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Carmel MC

Haifa, , Israel

Site Status RECRUITING

Rambam MC

Haifa, , Israel

Site Status RECRUITING

Hadassah MC

Jerusalem, , Israel

Site Status RECRUITING

Schneider MC

Petah Tikva, , Israel

Site Status RECRUITING

Sheba MC

Ramat Gan, , Israel

Site Status RECRUITING

Countries

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Israel

Central Contacts

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Einat Dekel, DVM

Role: CONTACT

Yasmin Omer Azulay, MPH

Role: CONTACT

Facility Contacts

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Michal Shteinberg, M.D.

Role: primary

04-8250564

Lea Bentur, M.D.

Role: primary

04-7774360

Eitan Kerem, M.D.

Role: primary

02-6777749

Hanna Blau, M.D.

Role: primary

03-9253803

Ori Efrati, M.D.

Role: primary

03-5302884

Other Identifiers

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PB-110-CF02

Identifier Type: -

Identifier Source: org_study_id

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