Nasal Inhalation of Pulmozyme in Patients With Cystic Fibrosis and Chronic Rhinosinusitis

NCT ID: NCT00534079

Last Updated: 2014-12-04

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

23 participants

Study Classification

INTERVENTIONAL

Study Start Date

2007-09-30

Study Completion Date

2009-02-28

Brief Summary

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Rhinosinusitis disorders are often associated with Cystic Fibrosis. They can restrict quality of life enormously and give cause to repeated ENT surgery. The basic defect in CF is a dysfunction of chloride channels in exocrine glands, leading to retention of secretions and consecutive chronic inflammation with bacterial superinfections.

The prospective placebo controlled cross-over study aims at the evaluation of a nasally inhalation of Pulmozyme with respect to mucus retention and resulting inflammation.

Detailed Description

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Conditions

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Cystic Fibrosis Rhinosinusitis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

CROSSOVER

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Dornase alfa

28 days of sinonasal inhalation (Pari Sinus)

Group Type EXPERIMENTAL

Dornase alfa (Pulmozyme)

Intervention Type DRUG

1 x 2,5 ml per day, inhalation use, for 28 days

isotonic saline

Intervention Type DRUG

1 x 2,5 ml per day, inhalation use, for 28 days

isotonic saline

28 days of sinonasal inhalation (Pari Sinus)

Group Type PLACEBO_COMPARATOR

Dornase alfa (Pulmozyme)

Intervention Type DRUG

1 x 2,5 ml per day, inhalation use, for 28 days

isotonic saline

Intervention Type DRUG

1 x 2,5 ml per day, inhalation use, for 28 days

Interventions

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Dornase alfa (Pulmozyme)

1 x 2,5 ml per day, inhalation use, for 28 days

Intervention Type DRUG

isotonic saline

1 x 2,5 ml per day, inhalation use, for 28 days

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Subject has a confirmed diagnosis of cystic fibrosis based on: 3 positive sweat chloride tests and/or genetic characterisation
* Subject is 5 years of age or older
* Subject has chronic or recurrent rhinosinusitic disorders
* Subject is able to comply with the procedures scheduled in the protocol
* Women of childbearing potential are only included into the study, if they are using an effective method of birth control during the protocol (e.g. implants, combined oral contraceptives, injectables, some IUDs, sexual abstinence or vasectomised partner)

Exclusion Criteria

* Subject has a critical condition defined as: FEV1 \< 30% and / or SaO2 \< 93% without O2-substitution; need of O2-substitution
* Subject had an ENT surgery within 6 months prior to study
* Subject shows signs of nasal bleeding
* Subject has an ear drum perforation
* Subject had an acute rhinosinusitis or a pulmonary exacerbation at study entry with need of additional systemic antibiotic therapy
* Subject has a new therapy with nasal topic steroids during treatment interval
* Subject has a new systemic steroid therapy
* Subject is unlikely to comply with the procedures scheduled in the protocol
* Subject has a known allergic reaction to the medication
* Subject is pregnant or breastfeeding
* Patient participates in another clinical trial within 30 days prior to study entry or 30 days after end of the study.
Minimum Eligible Age

5 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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University of Jena

OTHER

Sponsor Role lead

Responsible Party

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PD Dr. Jochen G. Mainz

Head of CF Center

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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Jochen Mainz, M.D.

Role: STUDY_CHAIR

University of Jena

Locations

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Universitäts-Kinderklinik

Tübingen, Baden-Würtemberg, Germany

Site Status

Mukoviszidosezentrum der Friedrich-Schiller-Universität

Jena, Thuringia, Germany

Site Status

Countries

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Germany

References

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Mainz JG, Michl R, Arnold C. Response to Karadag. J Cyst Fibros. 2014 Sep;13(5):602-3. doi: 10.1016/j.jcf.2014.07.005. Epub 2014 Jul 28. No abstract available.

Reference Type BACKGROUND
PMID: 25081561 (View on PubMed)

Mainz JG, Schien C, Schiller I, Schadlich K, Koitschev A, Koitschev C, Riethmuller J, Graepler-Mainka U, Wiedemann B, Beck JF. Sinonasal inhalation of dornase alfa administered by vibrating aerosol to cystic fibrosis patients: a double-blind placebo-controlled cross-over trial. J Cyst Fibros. 2014 Jul;13(4):461-70. doi: 10.1016/j.jcf.2014.02.005. Epub 2014 Mar 1.

Reference Type RESULT
PMID: 24594542 (View on PubMed)

Other Identifiers

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pulmozyme-nasal-cf

Identifier Type: -

Identifier Source: org_study_id