Study of Denufosol Tetrasodium Inhalation Solution in Patients With Cystic Fibrosis (CF) Lung Disease

NCT ID: NCT00625612

Last Updated: 2015-11-02

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

466 participants

Study Classification

INTERVENTIONAL

Study Start Date

2008-02-29

Study Completion Date

2010-10-31

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The purpose of this trial is to evaluate the safety and effectiveness of one dose strength of Denufosol compared to placebo in patients with CF and a predicted FEV1 of greater than or equal to 75% but less than or equal to 110% predicted.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Cystic Fibrosis

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

2

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo - 0.9% w/v sodium chloride solution, three times daily for twelve months.

1

Denufosol Tetrasodium (INS37217) Inhalation Solution

Group Type EXPERIMENTAL

Denufosol Tetrasodium (INS37217) Inhalation Solution

Intervention Type DRUG

Drug: Denufosol Tetrasodium (INS37217) Inhalation Solution, Denufosol 60 mg is administered as an inhalation solution, three times daily for twelve months.

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Denufosol Tetrasodium (INS37217) Inhalation Solution

Drug: Denufosol Tetrasodium (INS37217) Inhalation Solution, Denufosol 60 mg is administered as an inhalation solution, three times daily for twelve months.

Intervention Type DRUG

Placebo

Placebo - 0.9% w/v sodium chloride solution, three times daily for twelve months.

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Have confirmed diagnosis of cystic fibrosis
* Have FEV1 of greater than or equal to 75% but less than or equal to 110%predicted normal for age, gender and height
* Be able to reproducibly perform spirometry
* Be clinically stable for at least 4 weeks before screening

Exclusion Criteria

* Have abnormal renal or liver function
* Have lung transplant
* Unable to discontinue use of hypertonic saline
* Participated in Inspire trial 08-108
Minimum Eligible Age

5 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Merck Sharp & Dohme LLC

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Felix Ratjen, MD, PhD

Role: PRINCIPAL_INVESTIGATOR

Toronto, Canada

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

Pediatric Breathing Disorders

Anchorage, Alaska, United States

Site Status

Phoenix Childrens Hospital

Phoenix, Arizona, United States

Site Status

University of Arizona/Arizona Health Sciences

Tucson, Arizona, United States

Site Status

Childrens Hospital of Los Angeles

Los Angeles, California, United States

Site Status

USC Cystic Fibrosis Center

Los Angeles, California, United States

Site Status

Bay Area Pediatric Pulmonary

Oakland, California, United States

Site Status

Kaiser Permanente Medical Center

Oakland, California, United States

Site Status

Children's Hospital of Orange County

Orange, California, United States

Site Status

Sanford University

Palo Alto, California, United States

Site Status

Capital Allergy & Respiratory Disease Center

Sacramento, California, United States

Site Status

UCSD Medical Center - Hillcrest & Thornton Hospitals

San Diego, California, United States

Site Status

UCSD Medical Center - Hillcrest and Thornton Hospitals

San Diego, California, United States

Site Status

Pediatric Diagnostic Center

Ventura, California, United States

Site Status

Yale School of Medicine

New Haven, Connecticut, United States

Site Status

Alfred I. duPont Hospital for Children

Wilmington, Delaware, United States

Site Status

Children's National Medical Center

Washington D.C., District of Columbia, United States

Site Status

Shands at University of Florida

Gainesville, Florida, United States

Site Status

Nemours Children's Clinic

Jacksonville, Florida, United States

Site Status

Nemours Children's Clinic

Pensacola, Florida, United States

Site Status

Pediatric Pulmonary Associates

St. Petersburg, Florida, United States

Site Status

Tampa General Hospital

Tampa, Florida, United States

Site Status

St. Mary's Medical Center

West Palm Beach, Florida, United States

Site Status

Emory University

Atlanta, Georgia, United States

Site Status

Children's Healthcare of Atlanta at Scottish Rite

Atlanta, Georgia, United States

Site Status

Medical College of Georgia

Augusta, Georgia, United States

Site Status

Children's Memorial Hospital

Chicago, Illinois, United States

Site Status

Cystic Fibrosis Institute

Glenview, Illinois, United States

Site Status

James Whitcomb RIley Hospital for Children

Indianapolis, Indiana, United States

Site Status

University of Kansas Medical Center

Kansas City, Kansas, United States

Site Status

Via Christa Research

Wichita, Kansas, United States

Site Status

University of Kentucky

Lexington, Kentucky, United States

Site Status

Tulane University Medical Center

New Orleans, Louisiana, United States

Site Status

Maine Medical Center

Portland, Maine, United States

Site Status

Johns Hopkins University School of Medicine

Baltimore, Maryland, United States

Site Status

Boston Children's Hospital

Boston, Massachusetts, United States

Site Status

University of Michigan Health System

Ann Arbor, Michigan, United States

Site Status

Spectrum Health Hospitals

Grand Rapids, Michigan, United States

Site Status

Children's Health Care

Minneapolis, Minnesota, United States

Site Status

University of Minnesota - Farview

Minneapolis, Minnesota, United States

Site Status

Childrens Mercy Hospital

Kansas City, Missouri, United States

Site Status

Saint Louis University

St Louis, Missouri, United States

Site Status

University of Nebraska Medical Center

Omaha, Nebraska, United States

Site Status

Children's Lung Specialists

Las Vegas, Nevada, United States

Site Status

Saint Barnabas Medical Center

Livingston, New Jersey, United States

Site Status

Monmouth Medical Center

Long Branch, New Jersey, United States

Site Status

The Respiratory Center for Children

Morristown, New Jersey, United States

Site Status

Albany Medical College

Albany, New York, United States

Site Status

Cystic Fibrosis Center of Schneider Children's Hospital

Great Neck, New York, United States

Site Status

New York Medical College

Hawthorne, New York, United States

Site Status

Long Island Jewish Medical Center

New Hyde Park, New York, United States

Site Status

St. Vincent's Catholic Medical Center

New York, New York, United States

Site Status

Columbia University Medical Center

New York, New York, United States

Site Status

University of Rochester

Rochester, New York, United States

Site Status

SUNY Upstate Medical University Hospital

Syracuse, New York, United States

Site Status

Duke University Medical Center

Durham, North Carolina, United States

Site Status

St. Alexius Medical Center

Bismarck, North Dakota, United States

Site Status

Children's Hospital Medical Center of Akron

Akron, Ohio, United States

Site Status

Cincinnati Children's Hospital Medical Center

Cincinnati, Ohio, United States

Site Status

University Hospital of Cleveland

Cleveland, Ohio, United States

Site Status

Columbus Children's Hospital

Columbus, Ohio, United States

Site Status

The Children's Medical Center of Dayton

Dayton, Ohio, United States

Site Status

Toledo Children's Hospital

Toledo, Ohio, United States

Site Status

Santiago Reyes, MD

Oklahoma City, Oklahoma, United States

Site Status

Oregon Health and Science University

Portland, Oregon, United States

Site Status

PennState Milton S Hershey Med

Hershey, Pennsylvania, United States

Site Status

The Childrens Hospital of Philadelphia

Philadelphia, Pennsylvania, United States

Site Status

Childrens Hospital of Pittsburgh

Pittsburgh, Pennsylvania, United States

Site Status

Medical University of South Carolina

Charleston, South Carolina, United States

Site Status

Sanford Childrens' Specialty Clinic

Sioux Falls, South Dakota, United States

Site Status

East Tennesse Children's Hospital - Pediatric Pulmonary and Respiratory Care

Knoxville, Tennessee, United States

Site Status

Austin Children's Chest Associates

Austin, Texas, United States

Site Status

Dallas Cystic Fibrosis Center

Dallas, Texas, United States

Site Status

Baylor College of Medicine

Houston, Texas, United States

Site Status

University of Utah

Salt Lake City, Utah, United States

Site Status

University of Virginia

Charlottesville, Virginia, United States

Site Status

Children's Hospital of the King's Daughters

Norfolk, Virginia, United States

Site Status

Naval Medical Center Portsmouth

Portsmouth, Virginia, United States

Site Status

Pediatric Pulmonary Clinic

Richmond, Virginia, United States

Site Status

West Virginia University

Morgantown, West Virginia, United States

Site Status

University of Wisconsin Hospital and Clinics

Madison, Wisconsin, United States

Site Status

University of Wisconsin School of Medicine and Pulbic Health

Madison, Wisconsin, United States

Site Status

John Hunter Hospital - Adults

New Lambton, New South Wales, Australia

Site Status

Westmead Adults

Westmead, New South Wales, Australia

Site Status

Prince Charles Hospital

Chermside, Queensland, Australia

Site Status

Royal Brisbane Children's Hospital

Herston, Queensland, Australia

Site Status

Royal Adelaide Hospital

Adelaide, South Australia, Australia

Site Status

Monash Medical Centre

Clayton, Victoria, Australia

Site Status

Alfred Hospital

Melbourne, Victoria, Australia

Site Status

Respiratory Medicine

Parkville, Victoria, Australia

Site Status

Sire Charles Gairdner Hospital

Nedlands, Western Australia, Australia

Site Status

Princess Margaret Hospital for Children

Perth, Western Australia, Australia

Site Status

The Children's Hospital of Westmead

Westmead, , Australia

Site Status

University of Calgary, Alberta Children's Hospital

Calgary, Alberta, Canada

Site Status

St. Paul's Hospital

Vancouver, British Columbia, Canada

Site Status

British Columbia Children's Hospital

Vancouver, British Columbia, Canada

Site Status

Eastern Health

St. John's, Newfoundland and Labrador, Canada

Site Status

Eastern Health

St. John's, Newfoundland and Labrador, Canada

Site Status

Queen Elizabeth II Health Sciences Centre

Halifax, Nova Scotia, Canada

Site Status

McMaster University

Hamilton, Ontario, Canada

Site Status

A. Lyttle Research COmpany

London, Ontario, Canada

Site Status

Ottawa Hospital

Ottawa, Ontario, Canada

Site Status

University of Toronto

Toronto, Ontario, Canada

Site Status

Hospital for Sick Children

Toronto, Ontario, Canada

Site Status

Centre Mere-Enfant du CHUL

Montreal, Quebec, Canada

Site Status

Green Lane Clinical Centre (NZ)

Auckland, , New Zealand

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Australia Canada New Zealand

References

Explore related publications, articles, or registry entries linked to this study.

Ratjen F, Durham T, Navratil T, Schaberg A, Accurso FJ, Wainwright C, Barnes M, Moss RB; TIGER-2 Study Investigator Group. Long term effects of denufosol tetrasodium in patients with cystic fibrosis. J Cyst Fibros. 2012 Dec;11(6):539-49. doi: 10.1016/j.jcf.2012.05.003. Epub 2012 Jun 8.

Reference Type DERIVED
PMID: 22682898 (View on PubMed)

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

08-110

Identifier Type: -

Identifier Source: secondary_id

P08640

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.