Safety and Anti-leukemic Activity of Vodobatinib (K0706) for Treatment of Ph+ CML Resistant/Intolerant to ≥3 Prior CML Therapies

NCT ID: NCT02629692

Last Updated: 2024-07-31

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE1/PHASE2

Total Enrollment

122 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-06-27

Study Completion Date

2026-08-31

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

Phase 1/2 study to determine safety, tolerability, pharmacokinetics, and anti-leukemic activity of Vodobatinib (K0706) in treatment-refractory/intolerant CML

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Part A ( for Healthy volunteers) of the study is completed.

Part B dose-escalation study is completed. Recruitment in dose expansion is completed.

Part C study in subjects with treatment-resistant/intolerant is ongoing for the enrolled subjects.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Healthy (For Part A) Chronic Myeloid Leukemia (for Part B and C)

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

NA

Intervention Model

SINGLE_GROUP

Part A: Single ascending dose in healthy volunteers.

Part B: Multiple ascending dose safety and tolerability study in subjects with CML or Ph + ALL.

Part C: Efficacy and safety study in subjects with treatment-resistant CML
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Part B and C: Single arm (Open-label)

Part A: 2 arms: Investigational agent arm and Placebo arm (Double-blind).

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Vodobatinib (K0706) capsules

Group Type EXPERIMENTAL

Vodobatinib (K0706) capsules

Intervention Type DRUG

Part A: Vodobatinib (K0706) capsules in single ascending doses.

Part B: Oral Vodobatinib (K0706) capsules in multiple ascending doses, once daily.

Part C: Oral Vodobatinib (K0706) capsules at recommended phase 2 dose of 174 mg, once daily.

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Vodobatinib (K0706) capsules

Part A: Vodobatinib (K0706) capsules in single ascending doses.

Part B: Oral Vodobatinib (K0706) capsules in multiple ascending doses, once daily.

Part C: Oral Vodobatinib (K0706) capsules at recommended phase 2 dose of 174 mg, once daily.

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Willing and able to give written, and dated, informed consent
* Male or female aged ≥ 18 years
* Willing and able to comply with the scheduled visits
* Eastern Cooperative Oncology Group (ECOG) performance status of 0, 1, or 2
* Subjects diagnosed with Ph+ CML-CP, Ph+ CML-AP, Ph+ CML-BP, who are resistant and/or intolerant to ≥ 3 prior TKIs one of which includes ponatinib (Part C).

Exclusion Criteria

* Presence of T315I (PART C)
* Any major surgery, as determined by the Investigator, within 4 weeks of IMP administration
* Inability to undergo venipuncture and/or tolerate venous access
* Positive exclusion tests: urine pregnancy tests (if applicable), HIV, hepatitis B surface antigen, or hepatitis C virus
* Known or suspected history of significant drug abuse as judged by the Investigator
* Received any other investigational agent within 30 days or a washout of at least 5 half-lives, whichever is longer of IMP administration
* Subjects who are eligible for potentially curative therapy that is available, including hematopoietic stem cell transplant
* Another primary malignancy within the past 3 years or earlier (except for adequately treated non-melanoma skin cancer or cervical cancer in situ
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Sun Pharma Advanced Research Company Limited

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

The Oncology Institute of Hope and Innovation, Innovative Clinical Research Institute

Downey, California, United States

Site Status

UCLA Hematologic Malignancy Program

Los Angeles, California, United States

Site Status

Mayo Clinic

Jacksonville, Florida, United States

Site Status

Board of Regents of the University System of Georgia

Augusta, Georgia, United States

Site Status

Memorial Sloan Kettering Cancer Center - MAIN

New York, New York, United States

Site Status

Baylor University Medical Center

Dallas, Texas, United States

Site Status

MD Anderson Cancer Center

Houston, Texas, United States

Site Status

Huntsman Cancer Institute University of Utah

Salt Lake City, Utah, United States

Site Status

Cliniques Universitaires Saint-Luc

Brussels, , Belgium

Site Status

Institut Paoli Calmettes

Marseille, Bouches-du-Rhône, France

Site Status

Centre Léon Bérard

Lyon, Rhone, France

Site Status

Centre Hospitalier Lyon Sud

Pierre-Bénite, Rhone, France

Site Status

Debreceni Egyetem

Debrecen, , Hungary

Site Status

Prince Aly Khan Hospital

Mumbai, Maharashtra, India

Site Status

Tata Memorial Hospital

Mumbai, Maharashtra, India

Site Status

Sahyadri Specialty Hospital

Pune, Maharashtra, India

Site Status

Meenakshi Mission Hospital & Research Centre

Madurai, Tamil Nadu, India

Site Status

Tata Medical Centre

Kolkata, West Bengal, India

Site Status

Istituto Scientifico Romagnolo Per Lo Studio e La Cura Dei Tumori

Meldola, Forli - Cesena, Italy

Site Status

Azienda Socio Sanitaria Territoriale di Monza (Presidio San Gerardo)

Monza, Milano, Italy

Site Status

Fondazione IRCCS CA' Granda Ospedale Maggiore Policlinico

Milan, , Italy

Site Status

Ospedale Sant'Eugenio

Roma, , Italy

Site Status

Azienda Ospedaliera Universitaria Policlinico Umberto I - Università di Roma La Sapienza

Roma, , Italy

Site Status

Spitalul Clinic Colentina

Bucharest, , Romania

Site Status

Institutul Oncologic "Prof. Dr. Ion Chiricuta" Cluj-Napoca

Cluj-Napoca, , Romania

Site Status

Spitalul Clinic Municipal Filantropia Craiova

Craiova, , Romania

Site Status

The Catholic University of Korea, Seoul St. Mary's Hospital

Seoul, Gyeonggi-do, South Korea

Site Status

The Catholic University of Korea, Seoul St. Mary's Hospital

Seoul, Gyeonggi-do, South Korea

Site Status

Uijeongbu Eulji Medical Center, Eulji University

Gyeonggi-do, , South Korea

Site Status

ICO Badalona - Hospital Universitari Germans Trias i Pujol

Badalona, Barcelona, Spain

Site Status

Hospital Universitari Vall d'Hebron

Barcelona, , Spain

Site Status

Hospital Universitario Ramon y Cajal

Madrid, , Spain

Site Status

Hospital Universitario 12 de Octubre

Madrid, , Spain

Site Status

Hospital Universitario La Paz

Madrid, , Spain

Site Status

Hacettepe University Hospital

Altındağ, , Turkey (Türkiye)

Site Status

Kayseri Erciyes University Hospital

Kayseri, , Turkey (Türkiye)

Site Status

King's College Hospital

London, Greater London, United Kingdom

Site Status

Hammersmith Hospital

London, Greater London, United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Belgium France Hungary India Italy Romania South Korea Spain Turkey (Türkiye) United Kingdom

References

Explore related publications, articles, or registry entries linked to this study.

Cortes JE, Kim DW, Saikia T, Khattry N, Rathnam K, Alvarado Y, Hannah G, Tantravahi SK, Apperley JF, Charbonnier A, Garcia-Gutierrez V, Lucchesi A, Dima D, Illes A, Popov VM, Abruzzese E, Nag A, Apte S, Badar T, Yao SL, Saxena U, Sreenivasan J, Inamdar S, Chimote G, Nicolini FE. Vodobatinib for patients with Philadelphia chromosome-positive chronic myeloid leukaemia resistant or intolerant to multiple lines of previous therapy: an open-label, multicentre, phase 1/2 trial. Lancet Haematol. 2025 Mar;12(3):e201-e213. doi: 10.1016/S2352-3026(24)00354-5. Epub 2025 Feb 7.

Reference Type DERIVED
PMID: 39929221 (View on PubMed)

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

CLR_15_03 V 12 Amendment 12

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

Study in Patients With Chronic Leukemia
NCT03807479 TERMINATED PHASE2
KRT-232 and TKI Study in Chronic Myeloid Leukemia
NCT04835584 RECRUITING PHASE1/PHASE2