A Phase II Study of Dasatinib in Children and Adolescents With Newly Diagnosed Chronic Phase Chronic Myelogenous Leukemia (CML) or With Ph+ Leukemias Resistant or Intolerant to Imatinib

NCT ID: NCT00777036

Last Updated: 2025-08-29

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

133 participants

Study Classification

INTERVENTIONAL

Study Start Date

2009-03-20

Study Completion Date

2025-01-27

Brief Summary

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The purpose of this study is to determine whether dasatinib is safe and effective in children and adolescents with newly diagnosed chronic myeloid leukemia (CML), or in children with Ph+ acute lymphoblastic leukemia (ALL), accelerated or blast phases CML who relapse after imatinib or who are resistant or intolerant to imatinib. The side effects of this oral investigational drug in children and adolescents will be evaluated

Detailed Description

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Conditions

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Leukemia

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Cohort 1: Imatinib-resistant/intolerant CP-CML

Dasatinib 60 mg/m² tablet every day (QD) \[with a maximum dose of 100 mg QD for subjects with high BSA\] for minimum of 24 months, may continue as long as deriving clinical benefit

OR

Dasatinib 72 mg/m² powder for oral suspension (PFOS) QD \[with a maximum dose of 120 mg QD for subjects with high BSA\] for minimum of 24 months, may continue as long as deriving clinical benefit

Group Type EXPERIMENTAL

Dasatinib

Intervention Type DRUG

Cohort 2: Ph+ALL or AP- or BP-CML

Dasatinib 80 mg/m² tablet QD \[with a maximum dose of 140 mg QD for subjects with high BSA\] for minimum of 24 months, may continue as long as deriving clinical benefit

OR

Dasatinib 96 mg/m² PFOS QD \[with a maximum dose of 170 mg QD for subjects with high BSA\] for minimum of 24 months, may continue as long as deriving clinical benefit

Group Type EXPERIMENTAL

Dasatinib

Intervention Type DRUG

Cohort 3: Newly diagnosed, treatment naïve CP-CML

Dasatinib 60 mg/m² tablet QD \[with a maximum dose of 100 mg QD for subjects with high BSA\] for minimum of 24 months, may continue as long as deriving clinical benefit

OR

Dasatinib 72 mg/m² PFOS QD \[with a maximum dose of 120 mg QD for subjects with high BSA\] for minimum of 24 months, may continue as long as deriving clinical benefit

Group Type EXPERIMENTAL

Dasatinib

Intervention Type DRUG

Interventions

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Dasatinib

Intervention Type DRUG

Other Intervention Names

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Sprycel (BMS-354825)

Eligibility Criteria

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Inclusion Criteria

* CP-CML who prove resistant or intolerant to imatinib (Cohort 1)
* Ph+ ALL, AP-CML, or BP-CML who are resistant or intolerant to or who relapse after imatinib therapy (Cohort 2)
* Newly diagnosed, treatment naive CP-CML (Cohort 3)
* Lansky or Karnofsky scale \>50
* Life expectancy ≥12 weeks
* Adequate hepatic and renal function
* Written informed consent
* Target Population for the PK substudy must obtain written informed consent from subject, or from parents or legal guardians for minor subjects, according to local law and regulation
* Target Population for the PK substudy subjects must have CP-CML and be taking daily dasatinib (tablets or PFOS) either as part of Cohort 1 or Cohort 3 of this protocol. Patients receiving commercial dasatinib tablets outside of this protocol may be invited to participate in this PK substudy
* Target Population for the PK substudy subjects with CP-CML who are tolerating dasatinib tablet dose of at least 60 mg/m2 or dasatinib PFOS dose of at least 72 mg/m2
* Target Population for the PK substudy prior exposure to imatinib or other TKI therapy is permissible

Exclusion Criteria

* Eligibility for potentially-curative therapy including hematopoietic stem-cell transplantation
* Symptomatic CNS involvement (other than signs and symptoms caused by leptomeningeal disease)
* Isolated extramedullary disease
* Prior therapy with Dasatinib
* Target Population for the PK substudy subjects are not allowed to use proton pump inhibitors, H2 antagonists, CYP3A4 inhibitors and inducers when entering the PK substudy
Minimum Eligible Age

1 Day

Maximum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Bristol-Myers Squibb

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Bristol-Myers Squibb

Role: STUDY_DIRECTOR

Bristol-Myers Squibb

Locations

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Local Institution

Birmingham, Alabama, United States

Site Status

Local Institution - 0005

Phoenix, Arizona, United States

Site Status

Phoenix Children'S Hospital

Phoenix, Arizona, United States

Site Status

Jonathan Jaques Children'S Cancer Center

Long Beach, California, United States

Site Status

Jonathan Jaques Children'S Cancer Center

Long Beach, California, United States

Site Status

Local Institution - 0001

Long Beach, California, United States

Site Status

Children'S Hospital Of Orange County

Orange, California, United States

Site Status

Local Institution - 0024

Orange, California, United States

Site Status

Children'S Hospital

Aurora, Colorado, United States

Site Status

Local Institution - 0004

Aurora, Colorado, United States

Site Status

Children's Healthcare Of Atlanta - Egleston

Atlanta, Georgia, United States

Site Status

Local Institution - 047

Atlanta, Georgia, United States

Site Status

Children's Hospital of Chicago

Chicago, Illinois, United States

Site Status

Local Institution - 0072

Chicago, Illinois, United States

Site Status

Local Institution

Chicago, Illinois, United States

Site Status

Dana Faber Cancer Institute

Boston, Massachusetts, United States

Site Status

Dana Farber Cancer Institute.

Boston, Massachusetts, United States

Site Status

Local Institution - 0040

Boston, Massachusetts, United States

Site Status

Stephen D. Hassenfeld Children'S Center

New York, New York, United States

Site Status

Local Institution - 0061

New York, New York, United States

Site Status

Memorial Sloan Kettering Cancer Center

New York, New York, United States

Site Status

Memorial Sloan Kettering Nassau

New York, New York, United States

Site Status

Oregon Health & Sci Univ

Portland, Oregon, United States

Site Status

Local Institution - 0002

Portland, Oregon, United States

Site Status

Oregon Health & Sci Univ

Portland, Oregon, United States

Site Status

Children'S Hospital Of Philadelphia

Philadelphia, Pennsylvania, United States

Site Status

Local Institution - 0014

Philadelphia, Pennsylvania, United States

Site Status

Children'S Hospital Of Pittsburgh

Pittsburgh, Pennsylvania, United States

Site Status

Local Institution - 0003

Pittsburgh, Pennsylvania, United States

Site Status

Local Institution - 0035

Houston, Texas, United States

Site Status

MD Anderson Cancer Center

Houston, Texas, United States

Site Status

Local Institution - 0048

Houston, Texas, United States

Site Status

Texas Children'S Cancer Center

Houston, Texas, United States

Site Status

Local Institution - 0028

Seattle, Washington, United States

Site Status

Seattle Children'S

Seattle, Washington, United States

Site Status

Local Institution - 0043

Bunos Aires, Buenos Aires, Argentina

Site Status

Local Institution

Bunos Aires, Buenos Aires, Argentina

Site Status

Hospital Nacional Profesor Alejandro Posadas

El Palomar, Buenos Aires, Argentina

Site Status

Local Institution - 0049

El Palomar, Buenos Aires, Argentina

Site Status

Local Institution - 0042

Córdoba, , Argentina

Site Status

Local Institution

Córdoba, , Argentina

Site Status

Local Institution - 065

Randwick, New South Wales, Australia

Site Status

Local Institution

Randwick, New South Wales, Australia

Site Status

Local Institution - 069

Westmead, New South Wales, Australia

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Local Institution

Westmead, New South Wales, Australia

Site Status

Local Institution - 0064

Sth Brisbane, Queensland, Australia

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Sth Brisbane, Queensland, Australia

Site Status

Local Institution - 067

North Adelaide, South Australia, Australia

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North Adelaide, South Australia, Australia

Site Status

Local Institution - 0066

Parkville, Victoria, Australia

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Local Institution

Parkville, Victoria, Australia

Site Status

Local Institution - 0021

Curitiba, Paraná, Brazil

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Local Institution

Curitiba, Paraná, Brazil

Site Status

Local Institution - 0022

Porto Alegre, Rio Grande do Sul, Brazil

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Local Institution

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Local Institution - 0019

São Paulo, São Paulo, Brazil

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Local Institution - 0020

Campinas, , Brazil

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Local Institution

Campinas, , Brazil

Site Status

Local Institution - 0039

São Paulo, , Brazil

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Local Institution

São Paulo, , Brazil

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Local Institution

São Paulo, , Brazil

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Alberta Children'S Hospital

Calgary, Alberta, Canada

Site Status

Local Institution - 0079

Calgary, Alberta, Canada

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Local Institution - 0078

Edmonton, Alberta, Canada

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Stollery Children'S Hospital

Edmonton, Alberta, Canada

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Bc Children'S Hospital

Vancouver, British Columbia, Canada

Site Status

Local Institution - 077

Vancouver, British Columbia, Canada

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Iwk Health Centre

Halifax, Nova Scotia, Canada

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Local Institution - 073

Halifax, Nova Scotia, Canada

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Children'S Hospital Of Eastern Ontario

Ottawa, Ontario, Canada

Site Status

Local Institution - 086

Ottawa, Ontario, Canada

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Local Institution - 076

Toronto, Ontario, Canada

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The Hospital For Sick Children

Toronto, Ontario, Canada

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Chu Ste-Justine

Montreal, Quebec, Canada

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Local Institution - 080

Montreal, Quebec, Canada

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Local Institution - 0030

Lyon, , France

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Lyon, , France

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Local Institution - 0032

Nantes, , France

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Nantes, , France

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Local Institution - 0037

Paris, , France

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Paris, , France

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Paris, , France

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Local Institution - 0029

Paris, , France

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Paris, , France

Site Status

Local Institution - 036

Poitiers, , France

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Poitiers, , France

Site Status

Local Institution - 075

Frankfurt, , Germany

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Frankfurt, , Germany

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Local Institution - 0074

Hanover, , Germany

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Hanover, , Germany

Site Status

Local Institution - 0089

Navrangpura, Ahmedabad, Gujarat, India

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Navrangpura, Ahmedabad, Gujarat, India

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Bangalore, Karnataka, India

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Mumbai, Maharashtra, India

Site Status

Local Institution - 0094

Pune, Maharashtra, India

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Pune, Maharashtra, India

Site Status

Local Institution - 0093

Madurai, Tamil Nadu, India

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Madurai, Tamil Nadu, India

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Local Institution

Vellore, Tamil Nadu, India

Site Status

Local Institution - 0088

Bangalore, , India

Site Status

Local Institution - 0082

Kolkata, , India

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Kolkata, , India

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Local Institution - 0085

Mumbai, , India

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Mumbai, , India

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Local Institution - 0084

Trivandrum, , India

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Trivandrum, , India

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Local Institution - 038

Bologna, , Italy

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Bologna, , Italy

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Local Institution - 006

Monza, , Italy

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Monza (MB), , Italy

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Local Institution - 070

Roma, , Italy

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Roma, , Italy

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Local Institution - 0059

Roma, , Italy

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Roma, , Italy

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Local Institution - 015

Torino, , Italy

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Torino, , Italy

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Hospital Civil De Guadalajara - Nuevo Dr. Juan I. Menchaca

Guadalajara, Jalisco, Mexico

Site Status

Local Institution - 0054

Guadalajara, Jalisco, Mexico

Site Status

Local Institution - 0051

Cuauhtémoc, Mexico City, Mexico

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Df, Mexico City, Mexico

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Local Institution - 0053

Mexico City, Mexico City, Mexico

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Mexico City, Mexico City, Mexico

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Local Institution - 0052

Mexico City, Mexico City, Mexico

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Mexico City, Mexico City, Mexico

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Mexico, D. F., Mexico City, Mexico

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Local Institution - 0050

Monterrey, Nuevo León, Mexico

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Monterrey, Nuevo León, Mexico

Site Status

Local Institution - 0060

Monterrey, N.l., Nuevo León, Mexico

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Monterrey, N.l., Nuevo León, Mexico

Site Status

Local Institution - 0007

Rotterdam, , Netherlands

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Rotterdam, , Netherlands

Site Status

Local Institution - 0099

Utrecht, , Netherlands

Site Status

Local Institution - 0095

Bucharest, , Romania

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Bucharest, , Romania

Site Status

Local Institution - 0097

Sector 2, , Romania

Site Status

Local Institution - 0017

Moscow, , Russia

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Moscow, , Russia

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Local Institution - 0023

Moscow, , Russia

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Moscow, , Russia

Site Status

Local Institution - 0018

Saint Petersburg, , Russia

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Saint Petersburg, , Russia

Site Status

Local Institution - 0071

Singapore, , Singapore

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Singapore, , Singapore

Site Status

Local Institution - 0055

Bloemfontein, Free State, South Africa

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Bloemfontein, Free State, South Africa

Site Status

Local Institution - 058

Pretoria, Gauteng, South Africa

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Local Institution

Pretoria, Gauteng, South Africa

Site Status

Local Institution - 0057

Cape Town, Western Cape, South Africa

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Cape Town, Western Cape, South Africa

Site Status

Local Institution - 062

Tygerberg, Western Cape, South Africa

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Tygerberg, Western Cape, South Africa

Site Status

Local Institution - 0092

Seoul, , South Korea

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Seoul, , South Korea

Site Status

Local Institution - 0091

Seoul, , South Korea

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Seoul, , South Korea

Site Status

Local Institution - 0013

Barcelona, , Spain

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Local Institution

Barcelona, , Spain

Site Status

Local Institution - 0012

Barcelona, , Spain

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Barcelona, , Spain

Site Status

Local Institution - 0011

Madrid, , Spain

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Madrid, , Spain

Site Status

Local Institution - 0010

Madrid, , Spain

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Madrid, , Spain

Site Status

Local Institution - 0041

Málaga, , Spain

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Málaga, , Spain

Site Status

Local Institution - 0033

Valencia, , Spain

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Local Institution

Valencia, , Spain

Site Status

Local Institution

Valencia, , Spain

Site Status

Local Institution - 0016

Glasgow, Central, United Kingdom

Site Status

Local Institution

Glasgow, Central, United Kingdom

Site Status

Local Institution - 0009

Sutton, Surrey, United Kingdom

Site Status

Local Institution

Sutton, Surrey, United Kingdom

Site Status

Local Institution - 0008

Birmingham, West Midlands, United Kingdom

Site Status

Local Institution

Birmingham, West Midlands, United Kingdom

Site Status

Countries

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United States Argentina Australia Brazil Canada France Germany India Italy Mexico Netherlands Romania Russia Singapore South Africa South Korea Spain United Kingdom

References

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Gore L, Kearns PR, de Martino ML, Lee, De Souza CA, Bertrand Y, Hijiya N, Stork LC, Chung NG, Cardos RC, Saikia T, Fagioli F, Seo JJ, Landman-Parker J, Lancaster D, Place AE, Rabin KR, Sacchi M, Swanink R, Zwaan CM. Dasatinib in Pediatric Patients With Chronic Myeloid Leukemia in Chronic Phase: Results From a Phase II Trial. J Clin Oncol. 2018 May 1;36(13):1330-1338. doi: 10.1200/JCO.2017.75.9597. Epub 2018 Mar 2.

Reference Type DERIVED
PMID: 29498925 (View on PubMed)

Related Links

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Other Identifiers

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2008-002260-33

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CA180-226

Identifier Type: -

Identifier Source: org_study_id

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