Pediatric Philadelphia Positive Acute Lymphoblastic Leukemia

NCT ID: NCT01460160

Last Updated: 2021-12-08

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

106 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-04-13

Study Completion Date

2021-06-01

Brief Summary

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The purpose of this study is to determine whether Dasatinib when added to standard chemotherapy is effective and safe in the treatment of pediatric philadelphia chromosome positive acute lymphoblastic leukemia

Detailed Description

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Conditions

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Leukemia, Pediatric

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Arm 1: Dasatinib

Group Type EXPERIMENTAL

Dasatinib

Intervention Type DRUG

Tablets, Oral, 60 mg/m2, Once daily, 2 years or until unacceptable toxicity

Interventions

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Dasatinib

Tablets, Oral, 60 mg/m2, Once daily, 2 years or until unacceptable toxicity

Intervention Type DRUG

Other Intervention Names

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Sprycel

Eligibility Criteria

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Inclusion Criteria

* Newly diagnosed Philadelphia chromosome positive Acute Lymphoblastic Leukemia (ALL)
* Age \>1 year and \< less than 18 years old
* Induction chemotherapy ≤ 14 days according to institutional standard of care
* Adequate liver, renal and cardiac function

Exclusion Criteria

* Prior treatment with a Oncogene fusion protein (BCR-ABL) inhibitor
* Extramedullary involvement of the testicles
* Active systemic bacterial, fungal or viral infection
* Down syndrome
Minimum Eligible Age

1 Year

Maximum Eligible Age

17 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Children's Oncology Group

NETWORK

Sponsor Role collaborator

EsPhALL

OTHER

Sponsor Role collaborator

Bristol-Myers Squibb

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Bristol-Myers Squibb

Role: STUDY_DIRECTOR

Bristol-Myers Squibb

Locations

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University Of Alabama At Birmingham

Birmingham, Alabama, United States

Site Status

Phoenix Children'S Hospital/Ctr. For Cancer & Blood Ctr.

Phoenix, Arizona, United States

Site Status

University Of Arkansas For Medical Sciences

Little Rock, Arkansas, United States

Site Status

Antranik Agop Bedros

Loma Linda, California, United States

Site Status

Miller Children's and Women Hospital

Long Beach, California, United States

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Children'S Hospital Of L.A.

Los Angeles, California, United States

Site Status

Southern California Permanente Medical Group

Los Angeles, California, United States

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Valley Children's Hospital

Madera, California, United States

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Children's Hospital of Orange County

Orange, California, United States

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Lpch & Sumc

Palo Alto, California, United States

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Kaiser Medical Center

Roseville, California, United States

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Ucsf - Hematology/Oncology

San Francisco, California, United States

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Children'S Hospital Colorado

Aurora, Colorado, United States

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Connecticut Children's Medical Center

Hartford, Connecticut, United States

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A. I. Dupont Hospital For Children

Wilmington, Delaware, United States

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Children'S National Medical Center

Washington D.C., District of Columbia, United States

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Lee Memorial Health System

Fort Myers, Florida, United States

Site Status

University Of Florida

Gainesville, Florida, United States

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Nemours Children'S Clinic

Jacksonville, Florida, United States

Site Status

Md Anderson Cancer Center Orlando

Orlando, Florida, United States

Site Status

Nemours Childrens Hospital

Orlando, Florida, United States

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All Children'S Hospital

St. Petersburg, Florida, United States

Site Status

St. Joseph's Children's Hospital

Tampa, Florida, United States

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St. Mary'S

West Palm Beach, Florida, United States

Site Status

Children's Healthcare Of Atlanta

Atlanta, Georgia, United States

Site Status

Kapiolani Medical Center For Women & Children

Honolulu, Hawaii, United States

Site Status

Mountain States Tumor Institute

Boise, Idaho, United States

Site Status

Ann & Robert H Lurie Children's Hospital Of Chicago

Chicago, Illinois, United States

Site Status

Loyola University Medical Center

Maywood, Illinois, United States

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Southern Illinois University School Of Medicine

Springfield, Illinois, United States

Site Status

James Whitcomb Riley Hospital For Children

Indianapolis, Indiana, United States

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Children'S Center For Cancer And Blood Diseases

Indianapolis, Indiana, United States

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University Of Kentucky

Lexington, Kentucky, United States

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Norton Children's Hospital

Louisville, Kentucky, United States

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Sinai Hospital Of Baltimore

Baltimore, Maryland, United States

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Johns Hopkins University

Baltimore, Maryland, United States

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Dana Farber Cancer Institute

Boston, Massachusetts, United States

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UMass Memorial Medical Center

Worcester, Massachusetts, United States

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Children'S Hospital Of Michigan

Detroit, Michigan, United States

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Helen Devos Children'S Hospital

Grand Rapids, Michigan, United States

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Michigan State University

Lansing, Michigan, United States

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Childrens Hospitals And Clinics Of Minnesota

Minneapolis, Minnesota, United States

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Univ Of Mississippi Med Ctr

Jackson, Mississippi, United States

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University Of Missouri Health Care

Columbia, Missouri, United States

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Children'S Mercy Hospital And Clinics

Kansas City, Missouri, United States

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Washington University Medical Center

St Louis, Missouri, United States

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Children'S Specialty Center Of Nevada

Las Vegas, Nevada, United States

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Hackensack University Medical Center

Hackensack, New Jersey, United States

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Goryeb Children'S Hospital

Morristown, New Jersey, United States

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The Cancer Institute Of New Jersey

New Brunswick, New Jersey, United States

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Newark Beth Israel Medical Center

Newark, New Jersey, United States

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St. Joseph's Regional Medical Center

Paterson, New Jersey, United States

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University Of New Mexico

Albuquerque, New Mexico, United States

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New York University

New York, New York, United States

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The Herbert Irving Pavilion

New York, New York, United States

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New York Presbyterian/Weill Cornell

New York, New York, United States

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SUNY Upstate Medical University

Syracuse, New York, United States

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New York Medical College

Valhalla, New York, United States

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Levine Children's Hospital

Charlotte, North Carolina, United States

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Wake Forest University

Winston-Salem, North Carolina, United States

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Cincinnati Children'S Hospital Medical Center

Cincinnati, Ohio, United States

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Nationwide Children'S Hospital

Columbus, Ohio, United States

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The Children'S Medical Center Of Dayton

Dayton, Ohio, United States

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The Toledo Children'S Hospital

Toledo, Ohio, United States

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Mercy Children's Hospital

Toledo, Ohio, United States

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University Of Oklahoma Health Sciences Center

Oklahoma City, Oklahoma, United States

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Legacy Emanuel Hospital & Health Center

Portland, Oregon, United States

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Oregon Health & Sci Univ

Portland, Oregon, United States

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Geisinger Medical Center

Danville, Pennsylvania, United States

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Penn State Hershey Medical Center

Hershey, Pennsylvania, United States

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Children'S Hospital Of Philadelphia

Philadelphia, Pennsylvania, United States

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Children's Hospital Of Pittsburgh Of UPMC

Pittsburgh, Pennsylvania, United States

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Rhode Island Hospital

Providence, Rhode Island, United States

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East Tennessee Children'S Hosp

Knoxville, Tennessee, United States

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Vanderbilt University

Nashville, Tennessee, United States

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Dell Children'S Medical Center Of Central Texas

Austin, Texas, United States

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Driscoll Children'S Hospital

Corpus Christi, Texas, United States

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Ut Southwestern

Dallas, Texas, United States

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Cook Children'S Hem/Onc Center

Fort Worth, Texas, United States

Site Status

Texas Children'S Cancer Center

Houston, Texas, United States

Site Status

Scott & White - McLane Children's Specialty Clinic

Temple, Texas, United States

Site Status

Primary Children's Medical Center

Salt Lake City, Utah, United States

Site Status

Inova Pediatric Specialty Center Ii

Fairfax, Virginia, United States

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Children'S Hosp-Kings Daughter

Norfolk, Virginia, United States

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Seattle Children'S

Seattle, Washington, United States

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St Vincent Hospital

Green Bay, Wisconsin, United States

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Kenneth Desantes, Md

Madison, Wisconsin, United States

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Medical College of Wisconsin

Milwaukee, Wisconsin, United States

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Local Institution

Sth Brisbane, Queensland, Australia

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Local Institution

Parkville, Victoria, Australia

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Local Institution

Nedlands, Western Australia, Australia

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Alberta Children'S Hospital

Calgary, Alberta, Canada

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Stollery Children'S Hospital

Edmonton, Alberta, Canada

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Local Institution

London, Ontario, Canada

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Children'S Hospital Of Eastern Ontario

Ottawa, Ontario, Canada

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Chu Ste-Justine

Montreal, Quebec, Canada

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The Montreal Children's Hospital of the MUHC

Montreal, Quebec, Canada

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Local Institution

Saskatoon, Saskatchewan, Canada

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Local Institution

Bologna, , Italy

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Local Institution

Cagliari, , Italy

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Local Institution

Catania, , Italy

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Local Institution

Florence, , Italy

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Genova, , Italy

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Monza, , Italy

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Local Institution

Napoli, , Italy

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Local Institution

Palermo, , Italy

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Local Institution

Roma, , Italy

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Roma, , Italy

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Torino, , Italy

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Trieste, , Italy

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San Juan, , Puerto Rico

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Local Institution

Bristol, Avon, United Kingdom

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Cardiff, Glamorgan, United Kingdom

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Aberdeen, Grampian, United Kingdom

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London, Greater London, United Kingdom

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Local Institution

Manchester, Greater Manchester, United Kingdom

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Local Institution

Southampton, Hampshire, United Kingdom

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Glasgow, Lanarkshire, United Kingdom

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Edinburgh, Lothian, United Kingdom

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Liverpool, Merseyside, United Kingdom

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Leeds, North Yorkshire, United Kingdom

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Nottingham, Nottinghamshire, United Kingdom

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Oxford, Oxfordshire, United Kingdom

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Sheffield, South Yorkshire, United Kingdom

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Sutton, Surrey, United Kingdom

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Newcastle upon Tyne, Tyne and Wear, United Kingdom

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Birmingham, West Midlands, United Kingdom

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Local Institution

Cambridge, , United Kingdom

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Countries

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United States Australia Canada Italy Puerto Rico United Kingdom

References

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Hunger SP, Tran TH, Saha V, Devidas M, Valsecchi MG, Gastier-Foster JM, Cazzaniga G, Reshmi SC, Borowitz MJ, Moorman AV, Heerema NA, Carroll AJ, Martin-Regueira P, Loh ML, Raetz EA, Schultz KR, Slayton WB, Cario G, Schrappe M, Silverman LB, Biondi A. Dasatinib with intensive chemotherapy in de novo paediatric Philadelphia chromosome-positive acute lymphoblastic leukaemia (CA180-372/COG AALL1122): a single-arm, multicentre, phase 2 trial. Lancet Haematol. 2023 Jul;10(7):e510-e520. doi: 10.1016/S2352-3026(23)00088-1.

Reference Type DERIVED
PMID: 37407142 (View on PubMed)

Tasian SK, Peters C. Targeted therapy or transplantation for paediatric ABL-class Ph-like acute lymphocytic leukaemia? Lancet Haematol. 2020 Dec;7(12):e858-e859. doi: 10.1016/S2352-3026(20)30369-0. No abstract available.

Reference Type DERIVED
PMID: 33242441 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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Other Identifiers

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2011-001123-20

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

AALL1122

Identifier Type: OTHER

Identifier Source: secondary_id

CA180-372

Identifier Type: -

Identifier Source: org_study_id