A Phase 3 Study to Evaluate the Safety of Sotagliflozin in Patients With Type 1 Diabetes Who Have Inadequate Glycemic Control With Insulin Therapy Alone

NCT ID: NCT02531035

Last Updated: 2020-02-12

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

1405 participants

Study Classification

INTERVENTIONAL

Study Start Date

2015-09-30

Study Completion Date

2017-04-30

Brief Summary

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This Phase 3 study was designed to demonstrate the net benefit of sotagliflozin versus placebo in patients with Type 1 Diabetes (T1D).

Detailed Description

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Conditions

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Type 1 Diabetes Mellitus (T1DM) High Level of Sugar (Glucose) in the Blood

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Placebo

Two placebo-matching to sotagliflozin tablets daily, orally, before the first meal of the day for 24 weeks.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo, once daily, before the first meal of the day

Sotagliflozin 400 mg

Sotagliflozin 400 milligram (mg) (two 200 mg tablets) once daily, orally, before the first meal of the day for 24 weeks.

Group Type EXPERIMENTAL

Sotagliflozin

Intervention Type DRUG

Sotagliflozin, once daily, before the first meal of the day

Interventions

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Sotagliflozin

Sotagliflozin, once daily, before the first meal of the day

Intervention Type DRUG

Placebo

Placebo, once daily, before the first meal of the day

Intervention Type DRUG

Other Intervention Names

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LX4211

Eligibility Criteria

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Inclusion Criteria

* Participants had given written informed consent to participate in the study in accordance with local regulations
* Adult participants 18 years and older with a diagnosis of T1DM made at least 1 year prior to informed consent
* Participants were being treated with insulin or insulin analog
* Willing and able to perform self-monitoring of blood glucose (SMBG) and complete the study diary as required per protocol
* At the Screening Visit, A1C was between 7.0% to 11.0%
* Females of childbearing potential used an adequate method of contraception and had a negative pregnancy test

Exclusion Criteria

* Use of antidiabetic agent other than insulin or insulin analog at the time of screening
* Use of sodium-glucose cotransporter (SGLT) inhibitors within 8 weeks prior to screening
* Chronic systemic corticosteroid use
* Type 2 diabetes mellitus (T2DM), or severely uncontrolled T1D as determined by the Investigator
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Sanofi

INDUSTRY

Sponsor Role collaborator

Lexicon Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Sangeeta Sawhney, MD

Role: STUDY_DIRECTOR

Lexicon Pharmaceuticals, Inc.

Locations

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Lexicon Investigational Site

Concord, California, United States

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Escondido, California, United States

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La Jolla, California, United States

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San Marcos, California, United States

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Ventura, California, United States

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Walnut Creek, California, United States

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Aurora, Colorado, United States

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New Haven, Connecticut, United States

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Orlando, Florida, United States

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West Palm Beach, Florida, United States

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Atlanta, Georgia, United States

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Macon, Georgia, United States

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Roswell, Georgia, United States

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New Orleans, Louisiana, United States

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Rockville, Maryland, United States

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Boston, Massachusetts, United States

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Bloomfield Hills, Michigan, United States

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Omaha, Nebraska, United States

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Las Vegas, Nevada, United States

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Albany, New York, United States

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The Bronx, New York, United States

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Asheville, North Carolina, United States

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Chapel Hill, North Carolina, United States

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Greenville, North Carolina, United States

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Morehead City, North Carolina, United States

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Grand Forks, North Dakota, United States

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Bend, Oregon, United States

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Sioux Falls, South Dakota, United States

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Austin, Texas, United States

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San Antonio, Texas, United States

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Shavano Park, Texas, United States

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Salt Lake City, Utah, United States

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Seattle, Washington, United States

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Córdoba, Córdoba Province, Argentina

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Buenos Aires, , Argentina

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Buenos Aires, , Argentina

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Coffs Harbour, New South Wales, Australia

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Merewether, New South Wales, Australia

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St Leonards, New South Wales, Australia

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Wollongong, New South Wales, Australia

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Herston, Queensland, Australia

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Keswick, South Australia, Australia

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Box Hill, Victoria, Australia

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Fitzroy, Victoria, Australia

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Parkville, Victoria, Australia

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Aalst, , Belgium

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Ghent, , Belgium

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Sint-Niklaas, , Belgium

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Plovdiv, , Bulgaria

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Rousse, , Bulgaria

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Smolyan, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Varna, , Bulgaria

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Vancouver, British Columbia, Canada

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Halifax, Nova Scotia, Canada

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Barrie, Ontario, Canada

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London, Ontario, Canada

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Markham, Ontario, Canada

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Oakville, Ontario, Canada

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Thornhill, Ontario, Canada

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Toronto, Ontario, Canada

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Saint-Laurent, Quebec, Canada

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Sherbrooke, Quebec, Canada

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Atlántico, , Colombia

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Cundinamarca, , Colombia

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Cundinamarca, , Colombia

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Cundinamarca, , Colombia

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Krnov, , Czechia

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Olomouc, , Czechia

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Ostrava, , Czechia

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Prague, , Czechia

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Prague, , Czechia

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Prague, , Czechia

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Corbeil-Essonnes, , France

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Pierre-Bénite, , France

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Mainz, Palatinate, Germany

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Sulzbach, Rosenberg Bavaria, Germany

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Münster, Westphalia, Germany

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Aschaffenburg, , Germany

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Aßlar, , Germany

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Budapest, , Hungary

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Budapest, , Hungary

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Budapest, , Hungary

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Budapest, , Hungary

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Eger, , Hungary

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Esztergom, , Hungary

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Győr, , Hungary

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Sátoraljaújhely, , Hungary

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Holon, , Israel

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Petach-Tikvah, , Israel

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Petah Tikva, , Israel

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Rehovot, , Israel

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Tel Litwinsky, , Israel

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Bologna, , Italy

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Catania, , Italy

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Catania, , Italy

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Latina, , Italy

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Milan, , Italy

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Rome, , Italy

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Epsom, Auckland, New Zealand

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Takapuna, Auckland, New Zealand

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Christchurch, Canterbury, New Zealand

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Dunedin, Otago, New Zealand

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Newtown, Wellington Region, New Zealand

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Christchurch, , New Zealand

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Otahuhu, , New Zealand

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Gdynia, , Poland

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Katowice, , Poland

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Katowice, , Poland

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Lublin, , Poland

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Warsaw, , Poland

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Warsaw, , Poland

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Warsaw, , Poland

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Bardejov, , Slovakia

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Bratislava, , Slovakia

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Bratislava, , Slovakia

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Levice, , Slovakia

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Goodwood, Cape Town, South Africa

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Middelburg, Mpumalanga, South Africa

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Bloemfontein, , South Africa

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Cape Town, , South Africa

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Cape Town, , South Africa

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Johannesburg, , South Africa

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Port Elizabeth, , South Africa

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Barcelona, , Spain

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Barcelona, , Spain

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Málaga, , Spain

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Seville, , Spain

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Seville, , Spain

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Dundee, Scotland, United Kingdom

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Blackburn, , United Kingdom

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Guildford, , United Kingdom

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Leicester, , United Kingdom

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Northampton, , United Kingdom

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Countries

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United States Argentina Australia Belgium Bulgaria Canada Colombia Czechia France Germany Hungary Israel Italy New Zealand Poland Slovakia South Africa Spain United Kingdom

References

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Garg SK, Henry RR, Banks P, Buse JB, Davies MJ, Fulcher GR, Pozzilli P, Gesty-Palmer D, Lapuerta P, Simo R, Danne T, McGuire DK, Kushner JA, Peters A, Strumph P. Effects of Sotagliflozin Added to Insulin in Patients with Type 1 Diabetes. N Engl J Med. 2017 Dec 14;377(24):2337-2348. doi: 10.1056/NEJMoa1708337. Epub 2017 Sep 13.

Reference Type DERIVED
PMID: 28899222 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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LX4211.312

Identifier Type: OTHER

Identifier Source: secondary_id

LX4211.1-312-T1DM

Identifier Type: -

Identifier Source: org_study_id

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