Phase 2/3, Randomized, Double-Masked, Sham-Controlled Trial of QPI-1007 in Subjects With Acute Nonarteritic Anterior Ischemic Optic Neuropathy (NAION)

NCT ID: NCT02341560

Last Updated: 2020-07-20

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2/PHASE3

Total Enrollment

732 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-02-24

Study Completion Date

2019-07-01

Brief Summary

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This study will determine the effect of QPI-1007 on visual function in subjects with recent-onset NAION and assess the safety and tolerability of intravitreal injections of QPI-1007 in this population. This study will also evaluate the structural changes in the retina following administration of QPI-1007.

Detailed Description

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This is a double masked, randomized, sham-controlled efficacy and safety study that will enroll approximately 800 subjects with recent-onset NAION. Subjects will be randomized into one of 3 groups in a 1:1:1 ratio, and assigned to receive QPI-1007 and/or a sham procedure. Subjects will have a two in three (66%) chance of receiving active treatment (no sham procedure) and a one in three (33%) chance of receiving sham procedure (no active treatment). Total study time involvement is approximately 12 months.

Conditions

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Non Arteritic Anterior Ischemic Optic Neuropathy

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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single dose or multiple dose

QPI-1007 Injection - 1.5 mg

Group Type ACTIVE_COMPARATOR

QPI-1007 Injection - 1.5 mg

Intervention Type DRUG

single or multiple dose

QPI-1007 Injection - 3.0 mg

Group Type ACTIVE_COMPARATOR

QPI-1007 Injection - 3.0 mg

Intervention Type DRUG

Sham

Sham injection procedure

Group Type SHAM_COMPARATOR

Sham Injection Procedure

Intervention Type OTHER

Sham Procedure

Interventions

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QPI-1007 Injection - 1.5 mg

Intervention Type DRUG

QPI-1007 Injection - 3.0 mg

Intervention Type DRUG

Sham Injection Procedure

Sham Procedure

Intervention Type OTHER

Other Intervention Names

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QPI-1007 QPI-1007 Sham

Eligibility Criteria

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Inclusion Criteria

* Positive diagnosis of first episode of NAION in the study eye with symptom onset within 14 days prior to planned study drug administration/sham procedure
* Best corrected visual acuity score in the study eye is better than or equal to 15 letter score, measured using the ETDRS visual acuity protocol at Day 1 prior to study drug administration/sham procedure.
* Clear ocular media and able to undergo adequate pupil dilation to allow a good fundus examination

Exclusion Criteria

* Present use or history of any treatment for the current episode of NAION, including systemic steroids, brimonidine, or traditional Chinese herbal medicine
* Prior episode of NAION in the study eye only
* Present use of drugs known to cause optic nerve or retinal toxicity at Day 1/Randomization, such as: chloroquine or hydroxychloroquine, ethambutol, Vigabatrin. Subjects who need to be prescribed any of these drugs during the course of the study will be discontinued from the trial.
* Any medical condition, concomitant therapy, or previous incisional or laser surgery that, in the opinion of the Investigator, would preclude IVT injection in the study eye only
* Clinical evidence of temporal arteritis
Minimum Eligible Age

50 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Quark Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Sharon Klier, M.D.

Role: STUDY_DIRECTOR

Quark Pharmaceuticals

Locations

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University of Arkansas Medical Center, Jones Eye Institute

Little Rock, Arkansas, United States

Site Status

Loma Linda University Eye Institute

Loma Linda, California, United States

Site Status

University of Southern California

Los Angeles, California, United States

Site Status

NeuroEyeOrbit Institute

Los Angeles, California, United States

Site Status

Stanford University

Palo Alto, California, United States

Site Status

Unversity of California, Los Angeles (UCLA)

Pasadena, California, United States

Site Status

University of Colorado Denver, Department of Neurology

Aurora, Colorado, United States

Site Status

Retina Consultants of Southern Colorado, PC

Colorado Springs, Colorado, United States

Site Status

The Eye Care Group

Waterbury, Connecticut, United States

Site Status

Cape Coral Eye Center

Cape Coral, Florida, United States

Site Status

University of Miami Miller School of Medicine/Bascom Palmer Eye Institute

Miami, Florida, United States

Site Status

Sarasota Retina Institute

Sarasota, Florida, United States

Site Status

Northwestern University

Chicago, Illinois, United States

Site Status

University of Illinois at Chicago, Department of Ophthalmology (MC 648)

Chicago, Illinois, United States

Site Status

NorthShore University Healthsystem

Glenview, Illinois, United States

Site Status

University of Kentucky, Department of Neurology

Lexington, Kentucky, United States

Site Status

Greater Baltimore Medical Center

Baltimore, Maryland, United States

Site Status

Bethesda Neurology, LLC

Bethesda, Maryland, United States

Site Status

Massachusetts Eye and Ear Infirmary

Boston, Massachusetts, United States

Site Status

Boston Medical Center

Boston, Massachusetts, United States

Site Status

University of Michigan

Ann Arbor, Michigan, United States

Site Status

University of Minnesota

Minneapolis, Minnesota, United States

Site Status

Mayo Clinic

Rochester, Minnesota, United States

Site Status

Washington University in St. Louis

St Louis, Missouri, United States

Site Status

University of Nebraska Medical Center and Truhlsen Eye Institute

Omaha, Nebraska, United States

Site Status

Rutgers, New Jersey Medical School

Newark, New Jersey, United States

Site Status

New York Eye and Ear Infirmary of Mount Sinai

New York, New York, United States

Site Status

Cornell University School of Medicine

New York, New York, United States

Site Status

University of Rochester, Flaum Eye Institute

Rochester, New York, United States

Site Status

State University of New York at Stony Brook

Stony Brook, New York, United States

Site Status

SUNY Upstate Medical University

Syracuse, New York, United States

Site Status

Duke University Eye Center

Durham, North Carolina, United States

Site Status

Raleigh Neurology Associates

Raleigh, North Carolina, United States

Site Status

Cleveland Clinic, Cole Eye Institute

Cleveland, Ohio, United States

Site Status

Dean McGee Eye Institute

Oklahoma City, Oklahoma, United States

Site Status

University of Pennsylvania, Scheie Eye Institute

Philadelphia, Pennsylvania, United States

Site Status

Retina Consultants of Charleston

Charleston, South Carolina, United States

Site Status

University of Houston, Neuro-Ophth of Texas

Houston, Texas, United States

Site Status

Houston Methodist Hospital, Blanton Eye Institute

Houston, Texas, United States

Site Status

Foresight Studies

San Antonio, Texas, United States

Site Status

University of Utah John A. Moran Eye Center

Salt Lake City, Utah, United States

Site Status

University of Virginia Health Sciences Center

Charlottesville, Virginia, United States

Site Status

Swedish Medical Center, CO/NOCNW

Seattle, Washington, United States

Site Status

University of Washington Department of Ophthalmology

Seattle, Washington, United States

Site Status

Sydney Eye Hospital/Save Sight Institute

Sydney, New South Wales, Australia

Site Status

Vision South Australia

Kent Town, South Australia, Australia

Site Status

The Royal Victorian Eye and Ear Hospital

Fitzroy, Victoria, Australia

Site Status

Royal Perth Hospital

Perth, Western Australia, Australia

Site Status

The Second Xiangya Hospital of Central South University

Changsha, Hunan, China

Site Status

Peking University Eye Center, The Third Hospital Peking University.

Beijing, , China

Site Status

Beijing Tongren Hospital, Capital Medical University

Beijing, , China

Site Status

Peking Union Medical College Hospital

Beijing, , China

Site Status

Tianjin Eye Hospital

Tianjin, , China

Site Status

Universitätsmedizin d. Johannes Gutenberg-Universität Mainz

Mainz, Rhineland-Palatinate, Germany

Site Status

Universitätsklinikum Aachen-Augenklinik

Aachen, , Germany

Site Status

Universitätsklinikum Carl Gustav Carus-Dresden-Klinik und Poliklinik für Augenheilkunde

Dresden, , Germany

Site Status

Universitätsklinikum Münster

Münster, , Germany

Site Status

Universitätsklinikum Regensburg-Klinik und Poliklinik für Augenheilkunde

Regensburg, , Germany

Site Status

Universitäts-Augenklinik Tübingen

Tübingen, , Germany

Site Status

L V Prasad Eye Institute

Hyderabad, Andhra Pradesh, India

Site Status

L V Prasad Eye Institute

Visakhapatnam, Andhra Pradesh, India

Site Status

Sri Sankaradeva Nethralaya

Guwahati, Assam, India

Site Status

Narayana Nethralaya

Bangalore, Karnataka, India

Site Status

PBMA'S H. V. Desai Eye Hospital

Pune, Maharashtra, India

Site Status

L V Prasad Eye Institute

Bhubaneswar, Odisha, India

Site Status

Sankara Nethralaya (Vision Research Foundation)

Chennai, Tami Nadu, India

Site Status

Aravind Eye Hospital

Madurai, Tamil Nadu, India

Site Status

Sanjay Gandhi Postgraduate Institute of Medical Sciences

Lucknow, Uttar Pradesh, India

Site Status

ICARE Research Centre and Post Graduate Institute

Noida, Uttar Pradesh, India

Site Status

Dr. Rajendra Prasad Centre for Ophthalmic Sciences, A.I.I.M.S.

New Delhi, , India

Site Status

Datta Meghe Institute of Medical Sciences

Wardha, , India

Site Status

Hadassah Medical Center

Jerusalem, Jerusalem, Israel

Site Status

Soroka University Medical Center

Beersheba, , Israel

Site Status

Bnai Zion Medical Center

Haifa, , Israel

Site Status

Rabin Medical Center, Belinson Campus

Petah Tikva, , Israel

Site Status

Kaplan Medical Center

Rehovot, , Israel

Site Status

The Tel-Aviv Sourasky Medical Center

Tel Aviv, , Israel

Site Status

The Chaim Sheba Medical Center

Tel Litwinsky, , Israel

Site Status

AOU Policlinico S. Orsola-Malpighi

Bologna, , Italy

Site Status

AOU Careggi

Florence, , Italy

Site Status

Scientific Institute Auxologico Italiano

Milan, , Italy

Site Status

Scientific institute San Raffaele

Milan, , Italy

Site Status

University Eye Clinic

Parma, , Italy

Site Status

Singapore National Eye Centre

Singapore, , Singapore

Site Status

Tan Tock Seng Hospital, Department of Ophthalmology

Singapore, , Singapore

Site Status

Countries

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United States Australia China Germany India Israel Italy Singapore

References

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Davis JL. The Blunt End: Surgical Challenges of Gene Therapy for Inherited Retinal Diseases. Am J Ophthalmol. 2018 Dec;196:xxv-xxix. doi: 10.1016/j.ajo.2018.08.038. Epub 2018 Sep 5.

Reference Type DERIVED
PMID: 30194931 (View on PubMed)

Other Identifiers

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QRK207

Identifier Type: -

Identifier Source: org_study_id

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