Safety Study of a Single IVT Injection of QPI-1007 in Chronic Optic Nerve Atrophy and Recent Onset NAION Patients

NCT ID: NCT01064505

Last Updated: 2013-05-13

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

48 participants

Study Classification

INTERVENTIONAL

Study Start Date

2010-02-28

Study Completion Date

2013-04-30

Brief Summary

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This is an open-label, dose escalation, safety, tolerability and pharmacokinetic study, where active study drug (QPI-1007) will be given to all patients who participate.

This study will determine whether QPI-1007 is safe when it is injected into the eye. The study will also reveal if there are any side effects of the drug and how long it takes for the body to clear the drug.

Detailed Description

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Patients will be enrolled according to one of two sets of criteria designated as Stratum I and Stratum II.

1. Stratum I will enroll Optic Nerve Atrophy patients who meet necessary criteria. Stratum I will consist of a maximum of 6 cohorts and each cohort will enroll 3 to 6 evaluable patients. Enrollment in Stratum I is now closed.
2. Stratum II will enroll patients diagnosed with acute Non Arteritic Anterior Ischemic Optic Neuropathy (NAION) within 28 days of symptom onset who meet necessary criteria. Stratum II will consist of a maximum of 3 cohorts and each cohort will enroll up to 10 evaluable patients. Enrollment in Stratum II is still open.

Conditions

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Optic Atrophy Non-arteritic Anterior Ischemic Optic Neuropathy

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Blinding Strategy

NONE

Study Groups

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QPI-1007

Group Type EXPERIMENTAL

QPI-1007 at various doses

Intervention Type DRUG

Single Intravitreal Injection

Interventions

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QPI-1007 at various doses

Single Intravitreal Injection

Intervention Type DRUG

Other Intervention Names

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QPI-1007 siRNA small interfering RNA short interfering RNA

Eligibility Criteria

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Inclusion Criteria

* "Legally blind" in the study eye as the result of an irreversible condition affecting the posterior segment of the eye.
* Clear ocular media and able to undergo adequate pupil dilation.
* Visual acuity and visual field in the non-study eye are better than or equal to the study eye
* At least 21 years old.


* Positive diagnosis of NAION with symptom onset within 28 days prior to planned dosing with QPI-1007.
* Visual acuity in the study eye is between 20/40 and light perception.
* Clear ocular media and able to undergo adequate pupil dilation.
* At least 50 years old.

Exclusion Criteria

* For the study eye only: history of any IVT injection or vitrectomy, vitreous hemorrhage, retinal detachment, or active inflammatory condition (e.g. conjunctivitis).
* For either eye: history of uveitis.

Enrollment is now closed in Stratum I.


* For the study eye only: Macular disease, retinopathy, or other eye disease limiting visual acuity; prior intraocular surgery (other than Lasik) and cataract surgery within 3 months prior to dosing; glaucoma laser surgery within 1 month prior to dosing; pain on or aggravated by eye movement; history of vitreous hemorrhage; history of retinal detachment; any active inflammatory condition (e.g. conjunctivitis); glaucoma or ocular hypertension; or intraocular pressure \> 26 mmHg.
* For either eye: History of optic neuritis; or history of uveitis.
* Received any treatment for NAION prior to dosing.
* Any other abnormality which in the opinion of the investigator is suggestive of a disease other than NAION in the study eye only.
* Clinical evidence of temporal arteritis.
* History of collagen vascular disease or other inflammatory disease, or history of multiple sclerosis.

Enrollment in Stratum II is still open.
Minimum Eligible Age

50 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Quark Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Rabia Ozden, MD

Role: STUDY_DIRECTOR

Quark Pharmaceuticals

Locations

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Retinal Consultants of Arizona

Phoenix, Arizona, United States

Site Status

Retina-Vitreous Associates Medical Group

Beverly Hills, California, United States

Site Status

Jules Stein Eye Institute, University of California, Los Angeles

Los Angeles, California, United States

Site Status

Rocky Mountain Multiple Sclerosis Center at Anschutz Medical Campus, University of Colorado

Aurora, Colorado, United States

Site Status

Bascom Palmer at the University of Miami

Miami, Florida, United States

Site Status

Sarasota Retina Institute

Sarasota, Florida, United States

Site Status

University of Illinois at Chicago, Eye and Ear Infirmary

Chicago, Illinois, United States

Site Status

Kansas University Medical Center

Kansas City, Kansas, United States

Site Status

University of Kentucky, Department of Ophthalmology

Lexington, Kentucky, United States

Site Status

University of Minnesota, Department of Ophthalmology

Minneapolis, Minnesota, United States

Site Status

Mason Eye Institute, University of Missouri

Columbia, Missouri, United States

Site Status

New York Eye and Ear Infirmary

New York, New York, United States

Site Status

Flaum Eye Institute, University of Rochester Medical Center

Rochester, New York, United States

Site Status

Western Carolina Retinal Associates

Asheville, North Carolina, United States

Site Status

Charlotte Eye, Ear, Nose and Throat Associates, PA

Charlotte, North Carolina, United States

Site Status

Duke Eye Center, Duke University Medical Center

Durham, North Carolina, United States

Site Status

Cole Eye Institute, Cleveland Clinic Foundation

Cleveland, Ohio, United States

Site Status

University of Pennsylvania, Department of Ophthalmology

Philadelphia, Pennsylvania, United States

Site Status

Allegheny Ophthalmic and Orbital Associates

Pittsburgh, Pennsylvania, United States

Site Status

Alkek Eye Center Baylor College of Medicine

Houston, Texas, United States

Site Status

John A. Moran Eye Center at the University of Utah

Salt Lake City, Utah, United States

Site Status

Virginia Commonwealth University

Richmond, Virginia, United States

Site Status

Soroka University Medical Center, Dept of Ophthalmology

Beersheba, , Israel

Site Status

Bnai Zion Medical Center

Haifa, , Israel

Site Status

Rabin Medical Center, Belinson Campus, Dept of Ophthalmology

Petah Tikva, , Israel

Site Status

Kaplan Medical Center, Department of Ophthalmology

Rehovot, , Israel

Site Status

The Tel-Aviv Sourasky Medical Center, Dept of Ophthalmology

Tel Aviv, , Israel

Site Status

The Chaim Sheba Medical Center, Dept of Ophthalmology

Tel Litwinsky, , Israel

Site Status

Countries

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United States Israel

Other Identifiers

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QRK.007

Identifier Type: -

Identifier Source: org_study_id

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