Clinical Study to Evaluate the Safety, Tolerability, and Preliminary Efficacy of Intravitreal (IVT) Injection of ABI-110 (AAV2.N54-VEGF Trap) in Subjects With Neovascular (Wet) Age-Related Macular Degeneration (wAMD), Including Symptomatic Macular Polypoidal Choroidal Vasculopathy (PCV)

NCT ID: NCT06550011

Last Updated: 2024-10-02

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE1/PHASE2

Total Enrollment

18 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-08-07

Study Completion Date

2030-02-28

Brief Summary

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This will be a clinical study to assess initial safety and tolerability of IVT ABI-110 in patients diagnosed with wet macular degeneration (wAMD), including symptomatic macular PCV.

Detailed Description

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This is a Phase 1/2a, open-label, multiple-cohort, dose-escalation study to evaluate the safety, tolerability, and preliminary efficacy of IVT ABI-110 (AAV2.N54-VEGF-Trap) injection in subjects with wAMD), including symptomatic macular PCV.

This trial will include a screening period, confirmation of response to EYLEA (aflibercept), single administration of ABI-110, and follow-up period of 104 weeks after IVT ABI-110 injection.

Conditions

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Neovascular (Wet) AMD

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SEQUENTIAL

Dose Escalation
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Dose level 1

Low Dose

Group Type EXPERIMENTAL

ABI-110 Low Dose

Intervention Type DRUG

Low dose. lower than the safety factor of 10 as recommended by the FDA

Dose level 2

Medium Dose

Group Type EXPERIMENTAL

ABI-110 Medium Dose

Intervention Type DRUG

Medium dose

Dose level 3

High Dose

Group Type EXPERIMENTAL

ABI-110 High Dose

Intervention Type DRUG

High Dose

Interventions

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ABI-110 Low Dose

Low dose. lower than the safety factor of 10 as recommended by the FDA

Intervention Type DRUG

ABI-110 Medium Dose

Medium dose

Intervention Type DRUG

ABI-110 High Dose

High Dose

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* General:

1. Must be willing and able to provide written, signed informed consent.
2. Age: Subjects ≥ 50 and ≤ 89 years of age at the time of signing the informed consent

Study eye:
3. Diagnosis of wAMD, including symptomatic macular PCV, confirmed by the Central Reading Center
4. The macular neovascularization lesion must be confirmed as determined by the Central Reading Center based on SD-OCT imaging at screening.
5. BCVA ≤ 20/32 and ≥ 20/250 (≤ 78L and ≥ 30L ETDRS letters)
6. History of ≥ 2 anti-VEGF injections prior to trial entry with meaningful response to anti-VEGF and continued need for anti-VEGF treatment
7. Response to anti-VEGF at trial entry
8. Must be pseudophakic

Exclusion Criteria

* Study or Fellow Eye:

1. Prior gene therapy, either eye
2. Any active ocular/intraocular infection or inflammation (e.g., blepharitis, infectious conjunctivitis, keratitis, scleritis, uveitis) or history of idiopathic or autoimmune-associated uveitis, either eye
3. History of retinal disease other than wAMD or PCV, study eye
4. Any condition preventing visual acuity improvement (e.g., fibrosis, atrophy, or retinal epithelial tear in the center of the fovea), study eye.
5. History of (or active) retinal detachment, study eye
6. Uncontrolled glaucoma (defined as IOP \> 25 mmHg despite treatment), study eye, or history of steroid-response ocular hypertension/glaucoma in either eye
7. History of intravitreal therapy, (other than anti-VEGF therapy) such as intravitreal steroid injection or investigational product, in the 6 months prior to screening, study eye
8. Any prior treatment with photodynamic therapy or laser photocoagulation, study eye
9. History of glaucoma filtration, vitrectomy, or other procedure that could affect drug distribution or clearance, study eye.
Minimum Eligible Age

50 Years

Maximum Eligible Age

89 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Avirmax Biopharma Inc

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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California Retina Consultants

Bakersfield, California, United States

Site Status RECRUITING

Bay Area Retina Associates

Walnut Creek, California, United States

Site Status RECRUITING

Retina Consultants of Texas - San Antonio

San Antonio, Texas, United States

Site Status RECRUITING

Retina Consultants of Texas

The Woodlands, Texas, United States

Site Status RECRUITING

Countries

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United States

Central Contacts

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Wendy Murahashi

Role: CONTACT

650-208-4233

Facility Contacts

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Study Coordinator

Role: primary

650-208-4233

Study Coordinator

Role: primary

650-208-4233

Study Coordinator

Role: primary

650-208-4233

Study Coordinator

Role: primary

650-208-4233

Other Identifiers

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Avirmax ABI-110

Identifier Type: -

Identifier Source: org_study_id

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