Safety and Efficacy of IONIS-FB-Lrx in up to 120 Patients 55 and Older With Geographic Atrophy (GA) Secondary to Age-Related Macular Degeneration (AMD)

NCT ID: NCT03446144

Last Updated: 2019-08-13

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

WITHDRAWN

Clinical Phase

PHASE2

Study Classification

INTERVENTIONAL

Study Start Date

2018-03-16

Study Completion Date

2018-10-10

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The purpose of this study is to assess the Safety and Efficacy of IONIS-FB-Lrx for up to 120 patients with Geographic Atrophy secondary to Age Related Macular Degeneration

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

This study will assess changes in complement factor B over a 69-week treatment period in a patient population 55 and older with well-demarcated Geographic Atrophy secondary to Age Related Macular Degeneration

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Geographic Atrophy Age Related Macular Degeneration

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators
Double Masked

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

IONIS-FB-Lrx

Group Type EXPERIMENTAL

IONIS-FB-Lrx

Intervention Type DRUG

Single Dose of IONIS-FB-Lrx administered once weekly for weeks 1-3, and every other week or less frequently until week 70

Placebo (sterile saline 0.9%)

Group Type PLACEBO_COMPARATOR

Placebo (sterline saline 0.9%)

Intervention Type DRUG

Calculated volume to match active comparator. Administered subcutaneously weekly for weeks 1-3, and every other week or less frequently until week 70

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

IONIS-FB-Lrx

Single Dose of IONIS-FB-Lrx administered once weekly for weeks 1-3, and every other week or less frequently until week 70

Intervention Type DRUG

Placebo (sterline saline 0.9%)

Calculated volume to match active comparator. Administered subcutaneously weekly for weeks 1-3, and every other week or less frequently until week 70

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

1. Must have given written informed consent and be able to comply with study requirements
2. Females must be non-pregnant and non-lactating, and either surgically sterile or post-menopausal. Males must be surgically sterile or, if engaged in sexual relations with a female of child bearing potential, the subject must be using an acceptable contraceptive method from the time of signing the informed consent form until at least a period of 13 weeks after the last dose of Study Drug (ISIS 696844 or placebo)
3. Well-demarcated Geographic Atrophy due to Age Related Macular Degeneration

Exclusion Criteria

1. Clinically-significant abnormalities in medical history
2. Diagnosis of primary or secondary immunodeficiencies of B lymphocyte function, splenectomy, glomerulonephritis or history of recurrent meningococcal disease
3. Diabetes mellitus or thyroid disease unless well controlled for a period of at least 3 months
4. Clinically-significant abnormalities in screening laboratory values
5. Unwillingness to be administered, or history of a serious reaction to protocol required vaccines
6. Known history of or positive test for human immunodeficiency virus (HIV), hepatitis C or chronic hepatitis B
7. History or presence of a disease other than AMD in study eye
Minimum Eligible Age

55 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Ionis Pharmaceuticals, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

IONIS Investigative Site

Phoenix, Arizona, United States

Site Status

IONIS Investigational Site

Beverly Hills, California, United States

Site Status

IONIS Investigative Site

Encino, California, United States

Site Status

IONIS Investigative Site

Irvine, California, United States

Site Status

IONIS Investigational Site

Mountain View, California, United States

Site Status

IONIS Investigational Site

Santa Barbara, California, United States

Site Status

IONIS Investigative Site

Clearwater, Florida, United States

Site Status

IONIS Investigational Site

Tampa, Florida, United States

Site Status

IONIS Investigational Site

Augusta, Georgia, United States

Site Status

IONIS Investigational Site

Leawood, Kansas, United States

Site Status

IONIS Investigative Site

Chesterfield, Missouri, United States

Site Status

IONIS Investigative Site

New York, New York, United States

Site Status

IONIS Investigative Site

Philadelphia, Pennsylvania, United States

Site Status

IONIS Investigative Site

Philadelphia, Pennsylvania, United States

Site Status

IONIS Investigative Site

Pittsburgh, Pennsylvania, United States

Site Status

IONIS Investigational Site

Ladson, South Carolina, United States

Site Status

IONIS Investigative Site

Rapid City, South Dakota, United States

Site Status

IONIS Investigative Site

Arlington, Texas, United States

Site Status

IONIS Investigational Site

Austin, Texas, United States

Site Status

IONIS Investigative Site

Dallas, Texas, United States

Site Status

IONIS Investigative Site

Houston, Texas, United States

Site Status

IONIS Investigative Site

McAllen, Texas, United States

Site Status

IONIS Investigative Site

San Antonio, Texas, United States

Site Status

IONIS Investigative Site

The Woodlands, Texas, United States

Site Status

Eye Clinic Albury Wodonga

Albury, New South Wales, Australia

Site Status

IONIS Investigational Site

Liverpool, New South Wales, Australia

Site Status

Marsden Eye Specialists

Paramatta, New South Wales, Australia

Site Status

Strathfield Retina Clinic

Strathfield, New South Wales, Australia

Site Status

Sydney Eye Hospital

Sydney, New South Wales, Australia

Site Status

Sydney Retina Clinic Day Surgery

Sydney, New South Wales, Australia

Site Status

Royal Adelaide Hospital

Adelaide, South Australia, Australia

Site Status

The Royal Victorian Eye and Ear Hospital

East Melbourne, Victoria, Australia

Site Status

Retinology Institute

Glen Iris, Victoria, Australia

Site Status

Eye Surgery Associates

Malvern, Victoria, Australia

Site Status

Eye Surgery Associates

Parkville, Victoria, Australia

Site Status

Lions Eye Institute

Nedlands, Western Australia, Australia

Site Status

Auckland Eye

Auckland, , New Zealand

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Australia New Zealand

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

ISIS 696844-CS3

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.