ß-SPECIFIC 4 Patients: Study of Pediatric EffiCacy and Safety wIth FIrst-line Use of Canakinumab

NCT ID: NCT02296424

Last Updated: 2019-07-09

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

182 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-11-17

Study Completion Date

2017-09-25

Brief Summary

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The purpose of this study was to evaluate the efficacy observed with canakinumab dose reduction in a subgroup of patients in the extension study CACZ885G2301E1.

Detailed Description

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This two-part open-label study was to assess 2 different canakinumab taper regimens in patients with clinical remission (inactive disease for at least 24 continuous weeks) on canakinumab treatment without concomitant corticosteroids (CS) or methotrexate (MTX). The study was also to collect long term safety and tolerability data on SJIA patients treated with canakinumab.

Conditions

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Systemic Juvenile Idiopathic Arthritis (SJIA)

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

A two-part open-label study that collected long-term efficacy, safety, and tolerability data from SJIA patients receiving canakinumab treatment who had inactive disease at the last visit in Study CACZ885G2301E1 (Cohort 1), and from SJIA patients who were canakinumab treatment-naïve and had active disease at the time of screening for this study (Cohort 2)
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

No blinding was required in this open-label study

Study Groups

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Canakinumab Dose Reduction

All patients received canakinumab 4mg/kg (300 mg max) every 4 weeks in Part I of the study. Patients eligible for Part II of the study were randomized to one of two treatment arms. This is Treatment Arm 1 in Part II of the study: Canakinumab was administered at a reduced dose (2 mg/kg every 4 weeks). If the patient continued to maintain inactive disease for 24 additional weeks, canakinumab was administered at 1mg/kg every 4 weeks. If the patient continued to maintain inactive disease for another 24 additional weeks, canakinumab treatment was discontinued.

Group Type EXPERIMENTAL

ACZ885 150 mg (Canakinumab)

Intervention Type DRUG

Active canakinumab in individual 2 mL glass vials, each containing 150 mg canakinumab liquid in vial.

Canakinumab Dose Interval Prolongation

All participants received canakinumab 4mg/kg (300 mg max) every 4 weeks in Part I of the study. Patients eligible for Part II of the study were randomized to one of two treatment arms. This is Treatment Arm 2 in Part II of the study: Canakinumab dose interval was prolonged to a regimen of 4mg/kg every 8 weeks. If the patient continued to be stable with inactive disease for 24 additional weeks, canakinumab dose interval was prolonged to a regimen of 4mg/kg every 12 weeks. If the patient was clinically stable with inactive disease for another 24 additional weeks, canakinumab treatment was discontinued.

Group Type EXPERIMENTAL

ACZ885 150 mg (Canakinumab)

Intervention Type DRUG

Active canakinumab in individual 2 mL glass vials, each containing 150 mg canakinumab liquid in vial.

Interventions

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ACZ885 150 mg (Canakinumab)

Active canakinumab in individual 2 mL glass vials, each containing 150 mg canakinumab liquid in vial.

Intervention Type DRUG

Other Intervention Names

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ACZ885 150 mg

Eligibility Criteria

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Inclusion Criteria

Cohort 1:

• Patients who are receiving canakinumab treatment (4 mg/kg every 4 weeks) for Systemic Juvenile Idiopathic Arthritis (SJIA) and have inactive disease at the last visit in Study CACZ885G2301E1

Cohort 2:

* Confirmed diagnosis of SJIA as per International League Against Rheumatism (ILAR) definition that must have occurred at least 2 months prior to enrollment with an onset of disease \< 16 years of age.
* Active SJIA defined as having 2 or more of the following:
* Documented spiking, intermittent fever (body temperature \> 38°C) for at least 1 day within 1 week before first canakinumab dose;
* At least 2 joints with active arthritis
* C-reactive protein (CRP) \> 30 mg/L (normal range \< 10 mg/L)
* Rash due to SJIA
* Serositis
* Lymphadenopathy
* Hepatosplenomegaly
* Negative TB screen (QuantiFERON or, if required by local guidelines, Purified Protein Derivative).

Exclusion Criteria

* With active or recurrent bacterial, fungal or viral infection at the time of enrollment, including patients with evidence of Human Immunodeficiency Virus (HIV) infection, Hepatitis B and Hepatitis C infection.
* With underlying metabolic, renal, hepatic, infectious or gastrointestinal conditions which in the opinion of the investigator immunocompromises the patient and /or places the patient at unacceptable risk for participation.
* With neutropenia (absolute neutrophil count \< 1500/mm3) at screening.
Minimum Eligible Age

2 Years

Maximum Eligible Age

20 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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Novartis Investigative Site

Los Angeles, California, United States

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Columbus, Ohio, United States

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Vienna, , Austria

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Brussels, , Belgium

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Laken, , Belgium

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Leuven, , Belgium

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Curitiba, Paraná, Brazil

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Rio de Janeiro, Rio de Janeiro, Brazil

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São Paulo, São Paulo, Brazil

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Vancouver, British Colombia, Canada

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Toronto, Ontario, Canada

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Bron, , France

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Le Kremlin-Bicêtre, , France

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Paris, , France

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Sankt Augustin, North Rhine-Westphalia, Germany

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Berlin, , Germany

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Berlin, , Germany

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Freiburg im Breisgau, , Germany

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Giessen, , Germany

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Hamburg, , Germany

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Hamburg, , Germany

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Heidelberg, , Germany

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Tübingen, , Germany

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Budapest, , Hungary

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Budapest, , Hungary

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Haifa, , Israel

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Jerusalem, , Israel

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Kfar Saba, , Israel

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Petah Tikva, , Israel

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Ramat Gan, , Israel

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Bologna, BO, Italy

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Genova, GE, Italy

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Milan, MI, Italy

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Roma, RM, Italy

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Napoli, , Italy

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Utrecht, , Netherlands

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Warsaw, , Poland

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Moscow, , Russia

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Saint Petersburg, , Russia

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Málaga, Andalusia, Spain

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Esplugues de Llobregat, Barcelona, Spain

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Valencia, Valencia, Spain

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Madrid, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Stockholm, , Sweden

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Istanbul, TUR, Turkey (Türkiye)

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Ankara, , Turkey (Türkiye)

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Istanbul, , Turkey (Türkiye)

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Novartis Investigative Site

Izmir, , Turkey (Türkiye)

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Countries

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United States Austria Belgium Brazil Canada France Germany Hungary Israel Italy Netherlands Poland Russia Spain Sweden Turkey (Türkiye)

References

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Quartier P, Alexeeva E, Constantin T, Chasnyk V, Wulffraat N, Palmblad K, Wouters C, I Brunner H, Marzan K, Schneider R, Horneff G, Martini A, Anton J, Wei X, Slade A, Ruperto N, Abrams K; Paediatric Rheumatology International Trials Organisation and the Pediatric Rheumatology Collaborative Study Group. Tapering Canakinumab Monotherapy in Patients With Systemic Juvenile Idiopathic Arthritis in Clinical Remission: Results From a Phase IIIb/IV Open-Label, Randomized Study. Arthritis Rheumatol. 2021 Feb;73(2):336-346. doi: 10.1002/art.41488. Epub 2020 Dec 11.

Reference Type DERIVED
PMID: 32783351 (View on PubMed)

Other Identifiers

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2013-004867-29

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CACZ885G2306

Identifier Type: -

Identifier Source: org_study_id

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