A Study to Evaluate the Safety and Efficacy of CCX168 in Subjects With ANCA-Associated Vasculitis

NCT ID: NCT01363388

Last Updated: 2025-03-13

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

67 participants

Study Classification

INTERVENTIONAL

Study Start Date

2011-09-30

Study Completion Date

2016-01-31

Brief Summary

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The aim of this trial is to optimize the treatment to induce remission for patients with non-life-threatening anti-neutrophil cytoplasmic antibody vasculitis (AAV). The intent is to reduce the toxicity of induction therapy by reducing the overall exposure to or eliminating entirely the use of systemic corticosteroids during the induction period with an inhibitor of the complement C5a receptor plus cyclophosphamide or rituximab.

Detailed Description

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The primary safety objective of this study is to evaluate the safety and tolerability of CCX168 in subjects with AAV on background cyclophosphamide or rituximab treatment.

The primary efficacy objective is to evaluate the efficacy of CCX168 based on the Birmingham Vasculitis Activity Score (BVAS) version 3.

The secondary objectives of this study include assessment of the feasibility of reducing or eliminating the use of corticosteroids in the treatment of subjects with ANCA-associated vasculitis without the need for rescue corticosteroid measures and the effect of CCX168 on several disease parameters.

Study acquired by Amgen and all disclosures were done by previous sponsor ChemoCentryx.

Conditions

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Vasculitis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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Placebo

Placebo plus a full dose of oral glucocorticoids for steps 1 and 2 of the study

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

BID for 84 days

CCX168

30 mg Active study medication, plus either two-thirds reduced dose of oral glucocorticoids for step 1 of the study, or no oral glucocorticoids for step 2 of the study

Group Type EXPERIMENTAL

CCX168

Intervention Type DRUG

BID for 84 days

Interventions

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Placebo

BID for 84 days

Intervention Type DRUG

CCX168

BID for 84 days

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Clinical diagnosis of granulomatosis with polyangiitis (Wegener's), microscopic polyangiitis or renal limited vasculitis
* Male and postmenopausal or surgically sterile female subjects aged at least 18 years with new or relapsed AAV where treatment with cyclophosphamide or rituximab would be required
* Positive indirect immunofluorescence (IIF) test for P-ANCA or C-ANCA, or positive ELISA test for anti-proteinase-3 (PR3) or anti-myeloperoxidase (MPO) at screening
* Estimated glomerular filtration rate (eGFR) ≥ 20mL/min
* Have at least one "major" item, or at least 3 non-major items, or at least 2 renal items on the BVAS version 3

Exclusion Criteria

* Severe disease as determined by rapidly progressive glomerulonephritis, alveolar hemorrhage, hemoptysis, rapid-onset mononeuritis multiplex or central nervous system involvement
* Any other multi-system autoimmune disease
* Medical history of coagulopathy or bleeding disorder
* Received cyclophosphamide within 12 weeks of screening; if on azathioprine, mycophenolate mofetil or methotrexate at the time of screening, these drugs must be withdrawn prior to receiving the cyclophosphamide or rituximab dose on Day 1
* Received high-dose intravenous corticosteroids within 4 weeks of screening
* On an oral dose of a corticosteroid of more than 10mg prednisone-equivalent at the time of screening
* Received rituximab or other B-cell antibody within 52 weeks of screening or 26 weeks provided B cell reconstitution has occurred; received anti-TNF treatment, abatacept, alemtuzumab, IVIg or plasma exchange within 12 weeks of screening
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Amgen

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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MD

Role: STUDY_DIRECTOR

Amgen

Locations

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Feldkirch, , Austria

Site Status

Innsbruck, , Austria

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Linz, , Austria

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Brussels, , Belgium

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Edegem, , Belgium

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Ghent, , Belgium

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Leuven, , Belgium

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Liège, , Belgium

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Roeselare, , Belgium

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Prague, , Czechia

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Bordeaux, , France

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Boulogne-sur-Mer, , France

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Brest, , France

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Colmar, , France

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Grenoble, , France

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Nantes, , France

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Paris, , France

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Saint-Jacques, , France

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Valenciennes, , France

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Berlin, , Germany

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Cologne, , Germany

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Dresden, , Germany

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Freiburg im Breisgau, , Germany

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Fulda, , Germany

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Heidelberg, , Germany

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Budapest, , Hungary

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Groningen, , Netherlands

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Leiden, , Netherlands

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Rotterdam, , Netherlands

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Utrecht, , Netherlands

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Bialystok, , Poland

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Katowice, , Poland

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Szczecin, , Poland

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Wroclaw, , Poland

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Linköping, , Sweden

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Lund, , Sweden

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Malmo, , Sweden

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Stockholm, , Sweden

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Birmingham, , United Kingdom

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Cambridge, , United Kingdom

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London, , United Kingdom

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Manchester, , United Kingdom

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Oxford, , United Kingdom

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Reading, , United Kingdom

Site Status

Countries

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Austria Belgium Czechia France Germany Hungary Netherlands Poland Sweden United Kingdom

References

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Cravedi P, Leventhal J, Lakhani P, Ward SC, Donovan MJ, Heeger PS. Immune cell-derived C3a and C5a costimulate human T cell alloimmunity. Am J Transplant. 2013 Oct;13(10):2530-9. doi: 10.1111/ajt.12405. Epub 2013 Sep 6.

Reference Type DERIVED
PMID: 24033923 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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https://jasn.asnjournals.org/content/28/9/2756

Randomized Trial of C5a Receptor Inhibitor Avacopan in ANCA-Associated Vasculitis

Other Identifiers

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CL002_168

Identifier Type: -

Identifier Source: org_study_id

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